NCT02687542

Brief Summary

The purpose of this study is to evaluate the efficacy, safety and tolerability of PF-06649751 in Parkinson's disease patients who experience motor-fluctuations.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
108

participants targeted

Target at P75+ for phase_2 parkinson-disease

Timeline
Completed

Started Mar 2016

Geographic Reach
6 countries

57 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 29, 2016

Completed
24 days until next milestone

First Posted

Study publicly available on registry

February 22, 2016

Completed
10 days until next milestone

Study Start

First participant enrolled

March 3, 2016

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 10, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 10, 2017

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

December 24, 2018

Completed
Last Updated

November 23, 2020

Status Verified

October 1, 2020

Enrollment Period

1.7 years

First QC Date

January 29, 2016

Results QC Date

October 30, 2018

Last Update Submit

October 28, 2020

Conditions

Keywords

Parkinson DiseaseMotor Fluctuation

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Daily OFF Time at Week 10

    A paper Hauser diary was utilized to record motor state for half-hour intervals. Participants completed the diary by answering whether they had been OFF for 3 consecutive days in the week prior to each visit (except Day 28 visit), including 3 consecutive days during the week prior to Day 0 (Randomization). The daily OFF time was calculated as the average of the 3 consecutive daily OFF hours from the Hauser diary at each visit.

    Week 10; Baseline was defined as the average daily OFF time (using 3 Hauser patient diary days) prior to Day -1 (study derived day and equalled to nominal visit day 0).

Secondary Outcomes (12)

  • Change From Baseline in Daily OFF Time

    Weeks 3, 5, 10 and 15; Baseline was defined as the average daily OFF time (using 3 Hauser patient diary days) prior to Day -1 (study derived day and equalled to nominal visit day 0).

  • Change From Baseline in Daily ON Time With Troublesome Dyskinesia

    Weeks 3, 5, 10 and 15; Baseline was defined as the average daily ON time with Troublesome Dyskinesia (using 3 Hauser patient diary Days) prior to Day -1 (study derived day and equalled to nominal visit Day 0).

  • Change From Baseline in Daily ON Time Without Troublesome Dyskinesia

    Weeks 3, 5, 10 and 15; Baseline was defined as the average daily ON time without Troublesome Dyskinesia (using 3 Hauser patient diary days) prior to Day -1 (study derived day and equalled to nominal visit Day 0)

  • Change From Baseline in Movement Disorder Society-Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Part III

    Weeks 1, 2, 3, 4, 5, 10 and 15; Baseline was defined as the Day -1 (study derived day and equalled to nominal visit Day 0) measurement

  • Change From Baseline in Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I, II, IV, and Total Score

    Weeks 5, 10 and 15; Baseline was defined as the Day -1 (study derived day and equalled to nominal visit Day 0) measurement

  • +7 more secondary outcomes

Study Arms (5)

Placebo

PLACEBO COMPARATOR

Placebo

Drug: Placebo

PF-06649751 low dose (1 mg QD)

EXPERIMENTAL

PF-06649751 low dose level (1 mg QD)

Drug: PF-06649751 low dose (1 mg QD)

PF-06649751 middle dose 1 (3 mg QD)

EXPERIMENTAL

PF-06649751 lower middle dose 1 (3 mg QD)

Drug: PF-06649751 middle dose 1 (3 mg QD)

PF-06649751 middle dose 2 (7 mg QD)

EXPERIMENTAL

PF-06649751 higher middle dose 2 (7 mg QD)

Drug: PF-06649751 middle dose 2 (7 mg QD)

PF-06649751 high dose (15 mg QD)

EXPERIMENTAL

PF-06649751 high dose (15 mg QD)

Drug: PF-06649751 high dose (15 mg QD)

Interventions

Placebo

Placebo

PF-06649751 low dose (1 mg QD)

PF-06649751 low dose (1 mg QD)

PF-06649751 lower middle dose 1 (3 mg QD)

PF-06649751 middle dose 1 (3 mg QD)

PF-06649751higher middle dose 2 (7 mg QD)

PF-06649751 middle dose 2 (7 mg QD)

PF-06649751 high dose (15 mg QD)

PF-06649751 high dose (15 mg QD)

Eligibility Criteria

Age40 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Females of non-childbearing potential and/or male subjects between the ages of 40 and 85 years, inclusive.
  • Clinical diagnosis of Parkinson's disease.
  • Able to refrain from any Parkinson's disease medication not permitted by the protocol.

