NCT02736149

Brief Summary

Ubenimex is being developed for the treatment of pulmonary arterial hypertension (PAH) (World Health Organization \[WHO\] Group 1) to improve exercise capacity and delay clinical worsening. This study is a Phase 2, open-label, extension study to evaluate long-term safety and efficacy of ubenimex in patients with PAH (WHO Group 1) who complete Study EIG-UBX-001.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
51

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Dec 2016

Geographic Reach
2 countries

28 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 4, 2016

Completed
9 days until next milestone

First Posted

Study publicly available on registry

April 13, 2016

Completed
8 months until next milestone

Study Start

First participant enrolled

December 1, 2016

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2018

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2018

Completed
4.5 years until next milestone

Results Posted

Study results publicly available

January 18, 2023

Completed
Last Updated

January 18, 2023

Status Verified

December 1, 2022

Enrollment Period

1.2 years

First QC Date

April 4, 2016

Results QC Date

November 3, 2022

Last Update Submit

December 21, 2022

Conditions

Outcome Measures

Primary Outcomes (1)

  • Treatment-emergent Adverse Events (TEAEs)

    Number of Patients with TEAEs collected for all patients and recorded on the Adverse Event Case Report Form

    At least 24 weeks of open-label treatment with ubenimex followed by 4 weeks follow-up

Study Arms (1)

ubenimex

EXPERIMENTAL

ubenimex capsules 150 mg three times a day (TID), administered orally, minimum of 24 weeks for all patients. The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.

Drug: ubenimex

Interventions

Also known as: UBX
ubenimex

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have completed Study EIG-UBX-001 through Week 24.
  • In the opinion of the Principal Investigator, has been generally compliant with study requirements during Study EIG-UBX-001.
  • Agrees to use a medically acceptable method of contraception throughout the entire study period.
  • Willing and able to comply with scheduled visits, treatment plans, and laboratory tests and other study procedures.

You may not qualify if:

  • Is pregnant or lactating.
  • Concurrent regular use of another leukotriene pathway inhibitor.
  • Any reason that, in the opinion of the investigator, precludes the patient from participating in the study.
  • Any condition that is unstable or that could jeopardize the safety of the patient and his/her compliance in the study
  • A serious uncontrolled medical disorder/condition that in the opinion of the investigator would impair the ability of the patient to receive protocol therapy
  • An ongoing, drug-related, serious adverse event (SAE).
  • Significant/chronic renal insufficiency.
  • Transaminases (alanine transaminase, aspartate transaminase) levels \>3 × upper limit of normal (ULN) and/or bilirubin level \>2 × ULN.
  • Absolute neutrophil count \<1500 mm3.
  • Hemoglobin concentration \<9 g/dL at Screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

California Heart Center Foundation, An Affiliate of Cedars-Sinai Heart Institute, Cedars-Sinai Medical Care Foundation

Beverly Hills, California, 90211, United States

Location

UCSD Medical Center

La Jolla, California, 92103, United States

Location

Stanford University Medical Center

Palo Alto, California, 94305, United States

Location

Harbor - UCLA Medical Center

Torrance, California, 90502, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

Cleveland Clinic, Florida

Weston, Florida, 33331, United States

Location

Kentuckiana Pulmonary Associates

Louisville, Kentucky, 40202, United States

Location

Chest Medicine Associates

South Portland, Maine, 04106, United States

Location

Johns Hopkins University, Pulmonary and Critical Care Medicine

Baltimore, Maryland, 21205, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Boston University School of Medicine

Boston, Massachusetts, 02118, United States

Location

University of Michigan

Ann Arbor, Michigan, 48103, United States

Location

Mayo Clinic College of Medicine

Rochester, Minnesota, 55905, United States

Location

Washington University

St Louis, Missouri, 63130, United States

Location

Weill Cornell Medicine

New York, New York, 10065, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Cleveland Clinic Respiratory Institute

Cleveland, Ohio, 44195, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Allegheny General Hospital

Pittsburgh, Pennsylvania, 15212, United States

Location

University of Pennsylvania Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Alpert Medical School of Brown University Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Houston Methodist Hospital

Houston, Texas, 77030, United States

Location

University Texas Health Science Center

San Antonio, Texas, 78229, United States

Location

London Health Sciences Centre

London, Ontario, N6A 5W9, Canada

Location

University of Ottawa Heart Institute

Ottawa, Ontario, K1Y 4W7, Canada

Location

Related Publications (2)

  • Tian W, Jiang X, Tamosiuniene R, Sung YK, Qian J, Dhillon G, Gera L, Farkas L, Rabinovitch M, Zamanian RT, Inayathullah M, Fridlib M, Rajadas J, Peters-Golden M, Voelkel NF, Nicolls MR. Blocking macrophage leukotriene b4 prevents endothelial injury and reverses pulmonary hypertension. Sci Transl Med. 2013 Aug 28;5(200):200ra117. doi: 10.1126/scitranslmed.3006674.

    PMID: 23986401BACKGROUND
  • Qian J, Tian W, Jiang X, Tamosiuniene R, Sung YK, Shuffle EM, Tu AB, Valenzuela A, Jiang S, Zamanian RT, Fiorentino DF, Voelkel NF, Peters-Golden M, Stenmark KR, Chung L, Rabinovitch M, Nicolls MR. Leukotriene B4 Activates Pulmonary Artery Adventitial Fibroblasts in Pulmonary Hypertension. Hypertension. 2015 Dec;66(6):1227-1239. doi: 10.1161/HYPERTENSIONAHA.115.06370. Epub 2015 Oct 5.

    PMID: 26558820BACKGROUND

MeSH Terms

Conditions

Pulmonary Arterial Hypertension

Interventions

ubenimex

Condition Hierarchy (Ancestors)

Hypertension, PulmonaryLung DiseasesRespiratory Tract Diseases

Results Point of Contact

Title
Senior VP, Clinical Development
Organization
Eiger BioPharmaceuticals, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 4, 2016

First Posted

April 13, 2016

Study Start

December 1, 2016

Primary Completion

March 1, 2018

Study Completion

August 1, 2018

Last Updated

January 18, 2023

Results First Posted

January 18, 2023

Record last verified: 2022-12

Locations