NCT02497001

Brief Summary

Study to Assess the Efficacy and Safety of PT010, PT003, and PT009 Compared With Symbicort® Turbuhaler® in Subjects with Moderate to Very Severe Chronic Obstructive Pulmonary Disease.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,902

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Aug 2015

Geographic Reach
4 countries

190 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 8, 2015

Completed
6 days until next milestone

First Posted

Study publicly available on registry

July 14, 2015

Completed
27 days until next milestone

Study Start

First participant enrolled

August 10, 2015

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 5, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 5, 2018

Completed
3 years until next milestone

Results Posted

Study results publicly available

December 24, 2020

Completed
Last Updated

December 24, 2020

Status Verified

December 1, 2020

Enrollment Period

2.4 years

First QC Date

July 8, 2015

Results QC Date

March 26, 2020

Last Update Submit

December 23, 2020

Conditions

Outcome Measures

Primary Outcomes (2)

  • FEV1 AUC0-4

    FEV1 AUC0-4 (L) for The Efficacy Estimand (Change from baseline in forced expiratory volume in 1 second (FEV1) area under the curve from 0 to 4 hours (AUC0-4) AUC was normalized for length of follow up (e.g. typically 4 hours)).

    at Week 24

  • Change From Baseline in Morning Pre-dose Trough FEV1

    Morning Pre-Dose Trough FEV1 (L) for The Efficacy Estimand

    at Week 24

Secondary Outcomes (11)

  • Change From Baseline in Morning Pre-dose Trough FEV1

    over 24 Weeks

  • Peak Change From Baseline in FEV1 Within 4 Hours Post-dosing

    at Week 24

  • Rate of Moderate or Severe COPD Exacerbations

    over 24 weeks

  • Percentage of Subjects Achieving a Minimal Clinically Important Difference (MCID) of 4 Units or More in SGRQ Total Score (SGRQ Responders)

    at Week 24

  • Change From Baseline in Average Daily Rescue Ventolin HFA Use

    over 24 Weeks

  • +6 more secondary outcomes

Study Arms (4)

BGF MDI (PT010) 320/14.4/9.6 μg ex-actuator

EXPERIMENTAL

BGF MDI 320/14.4/9.6 μg,Budesonide, Glycopyrronium, Formoterol Fumarate Inhalation Aerosol

Drug: BGF MDI 320/14.4/9.6 μg

GFF MDI (PT003) 14.4/9.6 μg ex-actuator

EXPERIMENTAL

GFF MDI 14.4/9.6 μg ex-actuator Glycopyrronium, Formoterol Fumarate Inhalation Aerosol

Drug: GFF MDI (PT003) 14.4/9.6 μg

BFF MDI (PT009) 320/9.6 μg ex-actuator

EXPERIMENTAL

BFF MDI 320/9.6 μg, Budesonide, Formoterol Fumarate Inhalation Aerosol

Drug: BFF MDI (PT009) 320/9.6 μg

Symbicort

ACTIVE COMPARATOR

Symbicort® Turbuhaler® (TBH) Inhalation Powder 200/6 μg

Drug: Symbicort® Turbuhaler® (TBH) Inhalation Powder

Interventions

Budesonide, Glycopyrronium, and Formoterol Fumarate Inhalation Aerosol (PT010, BGF metered dose inhaler \[MDI\])

Also known as: BGF
BGF MDI (PT010) 320/14.4/9.6 μg ex-actuator

Glycopyrronium and Formoterol Fumarate Inhalation Aerosol (PT003, GFF MDI)

Also known as: GFF
GFF MDI (PT003) 14.4/9.6 μg ex-actuator

Budesonide and Formoterol Fumarate Inhalation Aerosol (PT009, BFF MDI)

