NCT02633956

Brief Summary

This Phase 2, double-blind, randomized, placebo-controlled, multicenter study, with an open-label long-term safety extension (LTSE), will evaluate the effect of Obeticholic Acid, and the subsequent addition of statin therapy, on lipoprotein metabolism in subjects with nonalcoholic steatohepatitis (NASH) with fibrosis stage 1 to 4, but no evidence of hepatic decompensation.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
84

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Dec 2015

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 18, 2015

Completed
16 days until next milestone

Study Start

First participant enrolled

December 4, 2015

Completed
13 days until next milestone

First Posted

Study publicly available on registry

December 17, 2015

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 21, 2017

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 12, 2018

Completed
3 months until next milestone

Results Posted

Study results publicly available

June 4, 2018

Completed
Last Updated

June 4, 2018

Status Verified

May 1, 2018

Enrollment Period

1.3 years

First QC Date

November 18, 2015

Results QC Date

March 21, 2018

Last Update Submit

May 3, 2018

Conditions

Keywords

Non-alcoholic Fatty Liver DiseaseNAFLDFatty Liver DiseaseNASH

Outcome Measures

Primary Outcomes (3)

  • The Effect of Obeticholic Acid on Low-density Lipoprotein (LDL) Concentration (Least Squares Mean Change From Baseline at Week 16)

    The effect of Obeticholic Acid on LDL metabolism in subjects with biopsy confirmed nonalcoholic steatohepatitis (NASH) and the ability of atorvastatin to modulate this effect as measured by change (least squares mean) from baseline at week 16 in LDL concentration

    Baseline and Week 16

  • The Effect of Obeticholic Acid on LDL Particle Size (Least Squares Mean Change From Baseline at Week 16)

    The effect of Obeticholic Acid on LDL metabolism in subjects with biopsy confirmed NASH and the ability of atorvastatin to modulate this effect as measured by change from baseline (least squares mean) at week 16 in LDL particle size. It is LDL particle diameter size (nm) that is reported.

    Baseline and Week 16

  • The Effect of Obeticholic Acid on LDL Particle Concentration (Total) (Least Squares Mean Change From Baseline at Week 16)

    The effect of Obeticholic Acid on LDL metabolism in subjects with biopsy confirmed nonalcoholic NASH and the ability of atorvastatin to modulate this effect as measured by change (least squares mean) from baseline at week 16 in LDL particle concentration (total)

    Baseline and Week 16

Study Arms (4)

5 mg Obeticholic Acid

EXPERIMENTAL

5 mg Obeticholic Acid daily for the double-blind treatment period. 10 mg Atorvastatin titrating to 20mg.

Drug: Obeticholic AcidDrug: Atorvastatin

10 mg Obeticholic Acid

EXPERIMENTAL

10 mg Obeticholic Acid daily for the double-blind treatment period. 10 mg Atorvastatin titrating to 20mg.

Drug: Obeticholic AcidDrug: Atorvastatin

25 mg Obeticholic Acid

EXPERIMENTAL

25 mg Obeticholic Acid daily for the double-blind treatment period. 10 mg Atorvastatin titrating to 20mg.

Drug: Obeticholic AcidDrug: Atorvastatin

Placebo

PLACEBO COMPARATOR

One tablet daily for the double-blind treatment period. 10 mg Atorvastatin titrating to 20mg.

Drug: AtorvastatinDrug: Placebo

Interventions

Once a day (QD) by mouth (PO)

Also known as: OCA, 6alpha-ethylchenodeoxycholic acid (6-ECDCA), INT-747
10 mg Obeticholic Acid25 mg Obeticholic Acid5 mg Obeticholic Acid

Initiate treatment with Atorvastatin at Week 4 visit with a dose of 10 mg once daily (QD) by mouth (PO). Increase Atorvastatin to 20 mg once daily (QD) by mouth (PO) at Week 8 visit if 10 mg daily is tolerated. Atorvastatin may be titrated up or down at Week 12 visit as clinically indicated.

10 mg Obeticholic Acid25 mg Obeticholic Acid5 mg Obeticholic AcidPlacebo

Once a day (QD) by mouth (PO)

Placebo

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥18 years
  • Histologic evidence of NASH, as assessed by central reading of a liver biopsy obtained no more than 1 year prior to randomization, defined by the presence of all 3 key histological features of NASH with a score of at least 1 for each and a combined score of 4 or greater out of a possible 8 points according to NASH Clinical Research Network (CRN) criteria.
  • Histologic evidence of fibrosis stage 1 to stage 4 (as defined by NASH CRN scoring of fibrosis) without any evidence of hepatic decompensation.
  • If subject has type 2 diabetes, is on stable dose of anti-diabetic medication (except thiazolidinediones \[TZDs\]) for ≥3 months prior to Day 1.
  • Is either not taking or is on stable doses of TZDs and/or Vitamin E for ≥6 months prior to Day 1.
  • Contraception: Female subjects of childbearing potential must use ≥1 effective method of contraception during the study and until 30 days following the last dose of investigational product. Effective methods of contraception are considered to be the following: barrier method, ie, condom (male or female) with spermicide or diaphragm with spermicide, intrauterine device, vasectomy (partner), hormonal (eg, contraceptive pill, patch, intramuscular implant or injection), abstinence (defined as refraining from heterosexual intercourse).
  • Must provide written informed consent and agree to comply with the study protocol, including adherence to protocol-described statin withdrawal and statin therapy.

