NCT03162055

Brief Summary

This is a phase IIIb randomised, double-blind, double-dummy, multicentre, parallel group, 24 week study to assess the efficacy and safety of Glycopyrronium/Formoterol Fumarate (GFF) fixed-dose combination 7.2/4.8 μg 2 inhalations twice daily compared to Umeclidinium/Vilanterol (UV) 62.5/25 μg fixed-dose combination 1 inhalation once daily in Patients with moderate to very severe COPD.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,119

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started May 2017

Shorter than P25 for phase_3

Geographic Reach
7 countries

107 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 19, 2017

Completed
3 days until next milestone

First Posted

Study publicly available on registry

May 22, 2017

Completed
3 days until next milestone

Study Start

First participant enrolled

May 25, 2017

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 4, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 4, 2018

Completed
1 year until next milestone

Results Posted

Study results publicly available

May 22, 2019

Completed
Last Updated

May 22, 2019

Status Verified

April 1, 2019

Enrollment Period

11 months

First QC Date

May 19, 2017

Results QC Date

April 30, 2019

Last Update Submit

April 30, 2019

Conditions

Keywords

COPD

Outcome Measures

Primary Outcomes (3)

  • Mean Change From Baseline in Morning Pre-dose Trough Forced Expiratory Volume in 1 Second (FEV1) Over 24 Weeks

    To assess the effects of GFF relative to UV on lung function as measured by change from baseline in morning pre-dose trough FEV1 is defined as the average of the -60 and -30 minute pre-dose values at each visit minus baseline using spirometry. Baseline is defined as the mean of the non-missing -60 and -30 minute values obtained prior to dosing at randomization (Day 1). BR a/s = bronchodilator responsiveness to albuterol/salbutamol.

    From Baseline (Day 1) up to 24 weeks

  • Mean Peak Change From Baseline in FEV1 Within 2 Hours Post-dosing Over 24 Weeks in PP Analysis Set Population

    To assess the effects of GFF relative to UV on lung function in PP analysis set population as measured by peak change from baseline in FEV1 is defined as the maximum of the FEV1 assessments within the 2 hours post-dosing time windows at each visit minus baseline using spirometry. Baseline is defined as the mean of the non-missing -60 and -30 minute values obtained prior to dosing at randomization (Day 1).

    From Baseline (Day 1) up to 24 weeks

  • Mean Peak Change From Baseline in FEV1 Within 2 Hours Post-dosing Over 24 Weeks in FAS Population

    To assess the effects of GFF relative to UV on lung function in FAS population as measured by peak change from baseline in FEV1 is defined as the maximum of the FEV1 assessments within the 2 hours post-dosing time windows at each visit minus baseline using spirometry. Baseline is defined as the mean of the non-missing -60 and -30 minute values obtained prior to dosing at randomization (Day 1).

    From Baseline (Day 1) up to 24 weeks

Secondary Outcomes (4)

  • Percentage of Participants With Increase of FEV1 of >=100 mL From Baseline at 5 Minutes Post-dosing on Day 1

    5 minutes post-dose on Day 1

  • Mean Peak Change From Baseline in Inspiratory Capacity (IC) Within 2 Hours Post-dosing Over 24 Weeks

    From Baseline (Day 1) up to 24 weeks

  • Mean Transition Dyspnea Index (TDI) Focal Score Over 24 Weeks

    From Baseline (Day -7 or 1) up to 24 weeks

  • Mean Change From Baseline in Early Morning Symptoms of COPD Instrument (EMSCI) Over 24 Weeks

    From Baseline (Day -7) up to 24 weeks

Other Outcomes (3)

  • Mean Change From Baseline in Night-Time Symptoms of COPD Instrument (NiSCI) Over 24 Weeks

    From Baseline (Day -7) up to 24 weeks

  • Mean Change From Baseline in Daily Rescue (Albuterol/Salbutamol MDI) Use Over 24 Weeks

    From Baseline (Day -7) up to 24 weeks

  • Mean Change From Baseline in COPD Assessment Test (CAT) Score Over 24 Weeks

    From Baseline (Day -7 or 1) up to 24 weeks

Study Arms (2)

