NCT02224677

Brief Summary

This study is a multi-center, longitudinal cohort study of 125 infants with craniofacial microsomia (CFM) and 100 infants without craniofacial anomalies. Participants will undergo a series of evaluations between 0-3 years of age to comprehensively evaluate the developmental status of infants and toddlers with CFM. This research design will also explore specific pathways by which CFM may lead to certain outcomes. Specifically, the study explores (1) the longitudinal relations between facial asymmetry and emotion-related facial movements and socialization; and (2) associations among ear malformations, hearing and speech deficits and cognitive outcomes. Results of this research will ultimately lead to future investigations that assess new interventions and corresponding changes in current standards of care for children with CFM.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
417

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Nov 2013

Longer than P75 for all trials

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2013

Completed
10 months until next milestone

First Submitted

Initial submission to the registry

August 19, 2014

Completed
6 days until next milestone

First Posted

Study publicly available on registry

August 25, 2014

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 31, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 31, 2019

Completed
Last Updated

April 19, 2024

Status Verified

April 1, 2024

Enrollment Period

5.8 years

First QC Date

August 19, 2014

Last Update Submit

April 18, 2024

Conditions

Keywords

CFMfacial asymmetryskin tagfacial tagmissing earsmall earanotiamicrotiaepibulbar dermoidcolobomamacrostomialateral cleftinfanttoddlerbabyneurodevelopmentcognitionsocialization

Outcome Measures

Primary Outcomes (37)

  • Neurodevelopmental Outcome Measures

    BSID-III Cognitive Index

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    2D photographs and video

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    Medical and Surgical History

    T2 study visit (~24 months)

  • Neurodevelopmental Outcome Measures

    BSID-III Cognitive Index

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    BSID-III Fine \& Gross Motor

    T1 study visit (12-14 months of age)

  • Neurodevelopmental Outcome Measures

    PLS-V Auditory Comprehension

    T1 study visit (12-14 months of age)

  • Neurodevelopmental Outcome Measures

    PLS-V Expressive Language

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments Phenotypic Assessments Phenotypic Assessments

    3D photographs,

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    Medical and Surgical History

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    Medical/dental chart abstraction

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    IT-MAIS: Auditory Assessment

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    OMENS rating from 2D images

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    Baby FACS observational protocol

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    Clinical Hearing Test

    T1 study visit (12-14 months of age)

  • Phenotypic Assessments

    IT-MAIS: Auditory Assessment

    T2 study visit (~24 months)

  • Neurodevelopmental Outcome Measures

    BSID-III Fine \& Gross Motor

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Leiter-R Brief IQ

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Leiter-R Forward Memory

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Leiter-R Sustained Attention

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Leiter-R Associated Pairs

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Leiter-R Matching

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Leiter-R Picture Context

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    PLS-V Auditory Comprehension

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    PLS-V Expressive Language

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    NEPSY-II Phonological Processing

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    ITSEA Parent

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    ITSEA Teacher

    T3 study visit (~36 months)

  • Neurodevelopmental Outcome Measures

    Goldman-Fristoe Test of Articulation (GFTA-2)

    T3 study visit (~36 months)

  • Phenotypic Assessments

    2D photographs and video

    T3 study visit (~36 months)

  • Phenotypic Assessments

    3D photographs

    T3 study visit (~36 months)

  • Phenotypic Assessments

    Medical and Surgical History

    T3 study visit (~36 months)

  • Phenotypic Assessments

    Medical/dental chart abstraction

    T3 study visit (~36 months)

  • Phenotypic Assessments

    IT-MAIS: Auditory Assessment

    T3 study visit (~36 months)

  • Phenotypic Assessments

    OMENS rating from 2D images

    T3 study visit (~36 months)

  • Phenotypic Assessments

    Hearing Evaluation

    T3 study visit (~36 months)

  • Phenotypic Assessments

    Interview on willingness for future study

    T3 study visit (~36 months)

  • Phenotypic Assessments

    DNA collection (DNA)

    T3 study visit (~36 months)

Study Arms (5)

Children with Craniofacial Microsomia

125 children with craniofacial microsomia will be asked to come in for two study visits - when they are about 12 months old and again when they are about 36 months old. Procedures for children at the first visit include: assessment of development, video, photographs, and a hearing evaluation. Procedures for the final study visit include: assessment of development, photographs (2D \& 3D), video, saliva sample, hearing evaluation, speech assessment.

Children without Craniofacial Microsomia

Please note: we are not recruiting this group through ClinicalTrials.gov 100 children without craniofacial microsomia will be asked to come in for two study visits - when they are about 12 months old and again when they are about 36 months old. Procedures for the first visit include: assessment of development, video, and photographs. Procedures for the final study visit include: assessment of development, photographs (2D \& 3D), video, and speech assessment.