You may not qualify if:

  • Current or history of significant alcohol consumption for a period of more than 3 consecutive months within 1 year prior to Screening Visit 1 (significant alcohol consumption is defined as more than 2 units/day in females and more than 4 units/day in males, on average)
  • Prior intolerance to treatment with atorvastatin or other 3-hydroxy-3-methyl-glutaryl (HMG) Coenzyme A reductase inhibitors (including but not limited to rhabdomyolysis).
  • LDL cholesterol ≥190 mg/dL and already on statin therapy at Screening Visit 1.
  • LDL cholesterol \>200 mg/dL at any Screening Visit in subjects who are not on statin therapy, or at Screening Visit 2 in statin washout subjects.
  • Planned change in diet or exercise habits during participation in the double-blind period, or a significant weight change of \>5% in the prior 6 months.
  • Subjects who have undergone gastric bypass procedures (gastric lap band is acceptable) or ileal resection or plan to undergo either of these procedures.
  • History of biliary diversion
  • Uncontrolled diabetes defined as HbA1c ≥9.5% within 60 days prior to randomization (Day 1).
  • Administration of any of the following medications as specified below:
  • Prohibited 30 days prior to Day 1:
  • bile acid sequestrants (BAS) including cholestyramine and its derivatives, colesevelam, colestipol, or
  • omega-3 fatty acid-containing dietary supplements
  • Prohibited 3 months prior to Day 1:
  • nicotinic acid and derivatives, ezetimibe
  • any prescription or over-the-counter (OTC) medication or herbal remedy with putative NASH efficacy (except Vitamin E or TZDs)
  • +41 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

St. Joseph's Hospital and Medical Center

Phoenix, Arizona, 85013, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

Inland Empire Liver Foundation

Rialto, California, 92377, United States

Location

Nature Coast Clinical Research

Inverness, Florida, 34452, United States

Location

University of Miamai, Schiff Center for Liver Diseases

Miami, Florida, 33136, United States

Location

South Florida Center of Gastroenterology

Wellington, Florida, 33414, United States

Location

Florida Medical Clinic, P.A.

Zephyrhills, Florida, 33542, United States

Location

The Queen's Medical Center - Liver Center

Honolulu, Hawaii, 96813, United States

Location

Mercy Medical Center, Institute for Digestive Health & Liver Disease

Baltimore, Maryland, 21202, United States

Location

Kansas City Research Institute

Kansas City, Missouri, 64131, United States

Location

St. Louis University

St Louis, Missouri, 63104, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Cumberland Research Associates, LLC

Fayetteville, North Carolina, 28304, United States

Location

Consultants for Clinical Research

Cincinnati, Ohio, 45249, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

University Gastroenterology Liver Center

Providence, Rhode Island, 02905, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

ClinSearch

Chattanooga, Tennessee, 37421, United States

Location

Texas Clinical Research Institute, LLC

Arlington, Texas, 76012, United States

Location

Liver Associates of Texas, P.A.

Houston, Texas, 77030, United States

Location

American Research Corporation at the Texas Liver Institute

San Antonio, Texas, 78215, United States

Location

McGuire DVAMC

Richmond, Virginia, 23249, United States

Location

Related Publications (1)

  • Pockros PJ, Fuchs M, Freilich B, Schiff E, Kohli A, Lawitz EJ, Hellstern PA, Owens-Grillo J, Van Biene C, Shringarpure R, MacConell L, Shapiro D, Cohen DE. CONTROL: A randomized phase 2 study of obeticholic acid and atorvastatin on lipoproteins in nonalcoholic steatohepatitis patients. Liver Int. 2019 Nov;39(11):2082-2093. doi: 10.1111/liv.14209. Epub 2019 Sep 10.

MeSH Terms

Conditions

Non-alcoholic Fatty Liver Disease

Interventions

obeticholic acidAtorvastatin

Condition Hierarchy (Ancestors)

Fatty LiverLiver DiseasesDigestive System Diseases

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeptanoic AcidsFatty AcidsLipids

Results Point of Contact

Title
Medical Information
Organization
Intercept Pharmaceuticals, Inc

Study Officials

  • David Shapiro, MD

    Intercept Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 18, 2015

First Posted

December 17, 2015

Study Start

December 4, 2015

Primary Completion

March 21, 2017

Study Completion

March 12, 2018

Last Updated

June 4, 2018

Results First Posted

June 4, 2018

Record last verified: 2018-05

Locations