NCT03170271

Brief Summary

The purpose of this study is to investigate the effect of benralizumab on the rate of asthma exacerbations, patient reported quality of life and lung function during the 24-week treatment in patients with uncontrolled, severe asthma with an eosinophilic phenotype. A subset of patients will be assessed for their ongoing chronic rhinosinusitis with nasal polyps. The study design has been updated to include a 56-week open label ANDHI in Practice (ANDHI IP) sub study upon the completion of the 24-week double-blind period of the ANDHI study.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
660

participants targeted

Target at P75+ for phase_3 asthma

Timeline
Completed

Started Jul 2017

Longer than P75 for phase_3 asthma

Geographic Reach
14 countries

213 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 26, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

May 31, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

July 7, 2017

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 25, 2019

Completed
1.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 21, 2020

Completed
2 months until next milestone

Results Posted

Study results publicly available

December 16, 2020

Completed
Last Updated

November 1, 2021

Status Verified

October 1, 2021

Enrollment Period

2.2 years

First QC Date

May 26, 2017

Results QC Date

September 24, 2020

Last Update Submit

October 20, 2021

Conditions

Keywords

Asthma, Bronchial Diseases, Respiratory Tract Diseases, Lung Diseases, Obstructive Lung DiseasesAdditional relevant MeSH terms:AsthmaInflammationBronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung Diseases Respiratory HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System DiseasesPathologic Processes

Outcome Measures

Primary Outcomes (1)

  • Annualized Rate of Asthma Exacerbations Over the Treatment Period (up to Week 24)

    An asthma exacerbation was defined as a worsening of asthma that led to any of the following: * Use of systemic corticosteroids (or temporary increase in stable oral corticosteroids \[OCS\] background dose) for at least 3 days; a single depo-injectable dose of corticosteroids was considered equivalent to a 3-day course of systemic corticosteroids. * An emergency room/urgent care visit (defined as evaluation and treatment for \< 24 hours in an emergency department or urgent care center) due to asthma that required systemic corticosteroids (as per above). * An inpatient hospitalization (defined as admission to an inpatient facility and/or evaluation and treatment in a healthcare facility for ≥ 24 hours) due to asthma. Annual exacerbation rate = 365.25\*total number of exacerbations / total duration of follow-up within the treatment group. Annual asthma exacerbation rates over the 24-week period were estimated using a negative binomial model.

    Baseline (Week 0) up to Week 24

Secondary Outcomes (10)

  • Change From Baseline in Saint George Respiratory Questionnaire (SGRQ) Total Score to the EOT (Week 24)

    Baseline (Week 0) and Week 24

  • Change From Baseline in Pre-Bronchodilator (BD) Forced Expiratory Volume in First Second (FEV1) to the EOT (Week 24)

    Baseline (Week 0) and Week 24

  • Change From Baseline in Asthma Control Questionnaire 6 (ACQ-6) Score to the EOT (Week 24)

    Baseline (Week 0) and Week 24

  • Time to First Asthma Exacerbation (up to Week 24)

    Baseline (Week 0) up to Week 24

  • Change From Run-in Baseline Home Peak Expiratory Flow (PEF) (Morning and Evening) to the EOT (Week 24)

    Run-in baseline (from Day -28 to Day 0) and Week 24

  • +5 more secondary outcomes

Study Arms (2)

Benralizumab (Medi-563)

EXPERIMENTAL

Benralizumab (Medi563) Administered subcutaneously at Visit 4 (day 0), Visit 6 (day 28 +/- 3 days), Visit 7 (day 56 +/- 3 days) and Visit 9 (day 112 +/- 3 days) In the open label ANDHI IP sub study, all patients will receive benralizumab subcutaneously at Day 168 (Week 24), Day 196 (Week 28), Day 224 (Week 32), Day 280 (Week 40), Day 336 (Week 48), Day 392 (Week 56), Day 448 (Week 64), and Day 504 (Week 72).