Experimental

EXPERIMENTAL

glycopyrronium/formoterol fumarate 7.2/4.8 μg per actuation, twice daily

Drug: Glycopyrronium/Formoterol Fumarate

Active comparator

ACTIVE COMPARATOR

umeclidinium/vilanterol 62.5/ 25μg per inhalation, once daily

Drug: umeclidinium/vilanterol

Interventions

Metered dose inhaler (MDI), contains glycopyrronium/formoterol fumarate fixed-dose combination 7.2/4.8 μg per actuation

Experimental

Dry powder inhaler (DPI), Each metered dose contains umeclidinium/vilanterol 62.5/ 25μg fixed-dose combination per inhalation

Active comparator

Eligibility Criteria

Age40 Years - 95 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 40-95 years at screening
  • Current or former smoker with a history of at least 10 pack-years of cigarette smoking
  • Current clinical diagnosis of COPD, with COPD symptoms \> 1 year prior to screening, as defined by GOLD criteria or other current guidelines
  • COPD Severity defined by FEV1/FVC ratio \<0.70 and FEV1 \<80% of predicted normal value at screening and at randomisation
  • COPD treatment with rescue medication only, or stable dose of maintenance monotherapy (LAMA, LABA or ICS), or stable dose of double maintenance therapy (LAMA/LABA or ICS/LABA), for one month prior to screening
  • COPD Assessment Test (CAT) score ≥10 at randomisation
  • Documentation of a chest x-ray (as per local practice) or computed tomography (CT) within 6 months prior to screening, with no clinically significant pulmonary abnormalities other than related to COPD

You may not qualify if:

  • Respiratory disease other than COPD, including:
  • Current diagnosis of asthma
  • Alpha-1 Antitrypsin Deficiency as the cause of COPD
  • Other respiratory disorders and conditions as listed in the protocol
  • Severe COPD exacerbation (resulting in hospitalisation) not resolved within 8 weeks prior to screening, or moderate exacerbation not resolved within 4 weeks, or during screening
  • Pneumonia or lower respiratory tract infection that required antibiotics within 8 weeks prior to screening, or during screening.
  • Significant diseases or conditions other than COPD which may put the patient at risk, or influence the results of the study or the patient's ability to participate, including cardiac disease, advanced renal disease, and cancer that has not been in complete remission for at least 5 years.
  • Patients who have needed additions or alterations to their usual maintenance therapy for COPD due to worsening symptoms within 1 month prior to and during screening
  • Treatment with depot corticosteroids within 6 weeks, or other systemic corticosteroids within 4 weeks, prior to screening. (Patients maintained on an equivalent of 5 mg prednisone per day for at least 3 months prior to screening are allowed.)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (107)

Research Site

Tempe, Arizona, 85283, United States

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Escondido, California, 92025, United States

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Sacramento, California, 95821, United States

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Hollywood, Florida, 33021, United States

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Lawrenceville, Georgia, 30046, United States

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Rincon, Georgia, 31326, United States

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Farmington Hills, Michigan, 48336, United States

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The Bronx, New York, 10455, United States

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Gastonia, North Carolina, 28054, United States

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Dublin, Ohio, 43016, United States

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Pittsburgh, Pennsylvania, 15243, United States

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Greenville, South Carolina, 29615, United States

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Spartanburg, South Carolina, 29303, United States

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Sherman, Texas, 75092, United States

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Tomball, Texas, 77375, United States

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Dupnitsa, 2600, Bulgaria

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Dupnitsa, 2602, Bulgaria

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Haskovo, 6305, Bulgaria

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Kozloduy, 3320, Bulgaria

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Pazardzhik, 4400, Bulgaria

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Petrich, 2850, Bulgaria

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Pleven, 5800, Bulgaria

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Plovdiv, 4002, Bulgaria

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Razlog, 2760, Bulgaria

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Rousse, 7002, Bulgaria

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Sliven, 8800, Bulgaria

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Smolyan, 4700, Bulgaria

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Sofia, 1002, Bulgaria

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Sofia, 1233, Bulgaria

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Sofia, 1407, Bulgaria

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Sofia, 1408, Bulgaria

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Sofia, 1618, Bulgaria

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Stara Zagora, 6000, Bulgaria

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Varna, 9000, Bulgaria

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Vidin, 3700, Bulgaria

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Sherwood Park, Alberta, T8L 0N2, Canada

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Winnipeg, Manitoba, R2V 4W3, Canada

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Truro, Nova Scotia, B2N 1L2, Canada

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Burlington, Ontario, L7M 4Y1, Canada

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Burlington, Ontario, L7N 3V2, Canada

