NCT01994993

Brief Summary

The main purpose of this study is evaluate whether it is safe or not to use various combination of antibiotics (ampicillin, metronidazole, clindamycin, piperacillin-tazobactam, gentamicin) in treating infants with complicated intra-abdominal infections

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
260

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Dec 2013

Typical duration for phase_2

Geographic Reach
2 countries

50 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 18, 2013

Completed
8 days until next milestone

First Posted

Study publicly available on registry

November 26, 2013

Completed
5 days until next milestone

Study Start

First participant enrolled

December 1, 2013

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 15, 2017

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 20, 2017

Completed
10 months until next milestone

Results Posted

Study results publicly available

February 27, 2018

Completed
Last Updated

May 30, 2019

Status Verified

May 1, 2019

Enrollment Period

3.1 years

First QC Date

November 18, 2013

Results QC Date

January 15, 2018

Last Update Submit

May 28, 2019

Conditions

Keywords

Antibioticsampicillinmetronidazoleclindamycinpiperacillin-tazobactamSafetyInfantsIntra abdominal infections

Outcome Measures

Primary Outcomes (1)

  • Death

    Number of Participants who experienced Death

    Within 30 days after last dose of study drug, up to 40 days

Secondary Outcomes (1)

  • Number of Participants With Therapeutic Success at Day 30

    30 days after last dose of study drug

Other Outcomes (9)

  • Number of Participants With Feeding Intolerance

    90 days after last dose of study drug

  • Number of Participants With Grade 3 and/or Grade 4 Intraventricular Hemorrhage (IVH)

    90 days after last dose of study drug

  • Number of Participants With Short Bowel Syndrome

    90 days after last dose of study drug

  • +6 more other outcomes

Study Arms (5)

Group 1 (ampicillin +gentamycin +metronidazole)

ACTIVE COMPARATOR

Ampicillin and gentamycin and metronidazole

Drug: ampicillin and metronidazole and gentamicin

Group 2 (ampicillin +gentamicin+clindamycin)

ACTIVE COMPARATOR

ampicillin and gentamicin and clindamycin

Drug: ampicillin and gentamicin and clindamycin

Group 3 (piperacillin-tazobactam and gentamicin)

ACTIVE COMPARATOR

piperacillin-tazobactam and gentamicin

Drug: gentamicin and Piperacillin- tazobactam

Group 4 (metronidazole)

ACTIVE COMPARATOR

Per standard of care antibiotics, and Metronidazole

Drug: standard of care antibiotics and metronidazole

Group 5 (metronidazole/clindamycin/piperacillin-tazobactam)

ACTIVE COMPARATOR

metronidazole, clindamycin, or piperacillin-tazobactam

Drug: metronidazole, clindamycin, or piperacillin-tazobactam

Interventions

IV infusion of ampicillin and metronidazole and gentamicin for a total of 10 days. Dose based on postnatal age (PNA) and gestational age(GA)

Group 1 (ampicillin +gentamycin +metronidazole)

IV infusion of ampicillin and gentamicin and clindamycin for a total of 10 days. Dose based on postnatal age (PNA) and gestational age(GA)

Group 2 (ampicillin +gentamicin+clindamycin)

IV infusion of gentamicin and Piperacillin- tazobactam for a total of 10 days. Dose based on postnatal age (PNA) and gestational age(GA)

Group 3 (piperacillin-tazobactam and gentamicin)

IV infusion of standard of care antibiotics and metronidazole for a total of 10 days. Dose based on postnatal age (PNA) and gestational age(GA)

Group 4 (metronidazole)

IV infusion of metronidazole, clindamycin, or piperacillin-tazobactam with scheduled CSF procedures per standard of care. Study drug will be given for for a total of 10 days. Dose based on postnatal age (PNA) and gestational age(GA)

Group 5 (metronidazole/clindamycin/piperacillin-tazobactam)