Also known as: BFF
BFF MDI (PT009) 320/9.6 μg ex-actuator

Eligibility Criteria

Age40 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Given their signed written informed consent to participate.
  • Non-child bearing potential (ie, physiologically incapable of becoming pregnant, including any female who is 2 years post-menopausal); or Child bearing potential, has a negative serum pregnancy test at Visit 1, and agrees to acceptable contraceptive methods used consistently and correctly for the duration of the study.
  • Subjects with an established clinical history of COPD as defined by the American Thoracic Society (ATS)/European Respiratory Society (ERS), or other local applicable guidelines.
  • Current or former smokers with a history of at least 10 pack-years of cigarette smoking.
  • Forced expiratory volume in 1 second (FEV1)/Forced vital capacity (FVC) ratio must be \<0.70 and FEV1 must be \<80% predicted normal value calculated using NHANES III reference equations (or reference norms applicable to other regions).
  • Required COPD maintenance therapy:
  • All Subjects must have been on two or more inhaled maintenance therapies for the management of their COPD for at least 6 weeks prior to Screening. Scheduled SABA and/or scheduled SAMA are considered inhaled maintenance therapies

You may not qualify if:

  • Significant diseases or conditions other than COPD, which, in the opinion of the Investigator, may put the subject at risk because of participation in the study or may influence either the results of the study or the subject's ability to participate in the study.
  • Women who are pregnant or lactating, or are planning to become pregnant during the course of the study, or women of childbearing potential who are not using an acceptable method of contraception.
  • Subjects, who in the opinion of the Investigator, have a current diagnosis of asthma.
  • Subjects who have been hospitalized due to poorly controlled COPD within 3 months prior to Visit 1 (Screening) or during the Screening Period
  • Subjects who have poorly controlled COPD, defined as acute worsening of COPD that requires treatment with oral corticosteroids or antibiotics within 6 weeks prior to Visit 1 (Screening) or during the Screening Period
  • Immune suppression or severe neurological disorders affecting control of the upper airway or other risk factors that in the opinion of the Investigator would put the subject at substantial risk of pneumonia.
  • Subjects with a diagnosis of narrow angle glaucoma, who, in the opinion of the Investigator, have not been adequately treated.
  • Subjects who have a history of hypersensitivity to β2-agonists, budesonide or any other corticosteroid components, glycopyrronium or other muscarinic anticholinergics, or any other component of the IMPs.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (190)

Research Site

Andalusia, Alabama, 36420, United States

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Jasper, Alabama, 35501, United States

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Peoria, Arizona, 85381, United States

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Phoenix, Arizona, 85018, United States

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Fullerton, California, 92835, United States

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Gold River, California, 95670, United States

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Poway, California, 92064, United States

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Rolling Hills Estates, California, 90274, United States

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Sacramento, California, 95821, United States

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Clearwater, Florida, 33756, United States

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Miami, Florida, 33175, United States

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Miami, Florida, 33186, United States

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Ormond Beach, Florida, 32174, United States

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Pensacola, Florida, 32503, United States

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Tamarac, Florida, 33321, United States

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Tampa, Florida, 33603, United States

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Winter Park, Florida, 32789, United States

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Dacula, Georgia, 30019, United States

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Norcross, Georgia, 30071, United States

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Rincon, Georgia, 31326, United States

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Edina, Minnesota, 55435, United States

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Minneapolis, Minnesota, 55402, United States

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Minneapolis, Minnesota, 55407, United States

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Woodbury, Minnesota, 55125, United States

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Saint Charles, Missouri, 63301, United States

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St Louis, Missouri, 63141, United States

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Reno, Nevada, 89503, United States

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Albuquerque, New Mexico, 87108, United States

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Charlotte, North Carolina, 28207, United States

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Gastonia, North Carolina, 28054, United States

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Greensboro, North Carolina, 27408, United States

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Hendersonville, North Carolina, 28739, United States

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Mooresville, North Carolina, 28117, United States

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Wilmington, North Carolina, 28401, United States

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Winston-Salem, North Carolina, 27103, United States

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Cincinnati, Ohio, 45231, United States

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Cincinnati, Ohio, 45242, United States

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Cincinnati, Ohio, 45245, United States

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Columbus, Ohio, 43213, United States

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Columbus, Ohio, 43235, United States

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Dayton, Ohio, 45459, United States

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Dublin, Ohio, 43016, United States

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Medford, Oregon, 97504, United States

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Anderson, South Carolina, 29621, United States

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Charleston, South Carolina, 29406, United States

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Easley, South Carolina, 29640, United States

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Greenville, South Carolina, 29615, United States

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Mt. Pleasant, South Carolina, 29464, United States

