NCT03037164

Brief Summary

To evaluate the safety and efficacy of red blood cells (RBCs) prepared with the INTERCEPT Blood System for Red Blood Cells Pathogen Reduction Treatment (PRT) in comparison to conventional RBCs in patients who require RBC transfusion support.

Trial Health

78
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
692

participants targeted

Target at P75+ for phase_3

Timeline
6mo left

Started May 2017

Longer than P75 for phase_3

Geographic Reach
3 countries

16 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress94%
May 2017Dec 2026

First Submitted

Initial submission to the registry

January 26, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

January 31, 2017

Completed
3 months until next milestone

Study Start

First participant enrolled

May 11, 2017

Completed
9.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 31, 2026

Expected
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 30, 2026

Last Updated

March 20, 2026

Status Verified

March 1, 2026

Enrollment Period

9.2 years

First QC Date

January 26, 2017

Last Update Submit

March 18, 2026

Conditions

Keywords

INTERCEPTRed Blood CellsRBCPathogen InactivationZikaCerusPathogen Reduction

Outcome Measures

Primary Outcomes (3)

  • Adjusted hemoglobin increment

    The difference between the pre-transfusion and post transfusion episode hemoglobin values divided by the total hemoglobin content transfused, averaged over one or more transfusion episodes in patients without active bleeding at baseline (active bleeding is defined as WHO Grade 3 or 4 bleeding)

    15 minutes - 24 hours post transfusion

  • Adverse Events

    Proportion of patients with any treatment-emergent adverse events (AEs) possibly, probably, or definitely related to study RBC transfusion through 28 days after the last study transfusion.

    28 days

  • Treatment emergent antibodies

    The proportion of patients with treatment emergent antibodies with confirmed specificity to IBS RBCs

    75 days

Secondary Outcomes (8)

  • Adjusted hemoglobin consumption

    211 Days

  • HbA clearance

    211 days

  • Adverse Events

    28 Days after last study transfusion

  • Transfusion reactions related to study RBCs (test or control)

    28 Days after last study transfusion

  • RBC allo-antigens

    28 days

  • +3 more secondary outcomes

Study Arms (2)

INTERCEPT (Test)

EXPERIMENTAL

Red blood cell components treated with the INTERCEPT Blood System for Red Blood Cells ordered and administered to study patients by their treating physicians according to the local standards of care

Device: INTERCEPT Blood System for Red Blood Cells

Conventional (Control)

ACTIVE COMPARATOR

Conventional RBC components ordered and administered to study patients by their treating physicians according to the local standards of care

Device: Conventional (Control)

Interventions

The pathogen reduction process begins with a unit of RBCs derived from whole blood that is separated according to local regulations and standard operating procedures at the Blood Centers. RBCs are suspended in AS-5 or SAG-M for non-US sites. Leukocyte-reduction of whole blood or RBCs will be performed per manufacturer's instructions. The INTERCEPT Blood System process is performed on a single unit of leukocyte-depleted RBC in AS-5.

INTERCEPT (Test)

Conventional RBC components ordered and administered to study patients by their treating physicians according to the local standards of care

Conventional (Control)

Eligibility Criteria

Age4 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 4 years.
  • Patients who require or are expected to require a transfusion of RBC component(s), including red cell exchange transfusion
  • Signed and dated informed consent form.
  • Female patients of child-bearing potential must:
  • Have negative serum or urine pregnancy tests performed at the Screening visit within 30 days of randomization to rule out pregnancy, and
  • Agree to use to use at least one method of birth control that results in a low failure rate (i.e., less than 1% per year) when used consistently and correctly such as implants, injectables, combined oral contraceptives, some intrauterine devices (IUDs), sexual abstinence or vasectomized partner for the duration of study participation and an additional 28 days.
  • For 28-day +6-month extension study in patients requiring repeated simple transfusions:
  • A diagnosis of a bone marrow failure syndrome requiring repeated RBC transfusion for congenital or acquired chronic anemia (e.g., sickle cell anemia, thalassemia, other hemoglobinopathies, myelodysplastic syndrome, aplastic anemia, chemotherapy or stem cell transplant etc.)
  • For 28-day +6-month extension study in SCD patients requiring regular repeated RCE.
  • Diagnosis of SCD, either HbSS, HbSC or HbSB0 thalassemia, confirmed by Hb electrophoresis, deoxyribonucleic acid (DNA) analysis or high-performance liquid chromatography (HPLC)
  • Currently participating in an automated RCE transfusion program (for at least 3 months prior to enrollment) with 3-to-8 week intervals between RCE episodes