You may not qualify if:

  • Female of childbearing potential
  • History or presence of atypical Parkinsonian syndrome.
  • History of surgical intervention for Parkinson's disease.
  • Severe acute or chronic medical or psychiatric condition or laboratory abnormality.
  • Any condition possibly affecting drug absorption.
  • Participation in other studies involving investigational drug(s), or treatment with any investigational drug within 30 days.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (57)

Xenoscience, Inc

Phoenix, Arizona, 85004, United States

Location

St Joseph's Hospital and Medical Center

Phoenix, Arizona, 85013, United States

Location

Arcadia Neurology Center

Arcadia, California, 91006, United States

Location

Faculty Physicians and Surgeons of Loma Linda University School of Medicine

Loma Linda, California, 92354, United States

Location

Hoag Memorial Hospital Presbyterian

Newport Beach, California, 92658, United States

Location

Hoag Memorial Hospital

Newport Beach, California, 92663, United States

Location

SC3 Research Group, Inc

Pasadena, California, 91105, United States

Location

Neurosearch-Torrance

Torrance, California, 90505, United States

Location

Associated Neurologists of Southern Connecticut, PC

Fairfield, Connecticut, 06824, United States

Location

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, 33486, United States

Location

University of Florida Center for Movement Disorders and Neurorestoration

Gainesville, Florida, 32607, United States

Location

Neurology Associates of Ormond Beach

Ormond Beach, Florida, 32174, United States

Location

University of South Florida

Tampa, Florida, 33613, United States

Location

Vero Beach Neurology and Research Institute

Vero Beach, Florida, 32960, United States

Location

Atlanta Center for Medical Research

Atlanta, Georgia, 30331, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Indiana University Health Neuroscience Center

Indianapolis, Indiana, 46202, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

CRI Worldwide, LLC

Marlton, New Jersey, 08053, United States

Location

Dent Neurologic Institute

Amherst, New York, 14226, United States

Location

Dent Neurosciences Research Center ,Inc. DBA Dent Neurologic Institute

Amherst, New York, 14226, United States

Location

Dent Neurologic Institute

Orchard Park, New York, 14127, United States

Location

Duke University Medical center

Durham, North Carolina, 27705, United States

Location

Duke University/Duke Neurology/Department of Neurology

Durham, North Carolina, 27705, United States

Location

Wake Research Associates, LLC

Raleigh, North Carolina, 27612, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

University of Toledo

Toledo, Ohio, 43614, United States

Location

The Movement Disorder Clinic of Oklahoma

Tulsa, Oklahoma, 74136, United States

Location

Abington Neurological Associates, Ltd.

Willow Grove, Pennsylvania, 19090, United States

Location

Rhode Island Hospital/ Brown University Medical School

Providence, Rhode Island, 02903, United States

Location

AS Clinical Research Consultants of North Texas, PLLC

Greenville, Texas, 75401, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Booth Gardner Parkinson's Care Center

Kirkland, Washington, 98034, United States

Location

Montreal Neurological Hospital Research Pharmacy

Montreal, Quebec, H3A 2B4, Canada

Location

Montreal Neurological Institute and Hospital

Montreal, Quebec, H3A 2B4, Canada

Location

CHU de Grenoble Alpes

Grenoble, 38043 Cedex 9, France

Location

CHU de Grenoble Alpes

La Tronche, 38700, France

Location

CHRU de Lille-Hopital Roger Salengro

Lille, 59037 cedex, France

Location

Hopital de la Timone APHM

Marseille, 13385 cedex 05, France

Location

Hopital de La Timone

Marseille, 13385 cedex 05, France

Location

Hopital La Pitie-Salpetriere

Paris, 75013, France

Location

Universitaetsklinikum Freiburg

Freiburg im Breisgau, Baden-Wurttemberg, 79106, Germany

Location

St. Josef-Hospital GmbH

Bochum, 44791, Germany

Location

Universitaetsklinikum Carl Gustav Carus Klinik und Poliklinik fur Neurologie

Dresden, 01307, Germany

Location

Klinikum rechts der Isar der Technischen Universitaet Muenchen

München, 81675, Germany

Location

Universitaetsklinik Ulm

Ulm, 89081, Germany

Location

Asahikawa Medical center

Asahikawa, Hokkaido, 0708644, Japan

Location

Medical Corporation Abe Neurology Clinic

Morioka, Iwate, 020-0878, Japan

Location

Tazuke Kofukai Medical Research Institute Kitano Hospital

Kita-ku, Osaka, 530-8480, Japan

Location

Osaka University Hospital

Suita, Osaka, 565-0871, Japan

Location

Juntendo University Hospital

Bunkyo-ku, Tokyo, 113-8431, Japan

Location

Hospital Clinico Universitario

Santiago de Compostela, A Coruna, 15706, Spain

Location

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

Location

Policlinica de Guipuzcoa

Donostia / San Sebastian, Guipuzcoa, 20009, Spain

Location

Hospital Clinic i Provincial de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitario de la Princesa

Madrid, 28006, Spain

Location

Hospital Universitario y Politecnico la Fe

Valencia, 46026, Spain

Location

Related Links

MeSH Terms

Conditions

Parkinson Disease

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Limitations and Caveats

The study was terminated prematurely due to insufficient efficacy and not due to safety reasons.

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 29, 2016

First Posted

February 22, 2016

Study Start

March 3, 2016

Primary Completion

November 10, 2017

Study Completion

November 10, 2017

Last Updated

November 23, 2020

Results First Posted

December 24, 2018

Record last verified: 2020-10

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations