NCT02865915

Brief Summary

This is a Phase 2b double-blind, randomized, parallel-group, placebo-controlled study of MLE4901 versus placebo in women with PCOS.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
55

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jul 2016

Shorter than P25 for phase_2

Geographic Reach
1 country

31 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2016

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

August 10, 2016

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 15, 2016

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2017

Completed
2.8 years until next milestone

Results Posted

Study results publicly available

June 16, 2020

Completed
Last Updated

February 1, 2021

Status Verified

January 1, 2021

Enrollment Period

1.2 years

First QC Date

August 10, 2016

Results QC Date

June 1, 2020

Last Update Submit

January 28, 2021

Conditions

Keywords

AcneHirsutismMenstrual IrregularityAlopecia

Outcome Measures

Primary Outcomes (1)

  • Menstrual Cycle Duration

    Assessment of the number of days between menstrual cycles (i.e., days between the start of a menstrual period and the start of the next consecutive menstrual period) from baseline to end of 28 week double blind treatment period

    28 Week double blind treatment period

Secondary Outcomes (1)

  • Number of Menstrual Periods

    28 Week double blind treatment period

Study Arms (2)

Placebo

PLACEBO COMPARATOR

Plain, round, biconvex, white film-coated tablets that appear identical to MLE4901 tablets

Drug: Placebo

MLE4901

EXPERIMENTAL

Plain, round, biconvex, white film-coated tablets administered twice per day

Drug: MLE4901

Interventions

For 80% of subjects randomized to MLE4901 (n=24/30), the dose is 40 mg twice daily. Six subjects (20%) randomized to higher MLE4901 dose cohorts that were promptly discontinued.

MLE4901

Placebo to match active drug

Placebo

Eligibility Criteria

Age18 Years - 45 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Oligo-/amenorrhea
  • At least one of the following during Screening:
  • Clinical signs of hyperandrogenism, where clinical hyperandrogenism may include hirsutism (defined as excessive terminal hair that appears in a male pattern), acne, or androgenic alopecia
  • Biochemical hyperandrogenism refers to an elevated serum androgen level (i.e., total, bioavailable or free testosterone level ≥ULN)
  • Polycystic ovarian morphology, defined as the presence of 12 or more follicles 2-9 mm in diameter and/or an increased ovarian volume \>10 mL (without a cyst or dominant follicle) in either ovary
  • Body mass index (BMI) 22 to 45 kg/m2, inclusive
  • Must be willing to avoid use of all hair removal procedures and products during study participation
  • Must be willing to avoid all prescription treatments for acne and not increase the dose or frequency of their current non-prescription acne treatment regimen during study participation
  • Must be willing to avoid the use of all hair growth procedures and products during study participation
  • Permanently surgically sterilized (bilateral salpingectomy or tubal occlusion) \>2 years or male partner(s) has had a vasectomy \>2 years or must consent to use two permitted medically-acceptable methods of contraception throughout the study during any sexual intercourse with a male partner. Permitted medically-acceptable methods of birth control for this study are defined as use of a male condom plus one of the following: spermicide, diaphragm with spermicide, or an intrauterine device that does not contain steroid hormones.

You may not qualify if:

  • Menopausal or peri-menopausal, defined for this study as FSH (follicle stimulating hormone ) \>10 IU/L
  • Irregular vaginal/menstrual bleeding caused by conditions other than PCOS (e.g., uterine polyps or submucosal uterine fibroids)
  • Abnormal Papanicolaou (Pap) test during Screening requiring follow-up sooner than 1 year after the test
  • Uncontrolled hypo- or hyperthyroidism
  • Post-hysterectomy or endometrial ablation
  • Post-oophorectomy (unilateral or bilateral) or other ovarian surgery
  • Medical history of type 1 or type 2 diabetes mellitus

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (31)