Drug: Benralizumab (Medi-563)

Placebo

PLACEBO COMPARATOR

Administered subcutaneously at Visit 4 (day 0), Visit 6 (day 28 +/- 3 days), Visit 7 (day 56 +/- 3 days) and Visit 9 (day 112 +/- 3 days)

Drug: Placebo

Interventions

30mg Benralizumab administered as a subcutaneous injection at Visit 4 (day 0), Visit 6 (day 28 +/- 3 days), Visit 7 (day 56 +/- 3 days) and Visit 9 (day 112 +/- 3 days) In the open label ANDHI IP sub study, all patients will receive benralizumab subcutaneously at Day 168 (Week 24), Day 196 (Week 28), Day 224 (Week 32), Day 280 (Week 40), Day 336 (Week 48), Day 392 (Week 56), Day 448 (Week 64), and Day 504 (Week 72).

Benralizumab (Medi-563)

Placebo administered as a subcutaneous injection at Visit 4 (day 0), Visit 6 (day 28 +/- 3 days), Visit 7 (day 56 +/- 3 days) and Visit 9 (day 112 +/- 3 days)

Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Female and male patients aged 18 to 75 years inclusively at the time of Visit 1 with a history of physician-diagnosed asthma requiring treatment with medium-to-high dose Inhaled Corticosteroids (ICS) plus asthma controller, for at least 12 months prior to Visit 1.
  • Documented current treatment with high daily doses of ICS plus at least one other asthma controller for at least 3 months prior to Visit 1.
  • History of at least 2 asthma exacerbations while on ICS plus another asthma controller that required treatment with systemic corticosteroids (IM, IV, or oral) in the 12 months prior to Visit 1.
  • ACQ6 score ≥1.5 at Visit 1.
  • Screening pre-bronchodilator (pre-BD) FEV1 of \<80% predicted at Visit 2.
  • Excessive variability in lung function by satisfying ≥ 1 of the following criteria:
  • Airway reversibility (FEV1 ≥12%) using a short-acting bronchodilator demonstrated at Visit 2 or Visit 3.
  • Airway reversibility to short-acting bronchodilator (FEV1 ≥12%) documented during the 12 months prior to enrolment Visit 1.
  • Daily diurnal peak flow variability of \>10% when averaged over 7 continuous days during the study run-in period
  • An increase in FEV1 of ≥12% and 200 mL after a therapeutic trial of systemic corticosteroid (eg, OCS), given outside of an asthma exacerbation, documented in the 12 months prior enrolment Visit 1.
  • Airway hyper-responsiveness (methacholine: PC20 of \<8 mg/mL, histamine: PD20 of \<7.8 μmol, mannitol: decrease in FEV1 as per the labelled product instructions) documented in the 24 months prior to randomization Visit 4.
  • Peripheral blood eosinophil count either:
  • cells/μL assessed by central laboratory at either Visit 1 or Visit 2
  • ≥150 to \<300 cells/μL assessed by central laboratory at either Visit 1 or Visit 2, IF ≥1 of the following 5 clinical criteria (a to e) is met:
  • Using maintenance OCS (daily or every other day OCS requirement in order to maintain asthma control; maximum total daily dose 20 mg prednisone or equivalent) at screening
  • +6 more criteria

You may not qualify if:

  • Clinically important pulmonary disease other than asthma
  • Acute upper or lower respiratory infections within 30 days prior to the date informed consent.
  • A helminth parasitic infection diagnosed within 24 weeks prior to the date informed consent is obtained that has not been treated with, or has failed to respond to, standard of care therapy.
  • History of alcohol or drug abuse within 12 months prior to the date informed consent is obtained.
  • A history of known immunodeficiency disorder.
  • Current smokers or former smokers with a smoking history of ≥10 pack years.
  • Previously received benralizumab (MEDI-563).
  • Receipt of any investigational medication as part of a research study within approximately 5 half-lives prior to randomization.
  • Receipt of immunoglobulin or blood products within 30 days prior to the date informed consent is obtained.
  • Receipt of live attenuated vaccines 30 days prior to the date of randomization; other types of vaccines are allowed.
  • Concurrent enrolment in another interventional or post-authorization safety study
  • Patients who participated in the double-blind period but failed to complete the ANDHI EOT Visit 11. Patients who completed the ANDHI FU Visit 12 are not excluded from participation in the ANDHI IP sub study.
  • Unable to commit to the monthly visits as required by the protocol, or unable to commit to undergoing protocol guided reductions in asthma therapy, as directed by the Investigator.
  • Patients who experienced a severe or serious treatment-related AE during the double-blind period and, and those whom Investigator judges it is not in the patient's best interest to extend possible treatment with benralizumab.
  • Approved or off-label use of systemic immunosuppressive medications within 3 months prior to the first open label visit (Visit 13). These include but are not limited to small molecules such as methotrexate, cyclosporine, azathioprine, and immunosuppressive/immunomodulating biologics such as tumour necrosis factor (TNF) blockers. Regular use of systemic OCS is also excluded except for the indication of asthma.
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (213)

