NCT02574923

Brief Summary

The aim of this study is to assess the safety and effectiveness of autologous bone marrow mononuclear stem cells in patients with cerebral palsy.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
30

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Nov 2015

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 9, 2015

Completed
5 days until next milestone

First Posted

Study publicly available on registry

October 14, 2015

Completed
22 days until next milestone

Study Start

First participant enrolled

November 5, 2015

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 30, 2018

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2018

Completed
Last Updated

May 7, 2018

Status Verified

May 1, 2018

Enrollment Period

2.4 years

First QC Date

October 9, 2015

Last Update Submit

May 1, 2018

Conditions

Keywords

Cerebral PalsyStem Cells

Outcome Measures

Primary Outcomes (2)

  • Change in Total Score of Gross Motor Function Measure (GMFM)-88

    GMFM-88

    3 months and 6 months after transplantation

  • Change in Gross Motor Function Measure (GMFM)-66 Percentile

    GMFM-66 percentile

    3 months and 6 months after transplantation

Secondary Outcomes (4)

  • Change in Muscle tone

    3 months and 6 months after transplantation

  • Number of adverse events

    Through study completion, an average of 6 months

  • Change in Denver Developmental Score

    3 months and 6 months after transplantation

  • Change in Quality of Life

    3 months and 6 months after transplantation

Study Arms (1)

Stem cell transplantation

EXPERIMENTAL

2 intrathecal administrations of autologous bone marrow mononuclear cells at baseline and 3 months afterward

Biological: Autologous Bone Marrow Mononuclear Cells

Interventions

Transplantation of Autologous Bone Marrow Mononuclear Cells

Stem cell transplantation

Eligibility Criteria

Age2 Years - 15 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Cerebral palsy of any types caused by oxygen deprivation.

You may not qualify if:

  • Epilepsy
  • Hydrocephalus with ventricular drain
  • Coagulation disorders
  • Allergy to anesthetic agents
  • Severe health conditions such as cancer, failure of heart, lung, liver or kidney
  • Active infections

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Vinmec International Hospital

Hanoi, Vietnam

Location

Related Publications (3)

  • Sharma A, Sane H, Gokulchandran N, Kulkarni P, Gandhi S, Sundaram J, Paranjape A, Shetty A, Bhagwanani K, Biju H, Badhe P. A clinical study of autologous bone marrow mononuclear cells for cerebral palsy patients: a new frontier. Stem Cells Int. 2015;2015:905874. doi: 10.1155/2015/905874. Epub 2015 Feb 18.

    PMID: 25788947BACKGROUND
  • Than UTT, Nguyen LT, Nguyen PH, Nguyen XH, Trinh DP, Hoang DH, Nguyen PAT, Dang VD. Inflammatory mediators drive neuroinflammation in autism spectrum disorder and cerebral palsy. Sci Rep. 2023 Dec 18;13(1):22587. doi: 10.1038/s41598-023-49902-8.

  • Nguyen TL, Nguyen HP, Nguyen TK. The effects of bone marrow mononuclear cell transplantation on the quality of life of children with cerebral palsy. Health Qual Life Outcomes. 2018 Aug 14;16(1):164. doi: 10.1186/s12955-018-0992-x.

MeSH Terms

Conditions

Cerebral Palsy

Condition Hierarchy (Ancestors)

Brain Damage, ChronicBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Study Officials

  • Liem T Nguyen, MD., PhD.

    Vinmec Healthcare System

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 9, 2015

First Posted

October 14, 2015

Study Start

November 5, 2015

Primary Completion

March 30, 2018

Study Completion

April 30, 2018

Last Updated

May 7, 2018

Record last verified: 2018-05

Locations