NCT03087968

Brief Summary

This clinical investigation is a substudy within GS-US-416-2124, IND 129570, which is A Phase 2, Double-Blind, Randomized Study Evaluating the Safety, Tolerability, and Efficacy of GS-4997 in Combination with Prednisolone versus Prednisolone Alone in Subjects with Severe Alcoholic Hepatitis. The use of the HepQuant SHUNT test is to assess liver disease severity before, during, and after treatment with GS-4997 or placebo, to assess liver disease severity.

Trial Health

30
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Jul 2016

Geographic Reach
1 country

13 active sites

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 31, 2016

Completed
7 months until next milestone

First Submitted

Initial submission to the registry

March 9, 2017

Completed
14 days until next milestone

First Posted

Study publicly available on registry

March 23, 2017

Completed
6 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 13, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 13, 2017

Completed
Last Updated

August 30, 2021

Status Verified

September 1, 2017

Enrollment Period

1.1 years

First QC Date

March 9, 2017

Last Update Submit

August 27, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • To compare the change in (DSI ) Disease Severity Index between GS-4997 treatment and placebo arms

    Using the SHUNT DSI to evaluate the liver, this outcome will compare the two arms to determine if SHUNT DSI is able to measure a change between the experimental and control groups.

    HepQuant Shunt testing will be done at baseline (Day1), Week 1, Week 4, Week 12, Week 24

Secondary Outcomes (4)

  • Secondary Outcome 1

    HepQuant Shunt testing will be done at baseline (Day1), Week 1, Week 4, Week 12, Week 24

  • Secondary Outcome 2

    HepQuant Shunt testing will be done at baseline (Day1), Week 1, Week 4, Week 12, Week 24

  • Secondary Outcome 3

    HepQuant Shunt testing will be done at baseline (Day1), Week 1, Week 4, Week 12, Week 24

  • Secondary Outcome 4

    HepQuant Shunt testing will be done at baseline (Day1), Week 1, Week 4, Week 12, Week 24

Study Arms (2)

GS-4997 + Prednisolone

EXPERIMENTAL

GS-4997 + Prednisolone for 28 days HepQuant SHUNT Test

Drug: GS-4997Drug: PrednisoloneDevice: HepQuant SHUNT Test

Prednisolone + Placebo

PLACEBO COMPARATOR

Placebo + Prednisolone for 28 days HepQuant SHUNT Test

Drug: PrednisoloneDevice: HepQuant SHUNT TestDrug: Placebo

Interventions

Experimental drug

GS-4997 + Prednisolone

Control drug that is also administered with the Experimental drug, GS-4997. This drug is used in both arms.

GS-4997 + PrednisolonePrednisolone + Placebo

The HepQuant SHUNT Liver Diagnostic Kit is intended for use in the quantitative detection of 13C-cholate and d4-cholate in blood serum, collected after the intravenous administration of 13C-cholate and the oral ingestion of d4-cholate. The device is indicated to assess the severity of liver disease. For use by health care professionals. Administer the test under a physician's supervision. The HepQuant Analytical Testing Laboratory must analyze the serum samples.

Also known as: SHUNT
GS-4997 + PrednisolonePrednisolone + Placebo

Placebo

Prednisolone + Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Willing and able to give informed consent prior to any study specific procedures being performed. In individuals with hepatic encephalopathy (HE) which may impair decision-making, consent will be obtained per hospital procedures (eg, by Legally Authorized Representative)
  • Clinical diagnosis of severe AH
  • Maddrey's DF ≥ 32 at screening

You may not qualify if:

  • Pregnant or lactating females;
  • Other causes of liver disease including chronic hepatitis B (hepatitis B surface antigen \[HBsAg\] positive), chronic hepatitis C (HCV RNA positive), acetaminophen hepatotoxicity, biliary obstruction, and autoimmune liver disease;
  • Serum AST \>400 U/L or ALT \>300 U/L;
  • MELD \>30 at screening;
  • Maddrey's DF \>60 at screening;
  • Grade 4 Hepatic Encephalopathy (HE) by West Haven criteria;
  • Concomitant or previous history of hepatocellular carcinoma;
  • History of liver transplantation;
  • HIV Ab positive;
  • Clinical suspicion of pneumonia;
  • Uncontrolled sepsis;
  • Uncontrolled gastrointestinal (GI) bleeding or controlled GI bleeding within 7 days of screening that was associated with shock or required transfusion of more than 3 units of blood;
  • Type 1 hepatorenal syndrome (HRS) or renal failure defined as a serum creatinine \>221 μmol/L (\>2.5 mg/dL) or the requirement for renal replacement therapy;
  • Individuals dependent on inotropic (eg, epinephrine or norepinephrine) or ventilatory support (ie, endotracheal intubation or positive-pressure ventilation);
  • Portal vein thrombosis;
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Southern California Research Center

Coronado, California, 92118, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, 75203, United States

Location

American Research Corporation at the Texas Liver Institute

San Antonio, Texas, 78215, United States

Location

Intermountain Medical Center

Murray, Utah, 84107, United States

Location

Liver Institute of Virginia

Newport News, Virginia, 23602, United States

Location

Liver Institute of Virginia

Richmond, Virginia, 23226, United States

Location

VCU Health System

Richmond, Virginia, 23298, United States

Location

University of Washington

Seattle, Washington, 98104, United States

Location

MeSH Terms

Conditions

Hepatitis, Alcoholic

Interventions

Prednisolone

Condition Hierarchy (Ancestors)

HepatitisLiver DiseasesDigestive System DiseasesLiver Diseases, AlcoholicAlcohol-Induced DisordersAlcohol-Related DisordersSubstance-Related DisordersChemically-Induced Disorders

Intervention Hierarchy (Ancestors)

PregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Study Officials

  • Greg Everson, MD

    HepQuant, LLC

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
interventional
Phase
early phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, CARE PROVIDER
Purpose
DIAGNOSTIC
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 9, 2017

First Posted

March 23, 2017

Study Start

July 31, 2016

Primary Completion

September 13, 2017

Study Completion

September 13, 2017

Last Updated

August 30, 2021

Record last verified: 2017-09

Locations