NCT02951026

Brief Summary

This long-term extension study is designed to monitor the long-term safety, tolerability, and efficacy of treatment of SM04690 or placebo previously injected in the target knee joints of subjects with moderately to severely symptomatic osteoarthritis (OA) from a Samumed-sponsored SM04690-OA phase 2 or phase 3 study. No additional SM04690 or placebo therapy will be administered in this study.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
703

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Sep 2016

Typical duration for all trials

Geographic Reach
1 country

62 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 19, 2016

Completed
18 days until next milestone

First Submitted

Initial submission to the registry

October 7, 2016

Completed
25 days until next milestone

First Posted

Study publicly available on registry

November 1, 2016

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 31, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 31, 2019

Completed
Last Updated

April 17, 2020

Status Verified

April 1, 2020

Enrollment Period

3.1 years

First QC Date

October 7, 2016

Last Update Submit

April 15, 2020

Conditions

Keywords

kneeosteoarthritisintra-articular injectionSM04690

Outcome Measures

Primary Outcomes (1)

  • Incidence rate of serious adverse events (SAEs)

    Compare the incidence rate of SAEs occurring in the (previously injected) SM04690 treatment arms to the (previously injected) placebo treatment arm by Month 60

    Month 60

Secondary Outcomes (43)

  • Adverse events (AEs) of interest

    Month 6

  • AEs of interest

    Month 12

  • AEs of interest

    Month 24

  • AEs of interest

    Month 36

  • AEs of interest

    Month 48

  • +38 more secondary outcomes

Study Arms (4)

0.03mg SM04690 (previously injected)

Subjects in this group received a single intra-articular injection of 0.03mg SM04690 into the target knee during the "parent" study prior to enrolling in this observational study.

Other: Not applicable (no therapy is administered as part of this study)

0.07mg SM04690 (previously injected)

Subjects in this group received a single intra-articular injection of 0.07mg SM04690 into the target knee during the "parent" study prior to enrolling in this observational study.

Other: Not applicable (no therapy is administered as part of this study)

0.23mg SM04690 (previously injected)

Subjects in this group received a single intra-articular injection of 0.23mg SM04690 into the target knee during the "parent" study prior to enrolling in this observational study.

Other: Not applicable (no therapy is administered as part of this study)

Placebo (previously injected)

Subjects in this group received a single intra-articular injection of placebo into the target knee during the "parent" study prior to enrolling in this observational study.

Other: Not applicable (no therapy is administered as part of this study)

Interventions

No experimental therapy or placebo is being administered in this study. All subjects in this observational study received a single intra-articular injection of SM04690 or placebo in a prior "parent" study.

0.03mg SM04690 (previously injected)0.07mg SM04690 (previously injected)0.23mg SM04690 (previously injected)Placebo (previously injected)

Eligibility Criteria

Age40 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Subjects can only participate in this study upon completion of a Samumed SM04690-OA phase 2 or phase 3 study.

You may qualify if:

  • Completion of scheduled end-of-study visit of Samumed-sponsored SM04690-OA phase 2 or phase 3 studies
  • Full understanding of the requirements of the study and willingness to comply with all study visits and assessments
  • Subjects must have read and understood the informed consent form, and must have signed it prior to any study-related procedure being performed

You may not qualify if:

  • Unable to undergo the radiograph procedures detailed within the protocol
  • Partial or complete joint replacement in the target knee
  • Subjects who are immediate family members (spouse, parent, child, or sibling; biological or legally adopted) of personnel directly affiliated with the study at the investigative site, or are directly affiliated with the study at the investigative site
  • Subjects employed by Samumed, LLC, or any of its affiliates or development partners (that is, an employee, temporary contract worker, or designee) responsible for the conduct of the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (62)

Research Site

Birmingham, Alabama, United States

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Oro Valley, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Canoga Park, California, United States

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Carmichael, California, United States

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Cerritos, California, United States

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El Cajon, California, United States

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Gold River, California, United States

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La Mesa, California, United States

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Palm Springs, California, United States

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Rancho Mirage, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Marcos, California, United States

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Spring Valley, California, United States

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Boulder, Colorado, United States

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Stamford, Connecticut, United States

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Trumbull, Connecticut, United States

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Waterbury, Connecticut, United States

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Clearwater, Florida, United States

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Coral Gables, Florida, United States

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DeLand, Florida, United States

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Edgewater, Florida, United States

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Lauderdale Lakes, Florida, United States

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Miami, Florida, United States

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Marietta, Georgia, United States

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Woodstock, Georgia, United States

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Chicago, Illinois, United States

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Newton, Kansas, United States

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Wichita, Kansas, United States

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Lexington, Kentucky, United States

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Frederick, Maryland, United States

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Boston, Massachusetts, United States

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Troy, Michigan, United States

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City of Saint Peters, Missouri, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Lincoln, Nebraska, United States

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Las Vegas, Nevada, United States

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Albuquerque, New Mexico, United States

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Orchard Park, New York, United States

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Rochester, New York, United States

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Charlotte, North Carolina, United States

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High Point, North Carolina, United States

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Raleigh, North Carolina, United States

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Salisbury, North Carolina, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Duncansville, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Mt. Pleasant, South Carolina, United States

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Rapid City, South Dakota, United States

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Knoxville, Tennessee, United States

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Austin, Texas, United States

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Bedford, Texas, United States

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Houston, Texas, United States

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San Angelo, Texas, United States

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Layton, Utah, United States

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Arlington, Virginia, United States

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Charlottesville, Virginia, United States

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Related Publications (1)

  • Swearingen CJ, Tambiah JRS, Simsek I, Ghandehari H, Kennedy S, Yazici Y. Evaluation of Safety and Efficacy of a Single Lorecivivint Injection in Patients with Knee Osteoarthritis: A Multicenter, Observational Extension Trial. Rheumatol Ther. 2025 Feb;12(1):157-171. doi: 10.1007/s40744-024-00731-9. Epub 2025 Jan 4.

MeSH Terms

Conditions

Osteoarthritis

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic Diseases

Study Officials

  • Yusuf Yazici, M.D.

    Biosplice Therapeutics, Inc.

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 7, 2016

First Posted

November 1, 2016

Study Start

September 19, 2016

Primary Completion

October 31, 2019

Study Completion

October 31, 2019

Last Updated

April 17, 2020

Record last verified: 2020-04

Locations