NCT02589847

Brief Summary

This study will evaluate efficacy and safety information about RBX2660 for the treatment of recurrent Clostridium difficile infection (CDI), and will compare the efficacy of one treatment with RBX2660 versus antibiotic-treated historical controls. Enrolled subjects will receive one treatment consisting of two doses of RBX2660 (microbiota suspension).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
272

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Oct 2015

Typical duration for phase_2

Geographic Reach
2 countries

30 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2015

Completed
25 days until next milestone

First Submitted

Initial submission to the registry

October 26, 2015

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 28, 2015

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2017

Completed
1.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2019

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

May 11, 2020

Completed
Last Updated

March 26, 2021

Status Verified

February 1, 2021

Enrollment Period

1.7 years

First QC Date

October 26, 2015

Results QC Date

April 28, 2020

Last Update Submit

March 25, 2021

Conditions

Keywords

Clostridium difficileC diffCDICDADFecal transplantFecal Microbiota transplantdiarrheaFMTmicrobiota restoration therapymicrobiota suspensionfecal bacteriotherapyC diff diarrhea

Outcome Measures

Primary Outcomes (1)

  • Number of Participants Who Were CDI-diarrhea Free Through 8 Weeks

    Participants were evaluated 8 weeks after study treatment to assess efficacy of RBX2660. Efficacy was assessed as the absence of CDI diarrhea without the need for retreatment with C. difficile anti-infective therapy or fecal transplant through 56 days after completion of study treatment.

    8 weeks after treatment

Secondary Outcomes (3)

  • Quality of Life (SF-36)

    Baseline

  • Quality of Life (SF-36)

    8-Weeks

  • Number of Participants With Major Complications of rCDI From Baseline Through 24 Months

    24 months

Study Arms (2)

RBX2660 Open-label

EXPERIMENTAL

RBX2660 (microbiota suspension)

Biological: RBX2660

Historical control antibiotics

OTHER

Retrospective Historical Control with standard of care

Drug: Standard of Care Antibiotics

Interventions

RBX2660BIOLOGICAL

suspension of intestinal microbes

RBX2660 Open-label

Standard of Care Antibiotics

Also known as: Antibiotics
Historical control antibiotics

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • ≥ 18 years old.
  • Medical record documentation of recurrent CDI including a positive C. difficile test within 60 days prior to enrollment and either: a) at least two recurrences after a primary episode and has completed at least two rounds of standard-of-care oral antibiotic therapy or b) has had at least two episodes of severe CDI resulting in hospitalization.
  • Documented history that the subject's recurrent CDI is controlled while on antibiotics even if the subject is not currently on antibiotics.
  • A positive stool test for the presence of C. difficile within 60 days prior to enrollment

You may not qualify if:

  • A known history of continued CDI diarrhea despite being on a course of antibiotics prescribed for CDI treatment.
  • Requires continuous antibiotic therapy for a condition other than CDI.
  • Previous successful (resolution of CDI diarrhea) fecal transplant for recurrent CDI \< 6 months prior to study enrollment.
  • Previous unsuccessful (recurrent CDI diarrhea was unresolved) fecal transplant.
  • Previous treatment with RBX2660.
  • Diagnosis of inflammatory bowel disease (IBD), e.g., ulcerative colitis, Crohn's disease, or microscopic colitis.
  • Diagnosis of irritable bowel syndrome (IBS) as determined by Rome III criteria.
  • History of chronic diarrhea.
  • History of celiac disease.
  • Disease symptoms caused by a confirmed intestinal pathogen other than C. difficile.
  • Colostomy.
  • Planned surgery requiring perioperative antibiotics within 3 months of study enrollment.
  • Life expectancy of \< 12 months.
  • Compromised immune system

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (30)

