NCT02848521

Brief Summary

This is a prospective, non-interventional study (NIS) measuring health-related quality of life (HRQoL), treatment satisfaction, and other patient-reported outcomes (PROs) of ADPKD patients in Europe.

Trial Health

50
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
407

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Oct 2016

Typical duration for all trials

Geographic Reach
7 countries

26 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 21, 2016

Completed
7 days until next milestone

First Posted

Study publicly available on registry

July 28, 2016

Completed
2 months until next milestone

Study Start

First participant enrolled

October 1, 2016

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2019

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2020

Completed
Last Updated

April 11, 2019

Status Verified

September 1, 2018

Enrollment Period

3 years

First QC Date

July 21, 2016

Last Update Submit

April 9, 2019

Conditions

Keywords

ADPKDCKDRapid progressorquality of lifeDCE

Outcome Measures

Primary Outcomes (1)

  • Mean rate of change (%) in Physical Health Composite Scale (PCS) scores of the 12-Item Short Form Survey (SF-12)

    Mean rate of change (%) in Physical Health Composite Scale (PCS) scores of the SF-12 from baseline to end of study, in the overall sample and per chronic kidney disease (CKD) stage.

    From Baseline to end of study (maximum of 18 months)

Secondary Outcomes (6)

  • Mean rate of change (%) in Mental Health Composite Scale (MCS) scores of the SF-12

    From Baseline to end of study (maximum of 18 months)

  • Mean ADPKD-IS score changes

    From Baseline to end of study (maximum of 18 months)

  • Mean Treatment Satisfaction Questionnaire for Medication (TSQM-9) score changes

    From Baseline to end of study (maximum of 18 months)

  • Mean ADPKD-Urinary Impact Scale (UIS) score changes

    From Baseline to end of study (maximum of 18 months)

  • Description of real-world ADPKD treatment patterns (number of subjects taking different treatments)

    From Baseline to end of study (maximum of 18 months)

  • +1 more secondary outcomes

Other Outcomes (2)

  • Mean ADPKD-Pain and Discomfort Scale(PDS) score change from baseline to end of study (exploratory)

    From Baseline to end of study (maximum of 18 months)

  • Overall odds ratio of discrete-choice experiment (DCE) for patient preference to the addition of a disease modifying treatment versus no change to local Standard of Care (SoC)

    At baseline and at the end of the study (18 months)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

The study population will be adult patients with ADPKD in CKD Stages 1 -3, with evidence of rapidly progressing disease according to the investigator. Investigator must be ADPKD experts qualified by experience and ability to perform the study and be working at an ADPKD reference centre.

You may qualify if:

  • Male and female aged ≥ 18 years.
  • Patient has a diagnosis of ADPKD between CKD Stages 1-3, and is deemed by their treating physician to likely have rapidly progressing disease.
  • Patient has a life expectancy greater than 18 months at time of enrolment.
  • Patient is able and willing to give informed consent, if required according to local regulations.
  • Patient is fluent in local language.

You may not qualify if:

  • Patient is currently participating in, or has in the last 12 months participated in an interventional clinical trial.
  • Presence of any condition/circumstance which in the opinion of the investigator could significantly limit the complete follow up of the patient.
  • Inability of the patient to complete PROs remotely.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (26)

AKH Wien

Vienna, Austria

Location

LKH Villach

Villach, Austria

Location

UCL Brussels

Brussels, Belgium

Location

UZ Brussels

Brussels, Belgium

Location

UZ Leuven/Gasthuisberg KUL

Leuven, Belgium

Location

CHU Liège - Domaine Universitaire du Sart Tilman

Liège, Belgium

Location

Clinique La Louviere

Lille, France

Location

CHU Nimes - Hôpital CAREMEAU

Nîmes, France

Location

Hopital Tenon

Paris, France

Location

Necker Hospital

Paris, France

Location

CHU TOURS - Hôpital Bretonneau

Tours, France

Location

Charite Berlin

Berlin, Germany

Location

Universitätsmedizin Göttingen

Göttingen, Germany

Location

University Medical Center Schleswig-Holstein

Lübeck, Germany

Location

Fundación Puigvert

Barcelona, Spain

Location

Hospital Clinic

Barcelona, Spain

Location

Hospital Vall d'Hebron

Barcelona, Spain

Location

Hospital Universitario de Getafe

Getafe, Spain

Location

University Hospital of Geneve

Geneva, Switzerland

Location

University Hospital of Zurich

Zurich, Switzerland

Location

Edinburgh Royal Infirmary

Edinburgh, United Kingdom

Location

Queen Elizabeth University Hospital

Glasgow, United Kingdom

Location

Aintree University Hospital

Liverpool, United Kingdom

Location

Royal Free Hospital

London, United Kingdom

Location

Royal London Hospital

London, United Kingdom

Location

Freeman Hospital

Newcastle, United Kingdom

Location

Related Publications (1)

  • Joly D, Quinn J, Mokiou S, O'Reilly K, Sanchez-Covisa J, Wang-Silvanto J, Doll H. Rationale and study protocol of ACQUIRE, a prospective, observational study measuring quality of life, treatment preference and treatment satisfaction of autosomal dominant polycystic kidney disease (ADPKD) patients in Europe. BMC Nephrol. 2020 Jul 24;21(1):298. doi: 10.1186/s12882-020-01927-1.

MeSH Terms

Conditions

Polycystic Kidney, Autosomal Dominant

Condition Hierarchy (Ancestors)

Polycystic Kidney DiseasesKidney Diseases, CysticKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesAbnormalities, MultipleCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCiliopathiesGenetic Diseases, Inborn

Study Officials

  • Medical Department

    Otsuka Europe

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 21, 2016

First Posted

July 28, 2016

Study Start

October 1, 2016

Primary Completion

October 1, 2019

Study Completion

March 1, 2020

Last Updated

April 11, 2019

Record last verified: 2018-09

Locations