NCT03196427

Brief Summary

The purpose of this study is to determine the safety profile of long-term vedolizumab IV treatment in pediatric participants with UC or CD.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
59

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jul 2018

Longer than P75 for phase_2

Geographic Reach
7 countries

23 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 20, 2017

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 22, 2017

Completed
1.1 years until next milestone

Study Start

First participant enrolled

July 30, 2018

Completed
6.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 3, 2025

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 17, 2025

Completed
8 months until next milestone

Results Posted

Study results publicly available

March 13, 2026

Completed
Last Updated

March 13, 2026

Status Verified

February 1, 2026

Enrollment Period

6.7 years

First QC Date

June 20, 2017

Results QC Date

January 14, 2026

Last Update Submit

February 20, 2026

Conditions

Keywords

Drug Therapy

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Treatment-emergent Adverse Events (TEAEs)

    AE defined as any untoward medical occurrence in clinical investigation participants administered drug; it does not necessarily have to have causal relationship with this treatment. An AE can therefore be any unfavorable and unintended sign (example, a clinically significant abnormal laboratory finding), symptom, or disease temporally associated with the use of a drug whether or not it was considered related to the drug. TEAE was defined as an AE whose date of onset occurred on or after the first dose of study drug, or an already-present AE that worsened in intensity or frequency following the treatment start, occurring from the first dose of study drug to the day of last dose of study drug.

    From first dose of study drug up to end of follow up (up to 6.8 years)

Secondary Outcomes (15)

  • Percentage of Participants With UC Who Achieved and Maintained Clinical Response Based on Complete Mayo Score

    At Week 32

  • Percentage of Participants With CD Who Achieved and Maintained Clinical Response Based on Simple Endoscopic Score for Crohn's Disease (SES-CD) Score and Crohn's Disease Activity Index (CDAI) at Week 32

    At Week 32

  • Time to Major Inflammatory Bowel Disease (IBD) - Related Events

    Up to 6.8 years

  • Change From Baseline in IMPACT-III - Total Score

    Baseline, Weeks 24, 48, 72, 96, 120, 144, 168, 192, 216, 240, 264, 288, and 312

  • Change From Baseline in IMPACT-III - Bowel Symptoms Domain Score

    Baseline, Weeks 24, 48, 72, 96, 120, 144, 168, 192, 216, 240, 264, 288, and 312

  • +10 more secondary outcomes

Study Arms (2)

Vedolizumab High Dose Group

EXPERIMENTAL

Participants with UC or CD having baseline weight of greater than or equal to (\>=) 30 kilogram (kg) will receive vedolizumab 300 mg and participants with UC or CD having baseline weight of less than (\<) 30 kg will receive vedolizumab 200 mg, IV infusion, every 8 weeks until vedolizumab IV is commercially available for pediatric indication(s) in the participant's country or until other drug access programs become available (whichever comes first), the participant turns 18 years of age and can be transitioned to commercial drug (up to approximately 8 years).

Drug: Vedolizumab

Vedolizumab Low Dose Group

EXPERIMENTAL

Participants with UC or CD having baseline weight of \>= 30 kg will receive vedolizumab 150 mg and participants with UC or CD having baseline weight of \< 30 kg will receive vedolizumab 100 mg IV infusion, every 8 weeks until vedolizumab IV is commercially available for pediatric indication(s) in the participant's country or until other drug access programs become available (whichever comes first), the participant turns 18 years of age and can be transitioned to commercial drug (up to approximately 8 years).

Drug: Vedolizumab

Interventions

Vedolizumab intravenous infusion

Also known as: MLN0002, ENTYVIO, KYNTELES
Vedolizumab High Dose GroupVedolizumab Low Dose Group

Eligibility Criteria

Age2 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Is male or female with UC or CD and was between 2 to 17 years, inclusive, at the time of randomization for Study MLN0002-2003.

You may not qualify if:

