NCT02308111

Brief Summary

Primary Biliary Cholangitis (PBC) is a serious, life-threatening, bile acid related liver disease of unknown cause. Without treatment, it frequently progresses to liver fibrosis and eventual cirrhosis requiring liver transplantation or resulting in death. The investigational drug, Obeticholic Acid (OCA) is a modified bile acid and FXR agonist that is derived from the primary human bile acid chenodeoxycholic acid. The key mechanisms of action of OCA, including its choleretic, anti-inflammatory, and anti-fibrotic properties, underlie its hepatoprotective effects and result in attenuation of injury and improved liver function in a cholestatic liver disease such as PBC. The study will assess the effect of OCA compared to placebo, combined with stable standard care, on clinical outcomes in PBC participants.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
334

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started Dec 2014

Longer than P75 for phase_4

Geographic Reach
28 countries

163 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 10, 2014

Completed
24 days until next milestone

First Posted

Study publicly available on registry

December 4, 2014

Completed
22 days until next milestone

Study Start

First participant enrolled

December 26, 2014

Completed
7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 23, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 23, 2021

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

March 9, 2023

Completed
Last Updated

March 9, 2023

Status Verified

February 1, 2023

Enrollment Period

7 years

First QC Date

November 10, 2014

Results QC Date

December 20, 2022

Last Update Submit

February 13, 2023

Conditions

Keywords

Primary Biliary CirrhosisPBCCirrhosisLiver

Outcome Measures

Primary Outcomes (2)

  • Time to the First Occurrence of Composite Endpoint

    To assess the effect of OCA, compared to placebo in conjunction with the established local standard of care, on clinical outcomes in participants with PBC as measured by time to the first occurrence of any of the following adjudicated events, derived as a composite event endpoint of death, liver transplant, model of end-stage liver disease (MELD) ≥15, uncontrolled ascites, or hospitalization for new onset or recurrence of variceal bleed, hepatic encephalopathy (as defined by a West Haven score of \>=2), or spontaneous bacterial peritonitis. The clinical events distribution was estimated using the Kaplan-Meier methodology. Point estimates and 95% confidence intervals (CIs) for the clinical events distribution percentiles (25th and 50th) are provided.

    Time to first occurrence from date of randomization until the time to accrue approximately 127 primary endpoint events (up to 7 years)

  • Time to the First Occurrence of Primary Clinical Event (Expanded Endpoint)

    Primary clinical outcome event is the first occurrence of the following events: death, liver transplant, MELD score \>=15 (MELD-Na score \>=12 baseline), MELD-Na score \>=15 (MELD-Na score \<12 baseline), hospitalization for new onset or recurrence of variceal bleed, hepatic encephalopathy, spontaneous bacterial peritonitis (confirmed by diagnostic paracentesis), or bacterial empyema, uncontrolled or refractory ascites (requiring large volume paracentesis), portal hypertension syndromes, progression to decompensated liver disease, and progression to clinical evidence of portal hypertension without decompensation (for participants without decompensation or clinical evidence of portal hypertension at baseline). 71 endpoint events were observed in the OCA arm, and 80 were observed in the Placebo arm. The clinical events distribution was estimated using the Kaplan-Meier methodology. Point estimates and 95% CIs for the clinical events distribution percentiles (25th and 50th) are provided.

    Time to first occurrence from date of randomization until the time to accrue approximately 127 primary endpoint events (up to 7 years)

Secondary Outcomes (134)

  • Time To First Occurrence Of Severe Decompensating Events of Expanded Composite Endpoint

    Time to first occurrence from date of randomization until the date of first documented progression or date of death from any cause, whichever came first (up to 7 years)

  • Time To Liver Transplant Or Death (All-cause)

    Time to first occurrence from date of randomization until the date of first documented liver transplant or date of death from any cause (up to 7 years)

  • Time to First Occurrence of Fatal Event (All-Cause)

