NCT02128490

Brief Summary

The purpose of this study is to evaluate the efficacy and safety of febuxostat 40 mg extended release (XR) and 80 mg XR in comparison with febuxostat 40 mg immediate release (IR) and 80 mg IR, respectively, in gout participants with moderate renal impairment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
189

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2014

Shorter than P25 for phase_2

Geographic Reach
1 country

89 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 29, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 1, 2014

Completed
Same day until next milestone

Study Start

First participant enrolled

May 1, 2014

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2015

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2015

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

November 3, 2016

Completed
Last Updated

November 3, 2016

Status Verified

September 1, 2016

Enrollment Period

1.3 years

First QC Date

April 29, 2014

Results QC Date

September 15, 2016

Last Update Submit

September 15, 2016

Conditions

Keywords

Drug therapy

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Serum Urate <5.0 mg/dL at Month 3

    Month 3

Secondary Outcomes (2)

  • Percentage of Participants With at Least One Gout Flare Requiring Treatment

    Baseline to Month 3

  • Percentage of Participants With Serum Urate <6.0 mg/dL at Month 3

    Month 3

Study Arms (5)

Febuxostat IR 40 mg

ACTIVE COMPARATOR

Febuxostat Immediate Release (IR) 40 mg over-encapsulated tablet, orally, once daily, and colchicine 0.6 mg tablet, orally, every other day, or, naproxen 250 mg tablets, orally, twice a day and lansoprazole 15 mg capsule, orally once daily, for 3 months.

Drug: Febuxostat IRDrug: ColchicineDrug: NaproxenDrug: Lansoprazole

Febuxostat IR 80 mg

ACTIVE COMPARATOR

Febuxostat IR 80 mg over-encapsulated tablet, orally, once daily, and colchicine 0.6 mg tablet, orally, every other day, or, naproxen 250 mg tablets, orally, twice a day and lansoprazole 15 mg capsule, orally once daily, for 3 months.

Drug: Febuxostat IRDrug: ColchicineDrug: NaproxenDrug: Lansoprazole

Febuxostat XR 40 mg

EXPERIMENTAL

Febuxostat Extended Release (XR) 40 mg over-encapsulated capsule, orally, once daily, and colchicine 0.6 mg tablet, orally, every other day, or, naproxen 250 mg tablets, orally, twice a day and lansoprazole 15 mg capsule, orally once daily, for 3 months.

Drug: Febuxostat XRDrug: ColchicineDrug: NaproxenDrug: Lansoprazole

Febuxostat XR 80 mg

EXPERIMENTAL

Febuxostat XR 80 mg over-encapsulated capsule, orally, once daily, and colchicine 0.6 mg tablet, orally, every other day, or, naproxen 250 mg tablets, orally, twice a day and lansoprazole 15 mg capsule, orally once daily, for 3 months.

Drug: Febuxostat XRDrug: ColchicineDrug: NaproxenDrug: Lansoprazole

Placebo

PLACEBO COMPARATOR

Febuxostat placebo-matching capsule, orally, once daily, and colchicine 0.6 mg tablet, orally, every other day, or, naproxen 250 mg tablets, orally, twice a day and lansoprazole 15 mg capsule, orally once daily, for 3 months.

Drug: Febuxostat placeboDrug: ColchicineDrug: NaproxenDrug: Lansoprazole

Interventions

Febuxostat IR over-encapsulated tablets

Also known as: Uloric
Febuxostat IR 40 mgFebuxostat IR 80 mg

Febuxostat over-encapsulated capsules

Febuxostat XR 40 mgFebuxostat XR 80 mg

Febuxostat IR and XR placebo-matching capsules

Placebo

Colchicine tablets

Febuxostat IR 40 mgFebuxostat IR 80 mgFebuxostat XR 40 mgFebuxostat XR 80 mgPlacebo

Naproxen tablets

Febuxostat IR 40 mgFebuxostat IR 80 mgFebuxostat XR 40 mgFebuxostat XR 80 mgPlacebo

