NCT02611089

Brief Summary

The objective of this work is to understand how the disruption of the muscle connective tissue contributes to the limb soft-tissue defects in radial dysplasia. In parallel, the researchers will investigate the role of muscle connective tissue in normal limb development.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
150

participants targeted

Target at P50-P75 for all trials

Timeline
125mo left

Started Feb 2016

Longer than P75 for all trials

Geographic Reach
1 country

5 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress50%
Feb 2016Aug 2036

First Submitted

Initial submission to the registry

November 16, 2015

Completed
4 days until next milestone

First Posted

Study publicly available on registry

November 20, 2015

Completed
3 months until next milestone

Study Start

First participant enrolled

February 20, 2016

Completed
10 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2026

Completed
10.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2036

Expected
Last Updated

August 27, 2025

Status Verified

August 1, 2025

Enrollment Period

10 years

First QC Date

November 16, 2015

Last Update Submit

August 26, 2025

Conditions

Keywords

Muscle connective tissueSmall leucine-rich proteoglycansLimb development

Outcome Measures

Primary Outcomes (2)

  • Characterisation of muscle connective tissue derivatives - structure

    The characterization of any structural difference in tissue organisation within muscle connective tissue derivatives, comparing normal control patients to patients with radial dysplasia.

    3 years

  • Characterisation of muscle connective tissue derivatives - function

    The characterization of any functional difference in gene expression within muscle connective tissue derivatives, comparing normal control patients to patients with radial dysplasia.

    3 years

Secondary Outcomes (2)

  • Identification of biomarker(s).

    3 years

  • Identification of muscle connective tissue progenitor-cell pool.

    3 years

Study Arms (2)

Radial dysplasia patients

Recruited participants will have 2-3 small tissue biopsy samples taken during 1-2 of their planned reconstructive surgical procedures for radial dysplasia, whilst under general anaesthesia in the operating theatre. Samples will be taken by scalpel or scissors, by the operating surgeon, from within the surgical site in the forearm and hand. The skin incision and deep dissection will have to be made as part of the normal course of reconstructive surgery, regardless of participation in this study.

Procedure: Tissue biopsy

Control patients

Recruited participants will have 2-3 small tissue biopsy samples taken during their planned reconstructive surgery for hand trauma, whilst under general anaesthesia in the operating theatre. Samples will be taken by scalpel or scissors, by the operating surgeon, from within the surgical site in the forearm and hand. The skin incision and deep dissection will have to be made as part of the normal course of reconstructive surgery, regardless of participation in this study.

Procedure: Tissue biopsy

Interventions

Tissue biopsyPROCEDURE

Sampling of tissue as described.

Control patientsRadial dysplasia patients

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Cases - Any patient attending Great Ormond Street Hospital or Guy's and St Thomas' Hospital for reconstructive hand surgery. Controls - Any patient attending Great Ormond Street Hospital, Guy's and St Thomas' Hospital Oxford University Hospitals, Chelsea and Westminster or the Royal Free Hospital for reconstructive hand surgery.

You may qualify if:

  • Patients with a clinical diagnosis of radial dysplasia, requiring reconstructive surgery
  • Either sex
  • Informed (parental) consent to participate

You may not qualify if:

  • Patients with a clinical diagnosis of radial dysplasia, but not requiring reconstructive surgery
  • Patients with a diagnosis other than radial dysplasia
  • Patients with extensive previous scarring to their forearm and hand.
  • Patients with a significant pathological skin or soft tissue lesion at the donor site.
  • Controls
  • Patients with an injury requiring reconstructive surgery
  • Either sex
  • Informed (parental) consent to participate
  • Patients with extensive previous scarring to their forearm and hand.
  • Patients with a significant pathological skin or soft tissue lesion at the donor site.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Oxford University Hospitals

Oxford, Oxfordshire, OX3 9DU, United Kingdom

RECRUITING

Royal Free Hospital

London, NW3 2QG, United Kingdom

RECRUITING

Guy's and St Thomas' Hospital

London, SE1 7EH, United Kingdom

RECRUITING

Chelsea and Westminster Hospital NHS Foundation Trust

London, SW10 9NH, United Kingdom

RECRUITING

Great Ormond Street Hospital for Children NHS Foundation Trust

London, WC1N 3JH, United Kingdom

RECRUITING

Related Links

Biospecimen

Retention: SAMPLES WITH DNA

Tissue biopsies measuring no more than 5 x 10 mm, consisting of muscle, muscle connective tissue, tendon, fat and skin, or a combination of the above, and / or; Tissue normally discarded during the patient's routine reconstructive hand surgery.

Study Officials

  • Malcolm Logan, PhD

    King's College London

    STUDY CHAIR
  • Branavan Sivakumar, FRCS(Plast)

    Great Ormond Street Hospital for Children NHS Foundation Trust

    PRINCIPAL INVESTIGATOR
  • Gill Smith, FRCS(Plast)

    Great Ormond Street Hospital for Children NHS Foundation Trust

    PRINCIPAL INVESTIGATOR
  • George Murphy, PhD FRCS

    Great Ormond Street Hospital for Children NHS Foundation Trust

    PRINCIPAL INVESTIGATOR
  • Lucy Cogswell, FRCS(Plas)

    Oxford University Hospitals

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Malcolm Logan, BSc PhD

CONTACT

George Murphy, PhD FRCS

CONTACT

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
CROSS SECTIONAL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 16, 2015

First Posted

November 20, 2015

Study Start

February 20, 2016

Primary Completion

February 1, 2026

Study Completion (Estimated)

August 1, 2036

Last Updated

August 27, 2025

Record last verified: 2025-08

Data Sharing

IPD Sharing
Will not share

Locations