NCT02151981

Brief Summary

A Phase III, Open Label, Randomized Study of Osimertinib versus Platinum-Based Doublet Chemotherapy for Patients with Locally Advanced or Metastatic Non-Small Cell Lung Cancer whose Disease has Progressed with Previous Epidermal Growth Factor Receptor Tyrosine Kinase Inhibitor Therapy and whose Tumours harbour a T790M mutation within the Epidermal Growth Factor Receptor Gene

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
421

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Aug 2014

Longer than P75 for phase_3

Geographic Reach
18 countries

150 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 15, 2014

Completed
18 days until next milestone

First Posted

Study publicly available on registry

June 2, 2014

Completed
2 months until next milestone

Study Start

First participant enrolled

August 4, 2014

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 15, 2016

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

July 21, 2017

Completed
6.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 15, 2023

Completed
Last Updated

January 7, 2025

Status Verified

December 1, 2024

Enrollment Period

1.7 years

First QC Date

May 15, 2014

Results QC Date

April 12, 2017

Last Update Submit

December 12, 2024

Conditions

Keywords

Advanced Non-Small Cell Lung Cancer; T790M Mutation Positive

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS) by Investigator Assessment

    Per Response Evaluation Criteria in Solid Tumours (RECIST v1.1) assessed by MRI or CT: Progressive Disease (PD): \>= 20% increase in the sum of diameters of TLs and an absolute increase in sum of diameters of \>=5mm (compared to the previous minimum sum) or progression of NTLs or a new lesion. PFS is the time from date of randomisation until the date of PD (by investigator assessment) or death (by any cause in the absence of progression) regardless of whether the patient withdrew from randomised therapy or received another anti-cancer therapy prior to progression. Patients who had not progressed or died at the time of analysis were censored at the time of the latest date of assessment from their last evaluable RECIST 1.1 assessment.

    RECIST tumour assessments every 6 weeks from randomisation until objective disease progression up to 19 months (at the time of the primary PFS analysis).

Secondary Outcomes (5)

  • Objective Response Rate (ORR) by Investigator Assessment

    RECIST tumour assessments every 6 weeks from randomisation until objective disease progression up to 19 months (at the time of the primary PFS analysis).

  • Duration of Response (DoR) by Investigator Assessment

    RECIST tumour assessments every 6 weeks from randomisation until objective disease progression up to 19 months (at the time of the primary PFS analysis).

  • Disease Control Rate (DCR) by Investigator Assessment

    RECIST tumour assessments every 6 weeks from randomisation until objective disease progression up to 19 months (at the time of the primary PFS analysis).

  • Tumour Shrinkage by Investigator Assessment

    RECIST tumour assessments every 6 weeks from randomisation until objective disease progression up to 19 months (at the time of the primary PFS analysis).

  • Secondary: Overall Survival (OS)

    From date of randomization until time of final OS analysis, a median follow-up of 43 months

Other Outcomes (2)

  • Time to First Subsequent Therapy (TFST)

    From date of randomisation until time of final OS analysis, a median follow-up of 43 months

  • Time to Second Subsequent Therapy (TSST)

    From date of randomisation until time of final OS analysis, a median follow-up of 43 months

Study Arms (2)

Osimertinib

EXPERIMENTAL

Osimertinib 80 mg, orally, once daily

Drug: ChemotherapyDrug: Cross-over to Osimertinib

Platinum-based doublet chemotherapy

ACTIVE COMPARATOR

pemetrexed 500mg/m2 + carboplatin AUC5 or pemetrexed 500mg/m2 + cisplatin 75mg/m2

Drug: Chemotherapy

Interventions

Randomization to either Osimertinib or platinum-based doublet-chemotherapy on Day 1 of every 21d cycle in a 2:1 (Osimertinib:platinum-based doublet-chemotherapy) ratio

Also known as: Osimertinib, Platinum-based Doublet-Chemotherapy
OsimertinibPlatinum-based doublet chemotherapy

Once subjects on the platinum-based doublet chemotherapy arm are determined to have objective radiological progression according to RECIST 1.1 by the investigator and confirmed by independent central imaging review, they will be given the opportunity to begin treatment with Osimertinib 80mg, once daily. These subjects may continue treatment with Osimertinib even after disease progression, as long as they are continuing to show clinical benefit, as judged by the investigator. Subjects who stop platinum-based doublet chemotherapy for reasons other than objective disease progression according to RECIST 1.1 will not be eligible to cross-over to Osimertinib.

