NCT02022540

Brief Summary

The objective of this study is to assess the safety and tolerability of topical ocular PAN-90806 in patients with active, subfoveal choroidal neovascularization associated with neovascular Age-Related Macular Degeneration (AMD).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Feb 2014

Typical duration for phase_1

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 20, 2013

Completed
7 days until next milestone

First Posted

Study publicly available on registry

December 27, 2013

Completed
1 month until next milestone

Study Start

First participant enrolled

February 1, 2014

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2016

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2016

Completed
Last Updated

September 28, 2016

Status Verified

September 1, 2016

Enrollment Period

2.1 years

First QC Date

December 20, 2013

Last Update Submit

September 27, 2016

Conditions

Keywords

Neovascular Age-Related Macular DegenerationAMDMacular DegenerationAge-Related Macular Degenerationwet AMDneovascular AMDexudative AMD

Outcome Measures

Primary Outcomes (1)

  • Safety

    Presence of any targeted adverse events (TAEs); safety endpoints include adverse events, vital signs, laboratory abnormalities, ophthalmic findings and outcomes

    3 months

Study Arms (6)

Stage 1 - Group 1

EXPERIMENTAL

Patients randomized to Group 1 will receive PAN-90806 Ophthalmic Solution daily for 8 weeks.

Drug: PAN-90806 Ophthalmic Solution

Stage 1 - Group 2

EXPERIMENTAL

Patients randomized to Group 2 will receive PAN-90806 Ophthalmic Solution daily for 8 weeks.

Drug: PAN-90806 Ophthalmic Solution

Stage 1- Group 3

EXPERIMENTAL

Patients randomized to Group 3 will receive PAN-90806 Ophthalmic Solution daily for 8 weeks.

Drug: PAN-90806 Ophthalmic Solution

Stage 1- Group 4

EXPERIMENTAL

Patients randomized to Group 4 will receive PAN-90806 Ophthalmic Solution daily for 8 weeks.

Drug: PAN-90806 Ophthalmic Solution

Stage 1 - Group 5

EXPERIMENTAL

Patients randomized to Group 5 will receive PAN-90806 Ophthalmic Solution daily for 8 weeks.

Drug: PAN-90806 Ophthalmic Solution

Stage 2

EXPERIMENTAL

Patients enrolled in Stage 2 will receive an intravitreal injection of ranibizumab and then 7-9 days later begin daily dosing with PAN-90806 Ophthalmic Solution for 12 weeks

Drug: PAN-90806 Ophthalmic SolutionDrug: Lucentis

Interventions

Also known as: PAN-90806 Eye Drops
Stage 1 - Group 1Stage 1 - Group 2Stage 1 - Group 5Stage 1- Group 3Stage 1- Group 4Stage 2
Also known as: ranibizumab
Stage 2

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis in the study eye of active, pathologic, newly diagnosed and previously untreated, subfoveal choroidal neovascular (CNV) lesions secondary to neovascular AMD
  • Aged 50 years or older
  • Demonstrate the ability, or have a family member who is willing and able, to instill topical ocular drops in the study eye

You may not qualify if:

  • No prior ocular or systemic treatment or surgery for neovascular AMD in the study eye
  • History of or current clinical evidence in the study eye of:
  • aphakia
  • diabetic macular edema
  • any ocular inflammation or infections
  • pathological myopia
  • retinal detachment
  • advanced glaucoma
  • significant media opacity, including cataract
  • History or evidence of the following surgeries in the study eye:
  • penetrating keratoplasty or vitrectomy;
  • corneal transplant;
  • corneal or intraocular surgery within 3 months of Screening
  • Uncontrolled hypertension despite use of antihypertensive medications
  • Participation in any investigational drug or device study, systemic or ocular, within past 3 months
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Unknown Facility

Colorado Springs, Colorado, United States

Location

Unknown Facility

Winter Haven, Florida, United States

Location

Unknown Facility

Shawnee Mission, Kansas, United States

Location

Unknown Facility

Wichita, Kansas, United States

Location

Unknown Facility

Boston, Massachusetts, United States

Location

Unknown Facility

Portsmouth, New Hampshire, United States

Location

Unknown Facility

Bloomfield, New Jersey, United States

Location

Unknown Facility

Charlotte, North Carolina, United States

Location

Unknown Facility

Durham, North Carolina, United States

Location

Unknown Facility

Statesville, North Carolina, United States

Location

Unknown Facility

Ashland, Oregon, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, United States

Location

Unknown Facility

West Columbia, South Carolina, United States

Location

Unknown Facility

Rapid City, South Dakota, United States

Location

Unknown Facility

Nashville, Tennessee, United States

Location

Unknown Facility

Abilene, Texas, United States

Location

Unknown Facility

Austin, Texas, United States

Location

Unknown Facility

Harlingen, Texas, United States

Location

Unknown Facility

McAllen, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Unknown Facility

Willow Park, Texas, United States

Location

Unknown Facility

Madison, Wisconsin, United States

Location

MeSH Terms

Conditions

Macular Degeneration

Interventions

Ranibizumab

Condition Hierarchy (Ancestors)

Retinal DegenerationRetinal DiseasesEye Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Martin Wax, M.D.

    PanOptica, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 20, 2013

First Posted

December 27, 2013

Study Start

February 1, 2014

Primary Completion

March 1, 2016

Study Completion

May 1, 2016

Last Updated

September 28, 2016

Record last verified: 2016-09

Locations