NCT02967822

Brief Summary

In order to understand the molecular mechanisms leading to Mayer-Rokitansky-Kuster-Hauser syndrome (MRKH), the research team has to identify molecular bases of this anomaly. Toward this goal, the research team would like to include in the study patients with MRKH syndrome, as well as their healthy relatives, in order to perform genetic analyses, especially whole exome sequencing. This study has been set up in order to collect biological samples from patients with MRKH and their relatives.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
410

participants targeted

Target at P75+ for all trials

Timeline
61mo left

Started May 2016

Longer than P75 for all trials

Geographic Reach
1 country

2 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress67%
May 2016May 2031

Study Start

First participant enrolled

May 1, 2016

Completed
7 months until next milestone

First Submitted

Initial submission to the registry

November 14, 2016

Completed
4 days until next milestone

First Posted

Study publicly available on registry

November 18, 2016

Completed
14.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2031

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2031

Last Updated

October 12, 2018

Status Verified

October 1, 2018

Enrollment Period

15 years

First QC Date

November 14, 2016

Last Update Submit

October 10, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of identified nucleotidic variation(s) whose consequences can explain the phenotype of MRKH syndrome

    Genetic cause identification

    15 years

Study Arms (2)

Patients with MRKH syndrome

Biological samples for patients. Inclusion of patients presenting MRKH syndrome, and who are followed in clinical centres participating in the study.

Genetic: Biological samples for patients

Healthy relatives

Biological samples for healthy relatives. Inclusion of healthy relatives of patients included in the study (parents, brothers, sisters)

Genetic: Biological samples for healthy relatives

Interventions

Blood samples. Sampling of uterine tissue during surgical intervention (collection of samples for the study only if samples remain after the routine care analyses)

Patients with MRKH syndrome

Blood samples.

Healthy relatives

Eligibility Criteria

Sexall
Healthy VolunteersYes
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Recruitment of patients presenting MRKH syndrome, as well as their healthy relatives, in order to perform genetic analyses

You may qualify if:

  • Patient with MRKH syndrome OR healthy relative of patient included
  • Having signed the Informed consent form (or parents in case of patient under 18 years)

You may not qualify if:

  • Refusal to participate in genetic analyses

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Necker - Enfants malades hospital

Paris, 75015, France

RECRUITING

Institut Mutualiste Montsouris

Paris, France

RECRUITING

Biospecimen

Retention: SAMPLES WITH DNA

* Blood samples (for patients and healthy relatives) * Uterine tissue (for patients who have a surgical intervention during their routine follow-up, and only if samples remain available after routine care analyses).

MeSH Terms

Conditions

Mullerian aplasia

Study Officials

  • Stanislas Lyonnet

    Institut Imagine

    STUDY DIRECTOR
  • Michel Polak

    Necker - Enfants malades hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2016

First Posted

November 18, 2016

Study Start

May 1, 2016

Primary Completion (Estimated)

May 1, 2031

Study Completion (Estimated)

May 1, 2031

Last Updated

October 12, 2018

Record last verified: 2018-10

Data Sharing

IPD Sharing
Will not share

Locations