Brief Summary

Up to 80% of infants with hemolytic disease due to maternal alloimmunization, treated with IUT, require at least one top-up transfusion for late anemia during the first 3 months of life. Erythropoietin deficiency is also considered as a possible contributing factor to late anemia and therefore we will assess the role of EPO (darbepoetin alfa) in the treatment of these infants.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
42

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Oct 2017

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 3, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 7, 2017

Completed
7 months until next milestone

Study Start

First participant enrolled

October 31, 2017

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2020

Completed
Last Updated

October 2, 2019

Status Verified

September 1, 2019

Enrollment Period

2.8 years

First QC Date

April 3, 2017

Last Update Submit

September 30, 2019

Conditions

Keywords

Hemolytic disease of the fetus and newbornHDFNRed blood cell alloimmunization

Outcome Measures

Primary Outcomes (1)

  • Number of top-up transfusions required per infant

    Number of top-up transfusions required per infant

    First 3 months of life

Secondary Outcomes (4)

  • The percentage of infants requiring a top-up transfusion

    First 3 months of life

  • Number of days of admission for top-up transfusions

    First 3 months of life

  • Occurrence of hypertension

    8 weeks (treatment course)

  • Occurrence of high ferritin levels

    8 weeks (treatment course)

Other Outcomes (1)

  • Long-term neurodevelopmental outcome

    2 years of age

Study Arms (2)

Darbepoetin alfa group

ACTIVE COMPARATOR

Group treated with darbepoetin alfa (Aranesp) 10microg/kg once a week for a period of 8 weeks.

Drug: Darbepoetin Alfa

Control group

NO INTERVENTION

"Standard care" which involves close monitoring of hemoglobin levels and if necessary, top-up red cell transfusion.

Interventions

Darbepoetin alfa dosage 10microg/kg once a week for 8 weeks

Also known as: Aranesp
Darbepoetin alfa group

Eligibility Criteria

AgeUp to 2 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • all (near)-term neonates (gestational age ≥ 35 weeks) admitted to the Leiden University Medical Center (LUMC) with HDFN, treated with IUT.

You may not qualify if:

  • none.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Leiden University Medical Center

Leiden, 2300RC, Netherlands

RECRUITING

Related Publications (1)

  • Ree IMC, de Haas M, van Geloven N, Juul SE, de Winter D, Verweij EJT, Oepkes D, van der Bom JG, Lopriore E. Darbepoetin alfa to reduce transfusion episodes in infants with haemolytic disease of the fetus and newborn who are treated with intrauterine transfusions in the Netherlands: an open-label, single-centre, phase 2, randomised, controlled trial. Lancet Haematol. 2023 Dec;10(12):e976-e984. doi: 10.1016/S2352-3026(23)00285-5.

MeSH Terms

Conditions

Erythroblastosis, Fetal

Interventions

Darbepoetin alfa

Condition Hierarchy (Ancestors)

Fetal DiseasesPregnancy ComplicationsFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesHematologic DiseasesHemic and Lymphatic DiseasesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfant, Newborn, DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

ErythropoietinColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesProteinsAmino Acids, Peptides, and Proteins

Study Officials

  • Masja de Haas, MD PhD

    Sanquin Research

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Isabelle MC Ree, MD

CONTACT

Enrico Lopriore, MD PhD

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: RCT with unblinded treatment allocation 1:1 ratio. Either treatment with darbepoetin alfa or "standard care". No placebo.
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 3, 2017

First Posted

April 7, 2017

Study Start

October 31, 2017

Primary Completion

August 1, 2020

Study Completion

August 1, 2020

Last Updated

October 2, 2019

Record last verified: 2019-09

Data Sharing

IPD Sharing
Will not share

Locations