    Time to first occurrence from date of randomization until the date of death from any cause (up to 7 years)

  • Time to First Occurrence of Liver Transplant

    Time to first occurrence from date of randomization until the date of first documented liver transplant or date of death from any cause (up to 5 years)

  • Time to First Occurrence of Hospitalization Due to Hepatic Events

    Time to first occurrence from date of randomization until the date of hospitalization, liver transplant or death from any cause, whichever came first (up to 5 years)

  • +129 more secondary outcomes

Study Arms (2)

Obeticholic Acid (OCA) 5 mg to 10 mg

EXPERIMENTAL

Obeticholic Acid (OCA) 5 mg for a minimum 3 months and then titrating up to a maximum 10 mg for the remainder of the trial (based on tolerability and CP Score).

Drug: Obeticholic Acid (OCA)

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Non-cirrhotic and classified as CP Class A: 5 mg tablet of OCA once daily titrating up to a maximum of 10 mg OCA once daily based on tolerability at 3 months for the duration of the study (majority of participants). Cirrhotic and classified as CP Class B and C: 5 mg tablet of OCA once weekly for at least 3 months, subsequently titrating up to a maximum dose and frequency of 10 mg OCA twice weekly based on tolerability and biochemical response for the duration of the study.

Also known as: 6alpha-ethylchenodeoxycholic acid (6-ECDCA), INT-747
Obeticholic Acid (OCA) 5 mg to 10 mg

One tablet daily (or a lower frequency depending on CP score) for the remainder of the study

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Definite or probable PBC diagnosis (consistent with American Association for the Study of Liver Diseases \[AASLD\] and the European Association for the Study of the Liver \[EASL\] practice guidelines; Lindor 2009; EASL 2009), as demonstrated by the presence of ≥2 of the following 3 diagnostic factors:
  • History of elevated Alkaline phosphatase levels for at least 6 months
  • Positive antimitochondrial antibody (AMA) titer or if AMA negative or in low titer (\<1:80) PBC-specific antibodies (anti-GP210 and/or anti-SP100 and/or antibodies against the major M2 components \[PDC-E2, 2-oxo-glutaric acid dehydrogenase complex\])
  • Liver biopsy consistent with PBC
  • A mean total bilirubin \>ULN and ≤5x ULN and/or a mean ALP \>3x ULN
  • Either is not taking UDCA (no UDCA dose in the past 3 months) or has been taking UDCA for at least 12 months with a stable dose for ≥3 months prior to Day 0

You may not qualify if:

  • History or presence of other concomitant liver diseases including:
  • Hepatitis C virus infection
  • Active Hepatitis B infection; however, subjects who have seroconverted (hepatitis B surface antigen and hepatitis B e antigen negative) may be included in this study after consultation with the medical monitor
  • Primary sclerosing cholangitis (PSC)
  • Alcoholic liver disease
  • Definite autoimmune liver disease or overlap hepatitis
  • Nonalcoholic steatohepatitis (NASH)
  • Gilbert's Syndrome
  • Presence of clinical complications of PBC or clinically significant hepatic decompensation, including:
  • Cirrhosis with complications, including history (within the past 12 months) or presence of:
  • Variceal bleed
  • Uncontrolled ascites
  • Encephalopathy
  • Spontaneous bacterial peritonitis
  • Known or suspected HCC
  • +14 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (181)

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Inland Empire Liver Foundation

Rialto, California, 92377, United States

Location

University of California Davis, Davis Medical Center

Sacramento, California, 95817, United States

Location

Stanford University

Stanford, California, 94304, United States

Location

University of Colorado Denver and Hospital

Aurora, Colorado, 80045, United States

Location

UF Hepatology Research at CTRB

Gainesville, Florida, 32610, United States

Location

Schiff Center for Liver Diseases/University of Miami

Miami, Florida, 33163, United States

Location

Piedmont Atlanta Hospital

Atlanta, Georgia, 30309, United States

Location

Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

Gastrointestinal Specialists of Georgia

Marietta, Georgia, 30060, United States

Location

Northwestern University Feinberg School of Medicine

Chicago, Illinois, 60637, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Indiana University

