NCT02972658

Brief Summary

This study is an extension of study I8D-MC-AZES (NCT02245737), the AMARANTH study. The purpose of this study is to evaluate the effectiveness of the study drug lanabecestat in participants with early Alzheimer's disease dementia at the time of entry into study I8D-MC-AZES.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
421

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2017

Geographic Reach
14 countries

133 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 21, 2016

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 23, 2016

Completed
4 months until next milestone

Study Start

First participant enrolled

March 15, 2017

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 2, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 2, 2018

Completed
9 months until next milestone

Results Posted

Study results publicly available

July 5, 2019

Completed
Last Updated

December 3, 2019

Status Verified

November 1, 2019

Enrollment Period

1.6 years

First QC Date

November 21, 2016

Results QC Date

June 11, 2019

Last Update Submit

November 19, 2019

Conditions

Keywords

Alzheimer's DiseaseDementiaBrain DiseasesNeurodegenerative DiseasesCentral Nervous System DiseasesNervous System DiseasesMental DisordersDelirium, Dementia, Amnestic, Cognitive DisordersTauopathiesMemoryAmyloid

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline Analysis on the 13-item Alzheimer's Disease Assessment Scale - Cognitive Subscale (ADAS-Cog13)

    ADAS-Cog13 (13-item version of ADAS-Cog) is a psychometric instrument that evaluates word recall, ability to follow commands, constructional praxis, naming, ideational praxis, orientation, word recognition, memory, comprehension of spoken language, word-finding, and language ability, with a measure of delayed word recall and concentration/ distractibility. The total score of the 13-item scale ranges from 0 to 85, with an increase in score indicating cognitive worsening. Least Squares (LS) mean was determined by mixed-model repeated measures (MMRM) model with factors for treatment, visit, treatment\*visit, baseline efficacy score, baseline efficacy score-by-visit interaction, disease status at baseline, apolipoprotein E4 (APOE4) status, acetylcholinesterase inhibitor (AChEI) use at baseline, age at baseline, and pooled country.

    AZES Baseline through AZFD Week 26

Secondary Outcomes (5)

  • Change From Baseline Analysis on the Alzheimer´s Disease Cooperative Study Activities of Daily Living Inventory Instrumental Items (ADCS-iADL)

    AZES Baseline through AZFD Week 26

  • Change From Baseline on the Functional Activities Questionnaire (FAQ) Score

    AZES Baseline through AZFD Week 26

  • Change From Baseline on the Integrated Alzheimer's Disease Rating Scale (iADRS) Score

    AZES Baseline through AZFD Week 26

  • Change From Baseline on the Mini-Mental Status Examination (MMSE)

    AZES Baseline through AZFD Week 26

  • Change From Baseline Analysis on the ADAS-Cog13

    AZES Baseline through AZFD Week 52

Study Arms (4)

AZES Lanabecestat 20 milligrams (mg)/AZFD Lanabecestat 20 mg

EXPERIMENTAL

Participants who received Lanabecestat 20 mg in the feeder study (AZES) were randomized to receive Lanabecestat 20 mg.

Drug: Lanabecestat

AZES Lanabecestat 50 mg/AZFD Lanabecestat 50 mg

EXPERIMENTAL

Participants who received Lanabecestat 50 mg in the feeder study (AZES) were randomized to receive Lanabecestat 50 mg.

Drug: Lanabecestat

AZES Placebo/AZFD Lanabecestat 20 mg

EXPERIMENTAL

Participants who received placebo in the feeder study (AZES) were randomized to receive Lanabecestat 20 mg.

Drug: Lanabecestat

AZES Placebo/AZFD Lanabecestat 50 mg

EXPERIMENTAL

Participants who received placebo in the feeder study (AZES) were randomized to receive Lanabecestat 50 mg.

Drug: Lanabecestat

Interventions

Administered orally

Also known as: LY3314814, AZD3293
AZES Lanabecestat 20 milligrams (mg)/AZFD Lanabecestat 20 mgAZES Lanabecestat 50 mg/AZFD Lanabecestat 50 mgAZES Placebo/AZFD Lanabecestat 20 mgAZES Placebo/AZFD Lanabecestat 50 mg

Eligibility Criteria

Age55 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants previously enrolled in AMARANTH (NCT02245737) who meet eligibility criteria for delayed-start I8D-MC-AZFD.

