NCT03142191

Brief Summary

This is a Phase 2, multicenter, multinational, randomized, double-blind, placebo-controlled study evaluating the efficacy, safety, pharmacokinetics (PK), quality of life and exploratory pharmacodynamics (PD) of two treatment doses of CC-90001, 200 mg and 400 mg, compared with placebo, when delivered once daily per os (PO) in subjects with idiopathic pulmonary fibrosis (IPF). This study is designed to assess response to treatment by using measures of lung function, disease progression, fibrosis on radiography, and patient-reported outcomes. It will also assess dose response.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
138

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2017

Typical duration for phase_2

Geographic Reach
13 countries

112 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 24, 2017

Completed
11 days until next milestone

First Posted

Study publicly available on registry

May 5, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

July 26, 2017

Completed
4.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 24, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 24, 2021

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

June 28, 2023

Completed
Last Updated

June 28, 2023

Status Verified

June 1, 2023

Enrollment Period

4.4 years

First QC Date

April 24, 2017

Results QC Date

December 22, 2022

Last Update Submit

June 6, 2023

Conditions

Keywords

Idiopathic Pulmonary Fibrosis (IPF)Pulmonary FibrosisCC-90001SafetyEfficacyIPFidiopathic pulmonary fibrosis

Outcome Measures

Primary Outcomes (1)

  • Percentage Point Difference in % Predicted Forced Vital Capacity (FVC).

    Mean change from baseline in percentage point difference in % predicted forced vital capacity (FVC) FAS population is defined as all randomized participants who received at least one dose of the investigational product. Baseline is defined as day 1 of treatment.

    from baseline to week 24

Secondary Outcomes (16)

  • Mean Change From Baseline in Absolute Forced Vital Capacity (FVC).

    from baseline to week 24

  • Mean Change in Distance Walked in the 6-minute Walk Test (6MWT)

    From baseline up to week 104

  • Mean Change From Baseline in Dyspnea Rating on Borg Scale

    From baseline up to week 104

  • Percentage of Participants Who Had Disease Progression

    From Baseline up to week 24

  • Mean Change From Baseline in Total Score and Domains on the Saint George's Respiratory Questionnaire (SGRQ)

    From Baseline up to week 24

  • +11 more secondary outcomes

Study Arms (5)

CC-90001 400 mg PO QD

EXPERIMENTAL

55 subjects will be randomized to CC-90001 400mg

Drug: CC-90001

CC-90001 200 mg PO QD

EXPERIMENTAL

55 subjects will be randomized to CC-90001 200mg

Drug: CC-90001

Placebo PO QD

PLACEBO COMPARATOR

55 subjects will be randomized to placebo

Other: Placebo

CC-90001 400 mg PO QD- Sub-Study

EXPERIMENTAL

30 subjects will be randomized to CC-90001 400mg

Drug: CC-90001

Placebo PO QD- Sub-Study

PLACEBO COMPARATOR

15 subjects will be randomized to placebo

Other: Placebo

Interventions

CC-90001 is a potent, selective inhibitor of JNK.

CC-90001 200 mg PO QDCC-90001 400 mg PO QDCC-90001 400 mg PO QD- Sub-Study
PlaceboOTHER

Placebo

Placebo PO QDPlacebo PO QD- Sub-Study

Eligibility Criteria

Age40 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject understands and has voluntarily signed and dated an informed consent form
  • Subject is male or female ≥ 40 years of age
  • Diagnosis of IPF is supported by HRCT and historical lung biopsy (surgical lung biopsy \[SLB\] or cryobiopsy) if available according to guidelines.
  • No features supporting an alternative diagnosis on transbronchial biopsy, bronchoalveolar lavage (BAL), or SLB, if performed.
  • Percent predicted forced vital capacity (% FVC) ≥ 45% and ≤ 95% at Screening
  • Percent predicted diffusion capacity of the lung for carbon monoxide (DLCO) ≥ 25% and ≤ 90% predicted at Screening.
  • Able to walk ≥ 150 meters during the 6-minute walk test (6MWT) at Screening
  • Females of childbearing potential (FCBP) must commit to true abstinence or agree to use two effective birth control methods.
  • Male subjects must practice true abstinence or use a barrier method of contraception.
  • Progressive Pulmonary Fibrosis (PPF) Sub-Study:
  • Features of diffuse fibrosing lung disease of \> 10% on HRCT by central reading.
  • Investigator-documented ≥ 5% annualized relative decline in FVC in past 24 months from Screening Visit 1

You may not qualify if:

  • The presence of any of the following will exclude a subject from enrollment:
  • Subject has any significant medical condition, laboratory abnormality, or psychiatric illness that would prevent the subject from participating in the study.
  • Subject with a QTcF \> 450 msec.
  • Evidence of clinically relevant airways obstruction at Screening.
  • Subjects using therapy targeted to treat IPF.
  • History of latent or active TB, unless there is medical record documentation of successful completion of a standard course of treatment
  • History of hepatitis B and/or hepatitis C, including those considered successfully treated/cured
  • Pregnancy or lactation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (112)

Loma Linda Univ Medical Center

Loma Linda, California, 92354, United States

Location

Cedars Sinai Medical Center Rheumatology

Los Angeles, California, 90048, United States

Location

Local Institution - 514

Sacramento, California, 95817, United States

Location

University of California Davis Health System

Sacramento, California, 95817, United States

Location

Stanford University Pulmonary and Critical Care Clinic

Stanford, California, 94305, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

University of Miami and Sylvester Cancer Center

Miami, Florida, 33136, United States

Location

University of Louisville

Louisville, Kentucky, 40202, United States

Location

The Lung and Research Center, LLC

Chesterfield, Missouri, 63017, United States

Location

Mt. Sinai School of Medicine

New York, New York, 10029, United States

Location

Duke University Health System - Duke Pulmonary Transplant Clinic

Durham, North Carolina, 27710, United States

Location

University of Cincinnati Medical Center

Cincinnati, Ohio, 45267, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44121, United States

Location

Pulmonary & Sleep Center of Oklahoma

Tulsa, Oklahoma, 74137, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37212, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Local Institution - 502

Dallas, Texas, 75246, United States

Location

University of Utah Health Care

Salt Lake City, Utah, 84132, United States

Location

University of Vermont

Burlington, Vermont, 05405, United States

Location

Local Institution - 608

Camperdown, New South Wales, 2050, Australia

Location

Royal Prince Alfred Hospital

Camperdown, New South Wales, 2050, Australia

Location

Concord Repatriation General Hospital

Concord, New South Wales, 2139, Australia

Location

Mater Medical Centre

South Brisbane, Queensland, 4101, Australia

Location

Local Institution - 601

Adelaide, South Australia, 5000, Australia

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Flinders Medical Centre

Bedford Park, South Australia, 5042, Australia

Location

Local Institution - 605

Parkville, Victoria, 3050, Australia

Location

Royal Melbourne Hospital

Parkville, Victoria, 3050, Australia

Location

Fiona Stanley Hospital

Murdoch, Western Australia, 6150, Australia

Location

Institute for Respiratory Health Inc

Nedlands, Western Australia, 6009, Australia

Location

St Vincent Hospital - Sydney

Darlinghurst, 2010, Australia

Location

Clinica de Pneumologia S/S

Goiânia, Goiás, 74110-030, Brazil

Location

Irmandade da Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, 90085-074, Brazil

Location

Hospital Nossa Senhora da Conceicao

Porto Alegre, Rio Grande do Sul, 91350-200, Brazil

Location

Hospital Ernesto Dornelles

Porto Alegre, 90610-093, Brazil

Location

Universidade Federal do Rio de Janeiro (UFRJ)-Hospital Universitario Clementino Fraga Filho (HUCFF)

Rio de Janeiro, 21941, Brazil

Location

Faculdade de Medicina do ABC

Santo André, 09060-650, Brazil

Location

Incor - Instituto do Coracao HCFMUSP

São Paulo, 01414-001, Brazil

Location

Kelowna & Respiratory Allergy Clinic

Kelowna, British Columbia, V1W 1V3, Canada

Location

Local Institution - 621

Kelowna, British Columbia, V1W 1V3, Canada

Location

Local Institution - 620

Vancouver, British Columbia, V5Z 1M9, Canada

Location

The Lung Centre Respiratory Clinic - Vancouver General Hospital Location

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Dr. Syed Anees Medicine Professional Corporation