Indianapolis, Indiana, 46202, United States

Location

Indianapolis Gastroenterology Research Foundation

Indianapolis, Indiana, 46237, United States

Location

University of Louisville, Medical Dental Complex

Louisville, Kentucky, 40202, United States

Location

Tulane University Medical Center

New Orleans, Louisiana, 70112, United States

Location

Mercy Medical Center

Baltimore, Maryland, 21202, United States

Location

UMass Medical School

Worcester, Massachusetts, 01655, United States

Location

Henry Ford Health System

Novi, Michigan, 48377, United States

Location

Minnesota Gastroenterology, P.A.

Saint Paul, Minnesota, 55114, United States

Location

Southern Therapy and Advanced Research (STAR)

Jackson, Mississippi, 39216, United States

Location

Kansas City Research Institute

Kansas City, Missouri, 64131, United States

Location

Saint Louis University Gastroenterology & Hepatology

St Louis, Missouri, 63104, United States

Location

Saint Joseph's Regional Medical Center

Paterson, New Jersey, 07503, United States

Location

Mount Sinai Beth Israel

New York, New York, 10003, United States

Location

Weill Cornell Medical College

New York, New York, 10021, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Quality Medical Research, PLLC

Nashville, Tennessee, 37211, United States

Location

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, 75203, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Texas Digestive Disease Consultants

Dallas, Texas, 75246, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Brooke Army Medical Center

Fort Sam Houston, Texas, 78234, United States

Location

Baylor Scott and White Research Institute

Fort Worth, Texas, 76104, United States

Location

Baylor College of Medicine - Advanced Liver Therapies

Houston, Texas, 77030, United States

Location

UT Health The University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

American Research Corporation at Texas Liver Institute

San Antonio, Texas, 78215, United States

Location

Texas Digestive Disease Consultants

Southlake, Texas, 76092, United States

Location

Clinical Research Centers of America

Murray, Utah, 84123, United States

Location

McGuire DVAMC

Richmond, Virginia, 23249, United States

Location

Swedish Organ Transplant & Liver Center

Seattle, Washington, 98104, United States

Location

Centro De Hepatología

La Plata, Buenos Aires, B1902AWL, Argentina

Location

Hospital Universitario Austral

Presidente Derqui, Buenos Aires, 1629, Argentina

Location

Dim Clínica Privada

Ramos Mejía, Buenos Aires, 1704, Argentina

Location

Hospital Privado Universitario de Cordoba S.A.

Córdoba, Córdoba Province, X5016KEH, Argentina

Location

Hospital Provincial del Centenario

Rosario, Santa Fe Province, S2002KDS, Argentina

Location

CIPREC - Centro de Investigacion y Prevencion Cardiovascular S.A.

