NCT02247557

Brief Summary

To evaluate the efficacy and safety of intravesical instillation of Lipotoxin for the treatment of IC/BPS

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
90

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Sep 2014

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2014

Completed
14 days until next milestone

First Submitted

Initial submission to the registry

September 15, 2014

Completed
10 days until next milestone

First Posted

Study publicly available on registry

September 25, 2014

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2017

Completed
Last Updated

March 9, 2017

Status Verified

March 1, 2017

Enrollment Period

2.4 years

First QC Date

September 15, 2014

Last Update Submit

March 7, 2017

Conditions

Keywords

IC/PBSVASBotulinum Toxin ALipotoxin

Outcome Measures

Primary Outcomes (1)

  • Change of the O'Leary-Sant symptom score

    Change of the O'Leary-Sant symptom score from baseline to 1 month after the treatment day

    Baseline and 1 month

Secondary Outcomes (10)

  • Net changes of the Visual Analog Scale (VAS)

    Baseline and 1 month

  • Net changes of the functional bladder capacity (FBC)

    Baseline and 1 month

  • Net changes of the voiding frequency at daytime as recorded in 3-day voiding diary

    Baseline and 1 month

  • Net changes of the voiding frequency at night time as recorded in 3-day voiding diary

    Baseline and 1 month

  • Net Change of the Global response assessment (GRA)

    Baseline and 1 month

  • +5 more secondary outcomes

Study Arms (3)

Group A: Liposome encapsulated BoNT-A

EXPERIMENTAL

Liposome encapsulated BoNT-A ( mixed BOTOX 200U/10ml in Liposome 80mg/40ml) in single intravesical instillation

Drug: Liposome encapsulated BoNT-A

Group B: BoNT-A 200 U in Normal saline

EXPERIMENTAL

BOTOX 200U in normal saline (BoNT-A/NS) 50ml in single intravesical instillation

Drug: BOTOX 200U in normal saline

Group C: Normal saline

PLACEBO COMPARATOR

Normal saline (N/S) 50ml in single intravesical instillation

Drug: Normal saline

Interventions

Liposome encapsulated BoNT-A ( mixed BOTOX 200U/10ml in Liposome 80mg/40ml) in single intravesical instillation

Also known as: Liposome, onabotulinumtoxinA 200U
Group A: Liposome encapsulated BoNT-A

BOTOX 200U in normal saline (BoNT-A/NS) 50ml in single intravesical instillation

Also known as: onabotulinumtoxinA 200U
Group B: BoNT-A 200 U in Normal saline

Normal saline (N/S) 50ml in single intravesical instillation

Also known as: Saline
Group C: Normal saline

Eligibility Criteria

Age20 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Adults with age of 20 years old or above
  • Patients with symptoms of frequency, urgency, nocturia, and/or bladder pain.
  • Proven to have glomerulations (at least grade 2) by cystoscopic hydrodistention under anesthesia in recent 1 year
  • Free of active urinary tract infection
  • Free of bladder outlet obstruction on enrollment
  • Free of overt neurogenic bladder dysfunction and limitation of ambulation
  • Patient or his/her legally acceptable representative has signed the written informed consent form

You may not qualify if:

  • Hunner's lesion proven by cystoscopy
  • Patients with severe cardiopulmonary disease and such as congestive heart failure, arrhythmia, poorly controlled hypertension, not able to receive regular follow-up
  • Patients with bladder outlet obstruction on enrollment
  • Patients with postvoid residual \>250ml
  • Patients with uncontrolled confirmed diagnosis of acute urinary tract infection
  • Patients have laboratory abnormalities at screening including: ALT\> 3 x upper limit of normal range, AST\> 3 x upper limit of normal range; Patients have abnormal serum creatinine level \> 2 x upper limit of normal range
  • Patients with any contraindication to be urethral catheterization during treatment
  • Female patients who is pregnant, lactating, or with child-bearing potential without contraception.
  • Myasthenia gravis, Eaton Lambert syndrome.
  • Patients with any other serious disease considered by the investigator not in the condition to enter the trial
  • Patient had received intravesical treatment for IC within recent 1 month
  • Patients participated investigational drug trial within 1 month before entering this study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Buddhist Tzu Chi General Hospital

Hualien City, 970, Taiwan

Location

Related Publications (1)

  • Imamura M, Scott NW, Wallace SA, Ogah JA, Ford AA, Dubos YA, Brazzelli M. Interventions for treating people with symptoms of bladder pain syndrome: a network meta-analysis. Cochrane Database Syst Rev. 2020 Jul 30;7(7):CD013325. doi: 10.1002/14651858.CD013325.pub2.

MeSH Terms

Conditions

Cystitis, Interstitial

Interventions

LiposomesBotulinum Toxins, Type ASaline SolutionSodium Chloride

Condition Hierarchy (Ancestors)

CystitisUrinary Bladder DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Membranes, ArtificialBiomedical and Dental MaterialsDrug CarriersDosage FormsPharmaceutical PreparationsManufactured MaterialsTechnology, Industry, and AgricultureBiomimetic MaterialsBotulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological FactorsCrystalloid SolutionsIsotonic SolutionsSolutionsChloridesHydrochloric AcidChlorine CompoundsInorganic ChemicalsSodium Compounds

Study Officials

  • Hann-Chorng Kuo, M.D.

    Department of Urology, Buddihisst Tzu Chi General Hospital and Tzu Chi University

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Masking Details
All participants, investigators and care providers do not know which regimen is given to patients of the three arms.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: This is a double-blind, randomized, placebo-controlled physician initiated study enrolled patients with refractory IC/BPS. Patients were assigned to intravesical instillation of lipotoxin (onabotulinumtoxinA 200 U with 80mg sphingomyelin), onabotulinumtoxinA 200 U in normal saline, or normal saline.
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Director of Urology

Study Record Dates

First Submitted

September 15, 2014

First Posted

September 25, 2014

Study Start

September 1, 2014

Primary Completion

February 1, 2017

Study Completion

February 1, 2017

Last Updated

March 9, 2017

Record last verified: 2017-03

Data Sharing

IPD Sharing
Will not share

IPD cannot be released unless researchers obtain the approval from the Ethics Committee of the Buddhist Tzu Chi General Hospital, Hualien, Taiwan

Locations