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Etobicoke, Ontario, M9W 4L6, Canada

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Windsor, Ontario, N8X 1T3, Canada

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Windsor, Ontario, N8X-5A6, Canada

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Gatineau, Quebec, J8Y 6S8, Canada

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Lévis, Quebec, G6W 0M5, Canada

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Québec, Quebec, G1G 3Y8, Canada

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Québec, Quebec, G1V 4G5, Canada

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Québec, Quebec, G3K 2P8, Canada

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Saint-Charles-Borromée, Quebec, J6E 2B4, Canada

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Besançon, 25030, France

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Brest, 29609, France

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Lyon, 69317, France

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Montpellier, 34295, France

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Nantes, 44277, France

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Pessac, 33604, France

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Poitiers, 86021, France

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Reims, 51092, France

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Balassagyarmat, 2660, Hungary

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Budapest, 1135, Hungary

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Debrecen, 4032, Hungary

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Debrecen, H-4031, Hungary

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Farkasgyepü, 8582, Hungary

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Hajdúnánás, 4080, Hungary

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Komárom, 2900, Hungary

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Komló, 7300, Hungary

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Miskolc, 3529, Hungary

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Püspökladány, 4150, Hungary

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Siófok, 8600, Hungary

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Szeged, H-6722, Hungary

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Szombathely, 9700, Hungary

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Vásárosnamény, 4800, Hungary

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Barnaul, 656038, Russia

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Barnaul, 656045, Russia

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Chelyabinsk, 454021, Russia

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Izhevsk, 426035, Russia

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Moscow, 109544, Russia

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Novosibirsk, 630051, Russia

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Penza, 440026, Russia

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Penza, 440067, Russia

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Ryazan, 390005, Russia

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Saint Petersburg, 191015, Russia

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Saint Petersburg, 191180, Russia

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Saint Petersburg, 194291, Russia

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Saint Petersburg, 196084, Russia

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Saint Petersburg, 197022, Russia

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Saint Petersburg, 197342, Russia

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Saint Petersburg, 198260, Russia

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Saratov, 410012, Russia

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Smolensk, 214006, Russia

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Tomsk, 634050, Russia

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Ulyanovsk, 432009, Russia

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Yekaterinburg, 620028, Russia

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Chernivtsi, 58000, Ukraine

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Chernivtsi, 58001, Ukraine

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Ivano-Frankivsk, 76012, Ukraine

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Kharkiv, 61002, Ukraine

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Kharkiv, 61035, Ukraine

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Kharkiv, 61058, Ukraine

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Kyiv, 03680, Ukraine

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Kyiv, 04107, Ukraine

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Lutsk, 43000, Ukraine

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Lviv, 79066, Ukraine

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Odesa, 65025, Ukraine

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Poltava, 36040, Ukraine

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Vinnytsia, 21001, Ukraine

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Vinnytsia, 21029, Ukraine

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Zaporizhzhia, 69096, Ukraine

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Related Publications (1)

  • Maltais F, Ferguson GT, Feldman GJ, Deslee G, Bourdin A, Fjallbrant H, Siwek-Posluszna A, Jenkins MA, Martin UJ. A Randomized, Double-Blind, Double-Dummy Study of Glycopyrrolate/Formoterol Fumarate Metered Dose Inhaler Relative to Umeclidinium/Vilanterol Dry Powder Inhaler in COPD. Adv Ther. 2019 Sep;36(9):2434-2449. doi: 10.1007/s12325-019-01015-3. Epub 2019 Jul 2.

MeSH Terms

Conditions

Pulmonary Disease, Chronic Obstructive

Interventions

GlycopyrrolateFormoterol FumarateGSK573719vilanterol

Condition Hierarchy (Ancestors)

Lung Diseases, ObstructiveLung DiseasesRespiratory Tract DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Quaternary Ammonium CompoundsAminesOrganic ChemicalsOnium CompoundsPyrrolidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsEthanolaminesAmino AlcoholsAlcohols

Results Point of Contact

Title
Vice President, Inhalation and Oral Respiratory
Organization
AstraZeneca

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 19, 2017

First Posted

May 22, 2017

Study Start

May 25, 2017

Primary Completion

May 4, 2018

Study Completion

May 4, 2018

Last Updated

May 22, 2019

Results First Posted

May 22, 2019

Record last verified: 2019-04

Locations