NCT03196375

Brief Summary

The COMMEND Study will assess the safety and effectiveness of FLX-787 in men and women with Motor Neuron Disease \[including Amyotrophic Lateral Sclerosis (ALS), Primary Lateral Sclerosis (PLS) or Progressive Muscular Atrophy (PMA)\] experiencing muscle cramps. Participants will be asked to take two study products during the course of the study. One of these study products will be a placebo. Approximately 120 participants in approximately 30 study centers across the United States are expected to take part. Participants will be in the study for approximately 3 months and visit the study clinic 3 times.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
54

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jul 2017

Shorter than P25 for phase_2

Geographic Reach
1 country

35 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 20, 2017

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 22, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

July 28, 2017

Completed
12 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 27, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 27, 2018

Completed
Last Updated

August 29, 2018

Status Verified

August 1, 2018

Enrollment Period

12 months

First QC Date

June 20, 2017

Last Update Submit

August 28, 2018

Conditions

Keywords

Motor Neuron DiseaseNeurodegenerative DiseasesNervous System DiseasesNeuromuscular DiseasesAmyotrophic Lateral SclerosisPrimary Lateral SclerosisProgressive Muscular AtrophyMuscle crampsMuscle crampingALSMNDPMAPLSFLX-787

Outcome Measures

Primary Outcomes (1)

  • Cramp frequency

    Cramp frequency measured over the 28-day treatment period

    28 days

Study Arms (2)

Experimental

EXPERIMENTAL
Drug: FLX-787-ODT (orally disintegrating tablet)

Placebo Comparator

PLACEBO COMPARATOR
Drug: Placebo ODT

Interventions

FLX-787-ODT taken three times daily for 28 days

Experimental

Placebo ODT taken three times daily for 28 days

Placebo Comparator

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Documented diagnosis of Motor Neuron Disease (MND) \[including Amyotrophic Lateral Sclerosis (ALS), Primary Lateral Sclerosis (PLS) or Progressive Muscular Atrophy (PMA)\]
  • Expected survival \> 6 months
  • Weekly muscle cramping (defined as: a sustained muscle contraction that's most often painful and lasts seconds to minutes)

You may not qualify if:

  • Presence of major gastrointestinal disorders, such as inflammatory bowel disease, diverticulitis, active peptic ulcer disease, or significant gastroesophageal reflux disease (i.e., not well-controlled on antacids or proton pump inhibitors), or oral or esophageal lesions/ulcers
  • Presence of laryngospasm or significant swallowing problems
  • Presence of percutaneous endoscopic gastrostomy, esophagogastroduodenoscopy, or G-tube
  • Unable or unwilling to discontinue medications for cramps and/or opiates
  • Inability to tolerate a spicy sensation in the mouth or stomach
  • Actively using illicit drugs or history of chronic substance abuse within the past year prior to screening, including abuse of alcohol
  • Intention to change the current level of tobacco use or use of nicotine-containing products (i.e., new smokers or those actively trying to quit may not enrolled)
  • Participated in a clinical study (except natural history studies without administration of an investigational product) within 30 days prior to screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

Honor Health Research Institute

Scottsdale, Arizona, 85251, United States

Location

Mayo Clinic

Scottsdale, Arizona, 85259, United States

Location

California Pacific Medical Center

Sacramento, California, 94115, United States

Location

University of California - Davis

Sacramento, California, 95817, United States

Location

University of California San Francisco

San Francisco, California, 94143, United States

Location

University of Colorado

Aurora, Colorado, 80045, United States

Location

Hospital for Special Care

New Britain, Connecticut, 06053, United States

Location

GW Medical Faculty Associates Inc.

Washington D.C., District of Columbia, 20037, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

University of South Florida Health

Tampa, Florida, 33612, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Indiana University Neuroscience Center

Indianapolis, Indiana, 46202, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Johns Hopkins Hospital

Baltimore, Maryland, 21205, United States

Location

Lahey Hospital and Medical Center

Burlington, Massachusetts, 01805, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Saint Louis University

St Louis, Missouri, 63104, United States

Location

Hospital for Special Surgery

New York, New York, 10021, United States

Location

Guilford Neurologic Associates

Greensboro, North Carolina, 27405, United States

Location

Wake Forest University

Winston-Salem, North Carolina, 27157, United States

Location

Providence Brain and Spine Institute

Portland, Oregon, 97213, United States

Location

Oregon Health Sciences University

Portland, Oregon, 97239, United States

Location

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

Temple University

Philadelphia, Pennsylvania, 19140, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Austin Neuromuscular Center

Austin, Texas, 78756, United States

Location

Baylor Scott and White Health

Round Rock, Texas, 78665, United States

Location

UT Health San Antonio

San Antonio, Texas, 78229, United States

Location

The University of Utah

Salt Lake City, Utah, 84112, United States

Location

University of Vermont Medical Center

Burlington, Vermont, 05405, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Saint Luke's Rehabilitation Institute

Spokane, Washington, 99202, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Motor Neuron DiseaseNeurodegenerative DiseasesNervous System DiseasesNeuromuscular DiseasesAmyotrophic Lateral SclerosisMuscular Atrophy, SpinalMuscle CrampSpasm

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesTDP-43 ProteinopathiesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic DiseasesMuscular DiseasesMusculoskeletal DiseasesNeuromuscular ManifestationsNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Study Officials

  • Bjorn Oskarsson, MD

    Mayo Clinic Jacksonville Florida

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 20, 2017

First Posted

June 22, 2017

Study Start

July 28, 2017

Primary Completion

July 27, 2018

Study Completion

July 27, 2018

Last Updated

August 29, 2018

Record last verified: 2018-08

Locations