Windsor, Ontario, N8X 1T3, Canada

Location

Local Institution - 623

Windsor, Ontario, N8X 1T3, Canada

Location

Centro de Reumatologia y Ortopedia SAS

Barranquilla, 080020, Colombia

Location

Local Institution - 631

Bogotá, 0, Colombia

Location

Centro Especializado en Enfermedades Pulmonares

Bogotá, Colombia

Location

Centro Medico Imbanaco

Cali, Colombia

Location

Helios Klinikum Emil Von Behring

Berlin, 14165, Germany

Location

Ruhrlandklinik University Hospital

Essen, 45239, Germany

Location

AGAPLESION EV. KRANKENHAUS MITTELHESSEN gGmbH

Giessen, 35398, Germany

Location

Local Institution - 642

Giessen, 35398, Germany

Location

Universitatsklinikum Heidelberg

Heidelberg, 69120, Germany

Location

Waldburg-Zeil Kliniken -Fachkliniken Wangen

Wangen, 88239, Germany

Location

Democritus University of Thrace

Alexandroupoli, 68100, Greece

Location

University General Hospital of Alexandroupolis

Alexandroupoli, 68100, Greece

Location

University General Hospital Attikon

Haidari, 12462, Greece

Location

University of Crete - University General Hospital of Heraklion

Heraklion, 711 10, Greece

Location

General Hospital of Heraklion Benizeleio Pananeio

Heraklion, 71409, Greece

Location

Spitalul Clinic de Pneumoftiziologie Leon Daniello Cluj Napoca

Cluj-Napoca, Romania

Location

Spitalul Clinic de Boli Infectioase si Pneumoftiziologie Dr. Victor Babes Timisoara

Timișoara, 300312, Romania

Location

City clinical hospital No 9

Izhevsk, 426063, Russia

Location

Federal State Budgetary Scientific Institution Research Institute for Complex Issues of Cardiovascul

Kemerovo, 650002, Russia

Location

TSBIH Territorial Clinical Hospital

Krasnoyarsk, 660022, Russia

Location

Russian Academy of Medical Sciences RAMS - Central Scientific Research Institute of Tuberculosis CTR

Moscow, 107564, Russia

Location

Federal Medico-Biological Agency FMBA - Federal Research Clinical Center FGUZ Clinical Hospital No.

Moscow, Russia

Location

Local Institution - 666

Nizhny Novgorod, 603011, Russia

Location

Nizhny Novgorod Research Institute of Hygiene and Occupational Pathology

Nizhny Novgorod, 603011, Russia

Location

Republican Hospital

Petrozavodsk, 185019, Russia

Location

FSBHI Clincial Research Institute of Phithisioplulmonoloyg

Saint Petersburg, 191036, Russia

Location

Local Institution - 667

Saint Petersburg, 191180, Russia

Location

Vvedenskaya Hospital

Saint Petersburg, 191180, Russia

Location

Saint-Petersburg State Institution of Healthcare

Saint Petersburg, 193312, Russia

Location

Pavlov First Saint Petersburg State Medical University

Saint Petersburg, 197022, Russia

Location

Local Institution - 675

Saratov, 410053, Russia

Location

Saratov Regional Clinical Hospital

Saratov, 410053, Russia

Location

SAIH of Yaroslavl region Clinical Hospital for Emergency Medical Care n.a. N.V.Solovyev

Yaroslavl, 150003, Russia

Location

Ural State Medical Academy - Medical Association Novaya Bolnitsa

Yekaterinburg, 620109, Russia

Location

Buddhist Dalin Tzu Chi General Hospital

Dalin, 62247, Taiwan

Location

Kaohsiung Medical University Hospital

Kaohsiung City, 807, Taiwan

Location

China Medical University Hospital

Taichung, 40447, Taiwan

Location

National Taiwan University Hospital

Taipei, Zhongzheng Dist., 10002, Taiwan

Location

Ege Universitesi Tip Fakultesi Hastanesi Ege University Medical Faculty Hospital

Bornova, 35100, Turkey (Türkiye)

Location

Local Institution - 681

Bornova, 35100, Turkey (Türkiye)

Location

Uludag Universitesi Tip Fakultesi

Bursa, 16059, Turkey (Türkiye)

Location

Istanbul Universitesi - Cerrahpasa Tip Fakultesi Cerrahpasa Medical Faculty

Istanbul, 34098, Turkey (Türkiye)

Location

Izmir Dr.Suat Seren Chest Diseases Hospital

Izmir, 35100, Turkey (Türkiye)

Location

Communal Institution Dnipropetrovsk City Clinical Hospital #6 of Dnipropetrovsk Regional Council

Dnipro, 49023, Ukraine

Location

Regional Phthisiopulmonological Center

Ivano-Frankivsk, 76018, Ukraine

Location

Kharkiv City Clinical Hospital #13

Kharkiv, 61124, Ukraine

Location

CI of Healthcare RCH - Center of Medical Emergency and Accident Medicine

Kharkiv, 61204, Ukraine

Location

State Institution National Scientific Center of Radiation Medicine of NAMS of Ukraine

