NCT03257046

Brief Summary

This is a Phase I/II randomized, double-blind, placebo-controlled, multiple rising dose study in patients with stable idiopathic Parkinson's disease (PD) to evaluate the safety, tolerability, pharmacokinetics and pharmacodynamics of ITI-214.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
40

participants targeted

Target at P50-P75 for phase_1 parkinson-disease

Timeline
Completed

Started Sep 2017

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 14, 2017

Completed
8 days until next milestone

First Posted

Study publicly available on registry

August 22, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

September 28, 2017

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 6, 2018

Completed
22 days until next milestone

Study Completion

Last participant's last visit for all outcomes

September 28, 2018

Completed
Last Updated

December 20, 2018

Status Verified

December 1, 2018

Enrollment Period

11 months

First QC Date

August 14, 2017

Last Update Submit

December 18, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of patients with reported or observed treatment-related adverse events

    Safety and tolerability

    7 days

Secondary Outcomes (3)

  • Maximum Plasma Concentration (Cmax)

    7 days

  • Area of the Curve (AUC)

    7 days

  • Motor and non-motor symptoms as assessed by the MDS-UPDRS

    7 days

Other Outcomes (1)

  • Exploratory biomarkers

    7 days

Study Arms (6)

1 mg ITI-214

EXPERIMENTAL

Administered once daily for 7 days

Drug: ITI-214

3 mg ITI-214

EXPERIMENTAL

Administered once daily for 7 days

Drug: ITI-214

10 mg ITI-214

EXPERIMENTAL

Administered once daily for 7 days

Drug: ITI-214

30 mg ITI-214

EXPERIMENTAL

Administered once daily for 7 days

Drug: ITI-214

90 mg ITI-214

EXPERIMENTAL

Administered once daily for 7 days

Drug: ITI-214

Placebo

PLACEBO COMPARATOR

Administered once daily for 7 days

Other: Placebo

Interventions

Oral

1 mg ITI-21410 mg ITI-2143 mg ITI-21430 mg ITI-21490 mg ITI-214
PlaceboOTHER

Oral

Placebo

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Clinical diagnosis of idiopathic Parkinson's disease (PD)
  • Severity of PD assessed by Hoehn and Yahr Staging score of 1 to 3
  • Maintenance on stable PD therapy

You may not qualify if:

  • Clinical signs of dementia
  • Suicidal ideation or behavior
  • Considered medically inappropriate for study participation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Atlanta Center for Medical Research

Atlanta, Georgia, 30331, United States

Location

Duke Early Phase Research Unit

Durham, North Carolina, 27708, United States

Location

MeSH Terms

Conditions

Parkinson Disease

Interventions

ITI-214

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Study Officials

  • Kimberly Vanover, PhD

    Intra-Cellular Therapies, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Multiple rising dose in sequential cohorts of 8 patients randomized in a 6:2 ratio to receive ITI-214 or placebo
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 14, 2017

First Posted

August 22, 2017

Study Start

September 28, 2017

Primary Completion

September 6, 2018

Study Completion

September 28, 2018

Last Updated

December 20, 2018

Record last verified: 2018-12

Locations