Osimertinib

Eligibility Criteria

Age18 Years - 130 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subjects with histologically or cytologically documented NSCLC.
  • Locally advanced or metastatic NSCLC
  • Radiological documentation of disease progression following 1st line EGFR TKI Treatment without any further treatment
  • Eligible to receive treatment with the selected doublet-chemotherapy
  • Central confirmation of T790M+ mutation status
  • World Health Organization (WHO) performance status 0-1
  • At least one lesion, not previously irradiated.

You may not qualify if:

  • Prior neo-adjuvant or adjuvant chemotherapy treatment within 6 months prior of starting 1st EGFR TKI treatment
  • Treatment with more than one prior line of treatment for advanced NSCLC
  • Treatment with an approved EGFR-TKI (e.g.,erlotinib, gefitinib, afatinib) within 8 days or approximately 5x half-life of the first dose of study treatment
  • Any investigational agents or other anticancer drugs from a previous treatment regimen or clinical study within 14 days of the first dose of study treatment
  • Previous treatment with Osimertinib, or a 3rd generation EGFR TKI
  • For subjects who cross-over to Osimertinib:
  • Once subjects on the platinum-based doublet chemotherapy arm are determined to have objective radiological progression according to RECIST 1.1 by the investigator and confirmed by independent central imaging review.
  • At least 14 days since last dose of platinum-based doublet chemotherapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (150)

Research Site

Anaheim, California, 92801, United States

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Orange, California, 92868, United States

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Santa Rosa, California, 95403, United States

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Norwalk, Connecticut, 06856, United States

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Gainesville, Florida, 32610, United States

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Orlando, Florida, 32804, United States

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Pembroke Pines, Florida, 33028, United States

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Atlanta, Georgia, 30322, United States

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Park Ridge, Illinois, 60068, United States

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Indianapolis, Indiana, 46202, United States

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Marrero, Louisiana, 70072, United States

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Chevy Chase, Maryland, 20815, United States

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Lebanon, New Hampshire, 03756, United States

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Brick, New Jersey, 08724, United States

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New York, New York, 10032, United States

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Hershey, Pennsylvania, 17033-0850, United States

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Charleston, South Carolina, 29425, United States

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Houston, Texas, 77030, United States

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Lacey, Washington, 98503, United States

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Tacoma, Washington, 98405, United States

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Milwaukee, Wisconsin, 53226, United States

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Darlinghurst, 2010, Australia

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Heidelberg, 3084, Australia

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Kogarah, 2217, Australia

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Nedlands, 6009, Australia

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Woolloongabba, 4102, Australia

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Edmonton, Alberta, T6G 1Z2, Canada

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Vancouver, British Columbia, V5Z 4E6, Canada

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Halifax, Nova Scotia, B3H 1V7, Canada

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Ottawa, Ontario, K1H 8L6, Canada

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Toronto, Ontario, M5G 2M9, Canada

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Montreal, Quebec, H2L 4M1, Canada

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Beijing, 100021, China

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Beijing, 100142, China

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Changchun, 130000, China

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Chongqing, 400038, China

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Chongqing, 400042, China

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Fuzhou, 350014, China

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Guangzhou, 510060, China

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Guangzhou, 510100, China

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Hangzhou, 310003, China

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Harbin, 150049, China

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Nanchang, 330006, China

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Shanghai, 200030, China

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Shanghai, CN-200433, China

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Tianjin, 300060, China

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Ürümqi, 830000, China

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Zhengzhou, 450008, China

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Clermont-Ferrand, 63003, France

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Dijon, 21079, France

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Lille, 59000, France

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Marseille, 13915, France

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Paris, 75020, France

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Strasbourg, 67091, France

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Toulouse, 31059, France

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Villejuif, 94800, France

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Essen, 45122, Germany

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Frankfurt, 60590, Germany

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Gerlingen, 70839, Germany

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Oldenburg, 26121, Germany

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Regensburg, 93053, Germany

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Würzburg, 97080, Germany

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Hong Kong, Hong Kong

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Shatin, 00000, Hong Kong

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Budapest, 1121, Hungary

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Avellino, 83100, Italy

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Meldola, 47014, Italy

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Milan, 20133, Italy

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Orbassano, 10043, Italy

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Roma, 00128, Italy

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Akashi-shi, 673-8558, Japan

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Bunkyō City, 113-8431, Japan

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Fukuoka, 812-8582, Japan

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Hirakata-shi, 573-1191, Japan

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Kanazawa, 920-8641, Japan

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Kitaadachi-gun, 362-0806, Japan

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Kobe, 650-0047, Japan

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Kurashiki-shi, 710-8602, Japan

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Kyoto, 606-8507, Japan

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Matsuyama, 791-0280, Japan

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Nagoya, 464-8681, Japan

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Natori-shi, 981-1293, Japan

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Niigata, 951-8566, Japan

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Okayama, 700-8558, Japan

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Osaka, 534-0021, Japan

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Osaka, 541-8567, Japan

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Sakaishi, 591-8555, Japan

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Sayama, 589-8511, Japan

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Shinjuku-ku, 160-0023, Japan