Eligibility Criteria

AgeUp to 120 Days
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Informed consent obtained from parent(s) or legal guardian(s) (Groups 1-5)
  • ≤33 weeks gestation at birth (Groups 1-3, 5)
  • ≥34 weeks gestation at birth (Groups 4 and 5)
  • PNA \<121 days (Groups 1-5)
  • Sufficient venous access to permit administration of study drug (intravenous \[IV\]) (Groups 1-5)
  • Presenting physical, radiological, and/or bacteriological findings of a complicated intra-abdominal infection within 48 hours prior to randomization/first study drug dose (Groups 1-4)\*\*. Complicated intra-abdominal infections include secondary peritonitis, NEC grade II or higher by Bell's criteria, Hirschsprung's disease with perforation, spontaneous intestinal perforation, meconium ileus with perforation, bowel obstruction with perforation, gastroschisis with necrosis and/or perforation, omphalocele with necrosis and/or perforation, neonatal appendicitis, intestinal pneumatosis or portal venous gas, free peritoneal air on abdominal radiographic examination, or abdominal abscess.
  • Suspected or confirmed infection for which the study drug may provide therapeutic benefit and planned CSF collection per standard of care (Group 5).

You may not qualify if:

  • History of anaphylaxis in response to study drugs (Groups 1-5)
  • Serum creatinine \>2 mg/dL within 48 hours on measurement prior to and closest to randomization /first study drug dose (Groups 1- 5)\*\*
  • Known ALT \>250 U/L or AST \>500 U/L on measurement closest to the time of randomization or first study drug dose (Groups 1-5)\*\*
  • Any condition that, in the judgment of the investigator, precludes participation because it could affect participant safety (Groups 1-5)
  • Do not apply for Group 5 participants receiving drug per standard of care
  • Criteria must be satisfied by randomization (randomized Groups 1-3) or first study drug dose (non-randomized Groups 1-3, Group 4 and Group 5), whichever comes first.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (50)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Arkansas Children's Hospital/Univ of Arkansas for Medical Sciences

Little Rock, Arkansas, 72202, United States

Location

Loma Linda University Medical Center

Loma Linda, California, 92354, United States

Location

Stanford University School of Medicine

Palo Alto, California, 94304, United States

Location

Rady Children's Hospital and Health Center

San Diego, California, 92123, United States

Location

University of California San Diego Medical Center

San Diego, California, 92123, United States

Location

Sharp Mary Birch

San Diego, California, 92131, United States

Location

Connecticut Children's Medical Center

Hartford, Connecticut, 06106, United States

Location

University of Florida Jacksonville Healthcare, Inc.

Jacksonville, Florida, 32209, United States

Location

Wolfson Children's Hospital, Shands Medical Center

Jacksonville, Florida, 32209, United States

Location

Georgia Regents University

Augusta, Georgia, 30912, United States

Location

Kapiolani Medical Center for Women and Children

Honolulu, Hawaii, 96826, United States

Location

Riley Hospital

Indianapolis, Indiana, 46202, United States

Location

Wesley Medical Center

Wichita, Kansas, 67214, United States

Location

University of Kentucky Hospital

Lexington, Kentucky, 40536, United States

Location

Louisana State University Health Sciences Center

Shreveport, Louisiana, 71103, United States

Location

University of Maryland Hospital

Baltimore, Maryland, 21201, United States

Location

Floating Hospital for Children at Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

University of Minnesota Fairview University Medical Center

Minneapolis, Minnesota, 55455, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Kings County Hospital

Brooklyn, New York, 11203, United States

Location

Brookdale University Hospital

Brooklyn, New York, 11212, United States

Location

New York University School of Medicine

New York, New York, 10016, United States

Location

Columbia University Neonatology

New York, New York, 10032, United States

Location

Westchester Medical Center - New York Medical College

Valhalla, New York, 10595, United States

Location

University of North Carolina Hospital

Chapel Hill, North Carolina, 27514, United States

Location

Levine Children's Hospital

Charlotte, North Carolina, 28232, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

