NCT02610127

Brief Summary

The overall objective is to enroll patients with acquired hemophilia A (AHA) who are prescribed and treated with Obizur, to assess safety, and to describe factors related to safety, utilization and effectiveness in a real-world setting.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
53

participants targeted

Target at P25-P50 for all trials

Timeline
Completed

Started Dec 2015

Typical duration for all trials

Geographic Reach
1 country

16 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 29, 2015

Completed
22 days until next milestone

First Posted

Study publicly available on registry

November 20, 2015

Completed
1 month until next milestone

Study Start

First participant enrolled

December 30, 2015

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 7, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 7, 2019

Completed
Last Updated

August 5, 2021

Status Verified

August 1, 2021

Enrollment Period

3.4 years

First QC Date

October 29, 2015

Last Update Submit

August 4, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence of therapy-related SAEs and level of severity

    Throughout the study period of approximately 4 years

Secondary Outcomes (8)

  • Hemostatic effectiveness assessment for resolution of bleeding

    Throughout the study period, up to approximately 4 years

  • Time to bleeding resolution, participant study termination, or switch to another treatment

    Throughout the study period, up to approximately 4 years

  • Number of Obizur units/kg required for control of bleeding

    Throughout the study period, up to approximately 4 years

  • Number of Obizur infusions required for control of bleeding

    Throughout the study period, up to approximately 4 years

  • Titer of newly recognized anti-porcine Factor VIII (anti-pFVIII) neutralizing antibodies (inhibitors) or increase in titer of anti-pFVIII inhibitors from baseline and changes over time.

    Throughout the study period of approximately 4 years

  • +3 more secondary outcomes

Study Arms (2)

OBIZUR - Prospective Participants

Participants enrolled and treated with Obizur after the prospective study start date

Biological: OBIZUR

OBIZUR - Retrospective Participants

Retrospective chart review of participants treated with OBIZUR from product approval date until prior to the prospective study start date

Biological: OBIZUR

Interventions

OBIZURBIOLOGICAL

Treating physician will determine treatment regimen, frequency of laboratory and clinical assessments, according to routine clinical practice.

Also known as: rpFVIII, Recombinant pFVIII, Antihemophilic Factor (Recombinant), Porcine Sequence
OBIZUR - Prospective ParticipantsOBIZUR - Retrospective Participants

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participant is ≥18 years of age at the time of informed consent.
  • Participant has AHA, and is being treated/was treated with Obizur.
  • Participant or the participant's legally authorized representative is willing and able to provide informed consent, unless informed consent is not required

You may not qualify if:

  • Participant has a known anaphylactic reaction to the active substance, to any of the excipients, or to hamster protein.
  • Participant has a concomitant bleeding disorder(s) other than acquired hemophilia A (AHA).
  • Participant has participated in another clinical study involving a medicinal product or device within 30 days prior to enrollment or is scheduled to participate in another clinical study involving a medicinal product or device during the course of the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

University of Colorado Health

Aurora, Colorado, 80045, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Emory University School of Medicine

Atlanta, Georgia, 30322, United States

Location

Bleeding and Clotting Disorders Institute

Peoria, Illinois, 61615, United States

Location

Indiana Hemophilia and Thrombosis Center

Indianapolis, Indiana, 46260, United States

Location

University of Iowa Hospitals & Clinics

Iowa City, Iowa, 52242, United States

Location

Tulane University Hospital & Clinics

New Orleans, Louisiana, 70112, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Michigan State University

East Lansing, Michigan, 48823, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Comprehensive Cancer Center of Wake Forest Unversity

Winston-Salem, North Carolina, 27157, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

University of Pennsylvania Health System

Philadelphia, Pennsylvania, 19104, United States

Location

University of Utah Health Sciences Center

Salt Lake City, Utah, 84132, United States

Location

Blood Center of Southeast Wisconsin

Milwaukee, Wisconsin, 53225, United States

Location

Related Links

MeSH Terms

Conditions

Factor 8 deficiency, acquired

Interventions

Factor VIII

Intervention Hierarchy (Ancestors)

Blood Coagulation FactorsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsProtein PrecursorsBiological Factors

Study Officials

  • Study Director

    Shire

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 29, 2015

First Posted

November 20, 2015

Study Start

December 30, 2015

Primary Completion

June 7, 2019

Study Completion

June 7, 2019

Last Updated

August 5, 2021

Record last verified: 2021-08

Data Sharing

IPD Sharing
Will share

Takeda provides access to the de-identified individual participant data (IPD) for eligible studies to aid qualified researchers in addressing legitimate scientific objectives (Takeda's data sharing commitment is available on https://clinicaltrials.takeda.com/takedas-commitment?commitment=5). These IPDs will be provided in a secure research environment following approval of a data sharing request, and under the terms of a data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Access Criteria
IPD from eligible studies will be shared with qualified researchers according to the criteria and process described on https://vivli.org/ourmember/takeda/. For approved requests, the researchers will be provided access to anonymized data (to respect patient privacy in line with applicable laws and regulations) and with information necessary to address the research objectives under the terms of a data sharing agreement.
More information

Locations