NCT03249480

Brief Summary

To Evaluate the safety and efficacy of PEG Somatropin in the treatment of children with growth hormone deficiency, as well as to study the dosage of PEG Somatropin.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
900

participants targeted

Target at P75+ for phase_4

Geographic Reach
1 country

28 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2015

Completed
2.6 years until next milestone

First Submitted

Initial submission to the registry

July 24, 2017

Completed
8 days until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2017

Completed
14 days until next milestone

First Posted

Study publicly available on registry

August 15, 2017

Completed
Last Updated

August 15, 2017

Status Verified

July 1, 2017

Enrollment Period

2.6 years

First QC Date

July 24, 2017

Last Update Submit

August 10, 2017

Conditions

Outcome Measures

Primary Outcomes (3)

  • Ht SDSca (Height Standard Deviation Score for Chronological Age)

    Ht SDSca was calculated by dividing the difference between the actual height of a patient and the mean height of the population for that chronological age by the standard deviation (SD) of the height of the population for that chronological age

    Baseline

  • Change of yearly growth velocity from baseline to 26 weeks

    Height velocity calculate by formula

    Baseline, 26 weeks after initiating treatment

  • Ht SDSca

    Ht SDSca was calculated by dividing the difference between the actual height of a patient and the mean height of the population for that chronological age by the standard deviation (SD) of the height of the population for that chronological age

    26 weeks after initiating treatment

Secondary Outcomes (4)

  • Ht SDSBA (Height Standard Deviation Score for Bone Age)

    Baseline,26 weeks after initiating treatment

  • IGF-1 SDS (IGF-1 Standard Deviation Score)

    Baseline,26 weeks after initiating treatment

  • IGFBP-3 SDS (IGFBP-3 Standard Deviation Score)

    Baseline,26 weeks after initiating treatment

  • Skeletal maturity

    Baseline,26 weeks after initiating treatment

Study Arms (1)

PEG-somatropin

EXPERIMENTAL

30IU/10 mg/3ml/kit, 0.1-0.2mg /kg/w, once per day for 26 weeks.

Biological: PEG-somatropin

Interventions

PEG-somatropinBIOLOGICAL

30IU/10 mg/3ml/kit, 0.1-0.2mg /kg/w, once per day for 26 weeks.

PEG-somatropin

Eligibility Criteria

Age3 Years - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Diagnosed as GHD before starting treatment, according to medical history, clinical symptoms and signs, GH provocation tests and imaging and other examinations:
  • According to statistical height data of physical development of Chinese children in nine cities in 2005, the height is lower than 3rd percentile growth curve of the same age, same sex normal children;
  • Height velocity (HV) ≤5.0 cm / yr;
  • GH provocative tests (with two drugs of different mechanism of action) confirmed plasma GH peak \<10.0 ng / ml;
  • bone age for girl≤9 years old, for Boy≤10 years old, bone age is one year or more later than the actual age, that is the actual age - bone age ≥ 1 year;
  • Before puberty (Tanner I stage), age≥3 years old, male or female;
  • Have not received hormone therapy within 6 months;
  • Subjects is willing and able to cooperate to complete scheduled visits, treatment plans and laboratory tests and other procedures, to sign informed consent.

You may not qualify if:

  • Dysfunction of liver and kidney (ALT\> 2 times the upper limit of normal, Cr\> upper limit of normal);
  • Patients positive for hepatitis B c-antibody (HBcAb), hepatitis B surface antigen (HBsAg) or hepatitis B e antigen (HBeAg);
  • Patients with known hypersensitivity to PEG Somatropin or Somatropin or any other components of the study product;
  • Patients with severe cardiopulmonary or hematological diseases, a current or past history of malignant tumors, immunodeficiency diseases, or mental diseases;
  • Potential cancer patients (family history);
  • Patients with diabetics;
  • Patients with other growth disorders, such as Turner's syndrome, sexual physical delayed puberty, Laron syndrome, growth hormone receptor deficiency, girls with slowly growing who did not rule out chromosomal abnormalities;
  • Patients with congenital bone dysplasia or scoliosis;
  • Subjects took part in other clinical trial study during 3 months;
  • Other conditions in which the investigator preclude enrollment into the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