Lansoprazole capsules

Febuxostat IR 40 mgFebuxostat IR 80 mgFebuxostat XR 40 mgFebuxostat XR 80 mgPlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • In the opinion of the investigator, the participant is capable of understanding and complying with protocol requirements.
  • The participant or, when applicable, the participant's legally acceptable representative signs and dates a written, informed consent form and any required privacy authorization prior to the initiation of any study procedure.
  • Has a history or presence of gout defined as having one or more of the American Rheumatism Association (ARA) criteria for the diagnosis of gout:
  • A tophus proven to contain urate crystals by chemical or polarized light microscopic means, AND/OR;
  • Characteristic urate crystals in the joint fluid, AND/OR;
  • History of at least 6 of the following clinical, laboratory, and x-ray phenomena:
  • i. more than one attack of acute arthritis, ii. maximum inflammation developed within 1 day, iii. monoarticular arthritis, iv. redness observed over joints, v. first metatarsophalangeal joint painful or swollen, vi. unilateral first metatarsophalangeal joint attack, vii. unilateral tarsal joint attack, viii. tophus (proven or suspected), ix. Hyperuricemia, x. asymmetric swelling within a joint on x-ray, xi. subcortical cysts without erosions on x-ray, xii. joint fluid culture negative for organisms during attack.
  • Is male or female at least 18 years of age, inclusive.
  • A female participant of childbearing potential who is sexually active with a nonsterilized male partner agrees to use routinely adequate contraception from signing of informed consent throughout the duration of the study.
  • Have a serum urate (sUA) level ≥8.0 mg/dL at the Day -4 Visit or at the retest visit.
  • Has an estimated Glomerular Filtration Rate (eGRF) \[Modification of Diet in Renal Disease (MDRD)\] ≥30 mL/min and \<60 mL/min at Screening visit (Day -21 for participants on urate lowering therapy (ULT) and Day -4 for participants not on ULT) or at the retest visit.
  • Has at least one gout flare within 12 months prior to Screening visit.

You may not qualify if:

  • Has received any investigational compound within 30 days prior to Screening.
  • Is an immediate family member, study site employee, or is in a dependant relationship with a study site employee who is involved in conduct of this study (eg, spouse, parent, child, sibling) or may consent under duress.
  • Is breastfeeding or pregnant.
  • Has secondary hyperuricemia (eg, due to myeloproliferative disorder).
  • Has a history of xanthinuria.
  • Has received ULT (ie, allopurinol, probenecid, etc.) within 20 days prior to Day 1/Randomization Visit.
  • Has a known hypersensitivity to febuxostat or any components of their formulation; has a known hypersensitivity to naproxen, any other nonsteroidal anti-inflammatory drug (NSAID), aspirin, lansoprazole, colchicine or any components in their formulation.
  • Has active peptic ulcer disease.
  • Has a history of cancer (other than basal cell carcinoma of the skin) within 5 years prior to the Screening Visit.
  • Has alanine aminotransferase (ALT) and aspartate aminotransferase (AST) values \>2 x the upper limit of normal (ULN).
  • Has rheumatoid arthritis which requires treatment.
  • Has a significant medical condition and/or conditions that would interfere with the treatment, safety, or compliance with the protocol.
  • Has experienced either a myocardial infarction (MI), stroke, hospitalized unstable angina, cardiac or cerebrovascular revascularization procedure or hospitalized transient ischemic attack (TIA).
  • Has a history of drug abuse (defined as any illicit drug use) or a history of alcohol abuse within 5 years prior to the Screening visit. Participant consumes \>14 alcoholic beverages/week.
  • Has participated in another investigational study within the 30 days prior to the Screening Visit.
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (89)

Unknown Facility

Birmingham, Alabama, United States

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Muscle Shoals, Alabama, United States

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Phoenix, Arizona, United States

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Benny Green MD PA Family Practice

Little Rock, Arkansas, 72223, United States

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Little Rock, Arkansas, United States

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Bellflower, California, United States

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Escondido, California, United States

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Harbor City, California, United States

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Huntington Park, California, United States

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Irvine, California, United States

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Lomita, California, United States

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Long Beach Center for Clinical Research

Long Beach, California, 90807, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Brigid Freyne MD

Murrieta, California, 92563, United States

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Murrieta, California, United States

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Orange, California, United States

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Rancho Cucamonga, California, United States

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Redondo Beach, California, United States