You may not qualify if:

  • Participants who participate in AMARANTH (NCT02245737) who develop new conditions precluding them from enrolling into I8D-MC-AZFD.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (133)

Banner Alzheimer's Institute

Phoenix, Arizona, 85006, United States

Location

Territory Neurology & Research Institute

Tucson, Arizona, 85704, United States

Location

Pacific Research Network Inc

San Diego, California, 92103, United States

Location

Mile High Research Center

Denver, Colorado, 80218, United States

Location

Institute for Neurodegenerative Disorders

New Haven, Connecticut, 06510, United States

Location

Georgetown University Medical Center

Washington D.C., District of Columbia, 20057, United States

Location

Brain Matters Research

Delray Beach, Florida, 33445, United States

Location

Compass Research

Orlando, Florida, 32806, United States

Location

IMIC, Inc.

Palmetto Bay, Florida, 33157, United States

Location

Roskamp Institute

Sarasota, Florida, 34243, United States

Location

Suncoast Neuroscience Associates

St. Petersburg, Florida, 33713, United States

Location

Premiere Research Institute at Palm Beach Neurology

West Palm Beach, Florida, 33407, United States

Location

The Multiple Sclerosis Center of Atlanta

Atlanta, Georgia, 30327, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Community Clinical Research Center

Anderson, Indiana, 46011, United States

Location

Boston Center for Memory

Newton, Massachusetts, 02459, United States

Location

Hattiesburg Clinic

Hattiesburg, Mississippi, 39401, United States

Location

Memory Enhancement Center of America, Inc.

Eatontown, New Jersey, 07724, United States

Location

The Cognitive and Research Center of NJ

Springfield, New Jersey, 07081, United States

Location

Advanced Memory Research Institute of New Jersey

Toms River, New Jersey, 08755, United States

Location

Integrative Clinical Trials, LLC

Brooklyn, New York, 11229, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

University of Rochester School of Medicine

Rochester, New York, 14620, United States

Location

Valley Medical Primary Care

Centerville, Ohio, 45459, United States

Location

Lindner Research Center

Cincinnati, Ohio, 45219, United States

Location

Ohio State University Medical Center

Columbus, Ohio, 43210, United States

Location

Lehigh Valley Hospital

Allentown, Pennsylvania, 18103, United States

Location

Rhode Island Mood & Memory Research Institute

East Providence, Rhode Island, 02914, United States

Location

Radiant Research

Greer, South Carolina, 29651, United States

Location

Quillen College of Medicine, East TN State University

Johnson City, Tennessee, 37604, United States

Location

The Memory Clinic

Bennington, Vermont, 05201, United States

Location

Southern Neurology

Kogarah, New South Wales, 2217, Australia

Location

Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Eastern Clinical Research Unit