Anhui Provincial Children's Hospital

Hefei, Anhui, China

RECRUITING

Fuzhou Children s Hospital

Fuzhou, Fujian, China

RECRUITING

Sun Yat-Sen Memorial Hospital

Guangzhou, Guangdong, China

RECRUITING

The Second Hospital of Hebei Medical University

Shijiangzhuang, Hebei, China

RECRUITING

Children's Hospital of Hebei Province

Shijiazhuang, Hebei, China

RECRUITING

The First Affiliated Hospital of Harbin Medical University

Harbin, Heilongjiang, China

RECRUITING

Children's Hospital of Zhengzhou

Zhengzhou, Henan, China

RECRUITING

Henan Provincal People's Hospital

Zhengzhou, Henan, China

RECRUITING

The First Affiliated Hospital of Henan University of TCM

Zhengzhou, Henan, China

RECRUITING

Union Hospital, Tongji Medical College, HUST

Wuhan, Hubei, China

RECRUITING

Wuhan Children's Hospital

Wuhan, Hubei, China

RECRUITING

Hunan Children's Hospital

Changsha, Hunan, China

RECRUITING

Maternal & Child Health Hospital of Guangxi Zhuang Autonomous Region

Nanjing, Jiangsu, China

RECRUITING

Nanjing Children's Hospital

Nanjing, Jiangsu, China

RECRUITING

Children's Hospital of Soochow University

Suzhou, Jiangsu, China

RECRUITING

Wuxi Children's Hospital

Wuxi, Jiangsu, China

RECRUITING

Xuzhou Children's Hpspital

Xuzhou, Jiangsu, China

RECRUITING

Dalian Children's Hospital

Dalian, Liaoning, China

RECRUITING

The Second Affiliated Hospital of Xi'an Jiaotong University

Xi’an, Shanxi, China

RECRUITING

Xi'an Children's Hospital

Xi’an, Shanxi, China

RECRUITING

First Affiliated Hospital of Kunming Medical University

Kunming, Yunnan, China

RECRUITING

Kunming Children's Hospital

Kunming, Yunnan, China

RECRUITING

Second Affiliated Hospital of Kunming Medical University

Kunming, Yunnan, China

RECRUITING

The First People's Hospital of Yunnan Province

Kunming, Yunnan, China

RECRUITING

China-Japan Friendship Hospital

Beijing, China

RECRUITING

Peking University Third Hospital

Beijing, China

RECRUITING

Shenzhen Children's Hospital

Shenzhen, China

RECRUITING

Tianjin Medical University General Hospital

Tianjin, China

RECRUITING

Related Publications (1)

  • Chen J, Zhong Y, Wei H, Chen S, Su Z, Liu L, Liang L, Lu P, Chen L, Chen R, Ni S, Wang X, Li L, Wang Y, Xu X, Xiao Y, Yao H, Liu G, Jin R, Cao B, Wu D, Su C, Li W, Qin M, Li X, Luo X, Gong C. Polyethylene glycol recombinant human growth hormone in Chinese prepubertal slow-growing short children: doses reported in a multicenter real-world study. BMC Endocr Disord. 2022 Aug 9;22(1):201. doi: 10.1186/s12902-022-01101-8.

MeSH Terms

Conditions

Dwarfism, Pituitary

Condition Hierarchy (Ancestors)

DwarfismBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesBone Diseases, EndocrineHypopituitarismPituitary DiseasesHypothalamic DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesEndocrine System Diseases

Study Officials

  • Chunxiu Gong

    Beijing Children's Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 24, 2017

First Posted

August 15, 2017

Study Start

January 1, 2015

Primary Completion

August 1, 2017

Last Updated

August 15, 2017

Record last verified: 2017-07

Locations