Buenos Aires, 1119, Argentina

Location

Hospital De Clinicas University Of Buenos Aires

Buenos Aires, 1120, Argentina

Location

Hospital Italiano de Buenos Aires

Buenos Aires, 1181, Argentina

Location

Hospital de Gastroenterologia Dr. Carlos Bonorino Udaondo

Buenos Aires, 1264, Argentina

Location

Centrol Integral de Gastroenterologia

Buenos Aires, 1425, Argentina

Location

Hospital Aleman

Buenos Aires, C1118AAT, Argentina

Location

Hospital Britanico De Buenos Aires

Buenos Aires, C1280AEB, Argentina

Location

AW Morrow Gastroenterology and Liver Centre, Royal Prince Alfred Hospital

Camperdown, New South Wales, 2050, Australia

Location

Department of Gastroenterology & Hepatology, Nepean Hospital

Kingswood, New South Wales, 2747, Australia

Location

Gallipoli Medical Research Foundation

Brisbane, Queensland, 4120, Australia

Location

Department of Gastroenterology and Hepatology, Royal Adelaide Hospital

Adelaide, South Australia, 5000, Australia

Location

Flinders Medical Centre

Adelaide, South Australia, 5042, Australia

Location

Box Hill Hospital

Box Hill, Victoria, 3128, Australia

Location

St. Vincent's Hospital Melbourne

Fitzroy, Victoria, 3065, Australia

Location

Austin Hospital

Heidelberg, Victoria, 3084, Australia

Location

Fiona Stanley Hospital, Gastroenterology Department

Murdoch, Western Australia, 6150, Australia

Location

AKH, Medical University of Vienna

Vienna, 1090, Austria

Location

University Hospital Antwerp

Edegem, Antwerp, 2650, Belgium

Location

Uz Leuven

Leuven, Vlaams-Brabant, 3000, Belgium

Location

Cub Hôpital Erasme

Brussels, 1070, Belgium

Location

University Hospital Ghent

Ghent, 9000, Belgium

Location

Gastrocentro/ Universidade Estadual de Campinas (UNICAMP)

São Paulo, Campinas, 13083-878, Brazil

Location

Instituto Hospital de Base do Distrito Federal-IHBDF

Brasília, Distrito Federal Brazil, 70335-900, Brazil

Location

Hospital Sao Rafael

São Salvador, Estado de Bahia, 41253-190, Brazil

Location

Instituto Goiano de Gastroenterologia

Goiânia, Goiás, 74535-170, Brazil

Location

Cepec Huufma

São Luís, Maranhão, 65020-600, Brazil

Location

Hospital das Clinicas da Universidade Federal de Minas Gerais (UFMG)

Belo Horizonte, Minas Gerais, 30130-100, Brazil

Location

Hospital de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

Location

Hospital Universitario Professor Edgard Santos

Bahia, Salvador, 40110-060, Brazil

Location

Gastrocentro. Unidad Estadual de CAmpinas UNICAMP

Campinas, São Paulo, 13083-878, Brazil

Location

Universidade Federal do Estado do Rio de Janeiro - Hospital Universitario Gaffree e Guinle/HUGG/UNIRIO

Rio de Janeiro, 20270-004, Brazil

Location

Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo-HCFMUSP

São Paulo, 05403-000, Brazil

Location

St. Ivan Rilsky University Hospital

Sofia, 1431, Bulgaria

Location

University of Calgary Liver Unit (Heritage Medical Research Clinic)

Calgary, Alberta, T2N-4Z6, Canada

Location

University of Alberta, Walter C. Mackenzie Health Sciences Centre (WMC)

Edmonton, Alberta, T6G 2X8, Canada

Location

University Of Manitoba, Health Sciences Centre

Winnipeg, Manitoba, R3E 3P6, Canada

Location

London Health Sciences Centre-University Hospital

London, Ontario, N6A 5A5, Canada

Location

University Health Network, Toronto General Hospital

Toronto, Ontario, M5G 2C4, Canada

Location

Chum

Montreal, Quebec, H2X 3J4, Canada

Location

Centro De Investigaciones Clínicas Viña Del Mar

Viña del Mar, Región de Valparaíso, 2540488, Chile

Location

Aarhus University Hospital Department of Hepatology and Gastroenterology

Aarhus, Aarhus C, 8000, Denmark

Location

Medicinsk klinik for mave, tarm-og leversygdomme

København Ø, 2100, Denmark

Location

Odense University Hospital Afdeling for medicinske mave-tarmsygdomme S

Odense, 5000, Denmark

Location

East Tallinn Central Hospital Gastroenterology Center

Tallinn, Harju, 10138, Estonia

Location

Tartu University Hospital

Tartu, 51014, Estonia

Location

Helsinki University Central Hospital

Helsinki, 00290, Finland

Location

Turku University Central Hospital, Gastroenterology Outpatient Clinic

Turku, 20521, Finland

Location

Hospital Saint-Antoine, A.P.-H.P.