Box Hill, Victoria, 3128, Australia

Location

Delmont Private Hospital

Glen Iris, Victoria, 3146, Australia

Location

The Florey Institute of Neuroscience and Mental Health

Parkville, Victoria, 3052, Australia

Location

Australian Alzheimer's Research Foundation

Nedlands, Western Australia, 6009, Australia

Location

Neuro Trials Victoria Pty Ltd

Noble Park, 3174, Australia

Location

Jessa Ziekenhuis

Hasselt, Limburg, 3500, Belgium

Location

Hopital Universitaire Brugmann Brussel

Brussels, 1020, Belgium

Location

Hospital Universitaire Erasme Brussel

Brussels, 1070, Belgium

Location

Cliniques Universitaires Saint-Luc

Brussels, 1200, Belgium

Location

Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

Leuven, 3000, Belgium

Location

AZ Delta

Roeselare, 8800, Belgium

Location

Okanagan Clinical Trials

Kelowna, British Columbia, V1Y 1Z9, Canada

Location

True North Clinical Research Halifax, LLC

Halifax, Nova Scotia, B3S1M7, Canada

Location

Elizabeth Bruyere Health Centre

Ottawa, Ontario, KIN 5C8, Canada

Location

Kawartha Regional Memory Clinic

Peterborough, Ontario, K9H2P4, Canada

Location

Toronto Memory Program

Toronto, Ontario, M3B 2S7, Canada

Location

Clinique de la Memoire de l'Outaouais

Gatineau, Quebec, J8T 8J1, Canada

Location

NeuroSearch Developements

Greenfield Park, Quebec, J4V 2J2, Canada

Location

Hopital de L'Enfant Jesus

Québec, Quebec, G1J 1Z4, Canada

Location

Q&T Research Sherbrooke Inc

Sherbrooke, Quebec, J1J 2G2, Canada

Location

Centre Hospitalier Universitaire La Timone

Marseille, Cedex 05, 13385, France

Location

CHRU de Lille- Hôpital Roger Salengro

Lille, Cedex, 59037, France

Location

CHU de Toulouse Hopital Purpan

Toulouse, Cedex, 31059, France

Location

Hopital Neuro Pierre Wertheimer

Bron, 69677, France

Location

CHU Bocage CMRR

Dijon, 21079, France

Location

Hopital Broca

Paris, 75013, France

Location

Hôpital de la Pitié-Salpêtrière

Paris, 75013, France

Location

Hôpital Fernand Widal

Paris, 75475, France

Location

Chu de Nantes Hopital Laennec

Saint-Herblain, 44093, France

Location

Centre de Recherche Clinique du Gérontopôle Cité de la Santé

Toulouse, 31052, France

Location

Hopital des Charpennes

Villeurbanne, 69100, France

Location

Universitätsklinikum Ulm

Ulm, Baden-Wurttemberg, 89081, Germany

Location

Studien und Gedächtniszentrum München

München, Bavaria, 80331, Germany

Location

Klinikum Rechts der Isar der TU München

München, Bavaria, 81675, Germany

Location

Gemeinschaftspraxis für Neurologie und Psychiatrie

Westerstede, Lower Saxony, 26655, Germany

Location

DataMed Klinische Studien GmbH

Cologne, North Rhine-Westphalia, 50935, Germany

Location

Universitätsklinikum Köln

Cologne, North Rhine-Westphalia, 50937, Germany

Location

Neurologische Praxis Siegen

Siegen, North Rhine-Westphalia, 57076, Germany

Location

Pharm Studienzentrum Chemnitz

Mittweida, Saxony, 09648, Germany

Location

Charité Universitätsmedizin Berlin

Berlin, 10117, Germany

Location

Charité Universitätsmedizin Berlin

Berlin, 12203, Germany

Location

SE Neurologiai Klinika

Budapest, 1083, Hungary

Location

National Institute for Longevity Sciences NCGG

ÅŒbu, Aichi-ken, 474-0038, Japan

Location

National Chiba-East-Hospital

Chuo-ku, Chiba, 260-8712, Japan

Location

Tsukuba University Hospital

Tsukuba, Ibaraki, 305-8576, Japan

Location

Iwate Medical University Hospital

Morioka, Iwate, 020-8505, Japan

Location

Nihon Kokan Hospital

Kawasaki, Kanagawa, 210-0852, Japan

Location

Katayama Medical Clinic

Kurashiki, Okayama-ken, 701-0192, Japan

Location

Shiroma Clinic

Urasoe, Okinawa, 901-2102, Japan

Location

Sakaguchi Clinic

Sakai, Osaka, 593-8301, Japan

Location

National Sanatorium Toneyama Hospital

Toyonaka, Osaka, 560-8552, Japan

Location

Memory Clinic Ochanomizu

Bunkyo-ku, Tokyo, 113-0034, Japan

Location

Nippon Medical School Hospital

Bunkyo-Ku, Tokyo, 113-8603, Japan

Location

The University of Tokyo Hospital

Bunkyo-ku, Tokyo, 113-8655, Japan

Location

Tokyo Women's Medical University Hospital

Shinjuku-ku, Tokyo, 162-8666, Japan

Location

National Sanatorium Hokuriku Hospital

Nanto, Toyama, 939-1893, Japan

Location

Fukuoka University Hospital

Fukuoka, 814-0180, Japan

Location

Kyoto University Hospital

Kyoto, 606-8507, Japan

Location

Utano Hospital

Kyoto, 616-8255, Japan

Location

Osaka City University Hospital

Osaka, 637086, Japan

Location

Podlaskie Centrum Psychogeriatrii

Bialystok, Podlaskie Voivodeship, 15-732, Poland

Location

NZOZ Dom Sue Ryder - Pallmed Sp. z o.o.

