NCT01893138

Brief Summary

This randomized, double-blind, placebo-controlled, multicenter, confirmatory study will evaluate the efficacy and safety of Cook MyoSite Incorporated Autologous Muscle-Derived Cells (generic name Iltamiocel) compared to a placebo (vehicle) control dose in the treatment of stress urinary incontinence (SUI) in adult female patients.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
311

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Nov 2013

Longer than P75 for phase_3

Geographic Reach
3 countries

29 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 2, 2013

Completed
6 days until next milestone

First Posted

Study publicly available on registry

July 8, 2013

Completed
5 months until next milestone

Study Start

First participant enrolled

November 21, 2013

Completed
5.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2019

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

November 10, 2020

Completed
2.2 years until next milestone

Results Posted

Study results publicly available

January 5, 2023

Completed
Last Updated

January 5, 2023

Status Verified

December 1, 2022

Enrollment Period

5.9 years

First QC Date

July 2, 2013

Results QC Date

September 12, 2022

Last Update Submit

December 12, 2022

Conditions

Keywords

Urinary Incontinence, StressTissue Therapy (Cell Therapy)Transplantation, Autologous

Outcome Measures

Primary Outcomes (1)

  • Participants With ≥ 50% Reduction in Stress Incontinence Episode Frequency From Baseline to 12 Months Post-treatment; as Assessed by 3 Day Diary

    Baseline and 12 months

Secondary Outcomes (3)

  • Participants With at ≥ 75% Reduction in Stress Incontinence Episodes From Baseline at 12 Months

    Baseline and 12 months

  • Participants With 0 or 1 Stress Incontinence Episodes Based on 3 Day Diary Records at 12 Months

    Baseline and 12 months

  • Change in the Frequency of Stress Incontinence Episodes From Baseline at 12 Months

    Baseline and 12 months

Other Outcomes (2)

  • Association of Change in Quality of Life Scores With Change in Stress Incontinence Episode Frequency

    Baseline and 12 months

  • Treatment Durability at 24 Months

    Baseline, 12 months, and 24 months after injection with iltamiocel

Study Arms (2)

Placebo

PLACEBO COMPARATOR

Placebo control is the vehicle solution used for the study product.

Other: Placebo

Iltamiocel

EXPERIMENTAL

AMDC is the study product (autologous muscle-derived cells). The generic name is iltamiocel. Single intraurethral injection of 150 x 10\^6 cells.

Biological: Iltamiocel

Interventions

PlaceboOTHER

Placebo control is the vehicle solution used for the study product.

Placebo
IltamiocelBIOLOGICAL

AMDC is the study product (autologous muscle-derived cells). The generic name is iltamiocel. Single intraurethral injection of 150 x 10\^6 cells.

Also known as: Autologous muscle-derived cells (AMDC)
Iltamiocel

Eligibility Criteria

Age18 Years+
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Female patient has primary symptoms of SUI, as confirmed by patient medical history and clinical symptoms, including a focused incontinence evaluation.

You may not qualify if:

  • Patient has symptoms of pure urge incontinence as confirmed by basic evaluation of etiology from a patient medical history, including a focused incontinence history.
  • Patient has symptoms of mixed urinary incontinence where urge incontinence is the predominant factor.
  • Patient has had stress urinary incontinence symptoms less than 6 months prior to signing the informed consent.
  • Patient has not previously attempted conservative treatment prior to signing the informed consent. (Examples of conservative treatment include behavior modifications, bladder exercises, biofeedback, etc.)
  • Patient has more than 2 episode of awakening to void during normal sleeping hours.
  • Patient cannot be maintained on a stable dose and/or frequency of medication (including diuretics) known to affect lower urinary tract function, including but not limited to, anticholinergics, tricyclic antidepressants or alpha-adrenergic blockers, for at least 2 weeks prior to screening or is likely to change during the course of the study.
  • Patient is pregnant, lactating, or plans to become pregnant during the course of the study.
  • Patient refuses to provide written informed consent.
  • Patient is not at least 18 years of age.
  • Patient is not available for the follow-up evaluations as required by the protocol.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

