NCT02161757

Brief Summary

A 52-Week, Multicentre, Randomized, Double-Blind, Parallel Group, Placebo Controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Tralokinumab in Adults and Adolescents with Asthma Inadequately Controlled on Inhaled Corticosteroid Plus Long-Acting β2-Agonist

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,207

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jun 2014

Typical duration for phase_3

Geographic Reach
15 countries

243 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 5, 2014

Completed
7 days until next milestone

First Posted

Study publicly available on registry

June 12, 2014

Completed
1 day until next milestone

Study Start

First participant enrolled

June 13, 2014

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 28, 2017

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 18, 2017

Completed
9 months until next milestone

Results Posted

Study results publicly available

April 17, 2018

Completed
Last Updated

August 28, 2018

Status Verified

July 1, 2018

Enrollment Period

2.7 years

First QC Date

June 5, 2014

Results QC Date

December 21, 2017

Last Update Submit

July 30, 2018

Conditions

Keywords

AsthmaReactive AirwaysRespiratory Tract DiseaseObstructive Lung DiseaseLung Diseases

Outcome Measures

Primary Outcomes (1)

  • Annualised Asthma Exacerbation Rate (AAER) up to Week 52

    Asthma exacerbation was defined as a worsening of asthma that led to any of the following: * Use of systemic corticosteroids for at least 3 days; a single depo-injectable dose of corticosteroids was considered equivalent to a 3-day course of systemic corticosteroids. * An emergency room (ER) or urgent care (UC) visit (defined as evaluation and treatment for \<24 hours in an ER or UC centre) due to asthma that required systemic corticosteroids (see above). * An inpatient hospitalisation (defined as admission to an inpatient facility and/or evaluation and treatment in a healthcare facility for ≥24 hours) due to asthma. AAER = number of exacerbations\*365.25 / (follow-up date - date of randomisation + 1) (where maximum follow-up time for a patient was approximately 52 weeks). AAER in the tralokinumab group was compared to that seen in the placebo group up to Week 52 using a negative binomial model; rate ratios and rate reductions are both presented for comparative statistical analyses.

    Baseline (Week 0) up to Week 52

Secondary Outcomes (17)

  • Percent Change From Baseline to Week 52 in Pre-dose/Pre-bronchodilator (BD) Forced Expiratory Volume in 1 Second (FEV1)

    Baseline (Week 0) and Week 52

  • Change From Baseline to Week 52 in Total Asthma Symptom Score (Bi-weekly Means)

    Baseline (Week 0) and Week 52

  • Change From Baseline to Week 52 in Asthma Quality of Life Questionnaire for 12 Years and Older (AQLQ(S)+12) Total Score

    Baseline (Week 0) and Week 52

  • Change From Baseline to Week 52 in Asthma Control Questionnaire-6 (ACQ-6) Score

    Baseline (Week 0) and Week 52

  • AAER Associated With an ER/UC Visit, or a Hospitalisation up to Week 52

    Baseline (Week 0) up to Week 52

  • +12 more secondary outcomes

Study Arms (4)

Tralokinumab Dose Regimen 1

EXPERIMENTAL

Tralokinumab subcutaneous injection

Biological: Tralokinumab

Placebo Dose Regimen 1

PLACEBO COMPARATOR

Placebo subcutaneous injection

Other: Placebo

Tralokinumab Dose Regimen 2

EXPERIMENTAL

Tralokinumab subcutaneous injection

Biological: Tralokinumab

Placebo Dose Regimen 2

PLACEBO COMPARATOR

Placebo subcutaneous injection

Other: Placebo

Interventions

TralokinumabBIOLOGICAL

Subcutaneous injection

Tralokinumab Dose Regimen 1Tralokinumab Dose Regimen 2
PlaceboOTHER

Subcutaneous injection

Placebo Dose Regimen 1Placebo Dose Regimen 2

Eligibility Criteria

Age12 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Age 12 -75
  • Documented physician-diagnosed asthma.
  • Documented treatment with ICS at a total daily dose corresponding to ≥500μg fluticasone propionate dry powder formulation equivalents) and a LABA
  • Morning pre-BD FEV1 value of ≥40 and \<80% value (\<90% for patients 12 to 17 years of age) of their PNV.
  • Post-BD reversibility of ≥12% and ≥200 mL in FEV1
  • ACQ-6 score ≥1.5

You may not qualify if:

  • Pulmonary disease other than asthma
  • History of anaphylaxis following any biologic therapy
  • Hepatitis B, C or HIV
  • Pregnant or breastfeeding
  • History of cancer
  • Current tobacco smoking or a history of tobacco smoking for ≥ 10 pack-years
  • Previous receipt of tralokinumab

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (243)

Research Site

Birmingham, Alabama, 35209, United States

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Phoenix, Arizona, 85018, United States

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Arcadia, California, 91007, United States

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Los Angeles, California, 90036, United States

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Los Angeles, California, 90048, United States

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Newport Beach, California, 92663, United States

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Poway, California, 92064, United States

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San Jose, California, 95117, United States

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Tustin, California, 92780, United States

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Wildomar, California, 92595, United States

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Colorado Springs, Colorado, 80907, United States

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Denver, Colorado, 80206, United States

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Denver, Colorado, 80246, United States

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New Haven, Connecticut, 06519, United States

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Clearwater, Florida, 33765, United States

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Coral Gables, Florida, 33134, United States

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Cutler Bay, Florida, 33189, United States

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Fort Lauderdale, Florida, 33308, United States

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Hialeah, Florida, 33012, United States

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Hialeah, Florida, 33013, United States

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Homestead, Florida, 33030, United States

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Homestead, Florida, 33130, United States

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Jacksonville, Florida, 32277, United States

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Kissimmee, Florida, 34741, United States

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Miami, Florida, 33125, United States

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Miami, Florida, 33126, United States

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Miami, Florida, 33134, United States

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Miami, Florida, 33135, United States

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Miami, Florida, 33144, United States

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Miami, Florida, 33145, United States

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Miami, Florida, 33155, United States

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Miami, Florida, 33166, United States

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Miami, Florida, 33173, United States

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Miami, Florida, 33174, United States

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Miami, Florida, 33175, United States

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Miami, Florida, 33176, United States

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Ormond Beach, Florida, 32174, United States

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Pembroke Pines, Florida, 33029, United States

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Winter Park, Florida, 32789, United States

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Albany, Georgia, 31707, United States

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Atlanta, Georgia, 30331, United States

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Lawrenceville, Georgia, 30046, United States

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Meridian, Idaho, 83642, United States

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Twin Falls, Idaho, 83301, United States

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Fort Wayne, Indiana, 46804, United States

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South Bend, Indiana, 46617, United States

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Bowling Green, Kentucky, 42101, United States

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Bangor, Maine, 04401, United States

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Brockton, Massachusetts, 2301, United States

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Ann Arbor, Michigan, 48106, United States

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Farmington Hills, Michigan, 48334, United States

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Flint, Michigan, 48504, United States

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Ypsilanti, Michigan, 48197, United States

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Chesterfield, Missouri, 63017, United States

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St Louis, Missouri, 63141, United States

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St Louis, Missouri, 63143, United States

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Missoula, Montana, 59808, United States

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Las Vegas, Nevada, 89123, United States

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Union, New Jersey, 07083, United States

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Brooklyn, New York, 11229, United States

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Asheville, North Carolina, 28801, United States

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Charlotte, North Carolina, 28277, United States

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Cornelius, North Carolina, 28031, United States

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Hickory, North Carolina, 28078, United States

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Shelby, North Carolina, 28150, United States

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Winston-Salem, North Carolina, 27104, United States

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Columbus, Ohio, 43235, United States

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Middleburg Heights, Ohio, 44130, United States

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Toledo, Ohio, 43617, United States

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Oklahoma City, Oklahoma, 73112, United States

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Oklahoma City, Oklahoma, 73131, United States

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Monroeville, Pennsylvania, 15146, United States

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Philadelphia, Pennsylvania, 19115, United States

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Scottdale, Pennsylvania, 15683, United States

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Uniontown, Pennsylvania, 15683, United States

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Johnston, Rhode Island, 02919, United States

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Providence, Rhode Island, 02908, United States

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Warwick, Rhode Island, 02886, United States

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Anderson, South Carolina, 29621, United States

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Greenville, South Carolina, 29607, United States

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Myrtle Beach, South Carolina, 29588, United States

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Spartanburg, South Carolina, 29303, United States

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Boerne, Texas, 78006, United States

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Corsicana, Texas, 75110, United States

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Dallas, Texas, 75225, United States

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Fort Worth, Texas, 76104, United States

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Fort Worth, Texas, 76109, United States

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Houston, Texas, 77043, United States