Bydgoszcz, 85-796, Poland

Location

NZOZ Wielospecjalistyczna Poradnia Lekarska

Katowice, 40-123, Poland

Location

Centrum Zdrowia Psychicznego Biomed - Jan Latala

Kielce, 25-411, Poland

Location

Krakowska Akademia Neurologii

Krakow, 31-505, Poland

Location

Medycyna Milorzab

Lodz, 93-118, Poland

Location

Instytut Medycyny Wsi

Lublin, 20-950, Poland

Location

Centrum Medyczne Neuroprotect

Warsaw, 01-697, Poland

Location

Santa Cruz Behavioral PSC

Bayamón, 00961-6911, Puerto Rico

Location

SC Med Life SA

Bucharest, 010719, Romania

Location

SC Centrul Medical Sana SRL

Bucharest, 011025, Romania

Location

Dong-A University Medical Center

Seogu, Busan, 49201, South Korea

Location

Hanyang University Guri Hospital

Guri-si, Gyeonggido, 11923, South Korea

Location

Inha University Hospital

Junggu, Incheon, 22332, South Korea

Location

Samsung Medical Center

Seoul, Korea, 06351, South Korea

Location

Gachon University Gil Medical Center

Incheon, 21565, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Seoul St. Mary's Hospital

Seoul, 06591, South Korea

Location

Hospital General Universitario de Elche

Elche, Alicante, 03203, Spain

Location

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

Location

Hospital Virgen Del Puerto

Plasencia, Caceres, 10600, Spain

Location

Hospital Universitario De Getafe

Madrid, Getafe, 28905, Spain

Location

CITA Alzheimer

Donostia / San Sebastian, Guipuzcoa, 20009, Spain

Location

Centro de Atencion Especializada (CAE) OROITU

Getxo, Vizcaya, 48993, Spain

Location

Fundacion ACE-Institut Catala de Neurociences Aplicades

Barcelona, 08014, Spain

Location

Hospital Santa Creu I Sant Pau

Barcelona, 08025, Spain

Location

Hospital Clinic I Provincial

Barcelona, 08036, Spain

Location

Hospital De La Princesa

Madrid, 28006, Spain

Location

Hospital Universitario Ramon y Cajal

Madrid, 28034, Spain

Location

Hospital Son Espases

Palma de Mallorca, 07010, Spain

Location

Hospital Universitario Dr Pesset

Valencia, 46017, Spain

Location

Hospital Universitario La Fe de Valencia

Valencia, 46026, Spain

Location

Re-Cognition Health Ltd

London, Greater London, W1G 9JF, United Kingdom

Location

MAC Clinical Research-Manchester

Manchester, Greater Manchester, M13 9NQ, United Kingdom

Location

MAC Clinical Research

Blackpool, Lancashire, FY2 0JH, United Kingdom

Location

West London Mental Health NHS Trust

Isleworth, London, TW7 6FY, United Kingdom

Location

MAC Clinical Research

Cannock, Staffordshire, WS11 0BN, United Kingdom

Location

Re-Cognition Health Ltd

Guildford, Surrey, GU2 7YD, United Kingdom

Location

Glasgow Memory Clinic

Glasgow, G20 0XA, United Kingdom

Location

MAC Clinical Research

Leeds, LS10 1DU, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Alzheimer DiseaseDementiaBrain DiseasesNeurodegenerative DiseasesCentral Nervous System DiseasesNervous System DiseasesMental DisordersNeurocognitive DisordersTauopathies

Interventions

lanabecestat

Limitations and Caveats

This study was stopped after an independent assessment concluded that the feeder study AZES was futile. Because of this, the originally planned delayed-start analysis for this study was not performed.

Results Point of Contact

Title
AstraZeneca Information Center
Organization
AstraZeneca

Study Officials

  • Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

    Eli Lilly and Company

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 21, 2016

First Posted

November 23, 2016

Study Start

March 15, 2017

Primary Completion

October 2, 2018

Study Completion

October 2, 2018

Last Updated

December 3, 2019

Results First Posted

July 5, 2019

Record last verified: 2019-11

Data Sharing

IPD Sharing
Will share

Anonymized individual patient level data will be provided in a secure access environment upon approval of a research proposal and a signed data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
Data are available 6 months after the primary publication and approval of the indication studied in the US and EU, whichever is later. Data will be indefinitely available for requesting.
Access Criteria
A research proposal must be approved by an independent review panel and researchers must sign a data sharing agreement.
More information

Locations