NCT02591030

Brief Summary

Bile duct tumours are rare. They are the 6th most common type of digestive cancer. Their therapeutic management is complex and must be multidisciplinary in nature. Most of the time, an endoscopic or radiological biliary drainage is necessary before any tumour treatment. Their prognosis is poor due to the fact that they are normally diagnosed late, which makes curative surgery impossible. A population study in the Côte d'Or region of France reported a survival rate at 5 years of approximately 10%. For the locally advanced or metastatic forms, treatment has not been properly codified. With respect to chemotherapy, prospective studies, most often phase II, are difficult to interpret due to a limited number of patients and due to the heterogeneity of this type of tumour (bile duct and pancreas tumours). Treatment with 5FU alone provides an objective response in approximately 10% of cases. In combination with mitomycin or carboplatin, the objective response rate is 20%, with a median survival period of 5 months. Interferon combined with 5FU has a better response rate (30%), but occurrences of different types of toxicity are more frequent. More recently, gemcitabine and the 5FU-cisplatin combinations demonstrated objective tumour control in 50% of patients with a median survival period of 10 months. Gemcitabine combined with oxiplatin or with cisplatin has shown the same response rate but a median survival period of approximately 12 months. The benefit of this combination has been confirmed in a phase III trial that compared the gemcitabine-cisplatin combination to gemcitabine alone, in 410 patients with locally advanced unresectable and/or metastatic bile duct cancer. The results were in favour of the combined treatment with a median survival period of 11.7 months (versus 8.1 months - HR 0.64 \[0.52 - 0.80\]). This combination is currently the reference first-line treatment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
191

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2015

Typical duration for phase_2

Geographic Reach
1 country

42 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 26, 2015

Completed
3 days until next milestone

First Posted

Study publicly available on registry

October 29, 2015

Completed
2 months until next milestone

Study Start

First participant enrolled

December 15, 2015

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 27, 2018

Completed
1.6 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 16, 2020

Completed
Last Updated

February 24, 2022

Status Verified

February 1, 2022

Enrollment Period

2.5 years

First QC Date

October 26, 2015

Last Update Submit

February 23, 2022

Conditions

Keywords

Bile Duct Cancerphase II/IIIModified folfirinoxGemcis

Outcome Measures

Primary Outcomes (2)

  • percentage of patients who are alive without radiological progession

    In phase II, the primary endpoint is the percentage of patients alive without radiological progression (assessed according to the RECIST v1.1 criteria) at 6 months (after randomisation). Patients who are in radiological progression or who have died before the 6 months have elapsed will be considered a failure for the primary endpoint at 6 months (after randomisation). A medical review will be conducted to decide on patients without radiological progression at 6 months; in the light of their entire medical file, they may be considered a failure (i.e. in progression) or they may be considered to be truly non-assessable (a 5% surplus of patients has been planned for this situation).

    up to 6 months

  • overall survival

    In phase III, the primary endpoint is overall survival. This is defined as the period between the date of randomisation and the date of death (regardless of the cause). Patients who are lost to follow-up will be censored at the end-point for the analysis, or at the date when they were last heard of.

    up to 6 years

Secondary Outcomes (8)

  • overall survival

    up to 6 months

  • Tumour response

    up to 6 months

  • Tumour response

    up to 6 years

  • Toxicity of the treatment assessed according to NCI-CTC v 4.0

    up to 6 months

  • Toxicity of the treatment assessed according to NCI-CTC v 4.0

    up to 6 years

  • +3 more secondary outcomes

Study Arms (2)

GEMCIS

PLACEBO COMPARATOR
Drug: GEMCIS

mFOLFIRINOX

EXPERIMENTAL
Drug: mFolfirinox

Interventions

GEMCISDRUG

At D1 and D8 of each cycle, i.e. every 21 days for 6 months: * Cisplatin 25 mg/m² over 1 hour at D1 and D8 * Gemcitabine 1000 mg/m² over 30 minutes at D1 and D8.

GEMCIS

At D1 of each cycle, i.e. every 15 days for 6 months: * Oxiplatin: 85 mg/m² (IP/120 minutes) * Irinotecan: 180 mg/m² (IV/90 minutes) * Folinic acid: 400 mg/m² (or 200 mg/m² if Elvorine \[calcium levofolinate\]) (IV/2 hours), via a Y connector at the same time as irinotecan * 5-FU: 2400 mg/m² (IV over 46 hours) without 5FU bolus at D1

mFOLFIRINOX

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • \- WHO 0 or 1
  • Age ≥ 18 years
  • Tumour of the intrahepatic or extrahepatic (and/or hilar) bile ducts, or of the gallbladder
  • Measurable abdominal metastases (at least a lesion \>10 mm) and/or measurable, unresectable primary tumour
  • Disease proven by histopathology or cytology (on metastasis or primary tumour)
  • If there are no abdominal metastases, the unresectability must be confirmed by a hepatobiliary surgeon in a multidisciplinary team (MDT) meeting
  • Bilirubin \<1.5 N (after endoscopic or trance hepatic optimum biliary drainage, if necessary), AST and ALT \<10N
  • Serum creatinine \<130 µmol/L, creatinine clearance \>60 mL/min
  • Neutrophils ≥ 1500/mm3 and platelets ≥ 75,000/mm3
  • Prothrombin index \> 70%
  • Serum albumin \> 25 g/L
  • Patient registered with a social security scheme (including CMU)
  • Signed informed consent form