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Houston, Texas, 77084, United States

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Houston, Texas, 77099, United States

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Lampasas, Texas, 76550, United States

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McKinney, Texas, 75069, United States

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Plano, Texas, 75093, United States

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San Antonio, Texas, 78218, United States

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San Antonio, Texas, 78258, United States

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Murray, Utah, 84107, United States

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Provo, Utah, 84604, United States

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Salt Lake City, Utah, 84102, United States

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South Burlington, Vermont, 05403, United States

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Arlington, Virginia, 22203, United States

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Richmond, Virginia, 23225, United States

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Richland, Washington, 99352, United States

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Tacoma, Washington, 98405, United States

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Buenos Aires, C1414AIF, Argentina

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CABA, C1425BEN, Argentina

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Cap. Fed, 1280, Argentina

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Ciudad Autonomade Buenos Aires, 1426, Argentina

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Concepción del Uruguay, 3260, Argentina

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Córdoba, X5003DCE, Argentina

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Mendoza, 5500, Argentina

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Mendoza, M5500GIP, Argentina

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Quilmes, B1878FNR, Argentina

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Rosario, S2000DEJ, Argentina

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San Miguel de Tucumán, 4000, Argentina

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Brussels (Anderlecht), 1070, Belgium

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Erpent, 5101, Belgium

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Dupnitsa, 2600, Bulgaria

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Kozloduy, 3320, Bulgaria

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Pazardzhik, 4400, Bulgaria

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Pernik, 2307, Bulgaria

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Rousse, 7002, Bulgaria

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Sliven, 8800, Bulgaria

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Sofia, 1202, Bulgaria

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Sofia, 1407, Bulgaria

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Sofia, 1618, Bulgaria

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Stara Zagora, 6000, Bulgaria

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Varna, 9000, Bulgaria

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Veliko Tarnovo, 5000, Bulgaria

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Vratsa, 3000, Bulgaria

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Yambol, 8600, Bulgaria

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Armenia, 630004, Colombia

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Bogotá, 110311, Colombia

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Bogotá, Colombia

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Cali, 76001000, Colombia

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Aschaffenburg, 63739, Germany

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Augsburg, 86150, Germany

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Bad Lippspringe, 33175, Germany

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Geesthacht, 21502, Germany

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Herford, 32049, Germany

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Landsberg, 86899, Germany

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Leipzig, 04357, Germany

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München-Pasing, 81241, Germany

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Reinfeld, 23858, Germany

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Rodgau-Dudenhofen, 63110, Germany

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Warendorf, 48231, Germany

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Balassagyarmat, 2660, Hungary

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Edelény, 3780, Hungary

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Farkasgyepü, 8582, Hungary

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Komárom, 2900, Hungary

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Létavértes, 4281, Hungary

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Miskolc, 3529, Hungary

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Pécs, 7626, Hungary

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Pécs, 7635, Hungary

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Százhalombatta, 2440, Hungary

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Cusco, CUSCO 01, Peru

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Lima, 41, Peru

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Lima, L27, Peru

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Lima, LIMA 1, Peru

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Lima, LIMA 21, Peru

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Lima, LIMA 29, Peru

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Lima, LIMA 32, Peru

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Lima, LIMA 33, Peru

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Lima, LIMA 41, Peru

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Będzin, 42-500, Poland

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Bydgoszcz, 85-079, Poland

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Chorzów, 41-500, Poland

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Gdansk, 80-405, Poland

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Gdansk, 80-546, Poland

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Grudziądz, 86-300, Poland

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Kielce, 25-734, Poland

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Krakow, 31-209, Poland

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Lodz, 90-153, Poland

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Lubin, 59-300, Poland

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Lublin, 20-363, Poland

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Lublin, 20-468, Poland

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Mrozy, 05-320, Poland

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Olsztyn, 10-357, Poland

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Ostrowiec Świętokrzyski, 27-400, Poland

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Ostrów Wielkopolski, 63-400, Poland

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Oświęcim, 32-600, Poland

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Puławy, 24-100, Poland

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Racibórz, 47-400, Poland

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Skierniewice, 96-100, Poland