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Sunto-gun, 411-8777, Japan

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Takatsuki-shi, 569-8686, Japan

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Wakayama, 641-8510, Japan

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Yokohama, 236-0024, Japan

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Yokohama, 236-0051, Japan

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Yokohama, 241-8515, Japan

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México, 52763, Mexico

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Oaxaca City, 68000, Mexico

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Amsterdam, 1066 CX, Netherlands

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Amsterdam, 1081 HV, Netherlands

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Groningen, 9713 GZ, Netherlands

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Moscow, 115478, Russia

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Omsk, 644013, Russia

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Saint Petersburg, 197183, Russia

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Saint Petersburg, 197342, Russia

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Saint Petersburg, 197758, Russia

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Yekaterinburg, 620905, Russia

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Busan, 47392, South Korea

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Cheongju-si, 28644, South Korea

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Goyang-si, 10408, South Korea

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Incheon, 21565, South Korea

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Jinju, 660-702, South Korea

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Seongnam-si, 13620, South Korea

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Seoul, 03722, South Korea

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Seoul, 05505, South Korea

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Seoul, 06591, South Korea

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Seoul, 156-707, South Korea

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Seoul, 6351, South Korea

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Suwon, 16499, South Korea

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Ulsan, 44033, South Korea

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Madrid, 08035, Spain

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Madrid, 28034, Spain

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Madrid, 28041, Spain

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Málaga, 29010, Spain

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Seville, 41013, Spain

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Zaragoza, 50009, Spain

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Gothenburg, 413 45, Sweden

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Lund, 221 85, Sweden

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Stockholm, 171 76, Sweden

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Changhua, 500, Taiwan

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Hsinchu, 300, Taiwan

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Kaohsiung City, 81362, Taiwan

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Kaohsiung City, 82445, Taiwan

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Kaohsiung City, 83301, Taiwan

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Taichung, 40447, Taiwan

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Taichung, 40705, Taiwan

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Tainan, 704, Taiwan

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Taipei, 10002, Taiwan

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Taipei, 112, Taiwan

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Taoyuan District, 333, Taiwan

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Aberdeen, AB2 2ZB, United Kingdom

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Bristol, BS2 8ED, United Kingdom

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Edinburgh, EH4 2XU, United Kingdom

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Glasgow, G12 0YN, United Kingdom

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Huddersfield, HD3 3EA, United Kingdom

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London, SW10 9NH, United Kingdom

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London, W1G 6AD, United Kingdom

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Manchester, M20 4BX, United Kingdom

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Newcastle upon Tyne, NE7 7DN, United Kingdom

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Nottingham, NG5 1PB, United Kingdom

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Wolverhampton, WV10 0QP, United Kingdom

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Related Publications (11)

  • Markovets A, Merino Vega D, Abbosh C, Quinn K, Chang K, Wienke S, Hartmaier R, Barrett JC, Hodgson D. Variability of Circulating Tumor DNA Levels in Plasma Samples From Patients With Advanced Non-Small-Cell Lung Cancer in the Absence of Treatment. JCO Precis Oncol. 2025 Oct;9:e2500287. doi: 10.1200/PO-25-00287. Epub 2025 Oct 30.

  • Murat-Onana ML, Ramalingam SS, Janne PA, Gray JE, Ahn MJ, John T, Yatabe Y, Huang X, Rukazenkov Y, Javey M, Brown H, Li-Sucholeiki X. EGFR mutation testing across the osimertinib clinical program. Lung Cancer. 2025 Jun;204:108549. doi: 10.1016/j.lungcan.2025.108549. Epub 2025 Apr 18.

  • King-Kallimanis BL, Bhatnagar V, Horodniceanu EG, Chen TY, Kluetz PG. Timing is everything: The importance of patient-reported outcome assessment frequency when characterizing symptomatic adverse events. Clin Trials. 2022 Jun;19(3):267-273. doi: 10.1177/17407745221093935. Epub 2022 May 15.

  • Singh J, Bourke S, Dyer M, Devlin N, Longworth L. An Analysis of 5-Level Version of EQ-5D Adjusting for Treatment Switching: The Case of Patients With Epidermal Growth Factor Receptor T790M-Positive Nonsmall Cell Lung Cancer Treated With Osimertinib. Value Health. 2022 Jul;25(7):1205-1211. doi: 10.1016/j.jval.2022.01.022. Epub 2022 Apr 2.