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Sacramento, California, United States

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San Jose, California, United States

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San Ramon, California, United States

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Clearwater, Florida, United States

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Coral Gables, Florida, United States

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Coral Springs, Florida, United States

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Riverside Clinical Research

Edgewater, Florida, 32141, United States

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Edgewater, Florida, United States

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Hialeah, Florida, United States

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Miami, Florida, United States

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Miami Beach, Florida, United States

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Miami Lakes, Florida, United States

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Orlando, Florida, United States

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Pembroke Pines, Florida, United States

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Plantation, Florida, United States

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Port Charlotte, Florida, United States

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Saint Cloud, Florida, United States

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Vero Beach, Florida, United States

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Atlanta, Georgia, United States

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Dunwoody, Georgia, United States

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East Point, Georgia, United States

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Suwanee, Georgia, United States

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East West Medical Research Institute

Honolulu, Hawaii, 96814, United States

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Honolulu, Hawaii, United States

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Brownsburg, Indiana, United States

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Manhattan, Kansas, United States

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Wichita, Kansas, United States

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Elizabethtown, Kentucky, United States

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Central Kentucy Reseach Associates

Lexington, Kentucky, 40509, United States

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Lexington, Kentucky, United States

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Paducah, Kentucky, United States

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Mandeville, Louisiana, United States

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Metairie, Louisiana, United States

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Fall River, Massachusetts, United States

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Detroit, Michigan, United States

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Kalamazoo, Michigan, United States

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Hazelwood, Missouri, United States

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Washington, Missouri, United States

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Las Vegas, Nevada, United States

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Albuquerque, New Mexico, United States

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Columbiana, North Carolina, United States

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Greensboro, North Carolina, United States

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Salisbury, North Carolina, United States

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Wilmington, North Carolina, United States

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Fargo, North Dakota, United States

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Franklin, Ohio, United States

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COR Clinical Research LLC

Oklahoma City, Oklahoma, 73103, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Columbia, South Carolina, United States

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Greer, South Carolina, United States

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Old Point Station, South Carolina, United States

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Clarksville, Tennessee, United States

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Knoxville, Tennessee, United States

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Remesh C Gupta MD

Memphis, Tennessee, 38119, United States

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Memphis, Tennessee, United States

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Austin, Texas, United States

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Bellaire, Texas, United States

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3rd Coast Research Associates

Corpus Christi, Texas, 78413, United States

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Corpus Christi, Texas, United States

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Nassau Bay, Texas, United States

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Plano, Texas, United States

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Sun Research Institute

San Antonio, Texas, 78215, United States

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Briggs Clinical Research LLC

San Antonio, Texas, 78224, United States

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San Antonio, Texas, United States

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Bountiful, Utah, United States

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Newport News, Virginia, United States

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Norfolk, Virginia, United States

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Richmond, Virginia, United States

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Virginia Beach, Virginia, United States

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Related Publications (1)

  • Gunawardhana L, Becker MA, Whelton A, Hunt B, Castillo M, Saag K. Efficacy and safety of febuxostat extended release and immediate release in patients with gout and moderate renal impairment: phase II placebo-controlled study. Arthritis Res Ther. 2018 May 30;20(1):99. doi: 10.1186/s13075-018-1593-0.

MeSH Terms

Conditions

Gout

Interventions

FebuxostatColchicineNaproxenLansoprazole

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesCrystal ArthropathiesRheumatic DiseasesPurine-Pyrimidine Metabolism, Inborn ErrorsMetabolism, Inborn ErrorsGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

ThiazolesSulfur CompoundsOrganic ChemicalsAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsAlkaloidsNaphthaleneacetic AcidsNaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPolycyclic Compounds2-PyridinylmethylsulfinylbenzimidazolesSulfoxidesPyridinesBenzimidazolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Results Point of Contact

Title
Medical Director
Organization
Takeda

Study Officials

  • Medical Director Clinical Science

    Takeda

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 29, 2014

First Posted

May 1, 2014

Study Start

May 1, 2014

Primary Completion

September 1, 2015

Study Completion

October 1, 2015

Last Updated

November 3, 2016

Results First Posted

November 3, 2016

Record last verified: 2016-09

Locations