Paris, Paris, 75571, France

Location

CHRU Hôpital HURIEZ

Lille, 59037, France

Location

Chu De Bordeaux - Hôpital Haut Lévêque

Pessac, 33604, France

Location

Klinikum der Johann-Wolfgang Goethe, Universitaet Frankfurt am Main

Frankfurt am Main, Hesse, 60590, Germany

Location

Medizinische Hochschule Hannover, Klinik für Gastroenterologie, Hepatologie und Endokrinologie

Hanover, Lower Saxony, D-30625, Germany

Location

Friedrich-Alexander-Uniersitat Erlangen

Erlangen, QLD, 91054, Germany

Location

CHARITÉ, Campus Virchow Klinikum

Berlin, D-13353, Germany

Location

Univeritatsklinikum Hamburg Eppendorf, Medizinische Klinik und Poliklinik

Hamburg, 20246, Germany

Location

Universitaetsklinikum Heidelberg Medizinische Universitaetsklinik

Heidelberg, 69120, Germany

Location

Universität Leipzig KöR, Medizinische Fakultät

Leipzig, 04103, Germany

Location

University of Munich, LMU Klinikum Grosshadern

Munich, 81377, Germany

Location

Queen Mary Hospital

Hong Kong, Pokfulam, Hong Kong

Location

Prince Of Wales Hospital

Hong Kong, Shatin, Hong Kong

Location

Tuen Mun Hospital

Hong Kong, Tuen Mun, New Territories, Hong Kong

Location

Alice Ho Miu Ling Nethersole Hospital

Hong Kong, Hong Kong

Location

Humanity & Health Research Centre

Hong Kong, Hong Kong

Location

Békés Megyei Kozponti Korhaz - Dr. Rethy Pal Tagkorhaz

Békéscsaba, H-5600, Hungary

Location

Szent János Hospital

Budapest, H-1125, Hungary

Location

University Of Debrecen, Department Of Medicine, Division Of Gastroenterology

Debrecen, 4032, Hungary

Location

Hadassah Hebrew University Medical Center

Jerusalem, Nazareth Elit, POB 12000, 91120, Israel

Location

Soroka Medical Center

Beersheba, 84104, Israel

Location

Rambam Health Care Campus

Haifa, 31096, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 91031 02, Israel

Location

Rabin Medical Center

Petah Tikva, 49100, Israel

Location

Sheba Medical Center

Ramat Gan, 52656 01, Israel

Location

Sourasky Tel-Aviv Medical Center

Tel Aviv, 64239, Israel

Location

Azienda Ospedaliero - Universitaria di Cagliari - Centro per lo Studio delle Malattie del Fegato

Monserrato, Cagliari, 09042, Italy

Location

Università Politecnica delle Marche - Azienda Ospedaliero

Ancona, 71-60126, Italy

Location

AOU Policlinico Sant' Orsola Malpighi

Bologna, 40138, Italy

Location

Azienda Ospedaliero Universitaria Sant´ Orsola Malpighi

Bologna, 40138, Italy

Location

Azienda Ospedaliero Universitaria Careggi Universita di Firenze

Florence, 50139, Italy

Location

Azienda Socio-Sanitarla Territoriale (ASST) Santi Paolo e Carlo

Milan, 20142, Italy

Location

AOU Ospedale Civile S. Agostino Estense - UO Medicina Metabolica

Modena, 41126, Italy

Location

Azienda Socio Sanitaria Territoriale (ASST) di Monza

Monza, 20900, Italy

Location

Azienda Ospedaliero - Universita di Padova

Padua, 35128, Italy

Location

AOU Policlinico Paolo Giaccone - Di.Bi.M.I.S

Palermo, 90127, Italy

Location

Policlinico Universitario Agostino Gemelli - Universita Cattolica del Sacro Cuore

