NCT02846571

Brief Summary

The intervention in this trial is intraocular islet transplantation. A single dose of 1000 - 3000 Islet Equivalents (IEQ)/kg recipient body weight (BW) will be infused into the anterior chamber of the eye through a self-sealing incision in the peripheral cornea. The procedure is projected to take approximately 20-30 minutes. Transplant recipients in this study will receive localized maintenance immunosuppression via topical application of eye-drops.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2

participants targeted

Target at below P25 for phase_1 diabetes

Timeline
20mo left

Started Dec 2019

Longer than P75 for phase_1 diabetes

Geographic Reach
1 country

2 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress80%
Dec 2019Dec 2027

First Submitted

Initial submission to the registry

July 18, 2016

Completed
9 days until next milestone

First Posted

Study publicly available on registry

July 27, 2016

Completed
3.4 years until next milestone

Study Start

First participant enrolled

December 5, 2019

Completed
7.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2026

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2027

Last Updated

March 12, 2026

Status Verified

March 1, 2026

Enrollment Period

7.1 years

First QC Date

July 18, 2016

Last Update Submit

March 10, 2026

Conditions

Keywords

Islet TransplantationType 1 DiabetesImmune Tolerance InductionDiabetes ComplicationsIntraocular TransplantationEye Anterior ChamberKidney TransplantationImmunosuppressionType 2 DiabetesEye Drops Immunosuppressionlocalized immunosuppression

Outcome Measures

Primary Outcomes (3)

  • Absence of ocular complications

    Absence of, corneal decompensation, increased intraocular pressure (IOP), uveitis, cataract formation, retinal detachment, retinal bleeding, retinal vasculopathies, macular edema, optic neuropathy, and endophthalmitis in the transplanted eye

    24 months after transplant

  • Absence of sympathetic ophthalmia

    Absence of ophthalmic complications in the non-transplanted eye and assessment of diabetic retinopathy compared to baseline before transplant

    24 months after transplant

  • Confirmation of intraocular islet graft survival

    Confirmation of positive c-peptide (\>1 ng/ml) in the aqueous humor of the transplanted eye and assessment of intraocular islet graft integrity by slit-lamp microscopy and OCT imaging

    24 months after transplant

Study Arms (1)

Human Pancreatic Islet Transplantation

OTHER

Islet transplantation into the anterior chamber of the eye single arm

Biological: Human Pancreatic Islet Transplantation

Interventions

Human pancreatic islet transplantation in the eye anterior chamber of legally blind type 1 or type 2 diabetes patients with and without insulin-dependence

Human Pancreatic Islet Transplantation

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient with at least one eye with extensive loss of vision from hand motion to no light perception.
  • Phakic or pseudophakic with a stable intraocular lens in the blind eye.
  • Normal cornea with good visualization of the anterior segment.
  • Normal anterior segment anatomy including the iris bed.
  • Male and female subjects ages 18 to 75 years of age and no history of non-compliance.
  • Clinical history compatible with T1D or T2D with or without insulin-dependence at the time of enrollment.
  • Stable renal function of native or transplanted kidney if applicable.
  • Ability to provide written informed consent.
  • Mentally stable and able to comply with the procedures of the study protocol.

You may not qualify if:

