NCT03058666

Brief Summary

Study to test the hypothesis that aerosolized Infasurf can decrease the need for intubation and instillation of liquid surfactant to the airway.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
477

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2017

Shorter than P25 for phase_3

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 16, 2017

Completed
7 days until next milestone

First Posted

Study publicly available on registry

February 23, 2017

Completed
1 month until next milestone

Study Start

First participant enrolled

March 29, 2017

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2018

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 31, 2018

Completed
5.8 years until next milestone

Results Posted

Study results publicly available

May 29, 2024

Completed
Last Updated

May 29, 2024

Status Verified

May 1, 2024

Enrollment Period

1.2 years

First QC Date

February 16, 2017

Results QC Date

November 3, 2023

Last Update Submit

May 1, 2024

Conditions

Keywords

AerosolsurfactantcalfactantInfasurfRespiratory Distress SyndromeRDSPrematureNeonates

Outcome Measures

Primary Outcomes (1)

  • Intubation and Instillation of Liquid Surfactant

    Percent of at risk subjects receiving endotracheal intubation and instillation of surfactant within the first 72 hours.

    72 hours

Secondary Outcomes (2)

  • Respiratory Support Requirements

    28 days

  • Air Leak

    28 days

Study Arms (2)

Aerosolized Calfactant

EXPERIMENTAL

1. NICU Patients with a clinical diagnosis of RDS 2. Inspired oxygen ≥21% to maintain adequate oxygen saturation 3. Not Intubated 4. Requiring Nasal continuous positive airway pressure

Drug: Aerosolized CalfactantDevice: Solarys

Usual Care

NO INTERVENTION

There will be no protocol driven interventions in the usual care group.

Interventions

Aerosolization of Infasurf at 6ml/kg via the modified Solarys aerosol generator.

Also known as: Infasurf, Calfactant
Aerosolized Calfactant
SolarysDEVICE

Aerosolization of Infasurf at 6ml/kg via the modified Solarys aerosol generator.

Aerosolized Calfactant

Eligibility Criteria

Age1 Hour - 24 Hours
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • RDS Patients
  • NICU patient, ≥1hour of age and \<24 hours of age.
  • Clinical diagnosis of RDS, with or without chest X-ray data.
  • Inspired oxygen ≥21% to maintain adequate oxygen saturation.
  • Not intubated
  • Requiring:
  • nasal continuous positive airway pressure (nCPAP).

You may not qualify if:

  • Congenital anomaly limiting care options or requiring early surgery.
  • Cardiopulmonary decompensation.
  • hypotension with metabolic acidosis (base excess \< -10 meq/l).
  • Oxygen saturations \< 88% at start of aerosolization.
  • PaCO2 ≥ 60 mmHg at start of aerosolization.
  • Grade 3 or Grade 4 intraventricular hemorrhage by cranial ultrasound, if known.
  • Acute hypoxic encephalopathy with or without seizures.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

USA Children's & Women's Hospital

Mobile, Alabama, 36604, United States

Location

Banner - University Medical Center Phoenix

Phoenix, Arizona, 85006, United States

Location

Sharp Mary Birch Hospital for Women & Newborns

San Diego, California, 92123, United States

Location

Baptist Hospital of Miami

Miami, Florida, 33176, United States

Location

Adventist Healthcare System, Florida Hospital

Orlando, Florida, 32803, United States

Location

Johns Hopkins All Children's Hospital

St. Petersburg, Florida, 33701, United States

Location

University of South Florida, Tampa general

Tampa, Florida, 33606, United States

Location

Columbus Regional Hospital

Columbus, Georgia, 31904, United States

Location

OSF Saint Francis Medical Center

Peoria, Illinois, 61637, United States

Location

Kentucky Children's Hospital, University of Kentucky Medical Center

Lexington, Kentucky, 40506, United States

Location

Children's Hospital and Clinics

Minneapolis, Minnesota, 55404, United States

Location

Children's Hospital Minnesota

Saint Paul, Minnesota, 55102, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Sisters of Charity Hospital

Buffalo, New York, 14214, United States

Location

Pitt County Memorial Hospital

Greenville, North Carolina, 27835, United States

Location

The Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Jackson-Madison County General Hospital

Jackson, Tennessee, 38301, United States

Location

Vanderbilt university Medical Center

Nashville, Tennessee, 37232, United States

Location

North central Baptist Hospital

San Antonio, Texas, 78258, United States

Location

Timpanogos Regional Medical Center

Orem, Utah, 84057, United States

Location

Utah Valley Hospital

Provo, Utah, 84604, United States

Location

University of Virgina Medical Center

Charlottesville, Virginia, 22903, United States

Location

Related Publications (1)

  • Cummings JJ, Gerday E, Minton S, Katheria A, Albert G, Flores-Torres J, Famuyide M, Lampland A, Guthrie S, Kuehn D, Weitkamp JH, Fort P, Abu Jawdeh EG, Ryan RM, Martin GC, Swanson JR, Mulrooney N, Eyal F, Gerstmann D, Kumar P, Wilding GE, Egan EA; AERO-02 STUDY INVESTIGATORS. Aerosolized Calfactant for Newborns With Respiratory Distress: A Randomized Trial. Pediatrics. 2020 Nov;146(5):e20193967. doi: 10.1542/peds.2019-3967. Epub 2020 Oct 15.

MeSH Terms

Conditions

Respiratory Distress SyndromePremature Birth

Interventions

calfactant

Condition Hierarchy (Ancestors)

Lung DiseasesRespiratory Tract DiseasesRespiration DisordersObstetric Labor, PrematureObstetric Labor ComplicationsPregnancy ComplicationsFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital Diseases

Results Point of Contact

Title
James Cummings, MD
Organization
Ony Biotech

Study Officials

  • James Cummings, MD

    Albany Medical College

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 16, 2017

First Posted

February 23, 2017

Study Start

March 29, 2017

Primary Completion

June 1, 2018

Study Completion

July 31, 2018

Last Updated

May 29, 2024

Results First Posted

May 29, 2024

Record last verified: 2024-05

Data Sharing

IPD Sharing
Will not share

Locations