Rome, 00168, Italy

Location

Hospital of Lithuanian University of Health Sciences, Kauno klinikos

Kaunas, LT 50009, Lithuania

Location

Vilnius University Hospital Santaros klinikos

Vilnius, LT-08661, Lithuania

Location

Departamento De Gastroenterologia. Instituto Nacional De Ciencias Medicas Y Nutricion Salvador Zubiran

Mexico City, Mexico City, 14000, Mexico

Location

Medica Sur, S.A.B. de C.V.

Mexico City, Mexico City, 14050, Mexico

Location

Consultorio Médico de la Dra Alma Laura Ladrón de Guevara Cetina

Mexico City, Mexico City, 6700, Mexico

Location

Radboud UMC

Nijmegen, Gelderland, 6525 GA, Netherlands

Location

Vrije Universiteit Medisch Centrum (VUMC)

Amsterdam, North Holland, 1081HV, Netherlands

Location

Erasmus Mc

Rotterdam, South Holland, 3015 CE, Netherlands

Location

Amsterdam University Medical Centre (AMC)

Amsterdam, 1105 AZ, Netherlands

Location

University Medical Center Utrecht

Utrecht, 3584CX, Netherlands

Location

NZ Liver Transplant Unit, Auckland Hospital

Grafton, Auckland, 1023, New Zealand

Location

Gastroenterology, Christchurch Hospital

Christchurch, Canterbury, 4710, New Zealand

Location

Nzoz Vitamed

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, 85-078, Poland

Location

Wojewodzki Szpital Specjalistyczny im. J. Gromkowskiego, Pierwszy Oddzial Chorob Zakaznych

Wroclaw, Lover Silesia, 51-149, Poland

Location

Centrum Onkologii - Instytut im. Marii Skłodowskiej - Curie, Klinika Gastroenterologii Onkologicznej

Warsaw, Masovian Voivodeship, 02-781, Poland

Location

Medical University of Warsaw Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie (SPCSK in Warsaw

Warsaw, Masovia, 02-097, Poland

Location

Oddział Gastr. I Hepat. Uniwersyteckie Centrum Kliniczne Im. Prof. K. Gibińskiego Sum

Katowice, Silesian Voivodeship, 40-752, Poland

Location

Dep. Of Gastroenterology UM Lublin

Lublin, 20-094, Poland

Location

Centro Hospitalar Lisboa Norte, EPE - Hospital de Santa Maria

Lisbon, 1649-035, Portugal

Location

Clinic For Gastroenterology And Hepatology Clinical Center Of Serbia

Belgrade, 11000, Serbia

Location

Clinical Hospital Centre Zvezdara

Belgrade, 11000, Serbia

Location

Inje University Busan Paik Hospital

Busan, Busanjin-gu, 47392, South Korea

Location

Gangnam Severance Hospital

Seoul, Gangnam-gu, 06273, South Korea

Location

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, 13620, South Korea

Location

Seoul National University Hospital

Seoul, Jongno-Gu, 03080, South Korea

Location

Pusan National University Hospital

Busan, Seo-gu, 49241, South Korea

Location

Hospital Universitario Marqués De Valdecilla

Santander, Cantabria, 39008, Spain

Location

Hospital Universitario Puerta De Hierro Majadahonda

Majadahonda, Madrid, 28222, Spain

Location

Hospital Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Virgen De La Victoria University Hospital

Málaga, 29010, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

La Fe, Hospital ( Valence )

Valencia, 46026, Spain

Location

Karolinska University Hospital

Stockholm, Huddinge, 14186, Sweden

Location

Sahlgrenska Universitetssjukhuset

Gothenburg, 413 45, Sweden

Location

Inselspital, University Of Bern, UVCM, DMLL

Bern, 3010, Switzerland

Location

Kantonsspital St. Gallen, Clinic for Gastroeterologie and Hepatologie

Sankt Gallen, 9007, Switzerland

Location

USZ, Klinik für Gastroenterologie und Hepatologie

Zurich, 8091, Switzerland

Location

Ankara University School of Medicine Gastroenterology Dept.