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Old Point Station, South Carolina, 29707, United States

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Rock Hill, South Carolina, 29732, United States

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Seneca, South Carolina, 29678, United States

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Spartanburg, South Carolina, 29303, United States

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Union, South Carolina, 29379, United States

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Johnson City, Tennessee, 37601, United States

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Kingwood, Texas, 77339, United States

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Longview, Texas, 75605, United States

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San Antonio, Texas, 78229, United States

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Abingdon, Virginia, 24210, United States

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Newport News, Virginia, 23606, United States

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Richmond, Virginia, 23225, United States

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Richmond, Virginia, 23229, United States

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Tacoma, Washington, 98405, United States

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Morgantown, West Virginia, 26505, United States

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Truro, Nova Scotia, B2N 1L2, Canada

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Greater Sudbury, Ontario, P3A 1W8, Canada

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Mississauga, Ontario, L4V 1P1, Canada

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Toronto, Ontario, M3J 2C5, Canada

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Mirabel, Quebec, J7J 2K8, Canada

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Montreal, Quebec, H1M 1B1, Canada

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Québec, Quebec, G1V 4G5, Canada

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Trois-Rivières, Quebec, G8T 7A1, Canada

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Québec, G1W 4R4, Canada

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Anqing, 246003, China

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Baotou, 14010, China

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Beijing, 100048, China

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Beijing, 100730, China

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Beijing, 100853, China

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Beijing, CN-100029, China

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Changchun, 130021, China

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Changsha, 410002, China

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Changsha, 410011, China

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Guangzhou, 510000, China

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Guangzhou, 510120, China

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Guangzhou, 510150, China

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Guangzhou, 510180, China

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Haikou, 570311, China

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Hangzhou, 310014, China

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Heshan, 413000, China

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Hohhot, 010017, China

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Hohhot, 010050, China

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Jinan, 250013, China

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Lianyungang, 222 002, China

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Linhai, 317000, China

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Nanchang, 330006, China

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Pingxiang, 337055, China

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Shanghai, 200092, China

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Shanghai, 200120, China

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Shanghai, 200240, China

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Shanghai, 200433, China

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Shengyang, 110004, China

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Shenyang, 110001, China

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Shenyang, 110016, China

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Taiyuan, 030001, China

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Tianjin, 300052, China

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Ürümqi, 830054, China

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Wenzhou, 325027, China

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Wuhan, 430022, China

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Wuxi, 320204, China

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Xuzhou, 221006, China

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Yangzhou, 225012, China

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Zhuhai, 519099, China

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Bunkyō City, 113-8431, Japan

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Chūōku, 103-0022, Japan

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Chūōku, 103-0027, Japan

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Chūōku, 104-8560, Japan

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Date-gun, 969-1793, Japan

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Fukuoka, 814-0180, Japan

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Ginowan-shi, 901-2214, Japan

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Hakata-shi, 812-0033, Japan

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Hamamatsu, 430-0906, Japan

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Hamamatsu, 430-8525, Japan

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Hamamatsu, 434-8511, Japan

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Higashiokitama-gun, 992-0601, Japan

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Higashiosaka-shi, 577-0843, Japan

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Himeji-shi, 672-8064, Japan

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Hirakata-shi, 573-1191, Japan

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Iizuka-shi, 820-8505, Japan

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Itabashi-ku, 173-8610, Japan

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Iwata-shi, 438-8550, Japan

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Izumo-shi, 693-0068, Japan

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Izumo-shi, 693-8501, Japan

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Kagoshima, 892-0847, Japan

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Kahoku-gun, 920-0293, Japan

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Kakogawa-shi, 675-0023, Japan

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Kasaoka-shi, 714-0081, Japan

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Kasuga-shi, 816-0813, Japan

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Kishiwada-shi, 596-8501, Japan

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Kiyose-shi, 204-0023, Japan

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Kobe, 650-0017, Japan

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Koga-shi, 811-3195, Japan

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Kurashiki-shi, 711-0921, Japan

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Kure-shi, 737-0193, Japan

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Kure-shi, 737-8505, Japan

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Kyoto, 601-1434, Japan

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Kyoto, 601-8206, Japan

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Kyoto, 602-8026, Japan

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Kyoto, 607-8062, Japan

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Kyoto, 615-8087, Japan

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Maebashi, 371-0054, Japan

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Matsumoto-shi, 390-0872, Japan