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Staszów, 28-200, Poland

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Warsaw, 01-138, Poland

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Wieluń, 98-300, Poland

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Wołomin, 05-200, Poland

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Wroclaw, 50-220, Poland

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Wroclaw, 51-162, Poland

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Zamość, 22-400, Poland

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Zgierz, 95-100, Poland

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Humenné, 066 01, Slovakia

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Kežmarok, 060 01, Slovakia

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Prešov, 08001, Slovakia

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Sabinov, Slovakia

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Topoľčany, 955 01, Slovakia

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Bucheon-si, 14584, South Korea

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Cheongju-si, 362-804, South Korea

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Daegu, 42415, South Korea

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Incheon, 21431, South Korea

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Incheon, 405-760, South Korea

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Jeju City, 63241, South Korea

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Seoul, 02559, South Korea

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Seoul, 03080, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06591, South Korea

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Seoul, 08308, South Korea

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Seoul, 135-710, South Korea

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Seoul, 150-713, South Korea

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Suwon, 16499, South Korea

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Alicante, 03004, Spain

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Badalona, 08916, Spain

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Hospitalet de Llobregat(Barcel, 08907, Spain

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Santander, 39008, Spain

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Valencia, 46015, Spain

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Changhua, 500, Taiwan

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Kaohsiung City, Taiwan

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New Taipei City, 22056, Taiwan

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Taichung, 404, Taiwan

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Taipei, 100, Taiwan

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Taipei, 235, Taiwan

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Yilan, 260, Taiwan

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Chernivtsi, 58000, Ukraine

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Chernivtsi, 58001, Ukraine

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Ivano-Frankivsk, 76012, Ukraine

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Kharkiv, 61002, Ukraine

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Kharkiv, 61058, Ukraine

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Kharkiv, 61093, Ukraine

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Kyiv, 02125, Ukraine

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Lutsk, 43000, Ukraine

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Lviv, 79066, Ukraine

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Odesa, 65025, Ukraine

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Vinnytsia, 21001, Ukraine

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Zaporizhzhya, 69063, Ukraine

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Zaporizhzhya, 69065, Ukraine

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Can Tho, 900000, Vietnam

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Hanoi, 100000, Vietnam

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Hà Nội, 100000, Vietnam

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Ho Chi Minh City, 700000, Vietnam

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Hochiminh, Vietnam

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Related Publications (4)

  • Gottlow M, Svensson DJ, Lipkovich I, Huhn M, Bowen K, Wessman P, Colice G. Application of structured statistical analyses to identify a biomarker predictive of enhanced tralokinumab efficacy in phase III clinical trials for severe, uncontrolled asthma. BMC Pulm Med. 2019 Jul 17;19(1):129. doi: 10.1186/s12890-019-0889-4.

  • Carlsson M, Braddock M, Li Y, Wang J, Xu W, White N, Megally A, Hunter G, Colice G. Evaluation of Antibody Properties and Clinically Relevant Immunogenicity, Anaphylaxis, and Hypersensitivity Reactions in Two Phase III Trials of Tralokinumab in Severe, Uncontrolled Asthma. Drug Saf. 2019 Jun;42(6):769-784. doi: 10.1007/s40264-018-00788-w.

  • Panettieri RA Jr, Sjobring U, Peterffy A, Wessman P, Bowen K, Piper E, Colice G, Brightling CE. Tralokinumab for severe, uncontrolled asthma (STRATOS 1 and STRATOS 2): two randomised, double-blind, placebo-controlled, phase 3 clinical trials. Lancet Respir Med. 2018 Jul;6(7):511-525. doi: 10.1016/S2213-2600(18)30184-X. Epub 2018 May 20.

  • Panettieri RA Jr, Wang M, Braddock M, Bowen K, Colice G. Tralokinumab for the treatment of severe, uncontrolled asthma: the ATMOSPHERE clinical development program. Immunotherapy. 2018 Mar 1;10(6):473-490. doi: 10.2217/imt-2017-0191. Epub 2018 Mar 14.

MeSH Terms

Conditions

AsthmaRespiratory Tract DiseasesLung Diseases, ObstructiveLung Diseases

Interventions

tralokinumab

Condition Hierarchy (Ancestors)

Bronchial DiseasesRespiratory HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca

Study Officials

  • Reynold A Panettieri, M.D.

    University of Pennsylvania

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 5, 2014

First Posted

June 12, 2014

Study Start

June 13, 2014

Primary Completion

February 28, 2017

Study Completion

July 18, 2017

Last Updated

August 28, 2018

Results First Posted

April 17, 2018

Record last verified: 2018-07

Data Sharing

IPD Sharing
Will not share

This is commercially sensitive information.

Locations