Ankara, 6100, Turkey (Türkiye)

Location

Ege University School of Medicine Gastroenterology Dept.

Izmir, 35100, Turkey (Türkiye)

Location

University Hospitals Bristol NHS Foundation Trust

Bristol, Avon, BS2 8HW, United Kingdom

Location

Plymouth Hospitals NHS Trust, Derriford Hospital

Plymouth, Devon, PL6 8DH, United Kingdom

Location

Gartnavel General Hospital

Glasgow, Lanarkshire, G12 0YN, United Kingdom

Location

Forth Valley Royal Hospital

Larbert, Scotland, FK5 4WR, United Kingdom

Location

Institute of Cellular Medicine

Newcastle upon Tyne, Tyne and Wear, NE2 4HH, United Kingdom

Location

University Hospitals Birmingham NHS Foundation Trust

Birmingham, West Midlands, B15 2GW, United Kingdom

Location

Cambrigde University Hospitals NHS Foundation Trust

Cambridge, CB2 0QQ, United Kingdom

Location

The Royal Free Hospital

London, NW3 2QG, United Kingdom

Location

Nottingham University Hospital Nhs Trust

Nottingham, NG7 2UH, United Kingdom

Location

Related Publications (3)

  • Lindor KD, Gershwin ME, Poupon R, Kaplan M, Bergasa NV, Heathcote EJ; American Association for Study of Liver Diseases. Primary biliary cirrhosis. Hepatology. 2009 Jul;50(1):291-308. doi: 10.1002/hep.22906. No abstract available.

    PMID: 19554543BACKGROUND
  • European Association for the Study of the Liver. EASL Clinical Practice Guidelines: management of cholestatic liver diseases. J Hepatol. 2009 Aug;51(2):237-67. doi: 10.1016/j.jhep.2009.04.009. Epub 2009 Jun 6. No abstract available.

    PMID: 19501929BACKGROUND
  • Kowdley KV, Hirschfield GM, Coombs C, Malecha ES, Bessonova L, Li J, Rathnayaka N, Mells G, Jones DE, Trivedi PJ, Hansen BE, Smith R, Wason J, Hiu S, Kareithi DN, Mason AL, Bowlus CL, Muller K, Carbone M, Berenguer M, Milkiewicz P, Adekunle F, Villamil A. COBALT: A Confirmatory Trial of Obeticholic Acid in Primary Biliary Cholangitis With Placebo and External Controls. Am J Gastroenterol. 2025 Feb 1;120(2):390-400. doi: 10.14309/ajg.0000000000003029. Epub 2024 Aug 14.

MeSH Terms

Conditions

Liver Cirrhosis, BiliaryFibrosis

Interventions

obeticholic acid

Condition Hierarchy (Ancestors)

Cholestasis, IntrahepaticCholestasisBile Duct DiseasesBiliary Tract DiseasesDigestive System DiseasesLiver DiseasesLiver CirrhosisPathologic ProcessesPathological Conditions, Signs and Symptoms

Limitations and Caveats

The estimated effect of treatment from the ITT population was underpowered and potentially biased, resulting in difficulties in the interpretation of the tests of hypotheses for the primary and key secondary endpoints.

Results Point of Contact

Title
Medical Information
Organization
Intercept Pharmaceuticals, Inc.

Study Officials

  • Erik Ness, MD

    Intercept Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 10, 2014

First Posted

December 4, 2014

Study Start

December 26, 2014

Primary Completion

December 23, 2021

Study Completion

December 23, 2021

Last Updated

March 9, 2023

Results First Posted

March 9, 2023

Record last verified: 2023-02

Locations