NCT01994109

Brief Summary

This study will evaluate the efficacy and safety of MYOBLOC in the treatment of Sialorrhea (drooling), which can be a symptom of many disease conditions. MYOBLOC will be injected directly into the salivary glands. MYOBLOC has been shown in previous trials to safely decrease saliva production, thereby demonstrating its potential as a safe and effective treatment for troublesome sialorrhea.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
187

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Nov 2013

Typical duration for phase_3

Geographic Reach
3 countries

34 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2013

Completed
13 days until next milestone

First Submitted

Initial submission to the registry

November 14, 2013

Completed
11 days until next milestone

First Posted

Study publicly available on registry

November 25, 2013

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2016

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2017

Completed
2.6 years until next milestone

Results Posted

Study results publicly available

August 15, 2019

Completed
Last Updated

April 21, 2026

Status Verified

March 1, 2026

Enrollment Period

2.2 years

First QC Date

November 14, 2013

Results QC Date

May 2, 2019

Last Update Submit

March 31, 2026

Conditions

Keywords

SialorrheaParkinson's diseaseAmyotrophic lateral sclerosis (ALS)strokeneuroleptics

Outcome Measures

Primary Outcomes (2)

  • Unstimulated Salivary Flow Rate (USFR) at Week 4 Post-injection Visit (Part A)

    Change weight of expectorated saliva at a Week 4 post-injection visit.

    4 Weeks

  • Clinical Global Impression Change (CGI-C) at Week 4 Post-injection (Part A)

    CGI-C was assessed on a 7-point scale ranging from "very much improved" to "very much worse" with 1 assigned to "very much improved" and 7 assigned to "very much worse"; ranging from a minimum score of 1 and a maximum score of 7.

    4 weeks

Study Arms (3)

MYOBLOC 2500 U

ACTIVE COMPARATOR

Subjects will receive specified dose of MYOBLOC

Drug: MYOBLOC

MYOBLOC 3500 U

ACTIVE COMPARATOR

Subjects will receive specified dose of MYOBLOC

Drug: MYOBLOC

Placebo

PLACEBO COMPARATOR

Subjects will receive volume matched Placebo

Other: PLACEBO

Interventions

MYOBLOC (rimabotulinumtoxinB) Injection, or botulinum toxin type B, is the "B" serotype of botulinum toxin. It is the only commercially available "B" serotype, and also the only available botulinum toxin that does not require reconstitution for use.

Also known as: rimabotulinumtoxinB, botulinum toxin type B
MYOBLOC 2500 UMYOBLOC 3500 U
PLACEBOOTHER
Also known as: volume-matched placebo
Placebo

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Seeking treatment for troublesome sialorrhea for at least 3 months that is occurring secondary to any disorder or related to any cause

You may not qualify if:

  • Any known prior exposure to botulinum toxin type B, or known adverse reaction or sensitivity to botulinum toxin type A, or known sensitivity to any of the MYOBLOC solution components.
  • Prior botulinum toxin treatment to the salivary glands at any time

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (34)

Unknown Facility

Loma Linda, California, 92354, United States

Location

Unknown Facility

Los Angeles, California, 90033, United States

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Unknown Facility

National City, California, 91950, United States

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Unknown Facility

Aurora, Colorado, 80045, United States

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Unknown Facility

Washington D.C., District of Columbia, 20007, United States

Location

Unknown Facility

Boca Raton, Florida, 33486, United States

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Unknown Facility

Port Charlotte, Florida, 33980, United States

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Unknown Facility

Carmel, Indiana, 46032, United States

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Unknown Facility

Baltimore, Maryland, 21287, United States

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Unknown Facility

Elkridge, Maryland, 21075, United States

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Unknown Facility

Detroit, Michigan, 48334, United States

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Unknown Facility

St Louis, Missouri, 63110, United States

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Unknown Facility

Edison, New Jersey, 08818, United States

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Unknown Facility

Albany, New York, 12208, United States

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Unknown Facility

New York, New York, 10003, United States

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Unknown Facility

Cincinnati, Ohio, 45219, United States

Location

Unknown Facility

Tulsa, Oklahoma, 74136, United States

Location

Unknown Facility

Port Royal, South Carolina, 29935, United States

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Unknown Facility

Cordova, Tennessee, 38018, United States

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Unknown Facility

Houston, Texas, 77030, United States

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Unknown Facility

San Antonio, Texas, 78229, United States

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Unknown Facility

Salt Lake City, Utah, 84132, United States

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Unknown Facility

Kirkland, Washington, 98034, United States

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Unknown Facility

Tacoma, Washington, 98409, United States

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Unknown Facility

Irkutsk, Irkutsk Oblast, 664079, Russia

Location

Unknown Facility

Vsevolozhsk, Leningradskaya Oblast', 188643, Russia

Location

Unknown Facility

Saint Petersburg, Petrodvorets, 198510, Russia

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Unknown Facility

Krasnoyarsk, 660037, Russia

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Unknown Facility

Dnipropetrovsk, 49027, Ukraine

Location

Unknown Facility

Ivano-Frankivsk, 76008, Ukraine

Location

Unknown Facility

Kharkiv, 61068, Ukraine

Location

Unknown Facility

Lviv, 79010, Ukraine

Location

Unknown Facility

Rivne, 33010, Ukraine

Location

Unknown Facility

Uzhhorod, 88018, Ukraine

Location

Related Publications (3)

  • Chinnapongse R, Gullo K, Nemeth P, Zhang Y, Griggs L. Safety and efficacy of botulinum toxin type B for treatment of sialorrhea in Parkinson's disease: a prospective double-blind trial. Mov Disord. 2012 Feb;27(2):219-26. doi: 10.1002/mds.23929. Epub 2011 Sep 1.

  • Ondo WG, Hunter C, Moore W. A double-blind placebo-controlled trial of botulinum toxin B for sialorrhea in Parkinson's disease. Neurology. 2004 Jan 13;62(1):37-40. doi: 10.1212/01.wnl.0000101713.81253.4c.

  • Isaacson SH, Ondo W, Jackson CE, Trosch RM, Molho E, Pagan F, Lew M, Dashtipour K, Clinch T, Espay AJ; MYSTICOL Study Group. Safety and Efficacy of RimabotulinumtoxinB for Treatment of Sialorrhea in Adults: A Randomized Clinical Trial. JAMA Neurol. 2020 Apr 1;77(4):461-469. doi: 10.1001/jamaneurol.2019.4565.

MeSH Terms

Conditions

SialorrheaParkinson DiseaseAmyotrophic Lateral SclerosisStroke

Interventions

rimabotulinumtoxinB

Condition Hierarchy (Ancestors)

Salivary Gland DiseasesMouth DiseasesStomatognathic DiseasesParkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative DiseasesSpinal Cord DiseasesMotor Neuron DiseaseTDP-43 ProteinopathiesNeuromuscular DiseasesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic DiseasesCerebrovascular DisordersVascular DiseasesCardiovascular Diseases

Results Point of Contact

Title
Regulatory Affairs Associate
Organization
Solstice Neurosciences

Study Officials

  • Jonathan Rubin, MD

    Supernus Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 14, 2013

First Posted

November 25, 2013

Study Start

November 1, 2013

Primary Completion

January 1, 2016

Study Completion

January 1, 2017

Last Updated

April 21, 2026

Results First Posted

August 15, 2019

Record last verified: 2026-03

Locations