Research Site

Birmingham, Alabama, 35209, United States

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Tucson, Arizona, 85724, United States

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Little Rock, Arkansas, 72209, United States

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Bakersfield, California, 93301, United States

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Encinitas, California, 92024, United States

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Long Beach, California, 90806, United States

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Los Angeles, California, 90025, United States

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Mission Viejo, California, 92691, United States

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Newport Beach, California, 92663, United States

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Riverside, California, 92506, United States

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San Diego, California, 92108, United States

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Stockton, California, 95207, United States

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Walnut Creek, California, 94598, United States

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Aurora, Colorado, 80045, United States

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New Haven, Connecticut, 06519, United States

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Waterbury, Connecticut, 06708, United States

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Clearwater, Florida, 33765, United States

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Jacksonville, Florida, 32099, United States

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Kissimmee, Florida, 34741, United States

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Miami, Florida, 33126, United States

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Miami, Florida, 33173, United States

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Winter Park, Florida, 32789, United States

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Albany, Georgia, 31707, United States

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Savannah, Georgia, 31406, United States

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Peoria, Illinois, 61602, United States

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South Bend, Indiana, 46617, United States

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Iowa City, Iowa, 52242, United States

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West Des Moines, Iowa, 50266, United States

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Lakeside Park, Kentucky, 41017, United States

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Owensboro, Kentucky, 42301, United States

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Shreveport, Louisiana, 71106, United States

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Chevy Chase, Maryland, 20815, United States

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White Marsh, Maryland, 21162, United States

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North Dartmouth, Massachusetts, 02747, United States

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Ann Arbor, Michigan, 48109, United States

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Ypsilanti, Michigan, 48197, United States

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Minneapolis, Minnesota, 55402, United States

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St Louis, Missouri, 63156, United States

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Missoula, Montana, 59808, United States

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Lincoln, Nebraska, 68510, United States

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Highland Park, New Jersey, 08904, United States

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Marlton, New Jersey, 08053, United States

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Northfield, New Jersey, 08225, United States

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Piscataway, New Jersey, 08854, United States

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Toms River, New Jersey, 08755, United States

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Verona, New Jersey, 07044, United States

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Albuquerque, New Mexico, 87106, United States

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New Hyde Park, New York, 11042, United States

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New York, New York, 10016, United States

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Rochester, New York, 14618, United States

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Staten Island, New York, 10305, United States

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Staten Island, New York, 10310, United States

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The Bronx, New York, 10459, United States

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Charlotte, North Carolina, 28277, United States

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Elizabeth City, North Carolina, 27909, United States

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Gastonia, North Carolina, 28054, United States

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Greenville, North Carolina, 27834, United States

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High Point, North Carolina, 27262, United States

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Winston-Salem, North Carolina, 27103, United States

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Winston-Salem, North Carolina, 27157, United States

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Cincinnati, Ohio, 45231, United States

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Cincinnati, Ohio, 45242, United States

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Grove City, Ohio, 43123, United States

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Edmond, Oklahoma, 73034, United States

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Tulsa, Oklahoma, 74136, United States

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Clackamas, Oregon, 97015-5737, United States

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Philadelphia, Pennsylvania, 19107, United States

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Pittsburgh, Pennsylvania, 15213, United States

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Pittsburgh, Pennsylvania, 15241, United States

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Reading, Pennsylvania, 19610, United States

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Anderson, South Carolina, 29621, United States

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Gaffney, South Carolina, 29340, United States

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Greenville, South Carolina, 29607, United States

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Greenville, South Carolina, 29615, United States

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North Charleston, South Carolina, 29420-4211, United States

