NCT02079909

Brief Summary

The primary objective is to evaluate the efficacy of T-817MA as measured by ADAS-cog and ADCS-CGIC. The secondary objectives are:

  • To evaluate the safety and tolerability of T-817MA measured by clinical safety laboratories, physical examinations, ECGs and solicitation of adverse events.
  • To evaluate the efficacy of T-817MA as measured by ADCS-ADL, FAQ, Neuropsychiatric Inventory (NPI) and Mini-mental State Examination (MMSE).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
482

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2014

Typical duration for phase_2

Geographic Reach
1 country

50 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2014

Completed
3 days until next milestone

First Submitted

Initial submission to the registry

March 4, 2014

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 6, 2014

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 5, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 5, 2017

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

August 9, 2018

Completed
Last Updated

February 26, 2019

Status Verified

February 1, 2019

Enrollment Period

3.2 years

First QC Date

March 4, 2014

Results QC Date

May 7, 2018

Last Update Submit

February 12, 2019

Conditions

Keywords

Alzheimer's DiseaseAlzheimer's

Outcome Measures

Primary Outcomes (2)

  • ADAS-cog Change From Baseline to Week 52

    The ADAS-cog (Alzheimer's Disease Assessment Scale-cognitive subscale) is a structured scale that evaluates memory (word recall, word recognition), reasoning (following commands), language (naming, comprehension), orientation, ideational praxis (placing letter in envelope) and constructional praxis (copying geometric designs). Ratings of spoken language, language comprehension, word finding difficulty, and ability to remember test instructions are also obtained. The test is scored in terms of errors, with higher scores reflecting poorer performance and greater impairment. Scores can range from 0 (best) to 70 (worse).

    Baseline and 52 weeks

  • CGIC

    The ADCS-CGIC (Alzheimer's Disease Cooperative Study-Clinical Global Impression of Change) is a validated categorical measure of change in the patient's clinical condition between baseline and follow-up visits. It measures whether the effects of active treatment are substantial enough to be detected by a skilled and experienced clinician on the basis of a clinical interview and examination. It relies on both direct examination of the patient and an interview of the study partner. A skilled and experienced clinician who is blinded to treatment assignment rates the patient on a 7-point Likert scale, ranging from 1 (marked improvement) to 7 (marked worsening). It is suggested that the instrument has distinct clinical utility in assessing change in AD clinical trials.

    52 weeks

Secondary Outcomes (1)

  • ADCS-ADL Change From Baseline to Week 52

    Baseline and 52 weeks

Study Arms (3)

T-817MA-H

EXPERIMENTAL

224 mg T-817MA once daily for first 4 weeks and 448 mg T-817MA once daily for the following weeks.

Drug: T-817MA-H

T-817MA-L

EXPERIMENTAL

224 mg T-817MA once daily

Drug: T-817MA-L

Placebo

PLACEBO COMPARATOR

Placebo once daily

Drug: Placebo

Interventions

224 mg or 448 mg T-817 MA once daily

T-817MA-H

224 mg T-817 MA once daily

T-817MA-L

Placebo

Placebo

Eligibility Criteria

Age55 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female (post-menopausal or surgically sterile)
  • Patients with Mild to moderate Alzheimer's disease who are receiving donepezil (Aricept®) or rivastigmine transdermal system (Exelon® Patch), . Memantine (Namenda®) is allowed only when prescribed in combination with donepezil or rivastigmine transdermal system.
  • Age 55 to 85 inclusive
  • Patients must be living in the community
  • Patients must have an eligible informant or study partner (caregiver)
  • Patients and eligible informant or study partner (caregiver) must be able to read and understand English.
  • Informed consent obtained from both the patient and the caregiver

You may not qualify if:

  • Patients with clinically significant cardiac, hepatic or renal impairment
  • Patient have a dementia not of the Alzheimer's type etc (According to the protocol)
  • Patients who are taking any drug other than donepezil or rivastigmine transdermal system for Alzheimer's disease, including olal rivastigmine (Exelon®), galantamine (Razadyne®)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (50)

Banner Alzheimer's Institute

Phoenix, Arizona, United States

Location

Banner Sun Health Research Institute

Sun City, Arizona, United States

Location

University of Arizona Health Sciences Center

Tucson, Arizona, United States

Location

Neurology Center of North Orange County

Fullerton, California, United States

Location

UCSD Comprehensive Alzheimer's Program

La Jolla, California, United States

Location

UC Irvine Medical Center

Orange, California, United States

Location

Geriatric and Adult Psychiatry, LCC

Hamden, Connecticut, United States

Location

Yale University, Alzheimer's Disease Research Unit

New Haven, Connecticut, United States

Location

Research Center for Clinical Studies, Inc.