Kyiv, 03115, Ukraine

Location

SI F.H.Yanovskyi National Institute of Phthisiatry and Pulmonology of Academy of Medical Sciences

Kyiv, 03680, Ukraine

Location

Birmingham Chest Clinic

Birmingham, B3 3HX, United Kingdom

Location

Hull and East Yorkshire Hospitals NHS Trust - Castle Hill Hospital

Cottingham, HU16 5JQ, United Kingdom

Location

Hinchingbrooke Hospital

Huntingdon, PE29 6NT, United Kingdom

Location

The Leeds Teaching Hospitals NHS Trust - St James's University Hospital

Leeds, LS9 7TF, United Kingdom

Location

University Hospitals of Leicester NHS Trust - Glenfield Hospital - Institute for Lung Health ILH

Leicester, LE3 9QP, United Kingdom

Location

Aintree University Hospital

Liverpool (Walton Centre), L9 7LJ, United Kingdom

Location

University Hospital Llandough

Llandough, CF64 2XX, United Kingdom

Location

University College London Hospitals

London, NW1 2PG, United Kingdom

Location

Local Institution - 598

Newcastle, NE1 4LP, United Kingdom

Location

Royal Victoria Infirmary

Newcastle, NE1 4LP, United Kingdom

Location

Local Institution - 697

Norwich, NR4 7UY, United Kingdom

Location

Norfolk and Norwich University Hospital

Norwich, NR4 7UY, United Kingdom

Location

The University of Nottingham - Nottingham Respiratory Research Unit NRRU

Nottingham, NG5 1PB, United Kingdom

Location

Salford Royal

Salford, M6 8HD, United Kingdom

Location

Southampton General Hospital

Southhampton, SO01 6YD, United Kingdom

Location

Local Institution - 694

Westbury-on-Trym/ Bristol, BS10 5NB, United Kingdom

Location

Southmead Hospital

Westbury-on-Trym/ Bristol, BS10 5NB, United Kingdom

Location

Related Publications (3)

  • Mattos WLLD, Khalil N, Spencer LG, Bonella F, Folz RJ, Rolf JD, Mogulkoc N, Lancaster LH, Jenkins RG, Lynch DA, Noble PW, Maher TM, Cottin V, Senger S, Horan GS, Greenberg S, Popmihajlov Z. Phase 2, Double-Blind, Placebo-controlled Trial of a c-Jun N-Terminal Kinase Inhibitor in Idiopathic Pulmonary Fibrosis. Am J Respir Crit Care Med. 2024 Aug 15;210(4):435-443. doi: 10.1164/rccm.202310-1907OC.

  • Popmihajlov Z, Sutherland DJ, Horan GS, Ghosh A, Lynch DA, Noble PW, Richeldi L, Reiss TF, Greenberg S. CC-90001, a c-Jun N-terminal kinase (JNK) inhibitor, in patients with pulmonary fibrosis: design of a phase 2, randomised, placebo-controlled trial. BMJ Open Respir Res. 2022 Jan;9(1):e001060. doi: 10.1136/bmjresp-2021-001060.

  • Nagy MA, Hilgraf R, Mortensen DS, Elsner J, Norris S, Tikhe J, Yoon W, Paisner D, Delgado M, Erdman P, Haelewyn J, Khambatta G, Xu L, Romanow WJ, Condroski K, Bahmanyar S, McCarrick M, Benish B, Blease K, LeBrun L, Moghaddam MF, Apuy J, Canan SS, Bennett BL, Satoh Y. Discovery of the c-Jun N-Terminal Kinase Inhibitor CC-90001. J Med Chem. 2021 Dec 23;64(24):18193-18208. doi: 10.1021/acs.jmedchem.1c01716. Epub 2021 Dec 13.

Related Links

MeSH Terms

Conditions

Idiopathic Pulmonary FibrosisFibrosisIdiopathic Interstitial PneumoniasPathologic ProcessesLung Diseases, InterstitialLung DiseasesRespiratory Tract DiseasesPulmonary Fibrosis

Interventions

CC-90001

Condition Hierarchy (Ancestors)

Pathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Bristol-Myers Squibb Study Director
Organization
Bristol-Myers Squibb

Study Officials

  • Bristol-Myers Squibb

    Bristol-Myers Squibb

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 24, 2017

First Posted

May 5, 2017

Study Start

July 26, 2017

Primary Completion

December 24, 2021

Study Completion

December 24, 2021

Last Updated

June 28, 2023

Results First Posted

June 28, 2023

Record last verified: 2023-06

Locations