Hope Research Institute, LLC

Phoenix, Arizona, 85018, United States

Location

NEA Baptist Clinic

Jonesboro, Arkansas, 72401, United States

Location

Excell Research

Oceanside, California, 92056, United States

Location

Clinical Research Consulting, LLC

Milford, Connecticut, 06460, United States

Location

Avail Clinical Research, LLC

DeLand, Florida, 32720, United States

Location

Health Care Family Rehab & Research Center

Hialeah, Florida, 33012, United States

Location

University of Florida (UF)

Jacksonville, Florida, 32207, United States

Location

Palmetto Professional Research

Miami, Florida, 33175, United States

Location

Segal Institute for Clinical Research

North Miami, Florida, 33161, United States

Location

Compass Research, LLC

Orlando, Florida, 32806, United States

Location

Stedman Clinical Trials, LLC

Tampa, Florida, 33613, United States

Location

Atlanta Women's Research Institute

Atlanta, Georgia, 30342, United States

Location

Advanced Clinical Research

Boise, Idaho, 83642, United States

Location

Womens Health Practice

Champaign, Illinois, 61820, United States

Location

GTC Enterprises LLC

Shawnee Mission, Kansas, 66218, United States

Location

Montana Health Research Institute, Inc.

Billings, Montana, 59102, United States

Location

Upstate Clinical Research Associates

Williamsville, New York, 14221, United States

Location

PMG Research of Cary

Cary, North Carolina, 27518, United States

Location

Rapid Medical Research, Inc.

Cleveland, Ohio, 44122, United States

Location

Aventiv Research, Inc.

Columbus, Ohio, 43213, United States

Location

University Hospitals Cleveland Medical Center

Mayfield Heights, Ohio, 44124, United States

Location

Clinical Research of Tiffin

Tiffin, Ohio, 44883, United States

Location

Main Line Fertility and Reproductive Medicine

Bryn Mawr, Pennsylvania, 19010, United States

Location

The Pennsylvania State University (Penn State) Milton S. Hershey Medical Center

Hershey, Pennsylvania, 17033, United States

Location

University of Pennsylvania Perelman Center for Advanced Medicine - Penn Fertility Care

Philadelphia, Pennsylvania, 19104, United States

Location

Magnolia OB/GYN Research Center

Myrtle Beach, South Carolina, 29572, United States

Location

Texas Diabetes and Endocrinology, P.A. - South Austin

Austin, Texas, 78749, United States

Location

Wasatch Clinical Research

Salt Lake City, Utah, 84107, United States

Location

Highland Clinical Research

Salt Lake City, Utah, 84124, United States

Location

Charlottesville Medical Research Center, LLC

Charlottesville, Virginia, 22911, United States

Location

Tidewater Clinical Research, Inc.

Norfolk, Virginia, 23502, United States

Location

MeSH Terms

Conditions

Polycystic Ovary SyndromeAcne VulgarisHirsutismMenstruation DisturbancesAlopecia

Condition Hierarchy (Ancestors)

Ovarian CystsCystsNeoplasmsOvarian DiseasesAdnexal DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesGonadal DisordersEndocrine System DiseasesAcneiform EruptionsSkin DiseasesSkin and Connective Tissue DiseasesSebaceous Gland DiseasesHair DiseasesVirilismSigns and SymptomsPathological Conditions, Signs and SymptomsPathologic ProcessesHypotrichosisPathological Conditions, Anatomical

Limitations and Caveats

Due to termination of the study by the Sponsor, no patients completed the study. No efficacy data are available because study termination occurred prior to scheduled assessments.

Results Point of Contact

Title
Director of Clinical Operations
Organization
Millendo Therapeutics US, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 10, 2016

First Posted

August 15, 2016

Study Start

July 1, 2016

Primary Completion

September 1, 2017

Study Completion

September 1, 2017

Last Updated

February 1, 2021

Results First Posted

June 16, 2020

Record last verified: 2021-01

Data Sharing

IPD Sharing
Will not share

Locations