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Rock Hill, South Carolina, 29732, United States

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Sioux Falls, South Dakota, 57108, United States

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Franklin, Tennessee, 37067, United States

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Cypress, Texas, 77429, United States

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Dallas, Texas, 75225, United States

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Dallas, Texas, 75246, United States

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Fort Worth, Texas, 76109, United States

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Galveston, Texas, 77555, United States

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McKinney, Texas, 75069, United States

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San Antonio, Texas, 78229, United States

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San Antonio, Texas, 78249, United States

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San Antonio, Texas, 78251, United States

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Provo, Utah, 84604, United States

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South Burlington, Vermont, 05403, United States

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Abingdon, Virginia, 24210, United States

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Fairfax, Virginia, 22030, United States

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North Chesterfield, Virginia, 23225, United States

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Williamsburg, Virginia, 23188, United States

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Everett, Washington, 98208, United States

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Spokane, Washington, 99204, United States

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Tacoma, Washington, 98405, United States

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Madison, Wisconsin, 53792, United States

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Milwaukee, Wisconsin, 53226, United States

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Milwaukee, Wisconsin, 53228, United States

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West Allis, Wisconsin, 53227, United States

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Feldbach, A-8330, Austria

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Vienna, 1130, Austria

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Liège, 4000, Belgium

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Montigny-le-Tilleul, 6110, Belgium

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Namur, 5101, Belgium

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Calgary, Alberta, T2N 4Z6, Canada

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Kelowna, British Columbia, V1W 1V3, Canada

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Vancouver, British Columbia, V5Z 1M9, Canada

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Vancouver, British Columbia, V6Z 1Y6, Canada

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Winnipeg, Manitoba, R2H 2A6, Canada

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Ajax, Ontario, L1S 2J5, Canada

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Burlington, Ontario, L7N 3V2, Canada

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Mississauga, Ontario, L5A 3V4, Canada

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Toronto, Ontario, M5T 3A9, Canada

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Montreal, Quebec, H4A 3J1, Canada

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Québec, Quebec, G1V 4W2, Canada

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Aarhus N, 8200, Denmark

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Odense C, 5000, Denmark

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Vejle, 7100, Denmark

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Helsinki, 00290, Finland

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Turku, 20520, Finland

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Bayonne, 64100, France

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Besançon, 25030, France

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Brest, 29609, France

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Dijon, 21079, France

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Grenoble, 38043, France

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La Roche-sur-Yon, 85925, France

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Le Kremlin-Bicêtre, 94270, France

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Lille, 59037, France

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Lyon, 69317, France

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Marseille, 13015, France

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Montpellier, 34090, France

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Nantes, 44093, France

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Nice, 06002, France

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Paris, 75877, France

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Pessac, 33604, France

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Reims, 51092, France

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Rouen, 76031, France

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Saint-Quentin, 02321, France

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Strasbourg, 67091, France

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Toulouse, 31059, France

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Vandœuvre-lès-Nancy, 54511, France

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Berlin, 14059, Germany

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Bochum, 44789, Germany

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Bonn, 53105, Germany

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Cottbus, 03050, Germany

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Essen, 45239, Germany

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Hamburg, 20354, Germany

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Jena, 07747, Germany

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Marburg, 30625, Germany

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Oldenburg, 23758, Germany

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Regensburg, 93053, Germany

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Rheine, 48431, Germany

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Rüdersdorf, 15562, Germany

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Wangen, 88239, Germany

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Brescia, 25123, Italy

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Catania, 95123, Italy

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Catanzaro, 88100, Italy

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Cona, 44124, Italy

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Foggia, 71100, Italy

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Garbagnate Milanese, 20024, Italy

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Legnago, 37045, Italy

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Matera, Italy

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Milan, 20157, Italy

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Milan, 20122, Italy

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Modena, 41124, Italy

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Napoli, 80131, Italy

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Padua, 35128, Italy

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Palermo, 90127, Italy

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Pavia, 27100, Italy

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Piacenza, 29100, Italy

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Pietra Ligure, 17027, Italy

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Reggio Emilia, 42123, Italy

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Roma, 00168, Italy

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Rozzano, 20089, Italy

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Verona, 37126, Italy

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Amersfoort, 3813 TZ, Netherlands

