NCT02079896

Brief Summary

Dialysis patients regularly suffer from anemia which may be caused by various contributing factors, alone or in combination, including blood loss, low erythropoietin and iron sequestration. In most patients, the anemia is responsive to treatment with erythropoietin or other erythropoiesis stimulating agents (ESA) alone or in combination with intravenous (i.v.) iron. In about 10% of patients however, the anaemia does not respond appropriately to this standard treatment and high to very high doses of ESA and i.v. iron are used to maintain acceptable hemoglobin concentrations. In these patients, hepcidin was identified as a causative factor leading to anemia of chronic disease with functional iron deficiency and ESA-hyporesponsiveness. The Spiegelmer lexaptepid pegol (NOX-H94) offers a hepcidin-specific approach to the treatment of anemia of chronic disease. The safety and the activity of lexaptepid pegol are supported by data from healthy subjects and patients with multiple myeloma or lymphoma. The present study in dialysis patients with functional iron deficiency and ESA-hyporesponsiveness is conducted to demonstrate the safety of lexaptepid pegol in this population, to investigate its pharmacokinetic (PK) and pharmacodynamic (PD) profiles and its efficacy in increasing haemoglobin (Hb) in dialysis patients.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
33

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started May 2014

Geographic Reach
3 countries

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 28, 2014

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 6, 2014

Completed
2 months until next milestone

Study Start

First participant enrolled

May 1, 2014

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2015

Completed
Last Updated

November 24, 2015

Status Verified

November 1, 2015

Enrollment Period

1.5 years

First QC Date

February 28, 2014

Last Update Submit

November 23, 2015

Conditions

Keywords

Dialysis

Outcome Measures

Primary Outcomes (1)

  • Number of adverse events

    up to 8 weeks

Secondary Outcomes (3)

  • Pharmacokinetics

    Weeks 1, 2, 3, 4, 5, 6, 8

  • Pharmacodynamics

    0 to 48 hours

  • Efficacy

    Weeks 1, 2, 3, 4, 5, 6, 8

Study Arms (3)

Single dose cross-over pilot

EXPERIMENTAL

Single dose of lexaptepid pegol (NOX-H94) cross-over with single dose of placebo

Drug: Lexaptepid pegol (NOX-H94)Drug: Placebo

Control

PLACEBO COMPARATOR

Twice weekly doses of placebo, 9 total

Drug: Placebo

Lexaptepid pegol (NOX-H94)

EXPERIMENTAL

Twice weekly doses of lexaptepid pegol (NOX-H94), 9 total

Drug: Lexaptepid pegol (NOX-H94)

Interventions

anti-hepcidin L-RNA-aptamer (Spiegelmer)

Also known as: NOX-H94
Lexaptepid pegol (NOX-H94)Single dose cross-over pilot
ControlSingle dose cross-over pilot

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • End stage renal disease treated with maintenance hemodialysis.
  • Anemia : Hb 7 to 11 g/dL.
  • Functional iron deficiency: Transferrin saturation \<30%, Ferritin ≥300 ng/mL.
  • ESA-hyporesponsiveness with erythropoietin dose ≥12,000 IU/ week.

You may not qualify if:

  • Treatment with darbepoetin or methoxy-polyethyleneglycol-epoetin.
  • Uncontrolled / unstable cardiovascular , peripheral arterial or cerebrovascular disease.
  • Congestive heart failure: New York Heart Association Class III or IV.
  • Unstable angina, myocardial infarction, percutaneous transluminal coronary angioplasty/stents, or coronary artery bypass grafting \<3 months prior screening.
  • Any other medical conditions requiring a change in treatment within 4 weeks prior to screening or making study participation unadvisable.
  • History of clinically relevant hemolysis and/or blood loss.
  • AST, ALT, or bilirubin ≥2.0 times the upper limit of normal.
  • Known bone marrow fibrosis.
  • Treatment with i.v. iron \<4 weeks prior to screening or during the screening period or change in erythropoietin dose during last month.
  • Any acute or chronic infection, viral or bacterial within 4 weeks prior to screening or during the screening period considered as systemic infection.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

Dialysis Unit

Düsseldorf, Germany

Location

University Hospital

Halle, Germany

Location

Hospital

Leipzig, Germany

Location

Dialysis Unit

Villingen-Schwenningen, Germany

Location

Hospital

Siena, Italy

Location

Hospital

Swansea, Wales, United Kingdom

Location

Hospital

Leicester, United Kingdom

Location

Hospital

London, United Kingdom

Location

King's College London

London, United Kingdom

Location

Lister Hospital

Stevenage, United Kingdom

Location

Related Publications (1)

  • Park EJ, Choi J, Lee KC, Na DH. Emerging PEGylated non-biologic drugs. Expert Opin Emerg Drugs. 2019 Jun;24(2):107-119. doi: 10.1080/14728214.2019.1604684. Epub 2019 Apr 19.

MeSH Terms

Conditions

AnemiaKidney Failure, Chronic

Interventions

NOX-H94

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic DiseasesRenal Insufficiency, ChronicRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Kai Riecke, MD

    TME Pharma AG

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 28, 2014

First Posted

March 6, 2014

Study Start

May 1, 2014

Primary Completion

November 1, 2015

Study Completion

November 1, 2015

Last Updated

November 24, 2015

Record last verified: 2015-11

Locations