Parents of Children with Craniofacial Microsomia

125-250 parents of children with craniofacial microsomia will be asked to complete three visits - when their child is about 12 months old, 24 months old, and 36 months old. Parents will be asked to complete an interview at the first visit. The second visit consists of a telephone interview where parents will be asked about their child's hearing and health history. At the final study visit, parents will be asked to complete more questionnaires, have their picture taken, and donate saliva.

Parents of Children without Craniofacial Microsomia

Please note: we are not recruiting this group through ClinicalTrials.gov 100 parents of children without craniofacial microsomia will be asked to complete three visits - when their child is about 12 months old, 24 months old, and 36 months old. Parents will be asked to complete an interview at the first visit. The second visit consists of a telephone interview where parents will be asked about their child's hearing and health history. At the final study visit, parents will be asked to complete questionnaires and an interview.

Teacher/Day Care Provider

When the children participants are around 36 months old, we will ask parents for permission to contact their child's teacher/day care provider. We would like the teacher/day care provider to fill out a questionnaire.

Eligibility Criteria

Age12 Months - 24 Months
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

Children with and without craniofacial microsomia will be drawn from outpatient clinics, medical centers, and local pediatric practices near performance sites and local pediatric practices. Cases will be approached in their first 24 months by either a member of their craniofacial team, a member of the CLOCK study team, or one of their treating providers. Cases may find out about the study through ClinicalTrials.gov. Controls will initially be approached through a treating provider, a member of the CLOCK team, or through an announcement about the study.

You may qualify if:

  • Children with Craniofacial Microsomia:
  • Male or female infant participant is between 12 months and 24 months of age, or corrected age (for some infants born prior to their due date).
  • Infant participant has diagnosis of at least one of the following conditions:
  • Microtia
  • Anotia
  • Facial asymmetry AND Preauricular tag(s)
  • Facial asymmetry AND Facial tag(s)
  • Facial asymmetry AND Epibulbar dermoid
  • Facial asymmetry AND Macrostomia (i.e., lateral cleft)
  • Preauricular tag AND Epibulbar dermoid
  • Preauricular tag AND Macrostomia
  • Facial tag AND Epibulbar dermoid
  • Macrostomia AND Epibulbar dermoid
  • Infant participant has been diagnosed by a regional craniofacial team.
  • Legal guardian will provide written parental permission and informed consent prior to participation in study.
  • +5 more criteria

You may not qualify if:

  • Children with Craniofacial Microsomia:
  • Subject is diagnosed with a known syndrome that involves microtia and/or underdevelopment of the jaw (Townes-Brocks, Treacher Collins, branchiootorenal, Nager, or Miller syndromes).
  • Subject has abnormal chromosome studies (karyotype)
  • Subject has a major medical or neurological condition that prevents participation in the study (e.g., cancer, cerebral palsy) at time of recruitment
  • Subject was born before 34 weeks estimated gestational age
  • Anything that would place the subject at increased risk or preclude the subject's full compliance with or completion of the study.
  • Sibling already participating in the CLOCK study
  • Subject's consenting parent does not speak English or Spanish
  • Parents of Children with Craniofacial Microsomia
  • Anything that would preclude the subject's full compliance with or completion of the study.
  • Subject does not speak English or Spanish

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Children's Hospital Los Angeles

Los Angeles, California, 90027, United States

Location

University of Illinois at Chicago

Chicago, Illinois, 60607, United States

Location

University of North Carolina

Chapel Hill, North Carolina, 27599, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 90027, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98101, United States

Location

Biospecimen

Retention: SAMPLES WITH DNA

Saliva

MeSH Terms

Conditions

Goldenhar SyndromeCongenital MicrotiaFacial AsymmetryColobomaMacrostomia

Condition Hierarchy (Ancestors)

Mandibulofacial DysostosisCraniofacial DysostosisDysostosesBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesCraniofacial AbnormalitiesMusculoskeletal AbnormalitiesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesEar DiseasesOtorhinolaryngologic DiseasesPathological Conditions, AnatomicalPathological Conditions, Signs and SymptomsEye AbnormalitiesEye DiseasesEye Diseases, HereditaryMouth AbnormalitiesMouth DiseasesStomatognathic DiseasesStomatognathic System Abnormalities

Study Officials

  • Carrie L Heike, MD, MS

    Seattle Children's Hospital

    PRINCIPAL INVESTIGATOR
  • Matthew L Speltz, PhD

    Seattle Children's Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

August 19, 2014

First Posted

August 25, 2014

Study Start

November 1, 2013

Primary Completion

August 31, 2019

Study Completion

August 31, 2019

Last Updated

April 19, 2024

Record last verified: 2024-04

Locations