Unknown Facility

Phoenix, Arizona, 85054, United States

Location

Unknown Facility

North Little Rock, Arkansas, 72117, United States

Location

Unknown Facility

Sacramento, California, 95817, United States

Location

Unknown Facility

Bay Pines, Florida, 33744, United States

Location

Unknown Facility

Coral Springs, Florida, 33065, United States

Location

Unknown Facility

Gainesville, Florida, 32610, United States

Location

Unknown Facility

Miami, Florida, 33101, United States

Location

Unknown Facility

Idaho Falls, Idaho, 83404, United States

Location

Unknown Facility

Chicago, Illinois, 60637, United States

Location

Unknown Facility

Maywood, Illinois, 60153, United States

Location

Unknown Facility

Indianapolis, Indiana, 46260, United States

Location

Unknown Facility

Lafayette, Indiana, 47904, United States

Location

Unknown Facility

Lexington, Kentucky, 40506, United States

Location

Unknown Facility

Detroit, Michigan, 48202, United States

Location

Unknown Facility

Rochester, Minnesota, 55905, United States

Location

Unknown Facility

Saint Paul, Minnesota, 55130, United States

Location

Unknown Facility

St Louis, Missouri, 63110, United States

Location

Unknown Facility

Omaha, Nebraska, 68198, United States

Location

Unknown Facility

Flushing, New York, 11355, United States

Location

Unknown Facility

Rochester, New York, 14618, United States

Location

Unknown Facility

Syracuse, New York, 52325, United States

Location

Unknown Facility

The Bronx, New York, 10468, United States

Location

Unknown Facility

Fargo, North Dakota, 58122, United States

Location

Unknown Facility

Lima, Ohio, 45801, United States

Location

Unknown Facility

Jackson, Tennessee, 38305, United States

Location

Unknown Facility

Houston, Texas, 77025, United States

Location

Unknown Facility

Springfield, Virginia, 22150, United States

Location

Unknown Facility

Virginia Beach, Virginia, 23454, United States

Location

Unknown Facility

Vancouver, British Columbia, V5Z1M9, Canada

Location

Unknown Facility

Hamilton, Ontario, L8N4A6, Canada

Location

Related Publications (3)

  • Lee C, Feuerstadt P, Louie T, Bancke L, Guthmueller B, Harvey A, Hoeyer F, Orenstein R, Dubberke ER, Khanna S. Integrated analysis of the safety of fecal microbiota, live-jslm in adults with recurrent Clostridioides difficile infection from five prospective clinical trials: an update. Therap Adv Gastroenterol. 2025 Nov 12;18:17562848251395566. doi: 10.1177/17562848251395566. eCollection 2025.

  • Reveles KR, Gonzales-Luna AJ, Golan Y, Alonso CD, Guthmueller B, Tan X, Bidell MR, Pokhilko V, Crawford CV, Skinner AM. Efficacy of Fecal Microbiota, Live-jslm (REBYOTA(R)), Among Patients Exposed to Non-Clostridioides difficile Infection Antibiotics: Post Hoc Subgroup Analysis of a Phase 2 Open-Label Study. Open Forum Infect Dis. 2024 Jun 17;11(7):ofae341. doi: 10.1093/ofid/ofae341. eCollection 2024 Jul.

  • Orenstein R, Dubberke ER, Khanna S, Lee CH, Yoho D, Johnson S, Hecht G, DuPont HL, Gerding DN, Blount KF, Mische S, Harvey A. Durable reduction of Clostridioides difficile infection recurrence and microbiome restoration after treatment with RBX2660: results from an open-label phase 2 clinical trial. BMC Infect Dis. 2022 Mar 12;22(1):245. doi: 10.1186/s12879-022-07256-y.

MeSH Terms

Conditions

Clostridium InfectionsDiarrhea

Interventions

Anti-Bacterial Agents

Condition Hierarchy (Ancestors)

Gram-Positive Bacterial InfectionsBacterial InfectionsBacterial Infections and MycosesInfectionsSigns and Symptoms, DigestiveSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Anti-Infective AgentsTherapeutic UsesPharmacologic ActionsChemical Actions and Uses

Results Point of Contact

Title
Clinical Development
Organization
Rebiotix, Inc.

Study Officials

  • Arnab Ray, MD

    Ochsner Health System

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 26, 2015

First Posted

October 28, 2015

Study Start

October 1, 2015

Primary Completion

June 1, 2017

Study Completion

March 1, 2019

Last Updated

March 26, 2021

Results First Posted

May 11, 2020

Record last verified: 2021-02

Locations