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Matsusaka-shi, 515-8544, Japan

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Meguro-ku, 153-8515, Japan

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Mitaka-shi, 181-8611, Japan

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Mizunami-shi, 509-6134, Japan

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Nagaoka-shi, 940-2085, Japan

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Nagoya, 454-8502, Japan

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Nagoya, 457-8511, Japan

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Nagoya, 466-8560, Japan

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Naha, 902-0061, Japan

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Nishishirakawa-gun, 969-0213, Japan

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Obihiro-shi, 080-0013, Japan

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Ogaki-shi, 503-8502, Japan

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Okinawa-shi, 904-2143, Japan

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Ookawa-shi, 831-0016, Japan

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Osaka, 543-0035, Japan

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Osakasayama-shi, 589-8511, Japan

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Ōita, 870-0921, Japan

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Ōita, 870-0951, Japan

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Ōtsu, 520-0804, Japan

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Sakaide-shi, 762-8550, Japan

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Sakaishi, 591-8555, Japan

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Sapporo, 001-0901, Japan

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Sapporo, 064-0915, Japan

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Sendai, 980-8574, Japan

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Sendai, 983-0824, Japan

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Sendai, 984-8560, Japan

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Seto-shi, 489-8642, Japan

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Shinagawa-ku, 142-8666, Japan

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Shinjuku-ku, 162-0052, Japan

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Shizuoka, 420-8630, Japan

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Suita-shi, 564-0013, Japan

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Tachikawa-shi, 190-0014, Japan

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Takamatsu, 760-8538, Japan

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Toon-shi, 791-0281, Japan

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Toshima-ku, 171-0014, Japan

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Toyama, 930-0194, Japan

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Toyama, 931-8533, Japan

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Toyama, 939-8282, Japan

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Yanagawa-shi, 832-0059, Japan

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Yokohama, 236-0004, Japan

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Related Publications (12)

  • Patel M, Marshall J, Martinez FJ, Mushunje A, Bowen K, Jenkins M. Frequent productive cough in COPD relates to exacerbation risk and treatment benefit from budesonide/glycopyrrolate/formoterol fumarate: a post hoc analysis of KRONOS. Respir Med. 2025 Dec;250:108499. doi: 10.1016/j.rmed.2025.108499. Epub 2025 Nov 12.

  • Singh D, Bafadhel M, Arya N, Marshall J, Parikh H, Kisielewicz D, Movitz C, Bowen K, Patel M. Step up to triple therapy versus switch to dual bronchodilator therapy in patients with COPD on an inhaled corticosteroid/long-acting beta2-agonist: post-hoc analyses of KRONOS. Respir Res. 2025 May 8;26(1):175. doi: 10.1186/s12931-025-03234-5.

  • Muro S, Seki M, Hurst JR, Petullo D, Marshall J, Bowen K, Darken PF, Duncan EA, Megally A, Patel M. Triple Therapy with Budesonide/Glycopyrronium/Formoterol Fumarate Dihydrate versus Dual Therapies for Patients with COPD and Phenotypic Features of Asthma: A Pooled Post Hoc Analysis of KRONOS and ETHOS. Int J Chron Obstruct Pulmon Dis. 2024 Dec 12;19:2729-2737. doi: 10.2147/COPD.S478349. eCollection 2024.

  • Muro S, Kawayama T, Sugiura H, Seki M, Duncan EA, Bowen K, Marshall J, Megally A, Patel M. Benefits of budesonide/glycopyrronium/formoterol fumarate dihydrate on lung function and exacerbations of COPD: a post-hoc analysis of the KRONOS study by blood eosinophil level and exacerbation history. Respir Res. 2024 Aug 5;25(1):297. doi: 10.1186/s12931-024-02918-8.

  • Singh D, Hurst JR, Martinez FJ, Rabe KF, Bafadhel M, Jenkins M, Salazar D, Dorinsky P, Darken P. Predictive modeling of COPD exacerbation rates using baseline risk factors. Ther Adv Respir Dis. 2022 Jan-Dec;16:17534666221107314. doi: 10.1177/17534666221107314.

