NCT02339064

Brief Summary

This is a Phase 3, multicenter, open-label, safety and tolerability study of continuous apomorphine infusion in subjects with advanced Parkinson's Disease (PD) whose motor fluctuations remain unsatisfactory with levodopa (or levodopa/carbidopa) and at least one other class of drugs or mode of therapy for PD.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
99

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Feb 2015

Longer than P75 for phase_3

Geographic Reach
1 country

18 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 31, 2014

Completed
10 months until next milestone

First Posted

Study publicly available on registry

January 15, 2015

Completed
17 days until next milestone

Study Start

First participant enrolled

February 1, 2015

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2018

Completed
7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2025

Completed
Last Updated

June 19, 2025

Status Verified

June 1, 2025

Enrollment Period

3.8 years

First QC Date

March 31, 2014

Last Update Submit

June 18, 2025

Conditions

Keywords

Parkinson's disease,apomorphineApokyndopamine agonistlevodopaadvancedPDcarbidopapramipexoleropinirolerotigotineMAO-B inhibitorsCOMT inhibitorsoffdyskinesia

Outcome Measures

Primary Outcomes (1)

  • Percent of daily "off" time during the waking day

    Baseline Visit to Week 12

Secondary Outcomes (11)

  • Percent daily "on" time without troublesome dyskinesias during waking day

    Baseline Visit to Week 12

  • Percent of daily "off" time during the waking day

    Baseline Visit to Treatment Weeks 2, 4, 8, 20, 28, 36, 44, and 52; and all Treatment Extension Period Visits

  • Percent of daily "on" time without troublesome dyskinesias during the waking day

    Baseline Visit to Treatment Weeks 2, 4, 8, 20, 28, 36, 44, and 52; and all Treatment Extension Period Visits

  • Percent of daily "on" time without dyskinesias

    Baseline Visit to Treatment Weeks 2, 4, 8, 20, 28, 36, 44, and 52; and all Treatment Extension Period Visits

  • Unified Parkinson's Disease Rating Scale - Motor Score

    Baseline Visit to Week 12

  • +6 more secondary outcomes

Study Arms (1)

Apomorphine infusion

EXPERIMENTAL

Continuous subcutaneous apomorphine infusion

Drug: apomorphine infusion

Interventions

Treatment with apomorphine provided by continuous subcutaneous infusion using a portable external electronic pump device

Apomorphine infusion

Eligibility Criteria

Age30 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Advanced idiopathic PD consistent with UK Parkinson's Disease Society Brain Bank Clinical Diagnostic Criteria
  • Overall motor control is unsatisfactory in the opinion of the Investigator and subject despite optimized treatment with available therapies, which must include a stable regimen of daily maintenance levodopa (or levodopa/carbidopa), and at least one of the following other classes of therapies:
  • Dopamine agonists (note: APOKYN intermittent injection is not to be considered here)
  • Monoamine oxidase B \[MAO B\] inhibitors
  • Catechol-O-methyltransferase (COMT) inhibitors
  • Deep brain stimulation (DBS)
  • Levodopa/carbidopa intestinal gel surgery (Duopa, Duodopa)
  • Other - amantadine at doses of up to 400 mg per day)
  • Experiences "off" periods averaging ≥3.0 hours per waking day
  • Other criteria will be discussed in detail with potential subjects by site Investigator

You may not qualify if:

  • Planned surgical intervention for the treatment of Parkinson's disease during participation in the study
  • History of hypersensitivity to apomorphine hydrochloride or any of the ingredients of APOKYN PFS, including sodium metabisulfite
  • Known, suspected, or planned pregnancy or lactation.
  • Recent history (within the previous 12 months) of alcohol or substance abuse
  • History of impulsive/compulsive behaviors primarily associated with the use of dopamine agonists
  • History of previously treated or current diagnosis of malignant melanoma
  • Exhibits certain signs and symptoms of cardiovascular disease
  • Other criteria will be discussed in detail with potential subjects by site Investigator

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (18)

Unknown Facility

Phoenix, Arizona, 85013, United States

Location

Unknown Facility

Loma Linda, California, 92354, United States

Location

Unknown Facility

Los Angeles, California, 90033, United States

Location

Unknown Facility

Los Angeles, California, 90095, United States

Location

Unknown Facility

Aurora, Colorado, 80045, United States

Location

Unknown Facility

Englewood, Colorado, 80113, United States

Location

Unknown Facility

Boca Raton, Florida, 33486, United States

Location

Unknown Facility

Atlanta, Georgia, 30329, United States

Location

Unknown Facility

Augusta, Georgia, 30912, United States

Location

Unknown Facility

Chicago, Illinois, 60611, United States

Location

Unknown Facility

Chicago, Illinois, 60612, United States

Location

Unknown Facility

Kansas City, Kansas, 66160, United States

Location

Unknown Facility

West Bloomfield, Michigan, 48322, United States

Location

Unknown Facility

Albany, New York, 12208, United States

Location

Unknown Facility

Cincinnati, Ohio, 45219, United States

Location

Portland VA Medical Center

Portland, Oregon, 97239, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19107, United States

Location

Unknown Facility

Kirkland, Washington, 98034, United States

Location

MeSH Terms

Conditions

Parkinson DiseaseDyskinesias

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative DiseasesNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Study Officials

  • Gianpiera Ceresoli-Borroni, PhD

    Supernus Pharmaceuticals, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 31, 2014

First Posted

January 15, 2015

Study Start

February 1, 2015

Primary Completion

December 1, 2018

Study Completion

December 1, 2025

Last Updated

June 19, 2025

Record last verified: 2025-06

Locations