NCT01997437

Brief Summary

The proposed protocol will involve the replacement of the trachea using a synthetic bioengineered scaffold seeded with autologous mononuclear cells as an intraoperative solution for patients with with benign and malignant laryngo-tracheal diseases or other terminal conditions of the trachea. Tracheal transplant is indicated as the only therapeutic alternative in cases where instrumental, endoscopic and other evaluations show that the length of residual healthy airways (about 6 cm or longer than 50% of the airway length) and the localization and extension of the obstruction make it impossible to perform a surgical resection of the pathological segment. In addition to tracheal surgical transplant techniques, this protocol requires knowledge and experience with autologous cell preparation as well as scaffold seeding procedures.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
6

participants targeted

Target at below P25 for not_applicable

Timeline
Completed

Started Dec 2013

Typical duration for not_applicable

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 5, 2013

Completed
23 days until next milestone

First Posted

Study publicly available on registry

November 28, 2013

Completed
3 days until next milestone

Study Start

First participant enrolled

December 1, 2013

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

May 22, 2015

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2016

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2016

Completed
Last Updated

March 7, 2016

Status Verified

January 1, 2016

Enrollment Period

2.8 years

First QC Date

November 5, 2013

Results QC Date

January 3, 2014

Last Update Submit

January 25, 2016

Conditions

Keywords

Tissue-engineered tracheal transplantation

Outcome Measures

Primary Outcomes (2)

  • Safety of Stem-cell Seeded Bioartificial Tracheal Scaffold

    Safety of the tissue engineered trachea measured by occurrence of adverse events throughout 12 months post operative follow up

    12 months post operative follow up

  • Number of Mononuclear Cells (MNCs) Per ml

    MNCs were isolated from bone marrow fom each patient, and were counted by flow cytometry method. MNC were used for seeding on scaffold.

    1 time before seeding on scaffold

Secondary Outcomes (2)

  • Number of Survival Patients

    12 months post operative follow up

  • Number of Disease Free Survival Patients

    12 months post operative follow up

Study Arms (1)

Tissue-engineered airway transplantation

OTHER

Stem-cell seeded bioartificial tracheal scaffold

Device: Stem-cell seeded bioartificial tracheal scaffold

Interventions

Seeding the synthetic scaffold with autologous stem cells; scaffold' cultivation within 48-72 hours in bioreactor, injection of growth factors into scaffold in the first and last stages of the cultivation, replacement of the damaged trachea by generated tissue-engineered organ

Tissue-engineered airway transplantation

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Extended (\> 60% total length) benign and malignant diseases
  • Already maximally pretreated patients
  • No absolute surgical contraindications
  • No regional and/or micro-metastasis (BMB proven)
  • Normal psychological or psychiatric habitus
  • IRB, Ethics and National Transplant clearance
  • Written informed consent

You may not qualify if:

  • Presence of systemic metastatic lesions and positive mediastinal lymph nodes (malignancies);
  • Routine functional and psychological contraindication

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Clinical Regional Hospital #1

Krasnodar, 350029, Russia

Location

Related Publications (1)

  • Jungebluth, P, Alici, E, Baiguera S, et al. Tracheobronchial transplantation with a stem-cell-seeded bioartificial nanocomposite: a proof-of-concept study. Lancet 2011 Dec 10; 378 (9808):1997-2004; Macchiarini P, Jungebluth P, Go T, et al. Clinical transplantation of a tissue-engineered airway. Lancet 2008; 372, 2023-3030; Acocella F, Brizzola S, et al. Prefabricated tracheal prosthesis with partial biodegradable materials: a surgical and tissue engineering evaluation in vivo. Journal of Biomaterials Science; Polymer Edition 2007; 18(5):579-594; Bader A, Macchiarini P. Moving towards in situ tracheal regeneration: the bionic tissue engineered transplantation approach. J Cell Mol Med 2010; 14(7):1877-89; Jungebluth P, Moll G, Baiguera S, Macchiarini P. Tissue engineered airway: a regenerative solution. Clin Pharm Ther 2012; 91:81-93;

    BACKGROUND

Related Links

MeSH Terms

Conditions

Tracheal Diseases

Condition Hierarchy (Ancestors)

Respiratory Tract Diseases

Results Point of Contact

Title
Dr. Paolo Macchiarini
Organization
Kuban State Medical University

Study Officials

  • Paolo Macchiarini, MD, PhD

    Kuban State Medical University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 5, 2013

First Posted

November 28, 2013

Study Start

December 1, 2013

Primary Completion

September 1, 2016

Study Completion

December 1, 2016

Last Updated

March 7, 2016

Results First Posted

May 22, 2015

Record last verified: 2016-01

Locations