NCT03266588

Brief Summary

The purpose of this study is to evaluate safety and tolerability of BHV-3000 (rimegepant).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
3,019

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2017

Geographic Reach
1 country

98 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 23, 2017

Completed
7 days until next milestone

First Posted

Study publicly available on registry

August 30, 2017

Completed
Same day until next milestone

Study Start

First participant enrolled

August 30, 2017

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 15, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 15, 2019

Completed
12 months until next milestone

Results Posted

Study results publicly available

July 2, 2020

Completed
Last Updated

February 16, 2023

Status Verified

February 1, 2023

Enrollment Period

1.9 years

First QC Date

August 23, 2017

Results QC Date

June 16, 2020

Last Update Submit

February 14, 2023

Conditions

Outcome Measures

Primary Outcomes (2)

  • Number of Participants With SAEs and AEs Leading to Discontinuation During the Treatment Period

    An AE was defined as any new untoward medical occurrence or worsening of a pre-existing medical condition on-treatment in a patient or clinical investigation participant administered an investigational (medicinal) product and that did not necessarily have a causal relationship with this treatment. An SAE was defined as any event that met any of the following criteria: death; life-threatening; inpatient hospitalization or prolongation of existing hospitalization; persistent or significant disability/incapacity; congenital anomaly/birth defect in the offspring of a participant who received rimegepant; other important medical events that may not have resulted in death, be life-threatening, or required hospitalization, based upon appropriate medical judgment, they may have jeopardized the participant and may have required medical or surgical intervention.

    PRN (2-8) and PRN (9-14) groups: Up to 52 weeks; Scheduled EOD + PRN group: Up to 12 weeks

  • Number of Participants With Clinically Significant Laboratory Abnormalities During the Treatment Period

    Clinically significant laboratory abnormalities were defined as Grade 3 to 4 on-treatment laboratory test results according to numeric laboratory test criteria found in Common Technical Criteria for Adverse Events (CTCAE) Version 5.0 (2017) if available; otherwise, according to Division of Acquired Immune Deficiency Syndrome (DAIDS) Table for Grading the Severity of Adult and Pediatric Adverse Events Corrected Version 2.1 (2017) for Glucose, LDL-Cholesterol, Uric Acid, and Urinalysis. Laboratory test groups of clinical interest included hematology, serum chemistry, and urinalysis. Participants must have had a non-missing measurement in the on-treatment period to be included for a given parameter.

    PRN (2-8) and PRN (9-14) groups: Up to 52 weeks: Scheduled EOD + PRN group: Up to 12 weeks

Secondary Outcomes (2)

  • Percentage of Participants With Elevations of AST or ALT > 3 x Upper Limit of Normal (ULN) Concurrent With Total Bilirubin > 2 x ULN During the Treatment Period

    PRN (2-8) and PRN (9-14) groups: Up to 52 weeks; Scheduled EOD + PRN group: Up to 12 weeks

  • Number of Participants With Hepatic-related AEs and Hepatic-related AEs Leading to Discontinuation During the Treatment Period

    PRN (2-8) and PRN (9-14) groups: Up to 52 weeks; Scheduled EOD + PRN group: Up to 12 weeks

Study Arms (1)

Rimegepant

EXPERIMENTAL
Drug: Rimegepant

Interventions

75 mg oral tablet

Also known as: BHV-3000
Rimegepant

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects with 2-8 moderate to severe migraines/month
  • Age of onset of migraines prior to 50 years of age
  • Migraine attacks, on average, lasting 4-72 hours if untreated
  • Ability to distinguish migraine attacks from tension/cluster headaches
  • Patients with contraindications for use of triptans may be included provided they meet all other study entry criteria

You may not qualify if:

  • History of basilar migraine or hemiplegic migraine
  • History of HIV disease
  • History with current evidence of uncontrolled, unstable or recently diagnosed cardiovascular disease, such as ischemic heart disease, coronary artery vasospasm, and cerebral ischemia.
  • Uncontrolled hypertension or uncontrolled diabetes (however, patients can be included who have stable hypertension and /or diabetes for 3 months prior to screening
  • History of gastric or small intestinal surgery or has a disease that causes malabsorption
  • BMI ≥ 30
  • HbA1c ≥ 6.5%

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (98)

Central Research Associates, Inc

Birmingham, Alabama, 35205, United States

Location

Coastal Clinical Research, Inc.