Mayo Clinic Arizona Phoenix Campus

Phoenix, Arizona, 85054, United States

Location

The American Association of Female Pelvic Medicine Specialists

Agoura Hills, California, 91301, United States

Location

Ronald Reagan UCLA Medical Center

Los Angeles, California, 90024, United States

Location

Stanford University

Stanford, California, 94304, United States

Location

Cleveland Clinic Florida

Weston, Florida, 33331, United States

Location

Emory University

Atlanta, Georgia, 30033, United States

Location

NorthShore University HealthSystem

Skokie, Illinois, 60076, United States

Location

IU Health Physicians Urogynecology

Indianapolis, Indiana, 46202, United States

Location

Female Pelvic Medicine & Urogynecology Institute of Michigan

Grand Rapids, Michigan, 49503, United States

Location

Mercy Health Saint Mary's Campus

Grand Rapids, Michigan, 49503, United States

Location

William Beaumont Hospital

Royal Oak, Michigan, 48073, United States

Location

NYU Urology Associates

New York, New York, 10016, United States

Location

Premier Medical Group of the Hudson Valley PC

Poughkeepsie, New York, 12601, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

McKay Urology

Charlotte, North Carolina, 28207, United States

Location

The Carl and Edyth Lindner Center for Research and Education at The Christ Hospital

Cincinnati, Ohio, 45242, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Greenville Health System

Greenville, South Carolina, 29607, United States

Location

Sanford Female Pelvic Medicine and Reconstructive Surgery Clinic

Sioux Falls, South Dakota, 57105, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Methodist Urology Associates

Houston, Texas, 77030, United States

Location

Inova Fairfax Hospital

Falls Church, Virginia, 22042, United States

Location

Benaroya Research Institute at Virginia Mason

Seattle, Washington, 98101, United States

Location

University Hospital Leuven

Leuven, 3000, Belgium

Location

Universitätsklinikum Essen

Essen, 45147, Germany

Location

Praxisklinik Urologie Rhein-Ruhr (PUR/R)

Mülheim, 45468, Germany

Location

Related Publications (2)

  • Kaufman MR, Goldman HB, Chermansky CJ, Dmochowski R, Kennelly MJ, Peters KM, Quiroz LH, Bennett JB, Thomas S, Marguet CG, Benson KD, Lee UJ, Sokol ER, Wolter CE, Katz DM, Tarnay CM, Antosh D, Heit MH, Rehme C, Karram M, Snyder S, Canestrari E, Jankowski RJ, Chancellor MB. Iltamiocel Autologous Cell Therapy for the Treatment of Female Stress Urinary Incontinence: A Double-Blind, Randomized, Stratified, Placebo-Controlled Trial. Neurourol Urodyn. 2024 Nov;43(8):2290-2299. doi: 10.1002/nau.25588. Epub 2024 Sep 16.

  • Antosh DD, High R, Brown HW, Oliphant SS, Abed H, Philip N, Grimes CL. Feasibility of prophylactic salpingectomy during vaginal hysterectomy. Am J Obstet Gynecol. 2017 Nov;217(5):605.e1-605.e5. doi: 10.1016/j.ajog.2017.07.017. Epub 2017 Jul 20.

MeSH Terms

Conditions

Urinary Incontinence, Stress

Condition Hierarchy (Ancestors)

Urinary IncontinenceUrination DisordersUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesLower Urinary Tract SymptomsUrological ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Ron Jankowski, PhD
Organization
Cook MyoSite, Inc.

Study Officials

  • Melissa Kaufman, M.D., Ph.D.

    Vanderbilt University Medical Center, Department of Urologic Surgery

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 2, 2013

First Posted

July 8, 2013

Study Start

November 21, 2013

Primary Completion

November 1, 2019

Study Completion

November 10, 2020

Last Updated

January 5, 2023

Results First Posted

January 5, 2023

Record last verified: 2022-12

Data Sharing

IPD Sharing
Will not share

Locations