  • Liu J, He X, Wu J. Economic Evaluation of Triple Therapy with Budesonide/Glycopyrrolate/Formoterol Fumarate for the Treatment of Moderate to Very Severe Chronic Obstructive Pulmonary Disease in China Using a Semi-Markov Model. Appl Health Econ Health Policy. 2022 Sep;20(5):743-755. doi: 10.1007/s40258-022-00732-1. Epub 2022 Apr 28.

  • Muro S, Sugiura H, Darken P, Dorinsky P. Efficacy of budesonide/glycopyrronium/formoterol metered dose inhaler in patients with COPD: post-hoc analysis from the KRONOS study excluding patients with airway reversibility and high eosinophil counts. Respir Res. 2021 Jun 28;22(1):187. doi: 10.1186/s12931-021-01773-1.

  • Huang Y, Assam PN, Feng C, Su R, Dorinsky P, Gillen M. Ethnic pharmacokinetic comparison of budesonide/glycopyrrolate/formoterol fumarate metered dose inhaler (BGF MDI) between Asian and Western healthy subjects. Pulm Pharmacol Ther. 2020 Oct;64:101976. doi: 10.1016/j.pupt.2020.101976. Epub 2020 Nov 2.

  • Wang C, Yang T, Kang J, Chen R, Zhao L, He H, Assam PN, Su R, Bourne E, Ballal S, DeAngelis K, Dorinsky P. Efficacy and Safety of Budesonide/Glycopyrrolate/Formoterol Fumarate Metered Dose Inhaler in Chinese Patients with COPD: A Subgroup Analysis of KRONOS. Adv Ther. 2020 Apr;37(4):1591-1607. doi: 10.1007/s12325-020-01266-5. Epub 2020 Mar 6.

  • Ichinose M, Fukushima Y, Inoue Y, Hataji O, Ferguson GT, Rabe KF, Hayashi N, Okada H, Takikawa M, Bourne E, Ballal S, DeAngelis K, Aurivillius M, Reisner C, Dorinsky P. Long-Term Safety and Efficacy of Budesonide/Glycopyrrolate/Formoterol Fumarate Metered Dose Inhaler Formulated Using Co-Suspension Delivery Technology in Japanese Patients with COPD. Int J Chron Obstruct Pulmon Dis. 2019 Dec 23;14:2993-3002. doi: 10.2147/COPD.S220861. eCollection 2019.

  • Dunn LJ, Kerwin EM, DeAngelis K, Darken P, Gillen M, Dorinsky P. Pharmacokinetics of budesonide/glycopyrrolate/formoterol fumarate metered dose inhaler formulated using co-suspension delivery technology after single and chronic dosing in patients with COPD. Pulm Pharmacol Ther. 2020 Feb;60:101873. doi: 10.1016/j.pupt.2019.101873. Epub 2019 Dec 10.

  • Ferguson GT, Rabe KF, Martinez FJ, Fabbri LM, Wang C, Ichinose M, Bourne E, Ballal S, Darken P, DeAngelis K, Aurivillius M, Dorinsky P, Reisner C. Triple therapy with budesonide/glycopyrrolate/formoterol fumarate with co-suspension delivery technology versus dual therapies in chronic obstructive pulmonary disease (KRONOS): a double-blind, parallel-group, multicentre, phase 3 randomised controlled trial. Lancet Respir Med. 2018 Oct;6(10):747-758. doi: 10.1016/S2213-2600(18)30327-8. Epub 2018 Sep 16.

Related Links

MeSH Terms

Conditions

Pulmonary Disease, Chronic Obstructive

Condition Hierarchy (Ancestors)

Lung Diseases, ObstructiveLung DiseasesRespiratory Tract DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Pearl Therapeutics Inc.
Organization
Pearl Therapeutics Inc.

Study Officials

  • Paul Dorinsky, MD

    Pearl Therapeutics, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 8, 2015

First Posted

July 14, 2015

Study Start

August 10, 2015

Primary Completion

January 5, 2018

Study Completion

January 5, 2018

Last Updated

December 24, 2020

Results First Posted

December 24, 2020

Record last verified: 2020-12

Data Sharing

IPD Sharing
Will share

Locations