Mobile, Alabama, 36608, United States

Location

Thunderbird Internal Medicine / Radiant Research, Inc

Glendale, Arizona, 85306, United States

Location

Neurological Physicians of Arizona

Tempe, Arizona, 85202, United States

Location

Clinical Research Consortium Arizona

Tempe, Arizona, 85283, United States

Location

Woodland International Research Group, LLC

Little Rock, Arkansas, 72211, United States

Location

Woodland Research Northwest, LLC

Rogers, Arkansas, 72758, United States

Location

Pharmacology Research Institute

Encino, California, 91316, United States

Location

eStudySite

La Mesa, California, 91942, United States

Location

Collaborative Neuroscience Network, LLC

Long Beach, California, 90806, United States

Location

Pharmacology Research Institute

Los Alamitos, California, 90720, United States

Location

Pharmacology Research Institute

Newport Beach, California, 92660, United States

Location

Pacific Research Partners LLC

Oakland, California, 94607, United States

Location

National Research Institute

Panorama City, California, 91402, United States

Location

Optimus Medical Group

San Francisco, California, 94102, United States

Location

California Medical Clinic for Headache

Santa Monica, California, 90404, United States

Location

California Neuroscience Research Medical Group, Inc.

Sherman Oaks, California, 91403, United States

Location

Diablo Clinical Research, Inc

Walnut Creek, California, 94598, United States

Location

Clinical Trials of the Rockies

Denver, Colorado, 80209, United States

Location

AGA Clinical Trials

Hialeah, Florida, 33012, United States

Location

Clinical Neuroscience Solutions, Inc.

Jacksonville, Florida, 32256, United States

Location

Multi-Specialty Research Associates, Inc

Lake City, Florida, 32055, United States

Location

Renstar Medical Research

Ocala, Florida, 34471, United States

Location

Clinical Neuroscience Solutions, Inc

Orlando, Florida, 32801, United States

Location

Compass Research, LLC

Orlando, Florida, 32806, United States

Location

Ormond Medical Arts Pharmaceutical Research

Ormond Beach, Florida, 32174, United States

Location

Meridien Research

Tampa, Florida, 33634, United States

Location

Radiant Research, Inc.

Atlanta, Georgia, 30328, United States

Location

Meridian Clinical Research

Savannah, Georgia, 31406, United States

Location

Savannah Neurology Specialists

Savannah, Georgia, 31406, United States

Location

Christie Clinic, LLC

Champaign, Illinois, 61820, United States

Location

PMG Research of McFrland Clinic

Ames, Iowa, 50010, United States

Location

Heartland Research Associates, LLC

Augusta, Kansas, 67010, United States

Location

Heartland Research Associates, LLC

Newton, Kansas, 67114, United States

Location

Heartland Research Associates, LLC

Wichita, Kansas, 67205, United States

Location

Heartland Research Associates, LLC

Wichita, Kansas, 67207, United States

Location

Benchmark Research

Metairie, Louisiana, 70006, United States

Location

MedPharmics, LLC

Metairie, Louisiana, 70006, United States

Location

New Orleans Center for Clinical Research

New Orleans, Louisiana, 70119, United States

Location

Boston Clinical Trials, Inc.

Boston, Massachusetts, 02131, United States

Location

NECCR Primacare Research, LLC

Fall River, Massachusetts, 02721, United States

Location

Milford Emergency Associates, Inc.

Marlborough, Massachusetts, 01752, United States

Location

Michigan Head Pain and Neurological Institute

Ann Arbor, Michigan, 48104, United States

Location

Clinical Research Institute, Inc.