  • Papadimitrakopoulou VA, Mok TS, Han JY, Ahn MJ, Delmonte A, Ramalingam SS, Kim SW, Shepherd FA, Laskin J, He Y, Akamatsu H, Theelen WSME, Su WC, John T, Sebastian M, Mann H, Miranda M, Laus G, Rukazenkov Y, Wu YL. Osimertinib versus platinum-pemetrexed for patients with EGFR T790M advanced NSCLC and progression on a prior EGFR-tyrosine kinase inhibitor: AURA3 overall survival analysis. Ann Oncol. 2020 Nov;31(11):1536-1544. doi: 10.1016/j.annonc.2020.08.2100. Epub 2020 Aug 27.

  • Papadimitrakopoulou VA, Han JY, Ahn MJ, Ramalingam SS, Delmonte A, Hsia TC, Laskin J, Kim SW, He Y, Tsai CM, Hida T, Maemondo M, Kato T, Jenkins S, Patel S, Huang X, Laus G, Markovets A, Thress KS, Wu YL, Mok T. Epidermal growth factor receptor mutation analysis in tissue and plasma from the AURA3 trial: Osimertinib versus platinum-pemetrexed for T790M mutation-positive advanced non-small cell lung cancer. Cancer. 2020 Jan 15;126(2):373-380. doi: 10.1002/cncr.32503. Epub 2019 Nov 26.

  • Wu YL, Ahn MJ, Garassino MC, Han JY, Katakami N, Kim HR, Hodge R, Kaur P, Brown AP, Ghiorghiu D, Papadimitrakopoulou VA, Mok TSK. CNS Efficacy of Osimertinib in Patients With T790M-Positive Advanced Non-Small-Cell Lung Cancer: Data From a Randomized Phase III Trial (AURA3). J Clin Oncol. 2018 Sep 10;36(26):2702-2709. doi: 10.1200/JCO.2018.77.9363. Epub 2018 Jul 30.

  • Lee CK, Novello S, Ryden A, Mann H, Mok T. Patient-Reported Symptoms and Impact of Treatment With Osimertinib Versus Chemotherapy in Advanced Non-Small-Cell Lung Cancer: The AURA3 Trial. J Clin Oncol. 2018 Jun 20;36(18):1853-1860. doi: 10.1200/JCO.2017.77.2293. Epub 2018 May 7.

  • Akamatsu H, Katakami N, Okamoto I, Kato T, Kim YH, Imamura F, Shinkai M, Hodge RA, Uchida H, Hida T. Osimertinib in Japanese patients with EGFR T790M mutation-positive advanced non-small-cell lung cancer: AURA3 trial. Cancer Sci. 2018 Jun;109(6):1930-1938. doi: 10.1111/cas.13623. Epub 2018 May 31.

  • Mok TS, Wu Y-L, Ahn M-J, Garassino MC, Kim HR, Ramalingam SS, Shepherd FA, He Y, Akamatsu H, Theelen WS, Lee CK, Sebastian M, Templeton A, Mann H, Marotti M, Ghiorghiu S, Papadimitrakopoulou VA; AURA3 Investigators. Osimertinib or Platinum-Pemetrexed in EGFR T790M-Positive Lung Cancer. N Engl J Med. 2017 Feb 16;376(7):629-640. doi: 10.1056/NEJMoa1612674. Epub 2016 Dec 6.

  • Soria JC, Wu YL, Nakagawa K, Kim SW, Yang JJ, Ahn MJ, Wang J, Yang JC, Lu Y, Atagi S, Ponce S, Lee DH, Liu Y, Yoh K, Zhou JY, Shi X, Webster A, Jiang H, Mok TS. Gefitinib plus chemotherapy versus placebo plus chemotherapy in EGFR-mutation-positive non-small-cell lung cancer after progression on first-line gefitinib (IMPRESS): a phase 3 randomised trial. Lancet Oncol. 2015 Aug;16(8):990-8. doi: 10.1016/S1470-2045(15)00121-7. Epub 2015 Jul 6.

Related Links

MeSH Terms

Interventions

Drug Therapyosimertinib

Intervention Hierarchy (Ancestors)

Therapeutics

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca Clinical Study Information Center

Study Officials

  • Yilong Wu, MD

    Guangdong General Hospital, Guangdong, 510030, China

    PRINCIPAL INVESTIGATOR
  • Vassiliki A Papadimitrakopoulou, MD

    The University of Texas/M.D. Anderson Cancer Center, Houston, Tx, USA

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 15, 2014

First Posted

June 2, 2014

Study Start

August 4, 2014

Primary Completion

April 15, 2016

Study Completion

December 15, 2023

Last Updated

January 7, 2025

Results First Posted

July 21, 2017

Record last verified: 2024-12

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
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