NCT02605122

Brief Summary

This is a phase 2/3, randomized, open-label, active control, multi-center study to assess the safety and efficacy of solithromycin in children and adolescents with community-acquired bacterial pneumonia (CABP).

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
97

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Apr 2016

Geographic Reach
6 countries

58 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 10, 2015

Completed
6 days until next milestone

First Posted

Study publicly available on registry

November 16, 2015

Completed
5 months until next milestone

Study Start

First participant enrolled

April 1, 2016

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 21, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 21, 2018

Completed
10 months until next milestone

Results Posted

Study results publicly available

January 3, 2019

Completed
Last Updated

January 3, 2019

Status Verified

November 1, 2018

Enrollment Period

2 years

First QC Date

November 10, 2015

Results QC Date

November 6, 2018

Last Update Submit

December 12, 2018

Conditions

Keywords

pneumoniamacrolidepediatric

Outcome Measures

Primary Outcomes (1)

  • Overview of Adverse Events By Treatment Arm

    Summary of subjects experiencing Treatment Emergent Adverse Events (TEAE) through Day 16 visit and Treatment Emergent Serious Adverse Events (TESAE) through Day 28 visit (28 days +/- 4 days after randomization)

    Up to 28 days post-treatment

Secondary Outcomes (3)

  • Summary of Early Clinical Response

    During Treatment Days 3 to 4

  • Summary of Clinical Improvement

    Last day of Treatment (+48 hours)

  • Summary of Clinical Cure

    Short-term follow-up at 16 days (+/- 4 days)

Study Arms (2)

Solithromycin

EXPERIMENTAL

Solithromycin will be administered orally, as capsules or as a suspension, or intravenously. Patients may receive intravenous therapy initially and switch to an oral formulation. Dosage is weight based and age based.

Drug: Solithromycin

Standard of Care

ACTIVE COMPARATOR

Comparators will be selected according to subject age and are consistent with current recommendations for treatment of CABP in children. These include intravenous ceftriaxone, ampicillin, and amoxicillin and oral amoxicillin and amoxicillin-clavulanic acid. Azithromycin or erythromycin may be added as well.

Drug: Standard of Care

Interventions

Also known as: CEM-101
Solithromycin

Age- and weight-based dosing as appropriate per sites standard of care.

Also known as: ceftriaxone, ampicillin, amoxicillin, amoxicillin-clavulanic acid, Azithromycin, Erythromycin, Erythromycin lactobionate
Standard of Care

Eligibility Criteria

Age2 Months - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • History of and/or documented fever (rectal, ear, or oral temperature ≥38°C or axillary temperature ≥37.5°C) or hypothermia (rectal, ear, or oral temperature \<35°C or axillary temperature \<34.5°C)
  • Chest radiograph infiltrates consistent with bacterial pneumonia (or pneumonia caused by atypical bacterial agents); if a subject is outpatient and starting on oral therapy, a radiograph is not required.
  • Presence of at least 2 of the following signs or symptoms:
  • Cough
  • Difficulty breathing
  • Production of purulent sputum
  • Chest pain
  • Grunting
  • Hypotension
  • Tachycardia, defined as follows:
  • months to \<24 months: ≥160 beats/min 24 months to \<10 years: ≥140 beats/min
  • years: ≥100 beats/min
  • Tachypnea, defined as follows:
  • months to \<12 months: ≥50 breaths/min 12 months to \<5 years: ≥40 breaths/min
  • years: ≥20 breaths/min
  • +8 more criteria

You may not qualify if:

  • Ventilator-associated or hospital-acquired pneumonia
  • \>48 hours of systemic antibacterial therapy
  • confirmed or suspected bacterial meningitis
  • breast-feeding females
  • positive pregnancy test

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (58)

Unknown Facility

Little Rock, Arkansas, 72202, United States

Location

Unknown Facility

Los Angeles, California, 90095, United States

Location

Unknown Facility

Sacramento, California, 95817, United States

Location

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San Diego, California, 92123, United States

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Washington D.C., District of Columbia, 20010, United States

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Unknown Facility

Tampa, Florida, 33606, United States

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Louisville, Kentucky, 40202, United States

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Unknown Facility

Omaha, Nebraska, 68198-2162, United States

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Las Vegas, Nevada, 89102, United States

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Durham, North Carolina, 27710, United States

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Greenville, North Carolina, 27834, United States

