NCT02561234

Brief Summary

This is the first-in-human study of the safety of increasing dose levels of AEB1102 in patients with advanced cancers. The study will also evaluate the amounts of AEB1102 in blood, the effects of AEB1102 on blood amino acid levels and tumor growth.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
98

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Oct 2015

Typical duration for phase_1

Geographic Reach
1 country

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 25, 2015

Completed
1 month until next milestone

First Posted

Study publicly available on registry

September 28, 2015

Completed
3 days until next milestone

Study Start

First participant enrolled

October 1, 2015

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2019

Completed
Last Updated

November 5, 2021

Status Verified

November 1, 2021

Enrollment Period

3.6 years

First QC Date

August 25, 2015

Last Update Submit

November 3, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • maximum tolerated dose

    the dose level at which no more than 1/6 patients experiences dose-limiting toxicity

    4 weeks

Secondary Outcomes (1)

  • safety profile (changes in physical exam, laboratory measures, reported adverse events)

    4 weeks +

Study Arms (10)

AEB1102 Dose Escalation Cohort 1

EXPERIMENTAL

3 patients dosed at 0.01 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 2

EXPERIMENTAL

4 patients dosed at 0.02 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 3

EXPERIMENTAL

4 patients dosed at 0.04 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 4

EXPERIMENTAL

4 patients dosed at 0.08 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 5

EXPERIMENTAL

3 patients dosed at 0.12 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 6

EXPERIMENTAL

4 patients dosed at 0.18 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 7

EXPERIMENTAL

5 patients dosed at 0.27 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 8

EXPERIMENTAL

7 patients dosed at 0.40 mg/kg until MTD determined

Drug: Co-ArgI-PEG

AEB1102 Dose Escalation Cohort 9

EXPERIMENTAL

7 patients dosed at 0.33 mg/kg until MTD determined MTD determined at 0.33 mg/kg

Drug: Co-ArgI-PEG

AEB1102 Expansion

EXPERIMENTAL

Uveal: 11 patients dosed at 0.33 mg/kg Cutaneous Melanoma: 11 dosed at 0.33 mg/kg SCLC: 13 patients dosed at 0.33 mg/kg

Drug: Co-ArgI-PEG

Interventions

Administered IV

Also known as: AEB1102
AEB1102 Dose Escalation Cohort 1AEB1102 Dose Escalation Cohort 2AEB1102 Dose Escalation Cohort 3AEB1102 Dose Escalation Cohort 4AEB1102 Dose Escalation Cohort 5AEB1102 Dose Escalation Cohort 6AEB1102 Dose Escalation Cohort 7AEB1102 Dose Escalation Cohort 8AEB1102 Dose Escalation Cohort 9AEB1102 Expansion

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • For patients participating in any part of the trial:
  • has an advanced solid tumor previously treated with, or inability to tolerate, standard therapy for the disease, or for which a standard therapy does not exist, and as such is considered a candidate for Phase 1 treatment
  • has adequate organ function: Hgb ≥9 g/dL; absolute neutrophil count (ANC) ≥ 1.5x109/L; plt ≥ 100,000/μL; AST and ALT \< 2.5x ULN (\< 5x ULN in patients with liver metastases); total bilirubin \< 2.0 mg/dL; serum creatinine ≤ 1.5x ULN
  • ECOG performance score 0-2
  • For patients participating in any expansion group:
  • has measurable disease based on RECIST 1.1 as determined by the treating investigator. Tumor lesions in a previously irradiated area are considered measurable if progression has been demonstrated in such lesions
  • willing to consent for biopsy is strongly recommended but not mandatory
  • recovery of toxicities related to any prior treatments to at least Grade 1 by CTCAE v 4.03. Exceptions are patients with adverse event(s) that are clinically nonsignificant and/or stable on supportive therapy.
  • For patients participating in specific expansion groups:
  • Cutaneous Melanoma:
  • unresectable, locally advanced or metastatic (AJCC stage IIIB, IIIC, or IV) cutaneous malignant melanoma
  • relapsed or progressive disease after or unable to tolerate at least one prior systemic anticancer regimen for metastatic disease involving immunotherapy (anti-PD-1, anti-PD-L1, or anti-CTLA-4)
  • in tumors with a relevant BRAF mutation, relapsed, refactory, or unable to tolerate at least one prior systemic anticancer regimen for metastic disease involving a BRAF inhibitor
  • Uveal Melanoma:
  • uveal melanoma at metastic stage
  • +2 more criteria

You may not qualify if:

  • has primary CNS malignancy
  • history of untreated brain mets or leptomeningeal disease or spinal cord compression
  • effects of prior anticancer therapy recovered to grade \< 2
  • known HIV
  • active infection
  • major surgery within 2 weeks
  • history of another malignancy within 2 years prior

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Pinnacle Research

Phoenix, Arizona, 85258, United States

Location

UCLA

Los Angeles, California, 90024, United States

Location

University of Colorado

Aurora, Colorado, 80045, United States

Location

Research Center: Mid Florida Hematology/Oncology Centers

Orange City, Florida, 32763, United States

Location

Dana Farber

Boston, Massachusetts, 02114, United States

Location

Massachusetts General

Boston, Massachusetts, 02114, United States

Location

Washington University

St Louis, Missouri, 93110, United States

Location

Columbia University

New York, New York, 10032, United States

Location

Providence Cancer Center

Portland, Oregon, 97213, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15232, United States

Location

UTSW

Dallas, Texas, 75390-8852, United States

Location

Study Officials

  • Jim Joffrion

    Aeglea Biotherapeutics, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 25, 2015

First Posted

September 28, 2015

Study Start

October 1, 2015

Primary Completion

May 1, 2019

Study Completion

May 1, 2019

Last Updated

November 5, 2021

Record last verified: 2021-11

Locations