Minneapolis, Minnesota, 55402, United States

Location

Clinical Research Insitute

Plymouth, Minnesota, 55441, United States

Location

The Center for Pharmaceutical Research

Kansas City, Missouri, 64114, United States

Location

Sundance Clinical Research, LLC

St Louis, Missouri, 63141, United States

Location

Meridian Clinical Research -Norfolk

Norfolk, Nebraska, 68701, United States

Location

Meridian Clinical Research, LLC

Omaha, Nebraska, 68134, United States

Location

Clinical Research Consortium- Las Vegas

Las Vegas, Nevada, 89119, United States

Location

Hassman Research Institute, LLC

Berlin, New Jersey, 08009, United States

Location

Albuquerque Neuroscience, Inc.

Albuquerque, New Mexico, 87109, United States

Location

United Medical Associates

Binghamton, New York, 13901, United States

Location

SPRI Clinical Trials, LLC

Brooklyn, New York, 11235, United States

Location

Regional Clinical Research, Inc.

Endwell, New York, 13760, United States

Location

Radiant Research, Inc.

Jamaica, New York, 11432, United States

Location

Central New York Clinical Research

Manlius, New York, 13104, United States

Location

Fieve Clinical Research

New York, New York, 10168, United States

Location

Rochester Clinical Research, Inc

Rochester, New York, 14609, United States

Location

Montefiore Heachache Center

The Bronx, New York, 10461, United States

Location

PMG Research of Charlotte, LLC

Charlotte, North Carolina, 28209, United States

Location

PharmQuest, LLC

Greensboro, North Carolina, 27408, United States

Location

PMG Research of Raleigh, LLC

Raleigh, North Carolina, 27609, United States

Location

Wake Research Associates, LLC

Raleigh, North Carolina, 27612, United States

Location

PMG Research of Wilmington, LLC

Wilmington, North Carolina, 28401, United States

Location

CTI Clinical Research Center

Cincinnati, Ohio, 45227, United States

Location

Radiant Research, Inc.

Cincinnati, Ohio, 45236, United States

Location

Radiant Research, Inc.

Columbus, Ohio, 43212, United States

Location

Midwest Clinical Research Center

Dayton, Ohio, 45417, United States

Location

Neurology Diagnostics, Inc.

Dayton, Ohio, 45459, United States

Location

Aventiv Research, Inc.

Dublin, Ohio, 43016, United States

Location

Summit Research Network (Oregon), Inc.

Portland, Oregon, 97210, United States

Location

Oregon Center for Clinical Investigations, Inc

Salem, Oregon, 97301, United States

Location

Clinical Research of Philadelphia, LLC

Philadelphia, Pennsylvania, 19114, United States

Location

Fieve Clinical Research

Scranton, Pennsylvania, 18503, United States

Location

Preferred Primary Care Physicians

Uniontown, Pennsylvania, 15401, United States

Location

Omega Medical Research

Warwick, Rhode Island, 02886, United States

Location

Radiant Research, Inc.

Anderson, South Carolina, 29621, United States

Location

Coastal Carolina Research Center

Mt. Pleasant, South Carolina, 29464, United States

Location

Meridian Clinical Research

Dakota Dunes, South Dakota, 57049, United States

Location

PMG Research of Bristol, LLC

Bristol, Tennessee, 37620, United States

Location

Clinical Neuroscience Solutions, Inc

Memphis, Tennessee, 38119, United States

Location

Clinical Research Associates, Inc.

Nashville, Tennessee, 37203, United States

Location

FutureSearch Trials of Neurology, LP

Austin, Texas, 78731, United States

Location

Tekton Research- Austin

Austin, Texas, 78745, United States

Location

FutureSearch Trials of Neurology, LP

Dallas, Texas, 75231, United States

Location

Ventavia Research Group, LLC

Fort Worth, Texas, 76104, United States

Location

Texas Center for Drug Development

Houston, Texas, 77081, United States

Location

Red Star Research, LLC

Lake Jackson, Texas, 77566, United States

Location

FMC Science

Lampasas, Texas, 76550, United States

Location

PCP for Life

Magnolia, Texas, 77355, United States

Location

Research Across America - Mesquite

Mesquite, Texas, 75149, United States

Location

Doctors of Internal Medicine, LTD / Radiant Research Inc.