  • Has completed Study MLN0002-2003 and, at Week 22, achieved clinical response as defined by a reduction of partial Mayo score of \>=2 points and \>=25% from Baseline, or a reduction of the Paediatric Ulcerative Colitis Activity Index (PUCAI) of \>=20 points from baseline for participants with UC; or a reduction of the CDAI as defined by a \>=70-point decrease from Baseline or a decrease of Pediatric Crohn's Disease Activity Index (PCDAI) of \>=15 points for participants with CD.
  • May be receiving a therapeutic dose of the following drugs:
  • Oral 5-aminosalicylic acid (5-ASA) compounds.
  • Oral corticosteroid therapy (prednisone or equivalent steroid at a dose less than or equal to \[\<=\] 50 milligram per day \[mg/day\]) provided the participant was receiving this medication during prior participation in MLN0002-2003.
  • Topical (rectal) treatment with 5-ASA or corticosteroids.
  • Probiotics (example, Saccharomyces boulardii).
  • Antidiarrheals (example, loperamide, diphenoxylate with atropine) for control of chronic diarrhea.
  • Antibiotics used for the treatment of CD (i.e., ciprofloxacin, metronidazole).
  • Azathioprine (AZA) or 6-mercaptopurine (6-MP) or methotrexate (MTX), provided the participant was receiving this medication during prior participation in MLN0002-2003.
  • Is female and is lactating or pregnant.
  • Has hypersensitivity or allergies to vedolizumab or any of its excipients.
  • Has withdrawn from Study MLN0002-2003.
  • Has developed any new unstable or uncontrolled cardiovascular, heart failure moderate to severe (New York Class Association III or IV), pulmonary, hepatic, renal, gastrointestinal (GI), genitourinary, hematological, coagulation, immunological, endocrine/metabolic, neurological, or other medical disorder that, in the opinion of the investigator, would confound the study results or compromise participant safety.
  • Has a positive progressive multifocal leukoencephalopathy (PML) subjective symptom checklist prior to the administration of the first dose of study drug.
  • Currently requires major surgical intervention for UC or CD (example, bowel resection), or is anticipated to require major surgical intervention for UC or CD during the study.
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Children's Hospital of Orange County

Orange, California, 92868, United States

Location

University of California San Francisco

San Francisco, California, 94158, United States

Location

Connecticut Children's Medical Center

Hartford, Connecticut, 06106-3322, United States

Location

Nemours Childrens Specialty Care - Jacksonville

Jacksonville, Florida, 32207, United States

Location

Children's Center for Digestive Healthcare

Atlanta, Georgia, 30342, United States

Location

Columbia University Medical Center

New York, New York, 10031, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98105, United States

Location

Hopital Necker-Enfants Malades

Paris, Île-de-France Region, 75015, France

Location

BAZ Megyei Korhaz es Egyetemi Oktatokorhaz

Miskolc, Borsod-Abauj Zemplen county, 3526, Hungary

Location

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont

Szeged, Csongrád megye, 6720, Hungary

Location

Debreceni Egyetem Klinikai Kozpont

Debrecen, Hajdú-Bihar, 4032, Hungary

Location

The Edmond and Lily Safra Children's Hospital - Sheba Medical Center

Ramat Gan, Tel Aviv, 52621, Israel

Location

Carmel Medical Center

Haifa, 3436212, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 9103102, Israel

Location

Schneider Children's Medical Center of Israel

Petach Tiqwa, 4920235, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 6423906, Israel

Location

Uniwersytecki Szpital Dzieciecy w Krakowie

Krakow, Lesser Poland Voivodeship, 30-663, Poland

Location

Gabinet Lekarski Dr. Hab. N. Med. Bartosz Korczowski

Rzeszów, Podkarpackie Voivodeship, 35-302, Poland

Location

Centralny Szpital Kliniczny Uniwersytetu Medycznego w Lodzi Osrodek Pediatryczny im Marii Konopnic

Lodz, Łódź Voivodeship, 91-738, Poland

Location

Kharkiv Regional Clinical Children's Hospital

Kharkiv, 61093, Ukraine

Location

Barts and The London NHS Trust

London, England, E1 1BB, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Colitis, UlcerativeCrohn Disease

Interventions

vedolizumab

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Results Point of Contact

Title
Medical Director
Organization
Takeda

Study Officials

  • Study Director

    Takeda

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 20, 2017

First Posted

June 22, 2017

Study Start

July 30, 2018

Primary Completion

April 3, 2025

Study Completion

July 17, 2025

Last Updated

March 13, 2026

Results First Posted

March 13, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Takeda provides access to the de-identified individual participant data (IPD) for eligible studies to aid qualified researchers in addressing legitimate scientific objectives (Takeda's data sharing commitment is available on https://clinicaltrials.takeda.com/takedas-commitment?commitment=5). These IPDs will be provided in a secure research environment following approval of a data sharing request, and under the terms of a data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Access Criteria
IPD from eligible studies will be shared with qualified researchers according to the criteria and process described on https://vivli.org/ourmember/takeda/. For approved requests, the researchers will be provided access to anonymized data (to respect patient privacy in line with applicable laws and regulations) and with information necessary to address the research objectives under the terms of a data sharing agreement.
More information

Locations