Location

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Toledo, Ohio, 43606, United States

Location

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Portland, Oregon, 97239, United States

Location

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Hershey, Pennsylvania, 17033, United States

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Memphis, Tennessee, 38105, United States

Location

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Amarillo, Texas, 79106, United States

Location

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Houston, Texas, 77030, United States

Location

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Splendora, Texas, 77372, United States

Location

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Charlottesville, Virginia, 22905, United States

Location

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Richmond, Virginia, 29298, United States

Location

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Roanoke, Virginia, 24013, United States

Location

Unknown Facility

Pleven, 5800, Bulgaria

Location

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Plovdiv, 4000, Bulgaria

Location

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Rousse, 7002, Bulgaria

Location

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Sofia, 1233, Bulgaria

Location

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Sofia, 1407, Bulgaria

Location

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Sofia, 1431, Bulgaria

Location

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Vratsa, 3001, Bulgaria

Location

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Budapest, 1083, Hungary

Location

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Budapest, 1089, Hungary

Location

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Budapest, 1097, Hungary

Location

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Budapest, 1125, Hungary

Location

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Cegléd, 2700, Hungary

Location

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Debrecen, 4031, Hungary

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Győr, 9024, Hungary

Location

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Gyula, 5700, Hungary

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Mosdós, 7257, Hungary

Location

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Nagykanizsa, 8800, Hungary

Location

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Nyíregyháza, 4400, Hungary

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Szeged, 6720, Hungary

Location

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Székesfehérvár, 8000, Hungary

Location

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Törökbálint, 2045, Hungary

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Veszprém, 8200, Hungary

Location

Unknown Facility

Caloocan, 1400, Philippines

Location

Unknown Facility

Cebu City, 6000, Philippines

Location

Unknown Facility

City of Muntinlupa, 1781, Philippines

Location

Unknown Facility

Davao City, 8000, Philippines

Location

Unknown Facility

Iloilo City, 5000, Philippines

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Unknown Facility

Manila, 1000, Philippines

Location

Unknown Facility

Quezon City, 1100, Philippines

Location

Unknown Facility

Quezon City, 1104, Philippines

Location

Unknown Facility

Esplugues de Llobregat, Barcelona, 08950, Spain

Location

Unknown Facility

Donostia / San Sebastian, Guipuzcoa, 20014, Spain

Location

Unknown Facility

Barcelona, 08035, Spain

Location

Unknown Facility

Barcelona, 08916, Spain

Location

Unknown Facility

Madrid, 28046, Spain

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Unknown Facility

London, N18 1QX, United Kingdom

Location

Unknown Facility

London, SW17 0RE, United Kingdom

Location

MeSH Terms

Conditions

Pneumonia

Interventions

solithromycinStandard of CareCeftriaxoneAmpicillinAmoxicillinAmoxicillin-Potassium Clavulanate CombinationAzithromycinErythromycinerythromycin lactobionate

Condition Hierarchy (Ancestors)

Respiratory Tract InfectionsInfectionsLung DiseasesRespiratory Tract Diseases

Intervention Hierarchy (Ancestors)

Quality Indicators, Health CareQuality of Health CareHealth Services AdministrationHealth Care Quality, Access, and EvaluationCefotaximeCephacetrileCephalosporinsbeta-LactamsLactamsAmidesOrganic ChemicalsThiazinesSulfur CompoundsHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsPenicillin GPenicillinsClavulanic AcidClavulanic AcidsDrug CombinationsPharmaceutical PreparationsMacrolidesPolyketidesLactones

Limitations and Caveats

The study was discontinued early due to a company business decision. Study discontinuation was not related to safety or tolerability.

Results Point of Contact

Title
Melissa Allaband
Organization
Cempra Pharmeuticals, a wholly owned subsidary of Melinta Therapeutics, Inc.

Study Officials

  • Michael Cohen-Wolkowiez, MD, PhD

    Duke Clinical Research Institute

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Masking Details
A healthcare provider designated as a sub-investigator blinded to treatment allocation at the site documented clinical response at specified time points during the study.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 10, 2015

First Posted

November 16, 2015

Study Start

April 1, 2016

Primary Completion

March 21, 2018

Study Completion

March 21, 2018

Last Updated

January 3, 2019

Results First Posted

January 3, 2019

Record last verified: 2018-11

Data Sharing

IPD Sharing
Will not share

Locations