NCT02707523

Brief Summary

This randomized, double-blind, placebo-controlled phase 2 trial will be conducted at a single tertiary pediatric intensive care unit (PICU). The study will include children with RSV infection who were admitted to the pediatric intensive care unit and require respiratory support via positive pressure ventilation (invasive and noninvasive).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
48

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jan 2016

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2016

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

February 20, 2016

Completed
23 days until next milestone

First Posted

Study publicly available on registry

March 14, 2016

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 6, 2019

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

May 27, 2020

Completed
24 days until next milestone

Study Completion

Last participant's last visit for all outcomes

June 20, 2020

Completed
Last Updated

July 22, 2020

Status Verified

July 1, 2020

Enrollment Period

3.1 years

First QC Date

February 20, 2016

Results QC Date

May 8, 2020

Last Update Submit

July 7, 2020

Conditions

Keywords

RSVrespiratory supportICUAzithromycin

Outcome Measures

Primary Outcomes (4)

  • Number of Participants With Treatment-related Adverse Events as Assessed by CTCAE v4.0

    To determine the safety profile of AZM at 10 mg/kg and 20 mg/kg IV X 3 days in children with RSV-induced respiratory failure

    Baseline through Day 3

  • Nasal Total Matrix Metalloproteinase (MMP)-9 Level

    To determine the concentration of total MMP-9 levels in the nasal compartment

    Day 3

  • Pharmacokinetic-Plasma Half Life of AZM

    Measurement of AZM half life in the plasma

    From baseline to 72 hours post treatment

  • Pharmacokinetic-Lung Half Life of AZM

    Measurement of AZM half life in the lung

    From baseline to 72 hours post treatment

Secondary Outcomes (6)

  • Duration of Mechanical Ventilation in Days

    Pre-treatment through 2 weeks

  • Duration of BiPAP in Days

    Pre-treatment through 2 weeks

  • Duration of High Flow Nasal Cannula in Days

    Pre-treatment through 2 weeks

  • Duration of Oxygenation in Days

    Pre-treatment through 2 weeks

  • Duration of Hospitalization in Days

    Pre-treatment through 2 weeks

  • +1 more secondary outcomes

Other Outcomes (1)

  • Lung Matrix Metalloproteinase (MMP) Level

    Day 3

Study Arms (3)

Control

PLACEBO COMPARATOR

Placebo controlled (normal saline) daily for 3 days

Drug: Placebo

Azithromycin (10 mg/kg)

ACTIVE COMPARATOR

10 mg/kg IV Azithromycin daily for 3 days

Drug: Azithromycin 10 mg

Azithromycin (20 mg/kg)

ACTIVE COMPARATOR

20 mg/kg IV Azithromycin daily for 3 days

Drug: Azithromycin 20mg

Interventions

Also known as: Zithromax, Z-Pak
Azithromycin (10 mg/kg)
Also known as: Zithromax, Z-Pak
Azithromycin (20 mg/kg)
Control

Eligibility Criteria

AgeUp to 16 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Admission to the PICU with RSV infection
  • Need for positive pressure ventilation (invasive and non-invasive)
  • Randomization and drug/placebo initiation within 48 hours of admission to Pediatric Intensive Care Unit

You may not qualify if:

  • Azithromycin use within 7 days of PICU admission
  • Contraindication to azithromycin use including:
  • Patients with electrocardiogram QT interval corrected for heart rate (Qtc) ≥ 450 ms
  • Patients with significant hepatic impairment (direct bilirubin \>1.5 mg/dL)
  • Known hypersensitivity to azithromycin, erythromycin, any macrolide, or ketolide drug
  • Cardiac arrhythmia
  • History of pyloric stenosis
  • Immunocompromised children (any cause)
  • Current use of any medication known to cause QT prolongation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

UAB

Birmingham, Alabama, 35233, United States

Location

Related Publications (1)

  • Kong M, Zhang WW, Sewell K, Gorman G, Kuo HC, Aban I, Ambalavanan N, Whitley RJ. Azithromycin Treatment vs Placebo in Children With Respiratory Syncytial Virus-Induced Respiratory Failure: A Phase 2 Randomized Clinical Trial. JAMA Netw Open. 2020 Apr 1;3(4):e203482. doi: 10.1001/jamanetworkopen.2020.3482.

MeSH Terms

Interventions

Azithromycin

Intervention Hierarchy (Ancestors)

ErythromycinMacrolidesPolyketidesLactonesOrganic Chemicals

Results Point of Contact

Title
Dr. Michele Kong, PI
Organization
UAB

Study Officials

  • Michele Kong, MD

    University of Alabama at Birmingham

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Participant, clinical providers and study staff are masked to the intervention. The random assignment of treatment was determined by random permutation. A statistician generated the randomization schedule and provided the randomization schedule (with randomization IDs) in an excel file to the study pharmacist in charge of dispensing the appropriate treatment.
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor

Study Record Dates

First Submitted

February 20, 2016

First Posted

March 14, 2016

Study Start

January 1, 2016

Primary Completion

February 6, 2019

Study Completion

June 20, 2020

Last Updated

July 22, 2020

Results First Posted

May 27, 2020

Record last verified: 2020-07

Locations