NCT02246881

Brief Summary

The main objective of the study is to compare the pharmacokinetics of Optivate® with the subject's current FVIII concentrate when given as a bolus dose of 50IU/kg. The secondary objective is to compare the first and second pharmacokinetic assessments on Optivate® (and recovery if a subject changes batch) to evaluate Optivate® in terms of clinical tolerance and safety.

Trial Health

85
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Geographic Reach
2 countries

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2001

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2004

Completed
10.7 years until next milestone

First Submitted

Initial submission to the registry

September 2, 2014

Completed
21 days until next milestone

First Posted

Study publicly available on registry

September 23, 2014

Completed
Last Updated

February 15, 2018

Status Verified

February 1, 2018

Enrollment Period

2.3 years

First QC Date

September 2, 2014

Last Update Submit

February 14, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • PK parameters for FVIII:C

    Pre-dose, 15, 30 min, 1, 3, 6, 9, 24, 28, 32, 48 hours post-dose

Study Arms (2)

Current Factor VIII

ACTIVE COMPARATOR

Optivate® (Human Coagulation Factor VIII)

Biological: Optivate® (Human Coagulation Factor VIII)

Optivate®

EXPERIMENTAL

Optivate® (Human Coagulation Factor VIII)

Biological: Optivate® (Human Coagulation Factor VIII)

Interventions

Current Factor VIIIOptivate®

Eligibility Criteria

Age12 Years+
Sexall
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Previously treated subjects with severe Haemophilia A (\<2% basal FVIII activity) without inhibitor to Factor VIII, at least 12 years of age, currently receiving FVIII concentrate and with more than 20 exposure days.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Klinika Haematologii, Akademia Medyczna w Gdansku, ul.

Debinki 7, 80-211 Gdansk, Poland

Location

Klinika Haematologii, Akademia Medyczna w Lublinie, ul.

Dr K Jaczewskiego 8, 20-090, Lublin, Poland

Location

Klinika Haematologii, Akademia Medyczna w Lodzi, ul.

Pabianicka 62, 93-513 Lodz, Poland

Location

Haemophilia Centre, Addenbrooke's Hospital

Hills Road, Cambridge, Cambridgeshire, CB2 2QQ, United Kingdom

Location

Haemophilia Centre, University Hospital, Queens Medical Centre

Clifton Boulevard, Nottingham, N67 2UH, United Kingdom

Location

Sheffield Haemophilia & Thrombosis Centre, Royal Hallamshire Hospital

Glossop Road, Sheffield, S10 2JF, United Kingdom

Location

Haemophilia Centre, University Dept. of Haemophilia, Manchester Royal Infirmary

Manchester, M13 9WL, United Kingdom

Location

Haemophilia Centre, Southampton General Hospital

Tremona Road, Southampton, SO16 6YD, United Kingdom

Location

Related Links

MeSH Terms

Conditions

von Willebrand Diseases

Interventions

optivateFactor VIII

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersBlood Platelet DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Blood Coagulation FactorsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsProtein PrecursorsBiological Factors

Study Design

Study Type
interventional
Phase
phase 3
Purpose
TREATMENT
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 2, 2014

First Posted

September 23, 2014

Study Start

October 1, 2001

Primary Completion

January 1, 2004

Last Updated

February 15, 2018

Record last verified: 2018-02

Locations