East Carolina University

Greenville, North Carolina, 27834, United States

Location

WakeMed Faculty Neonatology

Raleigh, North Carolina, 27610, United States

Location

New Hanover Reginal Medical Center

Wilmington, North Carolina, 28403, United States

Location

Wake Forest University School of Medicine

Winston-Salem, North Carolina, 27157, United States

Location

Cincinnati Children's Hospital

Cincinnati, Ohio, 45229, United States

Location

Rainbow Babies and Children's Hospital

Cleveland, Ohio, 44106, United States

Location

University of Oklahoma Health Science Center

Oklahoma City, Oklahoma, 73104, United States

Location

Penn State Hershey Children's Hospital

Hershey, Pennsylvania, 17033, United States

Location

Womens and Infant Hospital of Rhode Island

Providence, Rhode Island, 02905, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Vanderbilt University

Nashville, Tennessee, 37232, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

Intermountain Medical Center

Salt Lake City, Utah, 84108, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

University of Virginia Health System

Charlottesville, Virginia, 22908, United States

Location

Carilion Roanoke Memorial Hospital

Roanoke, Virginia, 24014, United States

Location

University of Alberta - Royal Alexandra Hospital

Edmonton, Alberta, T5H 3V9, Canada

Location

University of British Columbia - British Columbia Women's Hospital

Vancouver, British Columbia, V6H 3V4, Canada

Location

Manitoba Institute of Child Health

Winnipeg, Manitoba, R3P 2C1, Canada

Location

Children's Hospital of Eastern Ontario

Ottawa, Ontario, K1H 8L1, Canada

Location

Hospital Sainte-Justine

Montreal, Quebec, T3T 1C5, Canada

Location

Related Publications (1)

  • Smith MJ, Boutzoukas A, Autmizguine J, Hudak ML, Zinkhan E, Bloom BT, Heresi G, Lavery AP, Courtney SE, Sokol GM, Cotten CM, Bliss JM, Mendley S, Bendel C, Dammann CEL, Weitkamp JH, Saxonhouse MA, Mundakel GT, Debski J, Sharma G, Erinjeri J, Gao J, Benjamin DK Jr, Hornik CP, Smith PB, Cohen-Wolkowiez M; Best Pharmaceuticals for Children Act-Pediatric Trials Network Steering Committee. Antibiotic Safety and Effectiveness in Premature Infants With Complicated Intraabdominal Infections. Pediatr Infect Dis J. 2021 Jun 1;40(6):550-555. doi: 10.1097/INF.0000000000003034.

MeSH Terms

Conditions

Intraabdominal Infections

Interventions

AmpicillinMetronidazoleGentamicinsClindamycinPiperacillin, Tazobactam Drug Combination

Condition Hierarchy (Ancestors)

Infections

Intervention Hierarchy (Ancestors)

Penicillin GPenicillinsbeta-LactamsLactamsAmidesOrganic ChemicalsSulfur CompoundsHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsNitroimidazolesNitro CompoundsImidazolesAzolesHeterocyclic Compounds, 1-RingAminoglycosidesGlycosidesCarbohydratesLincomycinLincosamidesPyrrolidinesTazobactamPenicillanic AcidPiperacillinSulfonesDrug CombinationsPharmaceutical Preparations

Results Point of Contact

Title
Michael Cohen-Wolkowiez, M.D
Organization
Duke University Medical Center

Study Officials

  • Micheal Cohen-Wolkowiez, MD, PhD

    Duke University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR INVESTIGATOR
PI Title
Associate Professor

Study Record Dates

First Submitted

November 18, 2013

First Posted

November 26, 2013

Study Start

December 1, 2013

Primary Completion

January 15, 2017

Study Completion

April 20, 2017

Last Updated

May 30, 2019

Results First Posted

February 27, 2018

Record last verified: 2019-05

Locations