You may not qualify if:

  • \- Non-measurable metastases and primary tumour
  • Ampullary carcinoma or cancer of the pancreas with infiltration of the bile ducts or mixed tumours (hepatocholangiocarcinoma)
  • Chemotherapy and/or radiotherapy within the last 4 months
  • Other malignant tumour except in situ basal cell carcinoma or curatively treated carcinoma of the uterine cervix or other malignant tumour that has been treated and has been considered cured for at least 5 years
  • Major comorbidity factors (unstable angina, myocardial infarction that has occurred within the last 6 months, heart failure ≥2 according to the NYHA classification, uncontrolled high blood pressure)
  • Woman who is pregnant or breastfeeding, or patient of either sex who is of childbearing age and not using an adequate contraceptive method
  • Not able to undergo the trial medical follow-up for geographical, social or psychological reasons.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (42)

Chu Picardie

Amiens, France

Location

Ico Paul Papin

Angers, France

Location

CH Victor Dupouy

Argenteuil, France

Location

CH de la Côte Basque

Bayonne, 64109, France

Location

CHRU Besançon

Besançon, France

Location

Hôpital Avicenne

Bobigny, France

Location

Hôpital Saint-André

Bordeaux, 33000, France

Location

Polyclinique Nord

Bordeaux, 33000, France

Location

Hôpital Duchenne

Boulogne-sur-Mer, France

Location

Centre François Baclesse

Caen, France

Location

Chu D'Estaing

Clermont-Ferrand, France

Location

Hôpitaux Civils

Colmar, France

Location

Ch Sud Francilien

Corbeil-Essonnes, 91100, France

Location

Centre de radiothérapie et oncologie du Parc

Dijon, 21000, France

Location

Centre Georges François Leclerc

Dijon, France

Location

Hôpital Michallon

Grenoble, France

Location

CHD Vendée

La Roche-sur-Yon, France

Location

Clinique du cap d'Or

La Seyne-sur-Mer, France

Location

CH Le Kremlin Bicetre

Le Kremlin-Bicêtre, France

Location

CHRU Lille

Lille, France

Location

Centre Hospitalier de Longjumeau

Longjumeau, 91160, France

Location

Clinique de la Sauvegarde

Lyon, 69000, France

Location

Centre Léon Bérard

Lyon, France

Location

Hôpital de la Croix Rousse

Lyon, France

Location

Hôpital Lyon Sud

Lyon, France

Location

Hôpital Saint-Joseph

Marseille, France

Location

Centre Catherine de Sienne

Nantes, France

Location

CHR Orléans

Orléans, France

Location

HEGP

Paris, France

Location

Hôpital Cochin

Paris, France

Location

Hôpital Saint-Jean

Perpignan, France

Location

CHU La Miletrie

Poitiers, France

Location

CHU Reims

Reims, France

Location

Centre Eugène Marquis

Rennes, France

Location

Hôpital Drôme Nord

Romans-sur-Isère, France

Location

Chu Rouen

Rouen, France

Location

CHU Saint-Etienne

Saint-Etienne, 42055, France

Location

CH Saint-Jean de Luz

Saint-Jean-de-Luz, 64500, France

Location

CH Saint-Quentin

Saint-Quentin, France

Location

Ch Robert Morlevat

Semur-en-Auxois, France

Location

CAC Paul Strauss

Strasbourg, 67065, France

Location

CHU Tours

Tours, France

Location

Related Publications (1)

  • Phelip JM, Desrame J, Edeline J, Barbier E, Terrebonne E, Michel P, Perrier H, Dahan L, Bourgeois V, Akouz FK, Soularue E, Ly VL, Molin Y, Lecomte T, Ghiringhelli F, Coriat R, Louafi S, Neuzillet C, Manfredi S, Malka D; PRODIGE 38 AMEBICA Investigators/Collaborators. Modified FOLFIRINOX Versus CISGEM Chemotherapy for Patients With Advanced Biliary Tract Cancer (PRODIGE 38 AMEBICA): A Randomized Phase II Study. J Clin Oncol. 2022 Jan 20;40(3):262-271. doi: 10.1200/JCO.21.00679. Epub 2021 Oct 18.

MeSH Terms

Conditions

Bile Duct Neoplasms

Condition Hierarchy (Ancestors)

Biliary Tract NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsBile Duct DiseasesBiliary Tract DiseasesDigestive System Diseases

Study Officials

  • Jean-Marc Phelip, PhD

    CHU SAINT-ETIENNE

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 26, 2015

First Posted

October 29, 2015

Study Start

December 15, 2015

Primary Completion

June 27, 2018

Study Completion

January 16, 2020

Last Updated

February 24, 2022

Record last verified: 2022-02

Data Sharing

IPD Sharing
Will not share

Locations