You may not qualify if:

  • Confirmed positive baseline serum/plasma antibody specific to IBS RBC (S- 303 treated RBC) as determined by INTERCEPT S 303 antibody screening panel prior to receiving the first study transfusion
  • Pregnant or breast feeding.
  • Presence of an RBC warm autoantibody with evidence of active hemolysis.
  • Positive DAT as defined below:
  • A polyspecific-DAT reaction strength \> 2+, or
  • A polyspecific-DAT (any strength) in conjunction with pan-reactivity with a commercial IAT antibody screening panel that precludes the identification of underlying alloantibodies or indicates the presence of autoantibody.
  • Patients presenting with or expected to have massive hemorrhage (≥10 RBC units within 24 hours) or expected to require massive transfusion protocols. Planned RCE does not apply.
  • Patients who require neonatal transfusions and intrauterine transfusions.
  • Pre-existing antibody to RBC antigens that may make the provision of compatible study RBC components difficult.
  • History of transfusion reactions requiring washed RBCs, volume reduced RBC, or RBCs with additive solution removed.
  • Patients with documented IgA deficiency or a history of severe allergic reactions to blood products.
  • For SCD patients to be enrolled into the 28-day +6-month repeated RCE arm of the study:
  • A history of acute chest syndrome in the last 6 months, or hyperhemolysis syndrome at any time.
  • Clinical evidence of splenic hyperfunction or splenic enlargement: ≥18 cm in longitudinal diameter (diagnosed at the Investigator's discretion according to the data available, with ultrasound data being preferable).
  • Currently receiving chemotherapy for treatment of cancer. Hydroxyurea for SCD is acceptable if subject has been on stable therapy for 3 months and no changes to dosage are planned.
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Phoenix Children's Hospital (PCH)

Phoenix, Arizona, 85016, United States

Location

Yale University

New Haven, Connecticut, 06520, United States

Location

Mayo Clinic Jacksonville

Jacksonville, Florida, 32224, United States

Location

Grady Health System

Atlanta, Georgia, 30303, United States

Location

CHOA (Children's Healthcare of Atlanta)

Atlanta, Georgia, 30316, United States

Location

University of Maryland School of Medicine

Baltimore, Maryland, 21201, United States

Location

C4TKs (Cure 4 The Kids)

Las Vegas, Nevada, 89135, United States

Location

St Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Baylor St. Luke's Medical Center

Houston, Texas, 77303, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Versiti

Wauwatosa, Wisconsin, 53226, United States

Location

Menonita General Hospital

Aibonito, 00705, Puerto Rico

Location

HIMA San Pablo Hospital

Caguas, 00725, Puerto Rico

Location

San Juan Bautista School of Medicine Clinical Research Unit

Caguas, 00725, Puerto Rico

Location

Ege University Hospital

Izmir, 35100, Turkey (Türkiye)

Location

MeSH Terms

Conditions

AnemiaZika Virus Infection

Interventions

Erythrocyte Count

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic DiseasesMosquito-Borne DiseasesVector Borne DiseasesInfectionsArbovirus InfectionsVirus DiseasesFlavivirus InfectionsFlaviviridae InfectionsRNA Virus Infections

Intervention Hierarchy (Ancestors)

Blood Cell CountCell CountCytological TechniquesClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisHematologic TestsInvestigative TechniquesCell Physiological PhenomenaBlood Physiological PhenomenaCirculatory and Respiratory Physiological Phenomena

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 26, 2017

First Posted

January 31, 2017

Study Start

May 11, 2017

Primary Completion (Estimated)

July 31, 2026

Study Completion (Estimated)

December 30, 2026

Last Updated

March 20, 2026

Record last verified: 2026-03

Locations