Norwalk, Connecticut, United States

Location

Georgetown University Clinical Research Unit

Washington D.C., District of Columbia, United States

Location

Infinity Clinical Research, LLC

Hollywood, Florida, United States

Location

University of Miami Miller-School of Medicine

Miami, Florida, United States

Location

Scientific Clinical Research, Inc

North Miami, Florida, United States

Location

Renstar Medical Research

Ocala, Florida, United States

Location

Meridien Research

Tampa, Florida, United States

Location

Neuro Trials Research, Inc

Atlanta, Georgia, United States

Location

Rush University Medical Center

Chicago, Illinois, United States

Location

SIU School of Medicine

Springfield, Illinois, United States

Location

Indiana Medical Research

Elkhart, Indiana, United States

Location

Indiana University Health Partners, Adult Neurology Clinic

Indianapolis, Indiana, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Location

University of Kansas/Clinical and Translational Science Unit

Fairway, Kansas, United States

Location

University of Kentucky Sanders-Brown Center on Aging Clinic

Lexington, Kentucky, United States

Location

Pennington Biomedical Research Center

Baton Rouge, Louisiana, United States

Location

Acadia Hospital

Bangor, Maine, United States

Location

Boston University Alzheimer's Disease Center

Boston, Massachusetts, United States

Location

University of Michigan Health System/ Michigan Clinical Research Unit

Ann Arbor, Michigan, United States

Location

Michigan State University

East Lansing, Michigan, United States

Location

Bronson Neurobehvioral Health

Paw Paw, Michigan, United States

Location

University of Nebraska Medical Center(Geri Psych)

Omaha, Nebraska, United States

Location

Cleveland Clinic Lou Ruvo Center for Brain Health

Las Vegas, Nevada, United States

Location

Global Medical Institutes, LLC;Princeton Medical Institute

Princeton, New Jersey, United States

Location

Dent Neurologic Institute

Amherst, New York, United States

Location

Alzheimer's Disease Research Center of Mount Sinai

New York, New York, United States

Location

Columbia University Medical Center Sergievsky Center Taub Institute

New York, New York, United States

Location

The Nathan S. Kline Instituite for Psychiatric Research

Orangeburg, New York, United States

Location

University of Rochester Medical Center

Rochester, New York, United States

Location

SUNY Upstate Medical University

Syracuse, New York, United States

Location

Wake Forest University (WFU) School of Medicine

Winston-Salem, North Carolina, United States

Location

Case Western Reserve University/ University Hospitals Case Medical Center

Beachwood, Ohio, United States

Location

Tulsa Clinical Research, LLC

Tulsa, Oklahoma, United States

Location

Hospital at the University of Pennsylvania, Penn Memory Center

Philadelphia, Pennsylvania, United States

Location

University of Pittsburgh, Alzheimer Disease Research Center

Pittsburgh, Pennsylvania, United States

Location

Abington Neurological Associates, LTD.

Willow Grove, Pennsylvania, United States

Location

Roper St. Francis Healthcare

Charleston, South Carolina, United States

Location

Vanderbilt University Medical Center -VUIIS

Nashville, Tennessee, United States

Location

University of North Texas Health Science Center

Fort Worth, Texas, United States

Location

Houston Methodist Hospital

Houston, Texas, United States

Location

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Location

Cary J. Kohlenberg MD., SC dba IPC Research

Waukesha, Wisconsin, United States

Location

Related Publications (1)

  • Schneider LS, Thomas RG, Hendrix S, Rissman RA, Brewer JB, Salmon DP, Oltersdorf T, Okuda T, Feldman HH; Alzheimer's Disease Cooperative Study TCAD Study Group. Safety and Efficacy of Edonerpic Maleate for Patients With Mild to Moderate Alzheimer Disease: A Phase 2 Randomized Clinical Trial. JAMA Neurol. 2019 Nov 1;76(11):1330-1339. doi: 10.1001/jamaneurol.2019.1868.

MeSH Terms

Conditions

Alzheimer Disease

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Results Point of Contact

Title
Project Manager
Organization
FUJIFILM Toyama Chemical

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 4, 2014

First Posted

March 6, 2014

Study Start

March 1, 2014

Primary Completion

May 5, 2017

Study Completion

May 5, 2017

Last Updated

February 26, 2019

Results First Posted

August 9, 2018

Record last verified: 2019-02

Locations