NCT02165085

Brief Summary

The purpose of this study is to determine whether patients with vascular Ehlers-Danlos syndrome present significant and specific changes of arterial endothelial and smooth muscular cell signalling/secretion, in comparison to matched healthy volunteers and patients with spontaneous arterial dissections.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
211

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jun 2013

Typical duration for all trials

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2013

Completed
11 months until next milestone

First Submitted

Initial submission to the registry

May 7, 2014

Completed
1 month until next milestone

First Posted

Study publicly available on registry

June 17, 2014

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2015

Completed
Last Updated

March 17, 2016

Status Verified

March 1, 2016

Enrollment Period

2.1 years

First QC Date

May 7, 2014

Last Update Submit

March 16, 2016

Conditions

Keywords

BiomarkersEhlers-Danlos syndrome, vascular typePathophysiology

Outcome Measures

Primary Outcomes (1)

  • Diagnostic value of plasma biomarkers SEDv

    Analysis of the diagnostic value of different levels of plasma concentrations of microRNAs

    At the end of study (2 years after period of inclusion for first patient)

Secondary Outcomes (1)

  • Reference value of biomarkers

    At the end of study (2 years after period of inclusion for first patient)

Study Arms (3)

Vascular-Ehlers Danlos syndrome

N=50 patients with vascular Ehlers-Danlos syndrome

Spontaneous arterial dissection(s)

N=50 patients

Healthy volunteers

n=100 Healthy volunteers

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Patients with vascular Ehlers-Danlos syndrome and patients with spontaneous dissection(s) will be recruited from the French National Referral Centre for Rare arterial diseases, Hopital Europeen Georges Pompidou, Paris, France. Healthy volunteers will be recruited by the clinical investigations center, Hopital Europeen Georges Pompidou, Paris, France (random community sample).

You may qualify if:

  • Patients with vascular Ehlers-Danlos syndrome must have been positively tested for a pathogenic mutation within the COL3A1 gene.
  • In patients with arterial dissection(s) any associated systemic arterial disease must have been ruled out, especially vascular Ehers-Danlos syndrome

You may not qualify if:

  • All subjects must not present any chronic systemic disease, any acute disease within seven days prior to enrollment, diabetes mellitus and arterial hypertension.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Hopital europeen Georges Pompidou

Paris, 75015, France

Location

Related Publications (1)

  • Morissette R, Schoenhoff F, Xu Z, Shilane DA, Griswold BF, Chen W, Yang J, Zhu J, Fert-Bober J, Sloper L, Lehman J, Commins N, Van Eyk JE, McDonnell NB. Transforming growth factor-beta and inflammation in vascular (type IV) Ehlers-Danlos syndrome. Circ Cardiovasc Genet. 2014 Feb;7(1):80-8. doi: 10.1161/CIRCGENETICS.113.000280. Epub 2014 Jan 6.

    PMID: 24399159BACKGROUND

Related Links

Biospecimen

Retention: SAMPLES WITHOUT DNA

Serum, Plasma

MeSH Terms

Conditions

Ehlers-Danlos Syndrome, Type IV

Condition Hierarchy (Ancestors)

Aortic DissectionDissection, Blood VesselAneurysmVascular DiseasesCardiovascular DiseasesEhlers-Danlos SyndromeHemostatic DisordersHemorrhagic DisordersHematologic DiseasesHemic and Lymphatic DiseasesSkin AbnormalitiesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSkin Diseases, GeneticGenetic Diseases, InbornCollagen DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesSkin Diseases

Study Officials

  • Michael Frank, MD

    Centre de Reference des Maladies Vasculaires Rares, Hopital Europeen Georges Pompidou, APHP, Paris France

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 7, 2014

First Posted

June 17, 2014

Study Start

June 1, 2013

Primary Completion

July 1, 2015

Study Completion

July 1, 2015

Last Updated

March 17, 2016

Record last verified: 2016-03

Locations