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Deventer, 7416 SE, Netherlands

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Enschede, 7513 ER, Netherlands

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Harderwijk, 3844 DG, Netherlands

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Helmond, 5707 HA, Netherlands

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Nijmegen, 6532 SZ, Netherlands

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Zwolle, 8025 AB, Netherlands

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Bergen, 5021, Norway

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Lørenskog, N-1478, Norway

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Badalona(Barcelona), 08916, Spain

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Barcelona, 08035, Spain

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Barcelona, 08036, Spain

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Benalmádena, 29631, Spain

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Jerez de la Frontera, 11407, Spain

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Laredo, 39770, Spain

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Madrid, 28031, Spain

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Madrid, 28034, Spain

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Málaga, 29730, Spain

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Palma de Mallorca, 07010, Spain

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Pozuelo de Alarcón, 28223, Spain

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Sabadell, 08208, Spain

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Salamanca, 37007, Spain

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Santiago de Compostela, 15706, Spain

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Seville, 41009, Spain

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Taco, 38108, Spain

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Valdemoro, 28342, Spain

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Lund, 221 85, Sweden

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Östersund, 831 83, Sweden

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Stockholm, SE-181 58, Sweden

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Birmingham, B9 5SS, United Kingdom

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Bradford, BND9 6RJ, United Kingdom

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Cambridge, CB2 2QQ, United Kingdom

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Chertsey, KT16 0PZ, United Kingdom

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Dundee, DD1 9SY, United Kingdom

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Glasgow, G51 4TF, United Kingdom

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London, EC1A 7BE, United Kingdom

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Nottingham, NG5 1PB, United Kingdom

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Related Publications (3)

  • Louis R, Harrison TW, Chanez P, Menzella F, Philteos G, Cosio BG, Lugogo NL, de Luiz G, Burden A, Adlington T, Keeling N, Kwiatek J, Garcia Gil E; ANDHI Study Investigators. Severe Asthma Standard-of-Care Background Medication Reduction With Benralizumab: ANDHI in Practice Substudy. J Allergy Clin Immunol Pract. 2023 Jun;11(6):1759-1770.e7. doi: 10.1016/j.jaip.2023.03.009. Epub 2023 Mar 21.

  • Chong LY, Piromchai P, Sharp S, Snidvongs K, Webster KE, Philpott C, Hopkins C, Burton MJ. Biologics for chronic rhinosinusitis. Cochrane Database Syst Rev. 2021 Mar 12;3(3):CD013513. doi: 10.1002/14651858.CD013513.pub3.

  • Harrison TW, Chanez P, Menzella F, Canonica GW, Louis R, Cosio BG, Lugogo NL, Mohan A, Burden A, McDermott L, Garcia Gil E, Zangrilli JG; ANDHI study investigators. Onset of effect and impact on health-related quality of life, exacerbation rate, lung function, and nasal polyposis symptoms for patients with severe eosinophilic asthma treated with benralizumab (ANDHI): a randomised, controlled, phase 3b trial. Lancet Respir Med. 2021 Mar;9(3):260-274. doi: 10.1016/S2213-2600(20)30414-8. Epub 2020 Dec 22.

Related Links

MeSH Terms

Conditions

AsthmaBronchial DiseasesRespiratory Tract DiseasesLung DiseasesLung Diseases, ObstructiveInflammationHypersensitivity, ImmediateHypersensitivityImmune System DiseasesPathologic Processes

Interventions

benralizumab

Condition Hierarchy (Ancestors)

Respiratory HypersensitivityPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca

Study Officials

  • Brad Goodman, MD

    Aero Allergy Research Lab of Savannah

    PRINCIPAL INVESTIGATOR
  • Vinay Sikand, MD

    Sikand Institute of Pulmonary Research

    PRINCIPAL INVESTIGATOR
  • Willaim Cherry, MD

    Riverside Medical Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 26, 2017

First Posted

May 31, 2017

Study Start

July 7, 2017

Primary Completion

September 25, 2019

Study Completion

October 21, 2020

Last Updated

November 1, 2021

Results First Posted

December 16, 2020

Record last verified: 2021-10

Data Sharing

IPD Sharing
Will share

Locations