  • Poor visualization of the anterior chamber (corneal opacity, corneal edema, Herpes Keratitis).
  • Aphakic status (no lens).
  • Narrow angle of iris anatomy: Spade Scale IV.
  • History of uncontrolled glaucoma or glaucoma that had required surgical intervention (e.g., trabeculectomy or shunting devices).
  • Active uncontrolled uveitis.
  • Presence of silicone in the anterior segment after complex diabetic retinopathy surgery.
  • History of allergy to topical steroids and immune-modulatory drugs including CSA and Tacrolimus.
  • HbA1c \>10%.
  • Blood Pressure: SBP \>160 mmHg or DBP \>100 mmHg.
  • Calculated GFR of ≤40 mL/min/1.73 m2 for patients with kidney transplant or \<80 mL/min/1.73 m2 for those without kidney transplant, using the subject's measured serum creatinine and the Chronic Kidney Disease Epidemiology Collaboration (CKD-EPI) equation1.
  • Strict vegetarians (vegans) will be excluded only if their estimated GFR is ≤35 mL/min/1.73 m2 for patients with kidney transplant or \<70 mL/min/1.73 m2 for those without kidney transplant.
  • Proteinuria (albumin/creatinine ratio or ACr \>300mg/dl) of new onset or since kidney transplantation if applicable.
  • Calculated panel-reactive anti-HLA antibodies \>20%.
  • Positive crossmatch.
  • Antibodies (i.e., presumed de-novo) to the kidney transplant donor, if applicable.
  • +16 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Bascom Palmer Eye Institute

Miami, Florida, 33136, United States

RECRUITING

Diabetes Research Institute, University of Miami Miller School of Medicine

Miami, Florida, 33136, United States

RECRUITING

Related Publications (4)

  • Perez VL, Caicedo A, Berman DM, Arrieta E, Abdulreda MH, Rodriguez-Diaz R, Pileggi A, Hernandez E, Dubovy SR, Parel JM, Ricordi C, Kenyon NM, Kenyon NS, Berggren PO. The anterior chamber of the eye as a clinical transplantation site for the treatment of diabetes: a study in a baboon model of diabetes. Diabetologia. 2011 May;54(5):1121-6. doi: 10.1007/s00125-011-2091-y. Epub 2011 Mar 1.

    PMID: 21360190BACKGROUND
  • Shishido A, Caicedo A, Rodriguez-Diaz R, Pileggi A, Berggren PO, Abdulreda MH. Clinical intraocular islet transplantation is not a number issue. CellR4 Repair Replace Regen Reprogram. 2016;4(4):e2120. Epub 2016 Jul 26.

    PMID: 29497631BACKGROUND
  • Tun SBB, Chua M, Hasan R, Kohler M, Zheng X, Ali Y, Abdulreda MH, Juntti-Berggren L, Barathi VA, Berggren PO. Islet Transplantation to the Anterior Chamber of the Eye-A Future Treatment Option for Insulin-Deficient Type-2 Diabetics? A Case Report from a Nonhuman Type-2 Diabetic Primate. Cell Transplant. 2020 Jan-Dec;29:963689720913256. doi: 10.1177/0963689720913256.

    PMID: 32264703BACKGROUND
  • Abdulreda MH, Berman DM, Shishido A, Martin C, Hossameldin M, Tschiggfrie A, Hernandez LF, Hernandez A, Ricordi C, Parel JM, Jankowska-Gan E, Burlingham WJ, Arrieta-Quintero EA, Perez VL, Kenyon NS, Berggren PO. Operational immune tolerance towards transplanted allogeneic pancreatic islets in mice and a non-human primate. Diabetologia. 2019 May;62(5):811-821. doi: 10.1007/s00125-019-4814-4. Epub 2019 Jan 31.

    PMID: 30701283BACKGROUND

Related Links

MeSH Terms

Conditions

Diabetes MellitusDiabetes Mellitus, Type 1Diabetes ComplicationsDiabetes Mellitus, Type 2

Condition Hierarchy (Ancestors)

Glucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Midhat H Abdulreda, Ph.D.

    University of Miami

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Midhat H Abdulreda, Ph.D.

CONTACT

Sonia Yoo, M.D.

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR INVESTIGATOR
PI Title
Associate Professor, Diabetes Research Institute

Study Record Dates

First Submitted

July 18, 2016

First Posted

July 27, 2016

Study Start

December 5, 2019

Primary Completion (Estimated)

December 31, 2026

Study Completion (Estimated)

December 31, 2027

Last Updated

March 12, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Locations