NCT02614911

Brief Summary

This study has been set up in order to characterize phenotypes and genotypes of patients with early onset enteropathies. In that goal, Investigators will collect biological samples (mainly blood) of patients suffering from early onset enteropathies and their healthy relatives.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,445

participants targeted

Target at P75+ for all trials

Timeline
342mo left

Started Jun 2014

Longer than P75 for all trials

Geographic Reach
1 country

12 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress30%
Jun 2014Jun 2054

Study Start

First participant enrolled

June 16, 2014

Completed
1.4 years until next milestone

First Submitted

Initial submission to the registry

November 10, 2015

Completed
15 days until next milestone

First Posted

Study publicly available on registry

November 25, 2015

Completed
38.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 15, 2054

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 15, 2054

Last Updated

April 30, 2025

Status Verified

April 1, 2025

Enrollment Period

40 years

First QC Date

November 10, 2015

Last Update Submit

April 29, 2025

Conditions

Keywords

Early Onset Entheropathy

Outcome Measures

Primary Outcomes (1)

  • Increasing the current rate (20%) of genetic characterization of early onset entheropathies

    Currently, around 20% of early onset entheropathies are genetically characterized. Investigators want to increase this rate via this research protocol. Our long term objective is to characterize phenotypes and genotypes of patients with early onset enteropathies.

    40 years

Study Arms (2)

Sick patients

Biological sampling of blood for all patients. Biological sampling of saliva, biopsies (skin and endoscopic), feces, for some patients

Other: Biological sampling

Healthy relatives

Biological sampling of blood for all healthy relatives

Other: Biological sampling

Interventions

Biological sampling including blood, feces, biopsies...

Healthy relativesSick patients

Eligibility Criteria

Sexall
Healthy VolunteersYes
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Inclusion of patients with chronic severe entheropathy and of their healthy relatives

You may qualify if:

  • Severe chronic enteropathy
  • Patients developing their first symptoms within the first 6 years of life and, in priority within the first two years of life, or patients with a disease of later onset, in case of a familial history suggestive of inherited mutations notably in families comprising several affected members
  • OR : Be a patient's relative, even if presenting with enteropathy of later onset.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Centre Hospitalier Pellegrin-Enfants

Bordeaux, 33076, France

RECRUITING

Hôpital pédiatrique de Lyon

Bron, 69677, France

RECRUITING

Hôpital Jeanne de Flandre, CHRU de Lille

Lille, 59037, France

RECRUITING

Hôpital d'enfants de la Timone

Marseille, 13385, France

RECRUITING

Hôpital Saint Antoine

Paris, 75012, France

RECRUITING

Necker - Enfants Malades Hospital

Paris, 75015, France

RECRUITING

Hôpital Robert Debré

Paris, 75019, France

RECRUITING

Hôpital Trousseau

Paris, 75020, France

RECRUITING

Hôpital Sud

Rennes, 35203, France

RECRUITING

CHU Hautepierre

Strasbourg, 67000, France

NOT YET RECRUITING

Hôpital des Enfants

Toulouse, 31059, France

RECRUITING

Hôpital Clocheville, CHU de Tours

Tours, 37000, France

RECRUITING

Biospecimen

Retention: SAMPLES WITH DNA

Collection of: * blood samples * feces * biopsies (intestine / skin) * saliva * urina

MeSH Terms

Conditions

Inflammatory Bowel Diseases

Condition Hierarchy (Ancestors)

GastroenteritisGastrointestinal DiseasesDigestive System DiseasesIntestinal Diseases

Study Officials

  • Frank Ruemmele

    Necker - Enfants Malades Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 10, 2015

First Posted

November 25, 2015

Study Start

June 16, 2014

Primary Completion (Estimated)

June 15, 2054

Study Completion (Estimated)

June 15, 2054

Last Updated

April 30, 2025

Record last verified: 2025-04

Locations