NCT02932449

Brief Summary

This is a 5-year, longitudinal, observational study of patients with PBC designed to specifically address important clinical questions that remain incompletely answered from registration trials. In addition to the study database, a bio specimen repository will also be included so that translational studies of genomics and biomarkers of response may be performed.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
711

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Oct 2016

Longer than P75 for all trials

Geographic Reach
1 country

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 7, 2016

Completed
24 days until next milestone

Study Start

First participant enrolled

October 1, 2016

Completed
12 days until next milestone

First Posted

Study publicly available on registry

October 13, 2016

Completed
8.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 23, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 23, 2025

Completed
Last Updated

February 18, 2026

Status Verified

February 1, 2026

Enrollment Period

8.3 years

First QC Date

September 7, 2016

Last Update Submit

February 16, 2026

Conditions

Outcome Measures

Primary Outcomes (4)

  • Evaluate PBC treatment regimens being used in clinical practice

    up to 5 years

  • Examine populations underrepresented in phase III clinical trials

    up to 5 years

  • Examine biochemical response and its association with long term outcomes

    up to 5 years

  • Estimate adverse event frequency and severity and describe management practices

    up to 5 years

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

adults with PBC who are being seen specifically to address this disease process

You may qualify if:

  • Adult patients (age 18 or older) being treated or managed for PBC

You may not qualify if:

  • Inability to provide written informed consent
  • Simultaneous enrollment in another prospective registry or clinical trial or study where PBC treatment outcomes are reported, except where approved or conducted as an adjunct project of TARGET-PBC

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Institute for Liver Health

Chandler, Arizona, 85224, United States

Location

Banner University Medical Center

Phoenix, Arizona, 85006, United States

Location

Mayo Clinic

Phoenix, Arizona, 85054, United States

Location

University of Arkansas

Little Rock, Arkansas, 72204, United States

Location

Stanford University Medical Center

Palo Alto, California, 94304, United States

Location

California Liver Research Institute

Pasadena, California, 91105, United States

Location

University of California Davis

Sacramento, California, 95817, United States

Location

University of Colorado- Anschutz Medical Campus

Aurora, Colorado, 80045, United States

Location

Yale Internal Medicine, Digestive Diseases

New Haven, Connecticut, 06520, United States

Location

Gastro Florida

Clearwater, Florida, 33762, United States

Location

University of Florida Hepatology Research

Gainesville, Florida, 32610, United States

Location

SCFLD/University of Miami

Miami, Florida, 33136, United States

Location

Piedmont Atlanta Hospital

Atlanta, Georgia, 30309, United States

Location

Illinois Gastroenterology Group

Arlington Heights, Illinois, 60005, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

Mercy Medical Center, GI Research

Baltimore, Maryland, 21202, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Southern Therapy and Advanced Research LLC (STAR)

Jackson, Mississippi, 39216, United States

Location

Saint Louis University

St Louis, Missouri, 63104, United States

Location

University of Nebraska

Omaha, Nebraska, 68106, United States

Location

Sandra Atlas Bass Center for Liver Diseases

Manhasset, New York, 11030, United States

Location

NYU Langone Health

New York, New York, 10016, United States

Location

Weill Cornell Medical College

New York, New York, 10021, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Center for Liver Disease and Transplant at CMC

Charlotte, North Carolina, 28204, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Ohio State University Medical Center

Columbus, Ohio, 43210, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Baylor,Scott and White All Saints

Fort Worth, Texas, United States

Location

Liver Associates of Texas, P.A.

Houston, Texas, 77030, United States

Location

Pinnacle Clinical Research

Live Oak, Texas, 78233, United States

Location

Bon Secours Liver Institute of Virginia

Richmond, Virginia, 23226, United States

Location

Virginia Commonwealth University (VCU)

Richmond, Virginia, 23298, United States

Location

University of Washington

Seattle, Washington, 98104, United States

Location

University of Wisconsin

Madison, Wisconsin, 53705, United States

Location

Biospecimen

Retention: SAMPLES WITH DNA

Participants enrolled in TARGET-PBC will be invited to participate in the optional Biorepository Specimen Bank (BSB). Blood samples for biomarker and DNA/RNA assays will be collected on a voluntary basis and participation in this project will not affect participation in the main study. Blood samples for exploratory genetic and biomarker studies can be used for research purposes to identify potential biomarkers predictive of PBC diagnosis, assess correlates of response to PBC treatment (in terms of mode of action, efficacy, dose, safety and tolerability), understand factors influencing disease progression, determine how best to monitor and treat PBC, aid in the development of a new medical products, or explore complications of PBC and treatment.

MeSH Terms

Conditions

Liver Cirrhosis, Biliary

Condition Hierarchy (Ancestors)

Cholestasis, IntrahepaticCholestasisBile Duct DiseasesBiliary Tract DiseasesDigestive System DiseasesLiver DiseasesLiver CirrhosisFibrosisPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 7, 2016

First Posted

October 13, 2016

Study Start

October 1, 2016

Primary Completion

January 23, 2025

Study Completion

January 23, 2025

Last Updated

February 18, 2026

Record last verified: 2026-02

Locations