Plano, Texas, 75093, United States

Location

DM Clinical Research

Tomball, Texas, 77375, United States

Location

J.Lewis Research Inc / Foothill Family Clinic South

Salt Lake City, Utah, 84121, United States

Location

Tidewater Integrated Medical Research

Virginia Beach, Virginia, 23454, United States

Location

Northwest Clinical Research Center

Bellevue, Washington, 98007, United States

Location

Seattle Women's:Health, Research & Gynecology

Seattle, Washington, 98105, United States

Location

Related Publications (8)

  • Ailani J, Pavlovic J, Pixton GC, Fullerton T. Rimegepant safety and patient-reported outcomes among triptan-naive, triptan-using, and triptan-failure participants: Subgroup analysis of an open-label, multicenter study. Cephalalgia. 2025 Jul;45(7):3331024251343309. doi: 10.1177/03331024251343309. Epub 2025 Jul 9.

  • Kudrow D, Hutchinson S, Pixton GC, Fullerton T. Safety of Rimegepant in Adults with Migraine and Anxiety, Depression, or Using Antidepressants: Analysis of a Multicenter, Long-Term, Open-Label Study. Pain Ther. 2025 Feb;14(1):237-255. doi: 10.1007/s40122-024-00675-6. Epub 2024 Nov 9.

  • True D, Mullin K, Croop R. Safety of Rimegepant in Adults with Migraine and Cardiovascular Risk Factors: Analysis of a Multicenter, Long-Term, Open-Label Study. Pain Ther. 2024 Oct;13(5):1203-1218. doi: 10.1007/s40122-024-00626-1. Epub 2024 Jul 10.

  • Fullerton T, Pixton G. Long-Term Use of Rimegepant 75 mg for the Acute Treatment of Migraine is Associated with a Reduction in the Utilization of Select Analgesics and Antiemetics. J Pain Res. 2024 May 15;17:1751-1760. doi: 10.2147/JPR.S456006. eCollection 2024.

  • Croop R, Berman G, Kudrow D, Mullin K, Thiry A, Lovegren M, L'Italien G, Lipton RB. A multicenter, open-label long-term safety study of rimegepant for the acute treatment of migraine. Cephalalgia. 2024 Apr;44(4):3331024241232944. doi: 10.1177/03331024241232944.

  • Johnston K, Harris L, Powell L, Popoff E, Coric V, L'Italien G, Schreiber CP. Monthly migraine days, tablet utilization, and quality of life associated with Rimegepant - post hoc results from an open label safety study (BHV3000-201). J Headache Pain. 2022 Jan 17;23(1):10. doi: 10.1186/s10194-021-01378-5.

  • Johnston KM, L'Italien G, Popoff E, Powell L, Croop R, Thiry A, Harris L, Coric V, Lipton RB. Mapping Migraine-Specific Quality of Life to Health State Utilities in Patients Receiving Rimegepant. Adv Ther. 2021 Oct;38(10):5209-5220. doi: 10.1007/s12325-021-01897-2. Epub 2021 Aug 29.

  • Mullin K, Kudrow D, Croop R, Lovegren M, Conway CM, Coric V, Lipton RB. Potential for treatment benefit of small molecule CGRP receptor antagonist plus monoclonal antibody in migraine therapy. Neurology. 2020 May 19;94(20):e2121-e2125. doi: 10.1212/WNL.0000000000008944. Epub 2020 Jan 13.

MeSH Terms

Conditions

Migraine Disorders

Interventions

rimegepant sulfate

Condition Hierarchy (Ancestors)

Headache Disorders, PrimaryHeadache DisordersBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Results Point of Contact

Title
Chief Medical Officer
Organization
Biohaven Pharmaceuticals, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 23, 2017

First Posted

August 30, 2017

Study Start

August 30, 2017

Primary Completion

July 15, 2019

Study Completion

July 15, 2019

Last Updated

February 16, 2023

Results First Posted

July 2, 2020

Record last verified: 2023-02

Data Sharing

IPD Sharing
Will not share

Locations