NCT03232177

Brief Summary

This study is to evaluate the efficacy and safety according to incremental dosing for 8 weeks and duration of administration for 1 year in patients with high-risk essential thrombocythemia.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
70

participants targeted

Target at P25-P50 for phase_4

Timeline
Completed

Started Jun 2017

Longer than P75 for phase_4

Geographic Reach
1 country

21 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 5, 2017

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

July 11, 2017

Completed
16 days until next milestone

First Posted

Study publicly available on registry

July 27, 2017

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 5, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 5, 2020

Completed
Last Updated

July 21, 2021

Status Verified

July 1, 2021

Enrollment Period

3.5 years

First QC Date

July 11, 2017

Last Update Submit

July 20, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • response rate for less than 60 X 10^4/ul in platelet count

    at week 8

Secondary Outcomes (5)

  • response rate for less than 60 X 10^4/ul in platelet count

    at week 52

  • changes from baseline in 50% reduction rate in platelet count

    up to 52 weeks

  • response rate for less than 40 X 10^4/ul in platelet count

    up to 52 weeks

  • cumulative incidence of essential thrombocythemia related events (e.g thromboembolic or hemorrhagic events)

    at 52 week

  • incidence of adverse events

    up to 52 weeks

Other Outcomes (2)

  • expression of MPN-oncogene(JAK2/CALR/MPL)

    at 52 week

  • genomic biomarker search for prediction of side effects of anagrelide

    at 52 week

Study Arms (1)

Anagre Cap.

EXPERIMENTAL

twice a day

Drug: Anagre Cap.

Interventions

from 0.5mg twice a day to maximally increase total10mg in 8 weeks and maintain maximal tolerable dose to 104 weeks

Anagre Cap.

Eligibility Criteria

Age19 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients with essential thrombocythemia according to WHO 2008
  • Any of the following as high-risk patient
  • Over 60 years old
  • \>100 X 10\^4/ul of platelet count
  • increased more than 300K of platelet count in 3 months
  • Hypertension, diabetes, past history of thromboembolic bleeding

You may not qualify if:

  • Patients with an adverse drug reaction or intolerability to anagrelide
  • Any of the following cardiac abnormalities;
  • Complete left bundle branch block on ECG
  • Patients using a pacemaker
  • Patients with a family history of congenital QT prolongation syndrome or known QT prolongation syndrome
  • Currently, there is no clinically uncontrolled ventricular or atrial tachycardia
  • Clinically significant bradycardia (\<less than 50 per minute)
  • History of clinically proven myocardial infarction and unstable angina within 3 months
  • Pregnant women, nursing mothers

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (21)

National Health Insurance Service Ilsan Hospital

Goyang-si, Gyeonggi-do, South Korea

Location

The Catholic University of Korea. ST. Vincents Hospital

Suwon, Gyeonggi-do, South Korea

Location

Hallym UNIV. Medical Center

Anyang, South Korea

Location

Daegu Catholic University Medical Center

Daegu, South Korea

Location

Keimyung University Dongsan Medical Center

Daegu, South Korea

Location

Kyungpook national university hospital

Daegu, South Korea

Location

Dongguk University Medical Center

Goyang, South Korea

Location

Cheonnam National University Hwasun Hospital

Hwasun, South Korea

Location

Gachon University Gil Medical Center

Incheon, South Korea

Location

Inha University Hospital

Incheon, South Korea

Location

Jeju National University Hospital

Jeju City, South Korea

Location

Pusan National University Hospital

Pusan, South Korea

Location

Ewha Wonans University Mokdong Hospital

Seoul, South Korea

Location

Hallym UNIV. Medical Center

Seoul, South Korea

Location

Inje University Sanggye Paik Hospital

Seoul, South Korea

Location

Korea University Anam Hospital

Seoul, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

SMG - SNU Boramae Medical Center

Seoul, South Korea

Location

Soon Chun Hyang University Hospital Seoul

Seoul, South Korea

Location

Veterans Health Service medical Center

Seoul, South Korea

Location

Yonsei University Health System, SEVERANCE HOSPITAL

Seoul, South Korea

Location

MeSH Terms

Conditions

Thrombocythemia, Essential

Condition Hierarchy (Ancestors)

Blood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesThrombocytosisBlood Platelet DisordersMyeloproliferative DisordersBone Marrow DiseasesHemorrhagic Disorders

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 11, 2017

First Posted

July 27, 2017

Study Start

June 5, 2017

Primary Completion

December 5, 2020

Study Completion

December 5, 2020

Last Updated

July 21, 2021

Record last verified: 2021-07

Data Sharing

IPD Sharing
Will not share

Locations