NCT02057211

Brief Summary

This project aims to evaluate the efficacy of autologous mesenchymal stem cell treatment to preserve insulin production and beta-cell mass in recently diagnosed patients with type 1 diabetes mellitus. The hypothesis to be tested is that an increased number of circulating mesenchymal stem cells will provide immune modulatory properties, and thereby stop the immune process in islets causing progressive beta-cell death.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Apr 2014

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 4, 2014

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 7, 2014

Completed
2 months until next milestone

Study Start

First participant enrolled

April 1, 2014

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2017

Completed
Last Updated

November 6, 2020

Status Verified

November 1, 2020

Enrollment Period

3.6 years

First QC Date

February 4, 2014

Last Update Submit

November 4, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • ∆-change of C-peptide Area Under the Curve (AUC) (0-120 min) for a mixed meal tolerance test at two year follow-up when compared to pre-treatment values at enrolment.

    ∆-change will be assessed as a difference between two years after transplantation/sham transplantation of mesenchymal stem cells when compared to before transplantation/sham transplantation, i.e. at time 0.

Study Arms (2)

sham transplantation of mesenchymal stem cells

PLACEBO COMPARATOR

control arm with sham transplantation

Procedure: sham transplantation of mesenchymal stem cells

autologous mesenchymal stem cell transplantation

ACTIVE COMPARATOR

Active arm with transplantation of cells

Biological: autologous mesenchymal stem cell transplantation

Interventions

autologous mesenchymal stem cell transplantation

Placebo control for transplantation of mesenchymal stem cells

sham transplantation of mesenchymal stem cells

Eligibility Criteria

Age18 Years - 40 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • fasting C-peptide \>0.12 nmol/l
  • within three weeks of diagnosis of type 1 diabetes

You may not qualify if:

  • body mass index (BMI) \>30
  • unstable cardiovascular status incl. New York Heart Association (NYHA) class III/IV
  • patients with known or previous malignancy
  • active infections incl. serological evidence of infection with HIV, Treponema pallidum, hepatitis B (patients with serology consistent with previous vaccination and a history of vaccination are acceptable) or hepatitis C.
  • immune suppressive treatment
  • women being pregnant or nursing, or women physiologically capable of becoming pregnant, unless they are using effective methods of contraception during study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Uppsala University Hospital

Uppsala, SE-75185, Sweden

Location

MeSH Terms

Conditions

Diabetes Mellitus, Type 1

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Per-Ola Carlsson, MD, PhD

    Uppsala University Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

February 4, 2014

First Posted

February 7, 2014

Study Start

April 1, 2014

Primary Completion

November 1, 2017

Study Completion

November 1, 2017

Last Updated

November 6, 2020

Record last verified: 2020-11

Locations